{"status":"ok","message-type":"work","message-version":"1.0.0","message":{"indexed":{"date-parts":[[2026,2,7]],"date-time":"2026-02-07T03:05:47Z","timestamp":1770433547279,"version":"3.49.0"},"reference-count":30,"publisher":"Elsevier BV","issue":"6","license":[{"start":{"date-parts":[[2007,6,1]],"date-time":"2007-06-01T00:00:00Z","timestamp":1180656000000},"content-version":"tdm","delay-in-days":0,"URL":"https:\/\/www.elsevier.com\/tdm\/userlicense\/1.0\/"},{"start":{"date-parts":[[2007,6,1]],"date-time":"2007-06-01T00:00:00Z","timestamp":1180656000000},"content-version":"tdm","delay-in-days":0,"URL":"https:\/\/www.elsevier.com\/legal\/tdmrep-license"},{"start":{"date-parts":[[2015,4,10]],"date-time":"2015-04-10T00:00:00Z","timestamp":1428624000000},"content-version":"vor","delay-in-days":2870,"URL":"http:\/\/creativecommons.org\/licenses\/by-nc-nd\/4.0\/"}],"content-domain":{"domain":["bbmt.org","clinicalkey.com","clinicalkey.com.au","clinicalkey.es","clinicalkey.fr","clinicalkey.jp","elsevier.com","sciencedirect.com"],"crossmark-restriction":true},"short-container-title":["Biology of Blood and Marrow Transplantation"],"published-print":{"date-parts":[[2007,6]]},"DOI":"10.1016\/j.bbmt.2007.01.082","type":"journal-article","created":{"date-parts":[[2007,4,7]],"date-time":"2007-04-07T07:17:16Z","timestamp":1175930236000},"page":"665-674","update-policy":"https:\/\/doi.org\/10.1016\/elsevier_cm_policy","source":"Crossref","is-referenced-by-count":83,"title":["Outcomes of Unrelated Umbilical Cord Blood Transplantation for X-Linked Adrenoleukodystrophy"],"prefix":"10.1016","volume":"13","author":[{"given":"Donald","family":"Beam","sequence":"first","affiliation":[],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"Michele D.","family":"Poe","sequence":"additional","affiliation":[],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"James M.","family":"Provenzale","sequence":"additional","affiliation":[],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"Paul","family":"Szabolcs","sequence":"additional","affiliation":[],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"Paul L.","family":"Martin","sequence":"additional","affiliation":[],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"Vinod","family":"Prasad","sequence":"additional","affiliation":[],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"Suhag","family":"Parikh","sequence":"additional","affiliation":[],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"Tim","family":"Driscoll","sequence":"additional","affiliation":[],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"Srini","family":"Mukundan","sequence":"additional","affiliation":[],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"Joanne","family":"Kurtzberg","sequence":"additional","affiliation":[],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"Maria L.","family":"Escolar","sequence":"additional","affiliation":[],"role":[{"role":"author","vocabulary":"crossref"}]}],"member":"78","reference":[{"key":"10.1016\/j.bbmt.2007.01.082_bib1","first-page":"217","article-title":"Adrenoleukodystrophy: studies of the phenotype, genetics and biochemistry","volume":"147","author":"Moser","year":"1980","journal-title":"Johns Hopkins Med J"},{"key":"10.1016\/j.bbmt.2007.01.082_bib2","doi-asserted-by":"crossref","first-page":"577","DOI":"10.1001\/archneur.1975.00490510033001","article-title":"Adrenoleukodystrophy","volume":"32","author":"Schaumburg","year":"1975","journal-title":"Arch Neurol"},{"key":"10.1016\/j.bbmt.2007.01.082_bib3","doi-asserted-by":"crossref","first-page":"265","DOI":"10.1093\/hmg\/3.2.265","article-title":"The gene responsible for adrenoleukodystrophy encodes a peroxisomal membrane protein","volume":"3","author":"Moser","year":"1994","journal-title":"Hum Mol Genet"},{"key":"10.1016\/j.bbmt.2007.01.082_bib4","doi-asserted-by":"crossref","first-page":"167","DOI":"10.1097\/00019052-199904000-00007","volume":"12","author":"Krivit","year":"1999","journal-title":"Curr Opin Neurol"},{"key":"10.1016\/j.bbmt.2007.01.082_bib5","doi-asserted-by":"crossref","first-page":"453","DOI":"10.1023\/A:1005656029200","article-title":"Bone marrow transplantation for the treatment of X-linked adrenoleukodystrophy","volume":"23","author":"Suzuki","year":"2000","journal-title":"J Inherit Metab Dis"},{"key":"10.1016\/j.bbmt.2007.01.082_bib6","doi-asserted-by":"crossref","first-page":"163","DOI":"10.1055\/s-2004-822629","article-title":"Hematopoietic stem cell transplantation for mucopolysaccharidoses and leukodystrophies","volume":"216","author":"Sauer","year":"2004","journal-title":"Klin Padiatr"},{"key":"10.1016\/j.bbmt.2007.01.082_bib7","doi-asserted-by":"crossref","first-page":"881","DOI":"10.1182\/blood-2003-10-3402","article-title":"Cerebral X-linked adrenoleukodystrophy: the international hematopoietic cell transplantation experience from 1982 to 1999","volume":"104","author":"Peters","year":"2004","journal-title":"Blood"},{"key":"10.1016\/j.bbmt.2007.01.082_bib8","doi-asserted-by":"crossref","first-page":"1174","DOI":"10.1056\/NEJM198910263211707","article-title":"Hematopoietic reconstitution in a patient with Fanconi\u2019s anemia by means of umbilical-cord blood from an HLA-identical sibling","volume":"321","author":"Gluckman","year":"1989","journal-title":"N Engl J Med"},{"key":"10.1016\/j.bbmt.2007.01.082_bib9","doi-asserted-by":"crossref","first-page":"157","DOI":"10.1056\/NEJM199607183350303","article-title":"Placental blood as a source of hematopoietic stem cells for transplantation into unrelated recipients","volume":"335","author":"Kurtzberg","year":"1996","journal-title":"N Engl J Med"},{"key":"10.1016\/j.bbmt.2007.01.082_bib10","doi-asserted-by":"crossref","first-page":"184","DOI":"10.1016\/j.bbmt.2005.09.016","article-title":"Results of the Cord Blood Transplantation Study (COBLT): outcomes of unrelated umbilcal cord transplantation in pediatric patients with lysosomal and peroxisomal storage disorders","volume":"12","author":"Martin","year":"2006","journal-title":"Biol Blood MarrowTransplant"},{"key":"10.1016\/j.bbmt.2007.01.082_bib11","doi-asserted-by":"crossref","first-page":"481","DOI":"10.1016\/S0387-7604(03)00033-0","article-title":"Gas chromatography\/mass spectrometry analysis of very long chain fatty acids, docosahexaenoic acid, phytanic acid and plasmalogen for the screening of peroxisomal disorders","volume":"25","author":"Takemoto","year":"2003","journal-title":"Brain Dev"},{"key":"10.1016\/j.bbmt.2007.01.082_bib12","doi-asserted-by":"crossref","first-page":"1960","DOI":"10.1056\/NEJMoa032613","article-title":"Cord-blood transplants from unrelated donors with Hurlers syndrome","volume":"350","author":"Staba","year":"2004","journal-title":"N Engl J Med"},{"key":"10.1016\/j.bbmt.2007.01.082_bib13","doi-asserted-by":"crossref","first-page":"2069","DOI":"10.1056\/NEJMoa042604","article-title":"Transplantation of umbilical-cord blood in babies with infantile Krabbe\u2019s disease","volume":"352","author":"Escolar","year":"2005","journal-title":"N Engl J Med"},{"key":"10.1016\/j.bbmt.2007.01.082_bib14","doi-asserted-by":"crossref","first-page":"855","DOI":"10.1038\/sj.bmt.1703010","article-title":"Oral busulfan pharmacokinetics and engraftment in children with Hurler Syndrome and other inherited metabolic storage diseases undergoing hematopoetic stem cell transplant","volume":"27","author":"Jacobson","year":"2001","journal-title":"Bone Marrow Transplant"},{"key":"10.1016\/j.bbmt.2007.01.082_bib15","doi-asserted-by":"crossref","first-page":"10119","DOI":"10.1073\/pnas.92.22.10119","article-title":"Processing and cryopreservation of placental\/umbilical cord blood for unrelated bone marrow reconstitution","volume":"92","author":"Rubinstein","year":"1995","journal-title":"Proc Natl Acad Sci U S A"},{"key":"10.1016\/j.bbmt.2007.01.082_bib16","first-page":"825","article-title":"1994 Consensus conference on acute GVHD grading","volume":"15","author":"Przepiorka","year":"1995","journal-title":"Bone Marrow Transplant"},{"key":"10.1016\/j.bbmt.2007.01.082_bib17","series-title":"The Mullen Scales of Early Learning","author":"Mullen","year":"1995"},{"key":"10.1016\/j.bbmt.2007.01.082_bib18","series-title":"The Differential Abilities Scales (DAS)","author":"Elliot","year":"1990"},{"key":"10.1016\/j.bbmt.2007.01.082_bib19","series-title":"Scales of Independent Behavior\u2014Revised","author":"Bruininks","year":"1996"},{"key":"10.1016\/j.bbmt.2007.01.082_bib20","series-title":"Peabody Developmental Motor Scales","author":"Folio","year":"2000"},{"key":"10.1016\/j.bbmt.2007.01.082_bib21","series-title":"Preschool Language Scale","author":"Zimmerman","year":"2002"},{"key":"10.1016\/j.bbmt.2007.01.082_bib22","series-title":"Clinical Evaluation of Language Fundamentals 3","author":"Eleanor","year":"2000"},{"key":"10.1016\/j.bbmt.2007.01.082_bib23","series-title":"Peabody Developmental Motor Scales","author":"Folio","year":"2000"},{"key":"10.1016\/j.bbmt.2007.01.082_bib24","series-title":"Bruininks-Oseretsky Test of Motor Proficiency","author":"Bruininks","year":"1978"},{"key":"10.1016\/j.bbmt.2007.01.082_bib25","first-page":"1761","article-title":"Adrenoleukodystrophy: a scoring method for brain MR observations","volume":"15","author":"Loes","year":"1994","journal-title":"Am J Neuroradiol"},{"key":"10.1016\/j.bbmt.2007.01.082_bib26","doi-asserted-by":"crossref","first-page":"40","DOI":"10.1097\/00004691-199401000-00010","article-title":"Guideline nine: guidelines on evoked potentials","volume":"11","author":"Society","year":"1994","journal-title":"J Clin Neurophysiol"},{"key":"10.1016\/j.bbmt.2007.01.082_bib27","doi-asserted-by":"crossref","first-page":"1073","DOI":"10.1001\/archneur.62.7.1073","article-title":"Follow up of 89 asymptomatic patients with adrenoleukodystrophy treated with Lorenzo\u2019s oil","volume":"62","author":"Moser","year":"2005","journal-title":"Arch Neurol"},{"key":"10.1016\/j.bbmt.2007.01.082_bib28","doi-asserted-by":"crossref","first-page":"227","DOI":"10.1055\/s-2000-9236","article-title":"X-Linked adrenoleukodystrophy: overview and prognosis as a function of age and brain magnetic resonance imaging abnormality","volume":"31","author":"Moser","year":"2000","journal-title":"Neuropediatrics"},{"key":"10.1016\/j.bbmt.2007.01.082_bib29","doi-asserted-by":"crossref","first-page":"369","DOI":"10.1212\/01.WNL.0000079050.91337.83","article-title":"Analysis of MRI patterns aids prediction of progression in X-linked adrenoleukodystrophy","volume":"61","author":"Loes","year":"2003","journal-title":"Neurology"},{"key":"10.1016\/j.bbmt.2007.01.082_bib30","doi-asserted-by":"crossref","first-page":"154","DOI":"10.7326\/0003-4819-64-1-154","article-title":"Two cases of busulfan toxicity","volume":"64","author":"Smalley","year":"1966","journal-title":"Ann Intern Med"}],"container-title":["Biology of Blood and Marrow Transplantation"],"original-title":[],"language":"en","link":[{"URL":"https:\/\/api.elsevier.com\/content\/article\/PII:S1083879107001437?httpAccept=text\/xml","content-type":"text\/xml","content-version":"vor","intended-application":"text-mining"},{"URL":"https:\/\/api.elsevier.com\/content\/article\/PII:S1083879107001437?httpAccept=text\/plain","content-type":"text\/plain","content-version":"vor","intended-application":"text-mining"}],"deposited":{"date-parts":[[2025,10,21]],"date-time":"2025-10-21T14:29:35Z","timestamp":1761056975000},"score":1,"resource":{"primary":{"URL":"https:\/\/linkinghub.elsevier.com\/retrieve\/pii\/S1083879107001437"}},"subtitle":[],"short-title":[],"issued":{"date-parts":[[2007,6]]},"references-count":30,"journal-issue":{"issue":"6","published-print":{"date-parts":[[2007,6]]}},"alternative-id":["S1083879107001437"],"URL":"https:\/\/doi.org\/10.1016\/j.bbmt.2007.01.082","relation":{},"ISSN":["1083-8791"],"issn-type":[{"value":"1083-8791","type":"print"}],"subject":[],"published":{"date-parts":[[2007,6]]},"assertion":[{"value":"Elsevier","name":"publisher","label":"This article is maintained by"},{"value":"Outcomes of Unrelated Umbilical Cord Blood Transplantation for X-Linked Adrenoleukodystrophy","name":"articletitle","label":"Article Title"},{"value":"Biology of Blood and Marrow Transplantation","name":"journaltitle","label":"Journal Title"},{"value":"https:\/\/doi.org\/10.1016\/j.bbmt.2007.01.082","name":"articlelink","label":"CrossRef DOI link to publisher maintained version"},{"value":"article","name":"content_type","label":"Content Type"},{"value":"Copyright \u00a9 2007 American Society for Blood and Marrow Transplantation. Published by Elsevier Inc. All rights reserved.","name":"copyright","label":"Copyright"}]}}