{"status":"ok","message-type":"work","message-version":"1.0.0","message":{"indexed":{"date-parts":[[2024,9,6]],"date-time":"2024-09-06T12:51:00Z","timestamp":1725627060689},"reference-count":10,"publisher":"Elsevier BV","license":[{"start":{"date-parts":[[2023,6,1]],"date-time":"2023-06-01T00:00:00Z","timestamp":1685577600000},"content-version":"tdm","delay-in-days":0,"URL":"https:\/\/www.elsevier.com\/tdm\/userlicense\/1.0\/"},{"start":{"date-parts":[[2023,6,1]],"date-time":"2023-06-01T00:00:00Z","timestamp":1685577600000},"content-version":"tdm","delay-in-days":0,"URL":"https:\/\/www.elsevier.com\/legal\/tdmrep-license"},{"start":{"date-parts":[[2023,3,13]],"date-time":"2023-03-13T00:00:00Z","timestamp":1678665600000},"content-version":"vor","delay-in-days":0,"URL":"http:\/\/creativecommons.org\/licenses\/by\/4.0\/"}],"content-domain":{"domain":["cell.com","elsevier.com","sciencedirect.com"],"crossmark-restriction":true},"short-container-title":["Molecular Therapy - Methods &amp; Clinical Development"],"published-print":{"date-parts":[[2023,6]]},"DOI":"10.1016\/j.omtm.2023.03.004","type":"journal-article","created":{"date-parts":[[2023,3,30]],"date-time":"2023-03-30T18:43:14Z","timestamp":1680201794000},"page":"160-161","update-policy":"http:\/\/dx.doi.org\/10.1016\/elsevier_cm_policy","source":"Crossref","is-referenced-by-count":1,"special_numbering":"C","title":["A gene therapy approach for the treatment of limb-girdle muscular dystrophy 2C\/R5"],"prefix":"10.1016","volume":"29","author":[{"given":"Hailey","family":"Hermann","sequence":"first","affiliation":[],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"Ryan D.","family":"Wuebbles","sequence":"additional","affiliation":[],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"Dean J.","family":"Burkin","sequence":"additional","affiliation":[],"role":[{"role":"author","vocabulary":"crossref"}]}],"member":"78","reference":[{"key":"10.1016\/j.omtm.2023.03.004_bib1","doi-asserted-by":"crossref","first-page":"1022","DOI":"10.1038\/s42003-022-03980-y","article-title":"The role of the dystrophin glycoprotein complex in muscle cell mechanotransduction","volume":"5","author":"Wilson","year":"2022","journal-title":"Commun. Biol."},{"key":"10.1016\/j.omtm.2023.03.004_bib2","doi-asserted-by":"crossref","first-page":"411","DOI":"10.2217\/nmt-2020-0066","article-title":"Unmet needs and evolving treatment for limb girdle muscular dystrophies","volume":"11","author":"Pozsgai","year":"2021","journal-title":"Neurodegener. Dis. Manag."},{"key":"10.1016\/j.omtm.2023.03.004_bib3","series-title":"Systemic AAV-Mediated \u03b3- Sarcoglycan\u00a0Gene Transfer Therapy Results in Dose-dependent Correction of Muscle Deficits in LGMD 2C\/R5 Mouse Model","author":"Seo","year":"2023"},{"key":"10.1016\/j.omtm.2023.03.004_bib4","doi-asserted-by":"crossref","first-page":"320","DOI":"10.1038\/sj.mt.6300027","article-title":"Design of tissue-specific regulatory cassettes for high-level rAAV- mediated expression in skeletal and cardiac muscle","volume":"15","author":"Salva","year":"2007","journal-title":"Mol. Ther."},{"key":"10.1016\/j.omtm.2023.03.004_bib5","doi-asserted-by":"crossref","first-page":"1021","DOI":"10.1016\/j.nmd.2021.07.014","article-title":"Sarcoglycanopathies: an update","volume":"31","author":"Vainzof","year":"2021","journal-title":"Neuromuscul. Disord."},{"key":"10.1016\/j.omtm.2023.03.004_bib6","doi-asserted-by":"crossref","first-page":"744","DOI":"10.2741\/4418","article-title":"The sarcoglycan complex in skeletal muscle","volume":"21","author":"Tarakci","year":"2016","journal-title":"Front. Biosci."},{"key":"10.1016\/j.omtm.2023.03.004_bib7","doi-asserted-by":"crossref","first-page":"177","DOI":"10.1111\/j.1600-0854.2006.00519.x","article-title":"Processing and assembly of the dystrophin glycoprotein complex","volume":"8","author":"Allikian","year":"2007","journal-title":"Traffic"},{"key":"10.1016\/j.omtm.2023.03.004_bib8","doi-asserted-by":"crossref","first-page":"34667","DOI":"10.1074\/jbc.273.52.34667","article-title":"Assembly of the sarcoglycan complex. Insights for muscular dystrophy","volume":"273","author":"Holt","year":"1998","journal-title":"J.\u00a0Biol. Chem."},{"key":"10.1016\/j.omtm.2023.03.004_bib9","doi-asserted-by":"crossref","first-page":"21785","DOI":"10.1074\/jbc.M101877200","article-title":"Overexpression of gamma-sarcoglycan induces severe muscular dystrophy. Implications for the regulation of Sarcoglycan assembly","volume":"276","author":"Zhu","year":"2001","journal-title":"J.\u00a0Biol. Chem."},{"key":"10.1016\/j.omtm.2023.03.004_bib10","doi-asserted-by":"crossref","first-page":"409","DOI":"10.1002\/mus.10566","article-title":"Specific assembly pathway of sarcoglycans is dependent on beta- and delta-sarcoglycan","volume":"29","author":"Shi","year":"2004","journal-title":"Muscle Nerve"}],"container-title":["Molecular Therapy - Methods &amp; Clinical Development"],"original-title":[],"language":"en","link":[{"URL":"https:\/\/api.elsevier.com\/content\/article\/PII:S2329050123000402?httpAccept=text\/xml","content-type":"text\/xml","content-version":"vor","intended-application":"text-mining"},{"URL":"https:\/\/api.elsevier.com\/content\/article\/PII:S2329050123000402?httpAccept=text\/plain","content-type":"text\/plain","content-version":"vor","intended-application":"text-mining"}],"deposited":{"date-parts":[[2024,5,17]],"date-time":"2024-05-17T10:20:08Z","timestamp":1715941208000},"score":1,"resource":{"primary":{"URL":"https:\/\/linkinghub.elsevier.com\/retrieve\/pii\/S2329050123000402"}},"subtitle":[],"short-title":[],"issued":{"date-parts":[[2023,6]]},"references-count":10,"alternative-id":["S2329050123000402"],"URL":"https:\/\/doi.org\/10.1016\/j.omtm.2023.03.004","relation":{},"ISSN":["2329-0501"],"issn-type":[{"value":"2329-0501","type":"print"}],"subject":[],"published":{"date-parts":[[2023,6]]},"assertion":[{"value":"Elsevier","name":"publisher","label":"This article is maintained by"},{"value":"A gene therapy approach for the treatment of limb-girdle muscular dystrophy 2C\/R5","name":"articletitle","label":"Article Title"},{"value":"Molecular Therapy - Methods & Clinical Development","name":"journaltitle","label":"Journal Title"},{"value":"https:\/\/doi.org\/10.1016\/j.omtm.2023.03.004","name":"articlelink","label":"CrossRef DOI link to publisher maintained version"},{"value":"simple-article","name":"content_type","label":"Content Type"},{"value":"\u00a9 2023 The Author(s).","name":"copyright","label":"Copyright"}]}}