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Francesca Gatta was a Bluebird Bio Europe employee at the time of data collection; she is currently an employee of Alexion, AstraZeneca Rare Disease, Switzerland. Immacolata Tartaglione had consulting fees from Bluebird Bio.","order":2,"name":"Ethics","group":{"name":"EthicsHeading","label":"Conflict of Interest"}},{"value":"The study was approved by the central ethics committee (n. 208\/2020) and also by each participant sites\u2019 ethics committee.","order":3,"name":"Ethics","group":{"name":"EthicsHeading","label":"Ethical Approval"}},{"value":"Participants who met eligibility criteria and provided signed online informed consent were granted access to the online platform and participated in the study.","order":4,"name":"Ethics","group":{"name":"EthicsHeading","label":"Consent to Participate"}},{"value":"Not applicable.","order":5,"name":"Ethics","group":{"name":"EthicsHeading","label":"Consent for Publication"}},{"value":"Not applicable.","order":6,"name":"Ethics","group":{"name":"EthicsHeading","label":"Code Availability"}},{"value":"This study was funded by Bluebird Bio Inc.","order":7,"name":"Ethics","group":{"name":"EthicsHeading","label":"Funding"}},{"value":"FG designed the study; IT gave consultancy during the entire duration of the study. FG, MCon., MCol. and IT drafted the paper. All the authors contributed to recruiting patients and they all reviewed and approved the final version of the manuscript.","order":8,"name":"Ethics","group":{"name":"EthicsHeading","label":"Authors\u2019 Contribution"}},{"value":"All data are available upon request to the corresponding author.","order":9,"name":"Ethics","group":{"name":"EthicsHeading","label":"Data Availability"}}]}}