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AG has received consulting fees for Ipsen, Sanofi and Theravia.\u00a0MM has received support for attending meetings and\/or travel from CSL-Behring and Roche and has served on advisory boards for Johnson&Johnson and Roche. PL has received research grants, consulting fees, speaker\u2019s honoraria, support for attending meetings and\/or travel from Biogen, Roche, Alexion, Johnson&Johnson, Ad Scientiam,\u00a0Amicus,\u00a0Astellas, Sanofi, Shionogi. He has served on advisory boards for Biogen, Roche, Alexion, Johnson&Johnson, Ad Scientiam,\u00a0Amicus,\u00a0Astellas, Sanofi, Shionogi and declares no stocks or shares. The other authors report no relevant disclosures.","order":2,"name":"Ethics","group":{"name":"EthicsHeading","label":"Conflicts of interest"}},{"value":"The protocols for the French GSD-III registry, Accelerix and NatHis DM1 studies were approved by the local Ethics Committee (CPP\u2013Ile de France VI\u2013Groupe Hospitalier Piti\u00e9 Salp\u00eatri\u00e8re, Paris, France) in accordance with the 1964 Declaration of Helsinki and its later amendments. Written informed consent was obtained from all participants.","order":3,"name":"Ethics","group":{"name":"EthicsHeading","label":"Ethical approval"}}],"article-number":"301"}}