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C.D. reports no disclosures. M.St. reports no disclosures. R.S. reports no disclosures. L.S. received consultancy honoraria from Vico Therapeutics and Novartis unrelated to the present manuscript. T.H. reports no disclosures. M.Sy. has received consultancy honoraria from Janssen, Ionis, Orphazyme, Servier, Reata, GenOrph, and AviadoBio, all unrelated to the present manuscript.","order":2,"name":"Ethics","group":{"name":"EthicsHeading","label":"Conflict of interest"}}]}}