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CC has served as an expert in a scientific meeting for Sanofi Genzyme.TM has served as an expert in scientific boards for Sanofi Genzyme. VAS has served as scientific expert on advisory boards for Biogen, Avexis, Sarepta, Santhera, and PTC Therapeutics and declares no conflict of interest for this project. AT has received some reimbursement from Sanofi Genzyme for assisting in teaching courses and for being a member of the Global Pompe Registry committee. GS has served as scientific expert and supervisor for a study grant on Pompe disease supported by Sanofi in 2018 and in the current year.","order":2,"name":"Ethics","group":{"name":"EthicsHeading","label":"Conflict of interest"}}]}}