{"status":"ok","message-type":"work","message-version":"1.0.0","message":{"indexed":{"date-parts":[[2026,7,31]],"date-time":"2026-07-31T00:09:56Z","timestamp":1785456596274,"version":"3.56.0"},"reference-count":24,"publisher":"Elsevier BV","issue":"8","license":[{"start":{"date-parts":[[2026,8,1]],"date-time":"2026-08-01T00:00:00Z","timestamp":1785542400000},"content-version":"tdm","delay-in-days":0,"URL":"https:\/\/www.elsevier.com\/tdm\/userlicense\/1.0\/"},{"start":{"date-parts":[[2026,8,1]],"date-time":"2026-08-01T00:00:00Z","timestamp":1785542400000},"content-version":"tdm","delay-in-days":0,"URL":"https:\/\/www.elsevier.com\/legal\/tdmrep-license"}],"content-domain":{"domain":["clinicalkey.com","clinicalkey.com.au","clinicalkey.es","clinicalkey.fr","clinicalkey.jp","elsevier.com","sciencedirect.com"],"crossmark-restriction":true},"short-container-title":["Transplantation and Cellular Therapy"],"published-print":{"date-parts":[[2026,8]]},"DOI":"10.1016\/j.jtct.2026.04.046","type":"journal-article","created":{"date-parts":[[2026,5,19]],"date-time":"2026-05-19T16:01:27Z","timestamp":1779206487000},"page":"972-977","update-policy":"https:\/\/doi.org\/10.1016\/elsevier_cm_policy","source":"Crossref","is-referenced-by-count":1,"title":["Hematopoietic Stem Cell Transplantation in Infantile Osteopetrosis: Lessons from a Resource-Limited Setting"],"prefix":"10.1016","volume":"32","author":[{"ORCID":"https:\/\/orcid.org\/0009-0005-8073-063X","authenticated-orcid":false,"given":"Hashim","family":"Khan","sequence":"first","affiliation":[],"role":[{"vocabulary":"crossref","role":"author"}]},{"ORCID":"https:\/\/orcid.org\/0000-0003-1279-7160","authenticated-orcid":false,"given":"Tariq","family":"Ghafoor","sequence":"additional","affiliation":[],"role":[{"vocabulary":"crossref","role":"author"}]},{"given":"Tariq Azam","family":"Khattak","sequence":"additional","affiliation":[],"role":[{"vocabulary":"crossref","role":"author"}]},{"given":"Raheel","family":"Iftikhar","sequence":"additional","affiliation":[],"role":[{"vocabulary":"crossref","role":"author"}]},{"given":"Uzma","family":"Rahim","sequence":"additional","affiliation":[],"role":[{"vocabulary":"crossref","role":"author"}]},{"given":"Beenish","family":"Hira","sequence":"additional","affiliation":[],"role":[{"vocabulary":"crossref","role":"author"}]},{"family":"Qudratullah","sequence":"additional","affiliation":[],"role":[{"vocabulary":"crossref","role":"author"}]},{"given":"Hamza","family":"Khan","sequence":"additional","affiliation":[],"role":[{"vocabulary":"crossref","role":"author"}]}],"member":"78","reference":[{"issue":"1","key":"10.1016\/j.jtct.2026.04.046_bib0001","doi-asserted-by":"crossref","first-page":"314","DOI":"10.1186\/s13023-021-01955-6","article-title":"Haploidentical haematopoietic stem cell transplantation for malignant infantile osteopetrosis and intermediate osteopetrosis: a retrospective analysis of a single centre","volume":"16","author":"Zhu","year":"2021","journal-title":"Orphanet J Rare Dis"},{"issue":"6","key":"10.1016\/j.jtct.2026.04.046_bib0002","doi-asserted-by":"crossref","DOI":"10.1002\/pbc.27010","article-title":"Successful hematopoietic stem cell transplantation for osteopetrosis using reduced intensity conditioning","volume":"65","author":"Shadur","year":"2018","journal-title":"Pediatr Blood Cancer"},{"issue":"2","key":"10.1016\/j.jtct.2026.04.046_bib0003","first-page":"135","article-title":"Osteopetrosis: classification, pathomorphology, genetic disorders, clinical manifestations (literature review and clinical case report)","volume":"9","author":"Povoroznyuk","year":"2019","journal-title":"\u0411\u043e\u043b\u044c \u0421\u0443\u0441\u0442\u0430\u0432\u044b \u041f\u043e\u0437\u0432\u043e\u043d\u043e\u0447\u043d\u0438\u043a"},{"issue":"3","key":"10.1016\/j.jtct.2026.04.046_bib0004","doi-asserted-by":"crossref","DOI":"10.1002\/pbc.28841","article-title":"How we approach malignant infantile osteopetrosis","volume":"68","author":"Even-Or","year":"2021","journal-title":"Pediatr Blood Cancer"},{"issue":"6","key":"10.1016\/j.jtct.2026.04.046_bib0005","doi-asserted-by":"crossref","first-page":"862","DOI":"10.1182\/bloodadvances.2018025890","article-title":"Stem cell transplantation for osteopetrosis in patients beyond the age of 5 years","volume":"3","author":"Stepensky","year":"2019","journal-title":"Blood Adv"},{"key":"10.1016\/j.jtct.2026.04.046_bib0006","series-title":"The EBMT Handbook: Hematopoietic Stem Cell Transplantation and Cellular Therapies","author":"Carreras","year":"2019"},{"issue":"9","key":"10.1016\/j.jtct.2026.04.046_bib0007","doi-asserted-by":"crossref","first-page":"522","DOI":"10.1038\/nrendo.2013.137","article-title":"Osteopetrosis: genetics, treatment and new insights into osteoclast function","volume":"9","author":"Sobacchi","year":"2013","journal-title":"Nat Rev Endocrinol"},{"key":"10.1016\/j.jtct.2026.04.046_bib0008","series-title":"StatPearls","article-title":"Osteopetrosis","author":"Bailey","year":"2023"},{"issue":"1","key":"10.1016\/j.jtct.2026.04.046_bib0009","doi-asserted-by":"crossref","first-page":"148","DOI":"10.1186\/s12881-017-0506-4","article-title":"Identification and in silico characterization of a novel p.P208PfsX1 mutation in V-ATPase a3 subunit associated with autosomal recessive osteopetrosis in a Pakistani family","volume":"18","author":"Ajmal","year":"2017","journal-title":"BMC Med Genet"},{"key":"10.1016\/j.jtct.2026.04.046_bib0010","series-title":"GeneReviews\u00ae","article-title":"CLCN7-related osteopetrosis","author":"Sobacchi","year":"2007"},{"issue":"5","key":"10.1016\/j.jtct.2026.04.046_bib0011","doi-asserted-by":"crossref","DOI":"10.1242\/dmm.048940","article-title":"Autosomal recessive osteopetrosis: mechanisms and treatments","volume":"14","author":"Penna","year":"2021","journal-title":"Dis Model Mech"},{"key":"10.1016\/j.jtct.2026.04.046_bib0012","article-title":"The European Blood and Marrow Transplantation Textbook for Nurses: Under the Auspices of EBMT [Internet]","author":"Hutt","year":"2018"},{"issue":"4","key":"10.1016\/j.jtct.2026.04.046_bib0013","doi-asserted-by":"crossref","first-page":"605","DOI":"10.1016\/j.bbmt.2015.09.014","article-title":"The incidence and severity of oral mucositis among allogeneic hematopoietic stem cell transplantation patients: a systematic review","volume":"22","author":"Chaudhry","year":"2016","journal-title":"Biol Blood Marrow Transpl"},{"issue":"2","key":"10.1016\/j.jtct.2026.04.046_bib0014","doi-asserted-by":"crossref","first-page":"82","DOI":"10.2991\/chi.d.200426.001","article-title":"Comparison of conventional cyclophosphamide versus fludarabine-based conditioning in high-risk aplastic anemia patients undergoing matched-related donor transplantation","volume":"2","author":"Iftikhar","year":"2020","journal-title":"Clin Hematol Int"},{"key":"10.1016\/j.jtct.2026.04.046_bib0015","series-title":"StatPearls","article-title":"Oral mucositis","author":"Bell","year":"2023"},{"issue":"8","key":"10.1016\/j.jtct.2026.04.046_bib0016","doi-asserted-by":"crossref","first-page":"1361","DOI":"10.1038\/s41409-019-0492-6","article-title":"Validation of treatment outcomes according to revised severity criteria from European Society for Blood and Marrow Transplantation (EBMT) for sinusoidal obstruction syndrome\/veno-occlusive disease (SOS\/VOD)","volume":"54","author":"Yoon","year":"2019","journal-title":"Bone Marrow Transpl"},{"issue":"1","key":"10.1016\/j.jtct.2026.04.046_bib0017","doi-asserted-by":"crossref","first-page":"17","DOI":"10.1038\/s41409-023-02107-z","article-title":"Acute GVHD classification based on the dynamics of GVHD skin involvement from its appearance to the start of systemic treatment","volume":"59","author":"Milone","year":"2024","journal-title":"Bone Marrow Transpl"},{"issue":"3","key":"10.1016\/j.jtct.2026.04.046_bib0018","doi-asserted-by":"crossref","first-page":"389","DOI":"10.1016\/j.bbmt.2014.12.001","article-title":"National Institutes of Health Consensus Development Project on Criteria for Clinical Trials in Chronic Graft-versus-Host Disease: I. The 2014 Diagnosis and Staging Working Group report","volume":"21","author":"Jagasia","year":"2015","journal-title":"Biol Blood Marrow Transpl"},{"key":"10.1016\/j.jtct.2026.04.046_bib0019","doi-asserted-by":"crossref","DOI":"10.1016\/j.bone.2022.116634","article-title":"Hematopoietic stem cell transplantation, a curative approach in infantile osteopetrosis","volume":"167","author":"Schulz","year":"2023","journal-title":"Bone"},{"issue":"6 Pt 1","key":"10.1016\/j.jtct.2026.04.046_bib0020","doi-asserted-by":"crossref","first-page":"896","DOI":"10.1016\/S0022-3476(05)82004-9","article-title":"Bone marrow transplantation for autosomal recessive osteopetrosis. A report from the Working Party on Inborn Errors of the European Bone Marrow Transplantation Group","volume":"125","author":"Gerritsen","year":"1994","journal-title":"J Pediatr"},{"issue":"4","key":"10.1016\/j.jtct.2026.04.046_bib0021","doi-asserted-by":"crossref","first-page":"831","DOI":"10.1002\/pbc.21425","article-title":"Defibrotide in the prevention and treatment of veno-occlusive disease in autologous and allogeneic stem cell transplantation in children","volume":"50","author":"Qureshi","year":"2008","journal-title":"Pediatr Blood Cancer"},{"issue":"8","key":"10.1016\/j.jtct.2026.04.046_bib0022","doi-asserted-by":"crossref","first-page":"547","DOI":"10.1038\/sj.bmt.1705485","article-title":"Stem cell transplantation in children with infantile osteopetrosis is associated with a high incidence of VOD, which could be prevented with defibrotide","volume":"38","author":"Corbacioglu","year":"2006","journal-title":"Bone Marrow Transpl"},{"issue":"2","key":"10.1016\/j.jtct.2026.04.046_bib0023","doi-asserted-by":"crossref","first-page":"82","DOI":"10.1016\/j.bbmt.2007.12.228","article-title":"219: Hypercalcemia after Hematopoietic Stem Cell Transplantation for Osteopetrosis","volume":"14","author":"Martinez","year":"2008","journal-title":"Bio. Blood Marrow Trans."},{"key":"10.1016\/j.jtct.2026.04.046_bib0024","series-title":"The EBMT Handbook: Hematopoietic Cell Transplantation and Cellular Therapies","article-title":"Inborn errors of metabolism and osteopetrosis","author":"Wynn","year":"2024"}],"container-title":["Transplantation and Cellular Therapy"],"original-title":[],"language":"en","link":[{"URL":"https:\/\/api.elsevier.com\/content\/article\/PII:S2666636726003301?httpAccept=text\/xml","content-type":"text\/xml","content-version":"vor","intended-application":"text-mining"},{"URL":"https:\/\/api.elsevier.com\/content\/article\/PII:S2666636726003301?httpAccept=text\/plain","content-type":"text\/plain","content-version":"vor","intended-application":"text-mining"}],"deposited":{"date-parts":[[2026,7,30]],"date-time":"2026-07-30T12:37:12Z","timestamp":1785415032000},"score":1,"resource":{"primary":{"URL":"https:\/\/linkinghub.elsevier.com\/retrieve\/pii\/S2666636726003301"}},"subtitle":[],"short-title":[],"issued":{"date-parts":[[2026,8]]},"references-count":24,"journal-issue":{"issue":"8","published-print":{"date-parts":[[2026,8]]}},"alternative-id":["S2666636726003301"],"URL":"https:\/\/doi.org\/10.1016\/j.jtct.2026.04.046","relation":{},"ISSN":["2666-6367"],"issn-type":[{"value":"2666-6367","type":"print"}],"subject":[],"published":{"date-parts":[[2026,8]]},"assertion":[{"value":"Elsevier","name":"publisher","label":"This article is maintained by"},{"value":"Hematopoietic Stem Cell Transplantation in Infantile Osteopetrosis: Lessons from a Resource-Limited Setting","name":"articletitle","label":"Article Title"},{"value":"Transplantation and Cellular Therapy","name":"journaltitle","label":"Journal Title"},{"value":"https:\/\/doi.org\/10.1016\/j.jtct.2026.04.046","name":"articlelink","label":"CrossRef DOI link to publisher maintained version"},{"value":"article","name":"content_type","label":"Content Type"},{"value":"\u00a9 2026 American Society for Transplantation and Cellular Therapy. Published by Elsevier Inc. All rights are reserved, including those for text and data mining, AI training, and similar technologies.","name":"copyright","label":"Copyright"}]}}