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Correction of disease-associated exon skipping by synthetic exon-specific activators.Nat Struct Biol 10: 120\u2013125, 2003.","journal-title":"Nat Struct Biol"},{"key":"30200235_CR71","doi-asserted-by":"crossref","first-page":"4114","DOI":"10.1073\/pnas.0633863100","volume":"100","author":"LA Skordis","year":"2003","unstructured":"Skordis LA, Dunckley MG, Yue B, Eperon IC, Muntoni F. Bi-functional antisense oligonucleotides provide a trans-acting splicing enhancer that stimulates SMN2 gene expression in patient fibroblasts.Proc Natl Acad Sci USA 100: 4114\u20134119, 2003.","journal-title":"Proc Natl Acad Sci USA"},{"key":"30200235_CR72","doi-asserted-by":"crossref","first-page":"1489","DOI":"10.1016\/j.chembiol.2004.08.024","volume":"11","author":"MR Lunn","year":"2004","unstructured":"Lunn MR, Root DE, Martino AM et al. 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