{"status":"ok","message-type":"work","message-version":"1.0.0","message":{"indexed":{"date-parts":[[2026,11,12]],"date-time":"2026-11-12T07:19:56Z","timestamp":1794467996678,"version":"4.9.1"},"reference-count":56,"publisher":"Elsevier BV","issue":"5","license":[{"start":{"date-parts":[[2022,5,1]],"date-time":"2022-05-01T00:00:00Z","timestamp":1651363200000},"content-version":"tdm","delay-in-days":0,"URL":"https:\/\/www.elsevier.com\/tdm\/userlicense\/1.0\/"},{"start":{"date-parts":[[2022,5,1]],"date-time":"2022-05-01T00:00:00Z","timestamp":1651363200000},"content-version":"tdm","delay-in-days":0,"URL":"https:\/\/www.elsevier.com\/legal\/tdmrep-license"},{"start":{"date-parts":[[2022,4,4]],"date-time":"2022-04-04T00:00:00Z","timestamp":1649030400000},"content-version":"vor","delay-in-days":0,"URL":"http:\/\/creativecommons.org\/licenses\/by-nc-nd\/4.0\/"}],"funder":[{"DOI":"10.13039\/100000002","name":"National Institutes of Health","doi-asserted-by":"publisher","award":["P01-NS058901"],"award-info":[{"award-number":["P01-NS058901"]}],"id":[{"id":"10.13039\/100000002","id-type":"DOI","asserted-by":"publisher"}]},{"DOI":"10.13039\/100000057","name":"NIGMS","doi-asserted-by":"publisher","award":["R01GM121862"],"award-info":[{"award-number":["R01GM121862"]}],"id":[{"id":"10.13039\/100000057","id-type":"DOI","asserted-by":"publisher"}]},{"DOI":"10.13039\/100000065","name":"NINDS","doi-asserted-by":"publisher","award":["P50NS04843"],"award-info":[{"award-number":["P50NS04843"]}],"id":[{"id":"10.13039\/100000065","id-type":"DOI","asserted-by":"publisher"}]},{"DOI":"10.13039\/100005202","name":"Muscular Dystrophy Association","doi-asserted-by":"publisher","award":["516314"],"award-info":[{"award-number":["516314"]}],"id":[{"id":"10.13039\/100005202","id-type":"DOI","asserted-by":"publisher"}]}],"content-domain":{"domain":["cell.com","elsevier.com","sciencedirect.com"],"crossmark-restriction":true},"short-container-title":["iScience"],"published-print":{"date-parts":[[2022,5]]},"DOI":"10.1016\/j.isci.2022.104198","type":"journal-article","created":{"date-parts":[[2022,4,4]],"date-time":"2022-04-04T21:01:14Z","timestamp":1649106074000},"page":"104198","update-policy":"https:\/\/doi.org\/10.1016\/elsevier_cm_policy","source":"Crossref","is-referenced-by-count":21,"title":["Molecular characterization of myotonic dystrophy fibroblast cell lines for use in small molecule screening"],"prefix":"10.1016","volume":"25","author":[{"given":"Jana R.","family":"Jenquin","sequence":"first","affiliation":[],"role":[{"vocabulary":"crossref","role":"author"}]},{"given":"Alana P.","family":"O\u2019Brien","sequence":"additional","affiliation":[],"role":[{"vocabulary":"crossref","role":"author"}]},{"given":"Kiril","family":"Poukalov","sequence":"additional","affiliation":[],"role":[{"vocabulary":"crossref","role":"author"}]},{"given":"Yidan","family":"Lu","sequence":"additional","affiliation":[],"role":[{"vocabulary":"crossref","role":"author"}]},{"given":"Jesus A.","family":"Frias","sequence":"additional","affiliation":[],"role":[{"vocabulary":"crossref","role":"author"}]},{"given":"Hannah K.","family":"Shorrock","sequence":"additional","affiliation":[],"role":[{"vocabulary":"crossref","role":"author"}]},{"given":"Jared I.","family":"Richardson","sequence":"additional","affiliation":[],"role":[{"vocabulary":"crossref","role":"author"}]},{"given":"Hormoz","family":"Mazdiyasni","sequence":"additional","affiliation":[],"role":[{"vocabulary":"crossref","role":"author"}]},{"given":"Hongfen","family":"Yang","sequence":"additional","affiliation":[],"role":[{"vocabulary":"crossref","role":"author"}]},{"ORCID":"https:\/\/orcid.org\/0000-0003-3811-2721","authenticated-orcid":false,"suffix":"III","given":"Robert W.","family":"Huigens","sequence":"additional","affiliation":[],"role":[{"vocabulary":"crossref","role":"author"}]},{"given":"David","family":"Boykin","sequence":"additional","affiliation":[],"role":[{"vocabulary":"crossref","role":"author"}]},{"given":"Laura P.W.","family":"Ranum","sequence":"additional","affiliation":[],"role":[{"vocabulary":"crossref","role":"author"}]},{"ORCID":"https:\/\/orcid.org\/0000-0001-7599-5995","authenticated-orcid":false,"given":"John Douglas","family":"Cleary","sequence":"additional","affiliation":[],"role":[{"vocabulary":"crossref","role":"author"}]},{"ORCID":"https:\/\/orcid.org\/0000-0003-2655-5525","authenticated-orcid":false,"given":"Eric T.","family":"Wang","sequence":"additional","affiliation":[],"role":[{"vocabulary":"crossref","role":"author"}]},{"given":"J. Andrew","family":"Berglund","sequence":"additional","affiliation":[],"role":[{"vocabulary":"crossref","role":"author"}]}],"member":"78","reference":[{"key":"10.1016\/j.isci.2022.104198_bib1","first-page":"487","article-title":"Immortalized human myotonic dystrophy muscle cell lines to assess therapeutic compounds","volume":"10","author":"Arandel","year":"2017","journal-title":"Dis. Model Mech."},{"key":"10.1016\/j.isci.2022.104198_bib2","doi-asserted-by":"crossref","first-page":"25","DOI":"10.1038\/75556","article-title":"Gene ontology: tool for the unification of biology. The Gene Ontology Consortium","volume":"25","author":"Ashburner","year":"2000","journal-title":"Nat. Genet."},{"key":"10.1016\/j.isci.2022.104198_bib3","doi-asserted-by":"crossref","first-page":"9770","DOI":"10.1021\/bi0108453","article-title":"Recognition of ATGA sequences by the unfused aromatic dication DB293 forming stacked dimers in the DNA minor groove","volume":"40","author":"Bailly","year":"2001","journal-title":"Biochemistry"},{"key":"10.1016\/j.isci.2022.104198_bib4","doi-asserted-by":"crossref","first-page":"311","DOI":"10.1016\/j.molcel.2014.08.027","article-title":"Loss of MBNL leads to disruption of developmentally regulated alternative polyadenylation in RNA-mediated disease","volume":"56","author":"Batra","year":"2014","journal-title":"Mol. Cell"},{"key":"10.1016\/j.isci.2022.104198_bib5","doi-asserted-by":"crossref","first-page":"485","DOI":"10.1021\/acschembio.9b00958","article-title":"Structure-specific cleavage of an RNA repeat expansion with a dimeric small molecule is advantageous over sequence-specific recognition by an oligonucleotide","volume":"15","author":"Benhamou","year":"2020","journal-title":"ACS Chem. Biol."},{"key":"10.1016\/j.isci.2022.104198_bib6","doi-asserted-by":"crossref","first-page":"223","DOI":"10.1016\/j.chembiol.2020.01.003","article-title":"A toxic RNA catalyzes the cellular synthesis of its own inhibitor, shunting it to endogenous decay pathways","volume":"27","author":"Benhamou","year":"2020","journal-title":"Cell Chem. Biol."},{"key":"10.1016\/j.isci.2022.104198_bib7","doi-asserted-by":"crossref","first-page":"1","DOI":"10.1016\/j.brainres.2016.02.050","article-title":"Roles for RNA-binding proteins in development and disease","volume":"1647","author":"Brinegar","year":"2016","journal-title":"Brain Res."},{"key":"10.1016\/j.isci.2022.104198_bib8","doi-asserted-by":"crossref","first-page":"799","DOI":"10.1016\/0092-8674(92)90154-5","article-title":"Molecular basis of myotonic dystrophy: expansion of a trinucleotide (CTG) repeat at the 3\u2032 end of a transcript encoding a protein kinase family member","volume":"68","author":"Brook","year":"1992","journal-title":"Cell"},{"key":"10.1016\/j.isci.2022.104198_bib9","doi-asserted-by":"crossref","first-page":"2843","DOI":"10.1038\/s41598-017-02829-3","article-title":"Expanded CCUG repeat RNA expression in Drosophila heart and muscle trigger Myotonic Dystrophy type 1-like phenotypes and activate autophagocytosis genes","volume":"7","author":"Cerro-Herreros","year":"2017","journal-title":"Sci. Rep."},{"key":"10.1016\/j.isci.2022.104198_bib10","doi-asserted-by":"crossref","first-page":"2528","DOI":"10.1021\/cb400431f","article-title":"Reducing levels of toxic RNA with small molecules","volume":"8","author":"Coonrod","year":"2013","journal-title":"ACS Chem. Biol."},{"key":"10.1016\/j.isci.2022.104198_bib11","doi-asserted-by":"crossref","first-page":"5","DOI":"10.1016\/j.nmd.2004.09.012","article-title":"RNA pathogenesis of the myotonic dystrophies","volume":"15","author":"Day","year":"2005","journal-title":"Neuromuscul. Disord."},{"key":"10.1016\/j.isci.2022.104198_bib12","doi-asserted-by":"crossref","first-page":"657","DOI":"10.1212\/01.WNL.0000054481.84978.F9","article-title":"Myotonic dystrophy type 2: molecular, diagnostic and clinical spectrum","volume":"60","author":"Day","year":"2003","journal-title":"Neurology"},{"key":"10.1016\/j.isci.2022.104198_bib13","doi-asserted-by":"crossref","first-page":"9042","DOI":"10.1038\/srep09042","article-title":"Loss of muscleblind-like 1 results in cardiac pathology and persistence of embryonic splice isoforms","volume":"5","author":"Dixon","year":"2015","journal-title":"Sci. Rep."},{"key":"10.1016\/j.isci.2022.104198_bib14","doi-asserted-by":"crossref","first-page":"187","DOI":"10.1038\/nsmb.1720","article-title":"Aberrant alternative splicing and extracellular matrix gene expression in mouse models of myotonic dystrophy","volume":"17","author":"Du","year":"2010","journal-title":"Nat. Struct. Mol. Biol."},{"key":"10.1016\/j.isci.2022.104198_bib15","doi-asserted-by":"crossref","first-page":"805","DOI":"10.1093\/hmg\/11.7.805","article-title":"Three proteins, MBNL, MBLL and MBXL, co-localize in\u00a0vivo with nuclear foci of expanded-repeat transcripts in DM1 and DM2 cells","volume":"11","author":"Fardaei","year":"2002","journal-title":"Hum. Mol. Genet."},{"key":"10.1016\/j.isci.2022.104198_bib16","doi-asserted-by":"crossref","first-page":"1256","DOI":"10.1126\/science.1546326","article-title":"An unstable triplet repeat in a gene related to myotonic muscular dystrophy","volume":"255","author":"Fu","year":"1992","journal-title":"Science"},{"key":"10.1016\/j.isci.2022.104198_bib17","doi-asserted-by":"crossref","first-page":"D325","DOI":"10.1093\/nar\/gkaa1113","article-title":"The Gene Ontology resource: enriching a GOld mine","volume":"49","year":"2021","journal-title":"Nucleic Acids Res."},{"key":"10.1016\/j.isci.2022.104198_bib18","doi-asserted-by":"crossref","first-page":"545","DOI":"10.1038\/355545a0","article-title":"Expansion of an unstable DNA region and phenotypic variation in myotonic dystrophy","volume":"355","author":"Harley","year":"1992","journal-title":"Nature"},{"key":"10.1016\/j.isci.2022.104198_bib19","series-title":"Myotonic Dystrophy","author":"Harper","year":"2001"},{"key":"10.1016\/j.isci.2022.104198_bib20","doi-asserted-by":"crossref","first-page":"2191","DOI":"10.1161\/ATVBAHA.118.310870","article-title":"Direct reprogramming of fibroblasts into smooth muscle-like cells with defined transcription factors-brief report","volume":"38","author":"Hirai","year":"2018","journal-title":"Arterioscler. Thromb. Vasc. Biol."},{"key":"10.1016\/j.isci.2022.104198_bib21","doi-asserted-by":"crossref","first-page":"3872","DOI":"10.1021\/jm980230c","article-title":"Extended aromatic furan amidino derivatives as anti-Pneumocystis carinii agents","volume":"41","author":"Hopkins","year":"1998","journal-title":"J.\u00a0Med. Chem."},{"key":"10.1016\/j.isci.2022.104198_bib22","doi-asserted-by":"crossref","first-page":"6732","DOI":"10.1016\/j.bmc.2013.08.006","article-title":"Synthesis and antiprotozoal activity of dicationic 2,6-diphenylpyrazines and aza-analogues","volume":"21","author":"Hu","year":"2013","journal-title":"Bioorg. Med. Chem."},{"key":"10.1016\/j.isci.2022.104198_bib23","doi-asserted-by":"crossref","first-page":"2708","DOI":"10.1021\/acschembio.8b00646","article-title":"Furamidine rescues myotonic dystrophy type I associated mis-splicing through multiple mechanisms","volume":"13","author":"Jenquin","year":"2018","journal-title":"ACS Chem. Biol."},{"key":"10.1016\/j.isci.2022.104198_bib24","doi-asserted-by":"crossref","first-page":"247","DOI":"10.1021\/acsptsci.9b00020","article-title":"Combination treatment of Erythromycin and furamidine provides additive and synergistic rescue of mis-splicing in myotonic dystrophy type 1 models","volume":"2","author":"Jenquin","year":"2019","journal-title":"ACS Pharmacol. Transl. Sci."},{"key":"10.1016\/j.isci.2022.104198_bib25","doi-asserted-by":"crossref","first-page":"1978","DOI":"10.1126\/science.1088583","article-title":"A muscleblind knockout model for myotonic dystrophy","volume":"302","author":"Kanadia","year":"2003","journal-title":"Science"},{"key":"10.1016\/j.isci.2022.104198_bib26","doi-asserted-by":"crossref","first-page":"68","DOI":"10.1016\/j.molcel.2007.07.027","article-title":"Increased steady-state levels of CUGBP1 in myotonic dystrophy 1 are due to PKC-mediated hyperphosphorylation","volume":"28","author":"Kuyumcu-Martinez","year":"2007","journal-title":"Mol. Cell"},{"key":"10.1016\/j.isci.2022.104198_bib27","doi-asserted-by":"crossref","first-page":"1887","DOI":"10.1002\/emmm.201303275","article-title":"Compound loss of muscleblind-like function in myotonic dystrophy","volume":"5","author":"Lee","year":"2013","journal-title":"EMBO Mol. Med."},{"key":"10.1016\/j.isci.2022.104198_bib28","doi-asserted-by":"crossref","first-page":"864","DOI":"10.1126\/science.1062125","article-title":"Myotonic dystrophy type 2 caused by a CCTG expansion in intron 1 of ZNF9","volume":"293","author":"Liquori","year":"2001","journal-title":"Science"},{"key":"10.1016\/j.isci.2022.104198_bib29","doi-asserted-by":"crossref","first-page":"1253","DOI":"10.1126\/science.1546325","article-title":"Myotonic dystrophy mutation: an unstable CTG repeat in the 3\u2032 untranslated region of the gene","volume":"255","author":"Mahadevan","year":"1992","journal-title":"Science"},{"key":"10.1016\/j.isci.2022.104198_bib30","doi-asserted-by":"crossref","first-page":"2165","DOI":"10.1093\/hmg\/10.19.2165","article-title":"Muscleblind localizes to nuclear foci of aberrant RNA in myotonic dystrophy types 1 and 2","volume":"10","author":"Mankodi","year":"2001","journal-title":"Hum. Mol. Genet."},{"key":"10.1016\/j.isci.2022.104198_bib31","doi-asserted-by":"crossref","first-page":"35","DOI":"10.1016\/S1097-2765(02)00563-4","article-title":"Expanded CUG repeats trigger aberrant splicing of ClC-1 chloride channel pre-mRNA and hyperexcitability of skeletal muscle in myotonic dystrophy","volume":"10","author":"Mankodi","year":"2002","journal-title":"Mol. Cell"},{"key":"10.1016\/j.isci.2022.104198_bib32","doi-asserted-by":"crossref","first-page":"209","DOI":"10.1038\/srep00209","article-title":"CUGBP1 and MBNL1 preferentially bind to 3\u2032 UTRs and facilitate mRNA decay","volume":"2","author":"Masuda","year":"2012","journal-title":"Sci. Rep."},{"key":"10.1016\/j.isci.2022.104198_bib33","doi-asserted-by":"crossref","DOI":"10.3791\/58687-v","article-title":"RNA-based reprogramming of human primary fibroblasts into induced pluripotent stem cells","author":"McGrath","year":"2018","journal-title":"J.\u00a0Vis. Exp."},{"key":"10.1016\/j.isci.2022.104198_bib34","first-page":"154","article-title":"Clinical aspects, molecular pathomechanisms and management of myotonic dystrophies","volume":"32","author":"Meola","year":"2013","journal-title":"Acta Myol."},{"key":"10.1016\/j.isci.2022.104198_bib35","doi-asserted-by":"crossref","first-page":"4439","DOI":"10.1093\/emboj\/19.17.4439","article-title":"Recruitment of human muscleblind proteins to (CUG)(n) expansions associated with myotonic dystrophy","volume":"19","author":"Miller","year":"2000","journal-title":"EMBO J."},{"key":"10.1016\/j.isci.2022.104198_bib36","doi-asserted-by":"crossref","first-page":"13732","DOI":"10.1021\/ja074560a","article-title":"Design of DNA minor groove binding diamidines that recognize GC base pair sequences: a dimeric-hinge interaction motif","volume":"129","author":"Munde","year":"2007","journal-title":"J.\u00a0Am. Chem. Soc."},{"key":"10.1016\/j.isci.2022.104198_bib37","doi-asserted-by":"crossref","first-page":"108634","DOI":"10.1016\/j.celrep.2020.108634","article-title":"Transcriptome alterations in myotonic dystrophy frontal cortex","volume":"34","author":"Otero","year":"2021","journal-title":"Cell Rep."},{"key":"10.1016\/j.isci.2022.104198_bib38","first-page":"876","article-title":"Diamidines for human African trypanosomiasis","volume":"11","author":"Paine","year":"2010","journal-title":"Curr. Opin. Investig. Drugs"},{"key":"10.1016\/j.isci.2022.104198_bib39","doi-asserted-by":"crossref","first-page":"181","DOI":"10.1016\/j.nbd.2009.07.009","article-title":"Absence of a differentiation defect in muscle satellite cells from DM2 patients","volume":"36","author":"Pelletier","year":"2009","journal-title":"Neurobiol. Dis."},{"key":"10.1016\/j.isci.2022.104198_bib40","doi-asserted-by":"crossref","first-page":"748","DOI":"10.2353\/ajpath.2009.090047","article-title":"Expression of RNA CCUG repeats dysregulates translation and degradation of proteins in myotonic dystrophy 2 patients","volume":"175","author":"Salisbury","year":"2009","journal-title":"Am. J. Pathol."},{"key":"10.1016\/j.isci.2022.104198_bib41","doi-asserted-by":"crossref","first-page":"40","DOI":"10.1038\/ng704","article-title":"Aberrant regulation of insulin receptor alternative splicing is associated with insulin resistance in myotonic dystrophy","volume":"29","author":"Savkur","year":"2001","journal-title":"Nat. Genet."},{"key":"10.1016\/j.isci.2022.104198_bib42","doi-asserted-by":"crossref","first-page":"2009","DOI":"10.1038\/s41467-018-04370-x","article-title":"rbFOX1\/MBNL1 competition for CCUG RNA repeats binding contributes to myotonic dystrophy type 1\/type 2 differences","volume":"9","author":"Sellier","year":"2018","journal-title":"Nat. Commun."},{"key":"10.1016\/j.isci.2022.104198_bib43","doi-asserted-by":"crossref","first-page":"E5593","DOI":"10.1073\/pnas.1419161111","article-title":"rMATS: robust and flexible detection of differential alternative splicing from replicate RNA-Seq data","volume":"111","author":"Shen","year":"2014","journal-title":"Proc. Natl. Acad. Sci. U\u00a0S\u00a0A"},{"key":"10.1016\/j.isci.2022.104198_bib44","doi-asserted-by":"crossref","first-page":"5770","DOI":"10.1021\/acs.jmedchem.5b00356","article-title":"Biological efficacy and toxicity of diamidines in myotonic dystrophy type 1 models","volume":"58","author":"Siboni","year":"2015","journal-title":"J.\u00a0Med. Chem."},{"key":"10.1016\/j.isci.2022.104198_bib45","doi-asserted-by":"crossref","first-page":"22","DOI":"10.15252\/emmm.201707850","article-title":"G-quadruplex-binding small molecules ameliorate C9orf72 FTD\/ALS pathology in\u00a0vitro and in\u00a0vivo","volume":"10","author":"Simone","year":"2018","journal-title":"EMBO Mol. Med."},{"key":"10.1016\/j.isci.2022.104198_bib46","doi-asserted-by":"crossref","DOI":"10.3390\/ijms19124104","article-title":"Dissecting pathogenetic mechanisms and therapeutic strategies in Drosophila models of myotonic dystrophy type 1","volume":"19","author":"Souidi","year":"2018","journal-title":"Int. J. Mol. Sci."},{"key":"10.1016\/j.isci.2022.104198_bib47","doi-asserted-by":"crossref","first-page":"4005","DOI":"10.1093\/nar\/gkw229","article-title":"Pharmacologic efficacy of PU.1 inhibition by heterocyclic dications: a mechanistic analysis","volume":"44","author":"Stephens","year":"2016","journal-title":"Nucleic Acids Res."},{"key":"10.1016\/j.isci.2022.104198_bib48","doi-asserted-by":"crossref","DOI":"10.3390\/ijms20133365","article-title":"Short tandem repeat expansions and RNA-mediated pathogenesis in myotonic dystrophy","volume":"20","author":"Sznajder","year":"2019","journal-title":"Int. J. Mol. Sci."},{"key":"10.1016\/j.isci.2022.104198_bib49","doi-asserted-by":"crossref","first-page":"4234","DOI":"10.1073\/pnas.1716617115","article-title":"Intron retention induced by microsatellite expansions as a disease biomarker","volume":"115","author":"Sznajder","year":"2018","journal-title":"Proc. Natl. Acad. Sci. U\u00a0S\u00a0A"},{"key":"10.1016\/j.isci.2022.104198_bib50","first-page":"325","article-title":"Reprogramming human dermal fibroblast into induced pluripotent stem cells using nonintegrative Sendai virus for transduction","volume":"40","author":"Tai","year":"2018","journal-title":"Malays. J. Pathol."},{"key":"10.1016\/j.isci.2022.104198_bib51","doi-asserted-by":"crossref","first-page":"995","DOI":"10.1083\/jcb.128.6.995","article-title":"Foci of trinucleotide repeat transcripts in nuclei of myotonic dystrophy cells and tissues","volume":"128","author":"Taneja","year":"1995","journal-title":"J.\u00a0Cell Biol."},{"key":"10.1016\/j.isci.2022.104198_bib52","doi-asserted-by":"crossref","first-page":"e1734","DOI":"10.1371\/journal.pntd.0001734","article-title":"Pharmacology of DB844, an orally active aza analogue of pafuramidine, in a monkey model of second stage human African trypanosomiasis","volume":"6","author":"Thuita","year":"2012","journal-title":"PLoS Negl. Trop. Dis."},{"key":"10.1016\/j.isci.2022.104198_bib53","doi-asserted-by":"crossref","first-page":"8474","DOI":"10.1021\/acs.jmedchem.1c00414","article-title":"A druglike small molecule that targets r(CCUG) repeats in myotonic dystrophy type 2 facilitates degradation by RNA quality control pathways","volume":"64","author":"Wagner-Griffin","year":"2021","journal-title":"J.\u00a0Med. Chem."},{"key":"10.1016\/j.isci.2022.104198_bib54","doi-asserted-by":"crossref","first-page":"710","DOI":"10.1016\/j.cell.2012.06.041","article-title":"Transcriptome-wide regulation of pre-mRNA splicing and mRNA localization by muscleblind proteins","volume":"150","author":"Wang","year":"2012","journal-title":"Cell"},{"key":"10.1016\/j.isci.2022.104198_bib55","doi-asserted-by":"crossref","first-page":"11418","DOI":"10.1523\/JNEUROSCI.2352-16.2016","article-title":"Dysregulation of mRNA localization and translation in genetic disease","volume":"36","author":"Wang","year":"2016","journal-title":"J.\u00a0Neurosci."},{"key":"10.1016\/j.isci.2022.104198_bib56","doi-asserted-by":"crossref","first-page":"18551","DOI":"10.1073\/pnas.0903234106","article-title":"Pentamidine reverses the splicing defects associated with myotonic dystrophy","volume":"106","author":"Warf","year":"2009","journal-title":"Proc. Natl. Acad. Sci. U\u00a0S\u00a0A"}],"container-title":["iScience"],"original-title":[],"language":"en","link":[{"URL":"https:\/\/api.elsevier.com\/content\/article\/PII:S2589004222004680?httpAccept=text\/xml","content-type":"text\/xml","content-version":"vor","intended-application":"text-mining"},{"URL":"https:\/\/api.elsevier.com\/content\/article\/PII:S2589004222004680?httpAccept=text\/plain","content-type":"text\/plain","content-version":"vor","intended-application":"text-mining"}],"deposited":{"date-parts":[[2025,11,8]],"date-time":"2025-11-08T19:40:27Z","timestamp":1762630827000},"score":1,"resource":{"primary":{"URL":"https:\/\/linkinghub.elsevier.com\/retrieve\/pii\/S2589004222004680"}},"subtitle":[],"short-title":[],"issued":{"date-parts":[[2022,5]]},"references-count":56,"journal-issue":{"issue":"5","published-print":{"date-parts":[[2022,5]]}},"alternative-id":["S2589004222004680"],"URL":"https:\/\/doi.org\/10.1016\/j.isci.2022.104198","relation":{},"ISSN":["2589-0042"],"issn-type":[{"value":"2589-0042","type":"print"}],"subject":[],"published":{"date-parts":[[2022,5]]},"assertion":[{"value":"Elsevier","name":"publisher","label":"This article is maintained by"},{"value":"Molecular characterization of myotonic dystrophy fibroblast cell lines for use in small molecule screening","name":"articletitle","label":"Article Title"},{"value":"iScience","name":"journaltitle","label":"Journal Title"},{"value":"https:\/\/doi.org\/10.1016\/j.isci.2022.104198","name":"articlelink","label":"CrossRef DOI link to publisher maintained version"},{"value":"article","name":"content_type","label":"Content Type"},{"value":"\u00a9 2022 The Author(s).","name":"copyright","label":"Copyright"}],"article-number":"104198"}}