{"status":"ok","message-type":"work","message-version":"1.0.0","message":{"indexed":{"date-parts":[[2026,9,29]],"date-time":"2026-09-29T10:23:17Z","timestamp":1790677397510,"version":"4.1.0"},"reference-count":31,"publisher":"Elsevier BV","issue":"4","license":[{"start":{"date-parts":[[2022,4,1]],"date-time":"2022-04-01T00:00:00Z","timestamp":1648771200000},"content-version":"tdm","delay-in-days":0,"URL":"https:\/\/www.elsevier.com\/tdm\/userlicense\/1.0\/"},{"start":{"date-parts":[[2022,4,1]],"date-time":"2022-04-01T00:00:00Z","timestamp":1648771200000},"content-version":"tdm","delay-in-days":0,"URL":"https:\/\/www.elsevier.com\/legal\/tdmrep-license"},{"start":{"date-parts":[[2022,2,9]],"date-time":"2022-02-09T00:00:00Z","timestamp":1644364800000},"content-version":"vor","delay-in-days":0,"URL":"http:\/\/creativecommons.org\/licenses\/by\/4.0\/"}],"content-domain":{"domain":["clinicalkey.com","clinicalkey.com.au","clinicalkey.es","clinicalkey.fr","clinicalkey.jp","nmd-journal.com","elsevier.com","sciencedirect.com"],"crossmark-restriction":true},"short-container-title":["Neuromuscular Disorders"],"published-print":{"date-parts":[[2022,4]]},"DOI":"10.1016\/j.nmd.2022.02.002","type":"journal-article","created":{"date-parts":[[2022,2,17]],"date-time":"2022-02-17T02:46:25Z","timestamp":1645065985000},"page":"284-294","update-policy":"https:\/\/doi.org\/10.1016\/elsevier_cm_policy","source":"Crossref","is-referenced-by-count":6,"title":["Safety and effectiveness of resistance training in patients with late onset Pompe disease - a pilot study"],"prefix":"10.1016","volume":"32","author":[{"given":"Caleb","family":"Bhatnagar","sequence":"first","affiliation":[],"role":[{"vocabulary":"crossref","role":"author"}]},{"given":"Jeet","family":"Shah","sequence":"additional","affiliation":[],"role":[{"vocabulary":"crossref","role":"author"}]},{"given":"Bhumi","family":"Ramani","sequence":"additional","affiliation":[],"role":[{"vocabulary":"crossref","role":"author"}]},{"given":"Abhilasha","family":"Surampalli","sequence":"additional","affiliation":[],"role":[{"vocabulary":"crossref","role":"author"}]},{"ORCID":"https:\/\/orcid.org\/0000-0003-4158-1086","authenticated-orcid":false,"given":"Mahima","family":"Avanti","sequence":"additional","affiliation":[],"role":[{"vocabulary":"crossref","role":"author"}]},{"given":"Shlomit","family":"Radom-Aizik","sequence":"additional","affiliation":[],"role":[{"vocabulary":"crossref","role":"author"}]},{"given":"Margaret","family":"Knight","sequence":"additional","affiliation":[],"role":[{"vocabulary":"crossref","role":"author"}]},{"given":"Lan","family":"Weiss","sequence":"additional","affiliation":[],"role":[{"vocabulary":"crossref","role":"author"}]},{"given":"Vince","family":"Caiozzo","sequence":"additional","affiliation":[],"role":[{"vocabulary":"crossref","role":"author"}]},{"ORCID":"https:\/\/orcid.org\/0000-0003-1567-4449","authenticated-orcid":false,"given":"Virginia","family":"Kimonis","sequence":"additional","affiliation":[],"role":[{"vocabulary":"crossref","role":"author"}]}],"member":"78","reference":[{"key":"10.1016\/j.nmd.2022.02.002_bib0001","unstructured":"Leslie N, Bailey L. Pompe Disease. 2007 Aug 31 [Updated 2017 May 11]. In: Adam MP, Ardinger HH, Pagon RA, et al., editors. GeneReviews\u00ae [Internet]. Seattle (WA): University of Washington, Seattle; 1993-2022. Available from: https:\/\/www.ncbi.nlm.nih.gov\/books\/NBK1261\/."},{"key":"10.1016\/j.nmd.2022.02.002_bib0002","doi-asserted-by":"crossref","first-page":"1396","DOI":"10.1056\/NEJMoa0909859","article-title":"A randomized study of alglucosidase alfa in late-onset Pompe's disease","volume":"362","author":"van der Ploeg","year":"2010","journal-title":"N Engl J Med"},{"key":"10.1016\/j.nmd.2022.02.002_bib0003","doi-asserted-by":"crossref","first-page":"2365","DOI":"10.1212\/WNL.0000000000004711","article-title":"Long-term benefit of enzyme replacement therapy in Pompe disease: a 5-year prospective study","volume":"89","author":"Kuperus","year":"2017","journal-title":"Neurology"},{"key":"10.1016\/j.nmd.2022.02.002_bib0004","doi-asserted-by":"crossref","first-page":"276","DOI":"10.21037\/atm.2019.06.48","article-title":"Variable clinical features and genotype-phenotype correlations in 18 patients with late-onset Pompe disease","volume":"7","author":"Alandy-Dy","year":"2019","journal-title":"Ann Transl Med"},{"key":"10.1016\/j.nmd.2022.02.002_bib0005","doi-asserted-by":"crossref","first-page":"70","DOI":"10.1002\/mus.20665","article-title":"Modification of the natural history of adult-onset acid maltase deficiency by nutrition and exercise therapy","volume":"35","author":"Slonim","year":"2007","journal-title":"Muscle Nerve"},{"key":"10.1016\/j.nmd.2022.02.002_bib0006","doi-asserted-by":"crossref","first-page":"282","DOI":"10.21037\/atm.2019.05.52","article-title":"Nutrition and exercise in Pompe disease","volume":"7","author":"Tarnopolsky","year":"2019","journal-title":"Ann Transl Med"},{"key":"10.1016\/j.nmd.2022.02.002_bib0007","doi-asserted-by":"crossref","first-page":"279","DOI":"10.1016\/j.ymgme.2011.05.013","article-title":"Effect of aerobic and resistance exercise training on late-onset Pompe disease patients receiving enzyme replacement therapy","volume":"104","author":"Terzis","year":"2011","journal-title":"Mol Genet Metab"},{"key":"10.1016\/j.nmd.2022.02.002_bib0008","doi-asserted-by":"crossref","first-page":"669","DOI":"10.1016\/j.ymgme.2012.10.020","article-title":"Effects of exercise training during infusion on late-onset Pompe disease patients receiving enzyme replacement therapy","volume":"107","author":"Terzis","year":"2012","journal-title":"Mol Genet Metab"},{"key":"10.1016\/j.nmd.2022.02.002_bib0009","doi-asserted-by":"crossref","first-page":"817","DOI":"10.1016\/j.apmr.2014.11.020","article-title":"Exercise training in adults with Pompe disease: the effects on pain, fatigue, and functioning","volume":"96","author":"Favejee","year":"2015","journal-title":"Arch Phys Med Rehabil"},{"key":"10.1016\/j.nmd.2022.02.002_bib0010","doi-asserted-by":"crossref","first-page":"87","DOI":"10.1186\/s13023-015-0303-0","article-title":"Safety and efficacy of exercise training in adults with Pompe disease: evalution of endurance, muscle strength and core stability before and after a 12 week training program","volume":"10","author":"van den Berg","year":"2015","journal-title":"Orphanet J Rare Dis"},{"key":"10.1016\/j.nmd.2022.02.002_bib0011","doi-asserted-by":"crossref","first-page":"417","DOI":"10.1016\/j.ymgme.2011.05.006","article-title":"Increased inspiratory and expiratory muscle strength following respiratory muscle strength training (RMST) in two patients with late-onset Pompe disease","volume":"104","author":"Jones","year":"2011","journal-title":"Mol Genet Metab"},{"key":"10.1016\/j.nmd.2022.02.002_bib0012","doi-asserted-by":"crossref","first-page":"120","DOI":"10.1016\/j.ymgme.2015.09.003","article-title":"Respiratory muscle training (RMT) in late-onset Pompe disease (LOPD): effects of training and detraining","volume":"117","author":"Jones","year":"2016","journal-title":"Mol Genet Metab"},{"key":"10.1016\/j.nmd.2022.02.002_bib0013","doi-asserted-by":"crossref","first-page":"904","DOI":"10.1016\/j.nmd.2020.09.023","article-title":"Respiratory muscle training in late-onset Pompe disease: results of a sham-controlled clinical trial","volume":"30","author":"Jones","year":"2020","journal-title":"Neuromusc Disord NMD"},{"key":"10.1016\/j.nmd.2022.02.002_bib0014","doi-asserted-by":"crossref","first-page":"133","DOI":"10.1007\/s00415-018-9112-4","article-title":"Safety and efficacy of short- and long-term inspiratory muscle training in late-onset Pompe disease (LOPD): a pilot study","volume":"266","author":"Wenninger","year":"2019","journal-title":"J Neurol"},{"key":"10.1016\/j.nmd.2022.02.002_bib0015","first-page":"67","article-title":"Respiratory muscle training with enzyme replacement therapy improves muscle strength in late - onset Pompe disease","volume":"5","author":"Jevnikar","year":"2015","journal-title":"Mol Genet Metab Rep"},{"key":"10.1016\/j.nmd.2022.02.002_bib0016","doi-asserted-by":"crossref","first-page":"555","DOI":"10.1007\/s00408-016-9881-4","article-title":"Inspiratory muscle training in late-onset Pompe disease: the effects on pulmonary function tests, quality of life, and sleep quality","volume":"194","author":"Aslan","year":"2016","journal-title":"Lung"},{"key":"10.1016\/j.nmd.2022.02.002_bib0017","doi-asserted-by":"crossref","first-page":"142","DOI":"10.1016\/j.nmd.2009.11.003","article-title":"Inclusion body myositis: MRC centre for neuromuscular diseases, IBM workshop, London, 13 June 2008","volume":"20","author":"Hilton-Jones","year":"2010","journal-title":"Neuromuscul Disord"},{"issue":"1","key":"10.1016\/j.nmd.2022.02.002_bib0018","doi-asserted-by":"crossref","first-page":"111","DOI":"10.1164\/ajrccm.166.1.at1102","article-title":"ATS statement: guidelines for the six-minute walk test","volume":"166","year":"2002","journal-title":"Am J Respir Crit Care Med"},{"key":"10.1016\/j.nmd.2022.02.002_bib0019","doi-asserted-by":"crossref","first-page":"518","DOI":"10.1164\/rccm.166.4.518","article-title":"ATS\/ERS statement on respiratory muscle testing","volume":"166","year":"2002","journal-title":"Am J Respir Crit Care Med"},{"key":"10.1016\/j.nmd.2022.02.002_bib0020","first-page":"1348","article-title":"The assessment of maximal respiratory mouth pressures in adults","volume":"54","author":"Evans","year":"2009","journal-title":"Respir Care"},{"key":"10.1016\/j.nmd.2022.02.002_bib0021","doi-asserted-by":"crossref","first-page":"55","DOI":"10.5271\/sjweh.1815","article-title":"Psychophysical scaling with applications in physical work and the perception of exertion","volume":"16","author":"Borg","year":"1990","journal-title":"Scand J Work Environ Health"},{"key":"10.1016\/j.nmd.2022.02.002_bib0022","first-page":"255","article-title":"Effects of respiratory muscle training (RMT) in children with infantile-onset Pompe disease and respiratory muscle weakness","volume":"7","author":"Jones","year":"2014","journal-title":"J Pediatr Rehabil Med"},{"key":"10.1016\/j.nmd.2022.02.002_bib0023","doi-asserted-by":"crossref","first-page":"52","DOI":"10.1186\/s13023-017-0598-0","article-title":"Maximum inspiratory pressure as a clinically meaningful trial endpoint for neuromuscular diseases: a comprehensive review of the literature","volume":"12","author":"Schoser","year":"2017","journal-title":"Orphanet J Rare Dis"},{"key":"10.1016\/j.nmd.2022.02.002_bib0024","doi-asserted-by":"crossref","first-page":"590","DOI":"10.1159\/000091392","article-title":"Evaluation of inspiratory muscle function in a healthy Austrian population-practical aspects","volume":"73","author":"Reiter","year":"2006","journal-title":"Respiration"},{"key":"10.1016\/j.nmd.2022.02.002_bib0025","first-page":"82","article-title":"The pressure-volume diagram of the thorax and lung","volume":"5","author":"Rahn","year":"1946","journal-title":"Fed Proc"},{"key":"10.1016\/j.nmd.2022.02.002_bib0026","first-page":"1524","article-title":"Treatment of respiratory impairment in patients with motor neuron disease in the Netherlands: patient preference and timing of referral","volume":"20","author":"Raaphorst","year":"2013","journal-title":"Eur J Neurol Off J Eur Fed Neurol Soc"},{"key":"10.1016\/j.nmd.2022.02.002_bib0027","doi-asserted-by":"crossref","first-page":"593","DOI":"10.1007\/s00415-014-7613-3","article-title":"Sniff nasal inspiratory pressure as a prognostic factor of tracheostomy or death in amyotrophic lateral sclerosis","volume":"262","author":"Morgan","year":"2015","journal-title":"J Neurol"},{"key":"10.1016\/j.nmd.2022.02.002_bib0028","doi-asserted-by":"crossref","first-page":"593","DOI":"10.1007\/s00415-014-7613-3","article-title":"Sniff nasal inspiratory pressure as a prognostic factor of tracheostomy or death in amyotrophic lateral sclerosis","volume":"262","author":"Capazzo","year":"2015","journal-title":"J Neurol"},{"key":"10.1016\/j.nmd.2022.02.002_bib0029","doi-asserted-by":"crossref","first-page":"616","DOI":"10.1136\/thx.38.8.616","article-title":"Respiratory muscle and pulmonary function in polymyositis and other proximal myopathies","volume":"38","author":"Braun","year":"1983","journal-title":"Thorax"},{"key":"10.1016\/j.nmd.2022.02.002_bib0030","doi-asserted-by":"crossref","first-page":"859","DOI":"10.1007\/s10072-019-04178-7","article-title":"Adapted physical activity and therapeutic exercise in late-onset Pompe disease (LOPD): a two-step rehabilitative approach","volume":"41","author":"Iolascon","year":"2020","journal-title":"Neurol Sciences"},{"key":"10.1016\/j.nmd.2022.02.002_bib0031","first-page":"241","article-title":"The role of rehabilitation in the management of late-onset Pompe disease: a narrative review of the level of evidence","volume":"37","author":"Iolascon","year":"2018","journal-title":"Acta Myol"}],"container-title":["Neuromuscular Disorders"],"original-title":[],"language":"en","link":[{"URL":"https:\/\/api.elsevier.com\/content\/article\/PII:S0960896622000359?httpAccept=text\/xml","content-type":"text\/xml","content-version":"vor","intended-application":"text-mining"},{"URL":"https:\/\/api.elsevier.com\/content\/article\/PII:S0960896622000359?httpAccept=text\/plain","content-type":"text\/plain","content-version":"vor","intended-application":"text-mining"}],"deposited":{"date-parts":[[2025,10,18]],"date-time":"2025-10-18T08:12:23Z","timestamp":1760775143000},"score":1,"resource":{"primary":{"URL":"https:\/\/linkinghub.elsevier.com\/retrieve\/pii\/S0960896622000359"}},"subtitle":[],"short-title":[],"issued":{"date-parts":[[2022,4]]},"references-count":31,"journal-issue":{"issue":"4","published-print":{"date-parts":[[2022,4]]}},"alternative-id":["S0960896622000359"],"URL":"https:\/\/doi.org\/10.1016\/j.nmd.2022.02.002","relation":{},"ISSN":["0960-8966"],"issn-type":[{"value":"0960-8966","type":"print"}],"subject":[],"published":{"date-parts":[[2022,4]]},"assertion":[{"value":"Elsevier","name":"publisher","label":"This article is maintained by"},{"value":"Safety and effectiveness of resistance training in patients with late onset Pompe disease - a pilot study","name":"articletitle","label":"Article Title"},{"value":"Neuromuscular Disorders","name":"journaltitle","label":"Journal Title"},{"value":"https:\/\/doi.org\/10.1016\/j.nmd.2022.02.002","name":"articlelink","label":"CrossRef DOI link to publisher maintained version"},{"value":"article","name":"content_type","label":"Content Type"},{"value":"\u00a9 2022 The Author(s). Published by Elsevier B.V.","name":"copyright","label":"Copyright"}]}}