{"status":"ok","message-type":"work","message-version":"1.0.0","message":{"indexed":{"date-parts":[[2026,1,8]],"date-time":"2026-01-08T06:59:44Z","timestamp":1767855584951,"version":"3.49.0"},"reference-count":28,"publisher":"Elsevier BV","issue":"5","license":[{"start":{"date-parts":[[2023,7,1]],"date-time":"2023-07-01T00:00:00Z","timestamp":1688169600000},"content-version":"tdm","delay-in-days":0,"URL":"https:\/\/www.elsevier.com\/tdm\/userlicense\/1.0\/"},{"start":{"date-parts":[[2023,7,1]],"date-time":"2023-07-01T00:00:00Z","timestamp":1688169600000},"content-version":"tdm","delay-in-days":0,"URL":"https:\/\/www.elsevier.com\/legal\/tdmrep-license"}],"content-domain":{"domain":["clinicalkey.fr","em-consulte.com","elsevier.com","sciencedirect.com"],"crossmark-restriction":true},"short-container-title":["Archives de P\u00e9diatrie"],"published-print":{"date-parts":[[2023,7]]},"DOI":"10.1016\/j.arcped.2023.03.006","type":"journal-article","created":{"date-parts":[[2023,5,3]],"date-time":"2023-05-03T07:35:47Z","timestamp":1683099347000},"page":"291-296","update-policy":"https:\/\/doi.org\/10.1016\/elsevier_cm_policy","source":"Crossref","is-referenced-by-count":4,"title":["Immunization status of patients with spinal muscular atrophy receiving nusinersen therapy"],"prefix":"10.1016","volume":"30","author":[{"ORCID":"https:\/\/orcid.org\/0000-0002-6166-5837","authenticated-orcid":false,"given":"Mehmet Can","family":"Ye\u015filmen","sequence":"first","affiliation":[],"role":[{"role":"author","vocabulary":"crossref"}]},{"ORCID":"https:\/\/orcid.org\/0000-0001-7860-6297","authenticated-orcid":false,"given":"\u00c7a\u011fatay","family":"G\u00fcnay","sequence":"additional","affiliation":[],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"Gamze","family":"Sar\u0131kaya Uzan","sequence":"additional","affiliation":[],"role":[{"role":"author","vocabulary":"crossref"}]},{"ORCID":"https:\/\/orcid.org\/0000-0001-8552-0504","authenticated-orcid":false,"given":"\u00d6zlem","family":"\u00d6zsoy","sequence":"additional","affiliation":[],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"Semra","family":"H\u0131z Kurul","sequence":"additional","affiliation":[],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"Ulu\u00e7","family":"Yi\u015f","sequence":"additional","affiliation":[],"role":[{"role":"author","vocabulary":"crossref"}]}],"member":"78","reference":[{"key":"10.1016\/j.arcped.2023.03.006_bib0001","doi-asserted-by":"crossref","first-page":"355","DOI":"10.1002\/ana.24864","article-title":"Emerging therapies and challenges in spinal muscular atrophy","volume":"81","author":"Farrar","year":"2017","journal-title":"Ann Neurol"},{"key":"10.1016\/j.arcped.2023.03.006_bib0002","doi-asserted-by":"crossref","first-page":"71","DOI":"10.1186\/1750-1172-6-71","article-title":"Spinal muscular atrophy","volume":"6","author":"D'Amico","year":"2011","journal-title":"Orphanet J Rare Dis"},{"key":"10.1016\/j.arcped.2023.03.006_bib0003","doi-asserted-by":"crossref","first-page":"729","DOI":"10.1371\/journal.pbio.0050073","article-title":"Enhancement of SMN2 exon 7 inclusion by antisense oligonucleotides targeting the exon","volume":"5","author":"Hua","year":"2007","journal-title":"PLoS Biol"},{"key":"10.1016\/j.arcped.2023.03.006_bib0004","doi-asserted-by":"crossref","first-page":"1","DOI":"10.1126\/scitranslmed.3001777","article-title":"Antisense oligonucleotides delivered to the mouse CNS ameliorate symptoms of severe spinal muscular atrophy","volume":"3","author":"Passini","year":"2011","journal-title":"Sci Transl Med"},{"key":"10.1016\/j.arcped.2023.03.006_bib0005","series-title":"Nusinersen [package insert]","year":"2018"},{"key":"10.1016\/j.arcped.2023.03.006_bib0006","doi-asserted-by":"crossref","first-page":"473","DOI":"10.1007\/s40265-017-0711-7","article-title":"Nusinersen: first global approval","volume":"77","author":"Hoy","year":"2017","journal-title":"Drugs"},{"key":"10.1016\/j.arcped.2023.03.006_bib0007","doi-asserted-by":"crossref","first-page":"1031","DOI":"10.1002\/jcph.884","article-title":"Population pharmacokinetics of nusinersen in the cerebral spinal fluid and plasma of pediatric patients with spinal muscular atrophy following intrathecal administrations","volume":"57","author":"Luu","year":"2017","journal-title":"J Clin Pharmacol"},{"key":"10.1016\/j.arcped.2023.03.006_bib0008","doi-asserted-by":"crossref","first-page":"356","DOI":"10.1002\/mus.26001","article-title":"Making sense of antisense oligonucleotides: a narrative review","volume":"57","author":"Goyal","year":"2018","journal-title":"Muscle Nerve"},{"key":"10.1016\/j.arcped.2023.03.006_bib0009","doi-asserted-by":"crossref","first-page":"135","DOI":"10.1016\/j.jpeds.2015.11.030","article-title":"Hospitalizations attributable to respiratory \u0131nfections among children with neurologic disorders","volume":"170","author":"Havers","year":"2016","journal-title":"J Pediatr"},{"key":"10.1016\/j.arcped.2023.03.006_bib0010","series-title":"Swaiman's pediatric neurology: principles and practice","first-page":"1057","article-title":"Genetic disorders affecting the motor neuron: spinal muscular atrophy","author":"Darras","year":"2017"},{"key":"10.1016\/j.arcped.2023.03.006_bib0011","series-title":"Neuromuscular disorders of infancy, childhood, and adolescence: a clinician's approach","first-page":"117","article-title":"Spinal muscular atrophies","author":"Darras","year":"2014"},{"key":"10.1016\/j.arcped.2023.03.006_bib0012","doi-asserted-by":"crossref","first-page":"103","DOI":"10.1016\/j.nmd.2017.11.005","article-title":"Diagnosis and management of spinal muscular atrophy: part 1: recommendations for diagnosis, rehabilitation, orthopedic and nutritional care","volume":"28","author":"Mercuri","year":"2018","journal-title":"Neuromuscul Disord"},{"key":"10.1016\/j.arcped.2023.03.006_bib0013","doi-asserted-by":"crossref","first-page":"75","DOI":"10.1016\/j.idc.2017.11.005","article-title":"Updates on \u0131nfluenza vaccination in children","volume":"32","author":"Campbell","year":"2018","journal-title":"Infect Dis Clin North Am"},{"key":"10.1016\/j.arcped.2023.03.006_bib0014","doi-asserted-by":"crossref","first-page":"278","DOI":"10.1186\/1471-2458-8-278","article-title":"A comparison of populations vaccinated in a public service and in a private hospital setting in the same area","volume":"8","author":"Pandolfi","year":"2008","journal-title":"BMC Public Health"},{"key":"10.1016\/j.arcped.2023.03.006_bib0015","doi-asserted-by":"crossref","first-page":"320","DOI":"10.1007\/s00431-005-1627-x","article-title":"Acceptance and timeliness of standard vaccination in children with chronic neurological deficits in north-western Switzerland","volume":"164","author":"Tillmann","year":"2005","journal-title":"Eur J Pediatr"},{"key":"10.1016\/j.arcped.2023.03.006_bib0016","doi-asserted-by":"crossref","first-page":"1970","DOI":"10.1080\/21645515.2018.1460986","article-title":"The immunization status of children with chronic neurological disease and serological assessment of vaccine-preventable diseases","volume":"14","author":"Dinleyici","year":"2018","journal-title":"Hum Vaccin Immunother"},{"key":"10.1016\/j.arcped.2023.03.006_bib0017","first-page":"1","article-title":"The \u201curban myth\u201d of the association between neurological disorders and vaccinations","volume":"56","author":"Gasparini","year":"2015","journal-title":"J Prev Med Hyg"},{"key":"10.1016\/j.arcped.2023.03.006_bib0018","first-page":"308","article-title":"[Coverage rate and adverse reactions of National Immunization Program vaccines in children with spinal muscular atrophy: a cross-sectional retrospective cohort study]","volume":"58","author":"Qu","year":"2020","journal-title":"Zhonghua Er Ke Za Zhi"},{"key":"10.1016\/j.arcped.2023.03.006_bib0019","series-title":"Health statistics yearbook 2018","year":"2019"},{"key":"10.1016\/j.arcped.2023.03.006_bib0020","doi-asserted-by":"crossref","first-page":"111","DOI":"10.1186\/s12883-019-1343-1","article-title":"Survival and mortality in cerebral palsy: observations to the sixth decade from a data linkage study of a total population register and National Death Index","volume":"19","author":"Blair","year":"2019","journal-title":"BMC Neurol"},{"key":"10.1016\/j.arcped.2023.03.006_bib0021","doi-asserted-by":"crossref","first-page":"1","DOI":"10.15585\/mmwr.rr7005a1","article-title":"Prevention and control of seasonal influenza with vaccines: recommendations of the advisory committee on immunization practices, united states, 2021-22 influenza season","volume":"70","author":"Grohskopf","year":"2021","journal-title":"MMWR Recomm Rep"},{"key":"10.1016\/j.arcped.2023.03.006_bib0022","unstructured":"WHO. [Internet] WHO and UNICEF estimates of immunization coverage: 2019 revision. 2020.https:\/\/www.who.int\/teams\/immunization-vaccines-and-biologicals\/immunization-analysis-and-insights\/global-monitoring\/immunization-coverage\/who-unicef-estimates-of-national-immunization-coverage. Accessed 11 May 2020"},{"key":"10.1016\/j.arcped.2023.03.006_bib0023","doi-asserted-by":"crossref","first-page":"1","DOI":"10.15585\/mmwr.rr6908a1","article-title":"Prevention and control of seasonal influenza with vaccines: recommendations of the advisory committee on immunization practices\u2014United States, 2020\u201321 influenza season","volume":"69","author":"Grohskopf","year":"2020","journal-title":"MMWR Recomm Rep"},{"key":"10.1016\/j.arcped.2023.03.006_bib0024","doi-asserted-by":"crossref","first-page":"2188","DOI":"10.1001\/jama.294.17.2188","article-title":"Neurological and neuromuscular disease as a risk factor for respiratory failure in children hospitalized with influenza infection","volume":"294","author":"Keren","year":"2005","journal-title":"JAMA"},{"key":"10.1016\/j.arcped.2023.03.006_bib0025","doi-asserted-by":"crossref","first-page":"796","DOI":"10.1542\/peds.2013-1493","article-title":"Influenza-associated pediatric deaths in the United States 2004\u20132012","volume":"132","author":"Wong","year":"2013","journal-title":"Pediatrics"},{"key":"10.1016\/j.arcped.2023.03.006_bib0026","doi-asserted-by":"crossref","first-page":"139","DOI":"10.1016\/S2213-2600(14)70252-8","article-title":"Identification of children at risk of influenza-related complications in primary andambulatory care: a systematic review and meta-analysis","volume":"3","author":"Gill","year":"2015","journal-title":"Lancet Respir Med"},{"key":"10.1016\/j.arcped.2023.03.006_bib0027","doi-asserted-by":"crossref","first-page":"5172","DOI":"10.1016\/j.vaccine.2011.02.099","article-title":"Immunization coverage and timeliness of vaccination in Italian children with chronic diseases","volume":"30","author":"Pandolfi","year":"2012","journal-title":"Vaccine"},{"key":"10.1016\/j.arcped.2023.03.006_bib0028","doi-asserted-by":"crossref","first-page":"814","DOI":"10.1097\/INF.0000000000001929","article-title":"Influenza vaccination coverage in children with neurologic disorders and their siblings July 2006 to June 2014","volume":"37","author":"Havers","year":"2018","journal-title":"Pediatr Infect Dis J"}],"container-title":["Archives de P\u00e9diatrie"],"original-title":[],"language":"en","link":[{"URL":"https:\/\/api.elsevier.com\/content\/article\/PII:S0929693X23000556?httpAccept=text\/xml","content-type":"text\/xml","content-version":"vor","intended-application":"text-mining"},{"URL":"https:\/\/api.elsevier.com\/content\/article\/PII:S0929693X23000556?httpAccept=text\/plain","content-type":"text\/plain","content-version":"vor","intended-application":"text-mining"}],"deposited":{"date-parts":[[2025,10,15]],"date-time":"2025-10-15T14:55:54Z","timestamp":1760540154000},"score":1,"resource":{"primary":{"URL":"https:\/\/linkinghub.elsevier.com\/retrieve\/pii\/S0929693X23000556"}},"subtitle":[],"short-title":[],"issued":{"date-parts":[[2023,7]]},"references-count":28,"journal-issue":{"issue":"5","published-print":{"date-parts":[[2023,7]]}},"alternative-id":["S0929693X23000556"],"URL":"https:\/\/doi.org\/10.1016\/j.arcped.2023.03.006","relation":{},"ISSN":["0929-693X"],"issn-type":[{"value":"0929-693X","type":"print"}],"subject":[],"published":{"date-parts":[[2023,7]]},"assertion":[{"value":"Elsevier","name":"publisher","label":"This article is maintained by"},{"value":"Immunization status of patients with spinal muscular atrophy receiving nusinersen therapy","name":"articletitle","label":"Article Title"},{"value":"Archives de P\u00e9diatrie","name":"journaltitle","label":"Journal Title"},{"value":"https:\/\/doi.org\/10.1016\/j.arcped.2023.03.006","name":"articlelink","label":"CrossRef DOI link to publisher maintained version"},{"value":"article","name":"content_type","label":"Content Type"},{"value":"\u00a9 2023 French Society of Pediatrics. Published by Elsevier Masson SAS. All rights reserved.","name":"copyright","label":"Copyright"}]}}