{"status":"ok","message-type":"work","message-version":"1.0.0","message":{"indexed":{"date-parts":[[2025,11,1]],"date-time":"2025-11-01T13:51:05Z","timestamp":1762005065956,"version":"build-2065373602"},"reference-count":30,"publisher":"Elsevier BV","license":[{"start":{"date-parts":[[2019,3,1]],"date-time":"2019-03-01T00:00:00Z","timestamp":1551398400000},"content-version":"tdm","delay-in-days":0,"URL":"https:\/\/www.elsevier.com\/tdm\/userlicense\/1.0\/"},{"start":{"date-parts":[[2019,3,1]],"date-time":"2019-03-01T00:00:00Z","timestamp":1551398400000},"content-version":"tdm","delay-in-days":0,"URL":"https:\/\/www.elsevier.com\/legal\/tdmrep-license"},{"start":{"date-parts":[[2018,11,6]],"date-time":"2018-11-06T00:00:00Z","timestamp":1541462400000},"content-version":"vor","delay-in-days":0,"URL":"http:\/\/creativecommons.org\/licenses\/by-nc-nd\/4.0\/"}],"content-domain":{"domain":["elsevier.com","sciencedirect.com"],"crossmark-restriction":true},"short-container-title":["Molecular Genetics and Metabolism Reports"],"published-print":{"date-parts":[[2019,3]]},"DOI":"10.1016\/j.ymgmr.2018.11.001","type":"journal-article","created":{"date-parts":[[2018,11,20]],"date-time":"2018-11-20T12:46:59Z","timestamp":1542718019000},"page":"1-6","update-policy":"https:\/\/doi.org\/10.1016\/elsevier_cm_policy","source":"Crossref","is-referenced-by-count":13,"special_numbering":"C","title":["Allogeneic stem cell transplantation with reduced intensity conditioning for patients with adrenoleukodystrophy"],"prefix":"10.1016","volume":"18","author":[{"given":"Koji","family":"Kato","sequence":"first","affiliation":[],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"Ryo","family":"Maemura","sequence":"additional","affiliation":[],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"Manabu","family":"Wakamatsu","sequence":"additional","affiliation":[],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"Ayako","family":"Yamamori","sequence":"additional","affiliation":[],"role":[{"role":"author","vocabulary":"crossref"}]},{"ORCID":"https:\/\/orcid.org\/0000-0002-2473-3730","authenticated-orcid":false,"given":"Motoharu","family":"Hamada","sequence":"additional","affiliation":[],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"Shinsuke","family":"Kataoka","sequence":"additional","affiliation":[],"role":[{"role":"author","vocabulary":"crossref"}]},{"ORCID":"https:\/\/orcid.org\/0000-0001-6518-4726","authenticated-orcid":false,"given":"Atsushi","family":"Narita","sequence":"additional","affiliation":[],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"Shunsuke","family":"Miwata","sequence":"additional","affiliation":[],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"Yuko","family":"Sekiya","sequence":"additional","affiliation":[],"role":[{"role":"author","vocabulary":"crossref"}]},{"ORCID":"https:\/\/orcid.org\/0000-0001-5700-4481","authenticated-orcid":false,"given":"Nozomu","family":"Kawashima","sequence":"additional","affiliation":[],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"Kyogo","family":"Suzuki","sequence":"additional","affiliation":[],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"Kotaro","family":"Narita","sequence":"additional","affiliation":[],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"Sayoko","family":"Doisaki","sequence":"additional","affiliation":[],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"Hideki","family":"Muramatsu","sequence":"additional","affiliation":[],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"Hirotoshi","family":"Sakaguchi","sequence":"additional","affiliation":[],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"Kimikazu","family":"Matsumoto","sequence":"additional","affiliation":[],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"Yuka","family":"Koike","sequence":"additional","affiliation":[],"role":[{"role":"author","vocabulary":"crossref"}]},{"ORCID":"https:\/\/orcid.org\/0000-0003-3354-5472","authenticated-orcid":false,"given":"Osamu","family":"Onodera","sequence":"additional","affiliation":[],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"Makiko","family":"Kaga","sequence":"additional","affiliation":[],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"Nobuyuki","family":"Shimozawa","sequence":"additional","affiliation":[],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"Nao","family":"Yoshida","sequence":"additional","affiliation":[],"role":[{"role":"author","vocabulary":"crossref"}]}],"member":"78","reference":[{"key":"10.1016\/j.ymgmr.2018.11.001_bb0005","doi-asserted-by":"crossref","first-page":"1485","DOI":"10.1093\/brain\/120.8.1485","article-title":"Adrenoleukodystrophy: phenotype, genetics, pathogenesis and therapy","volume":"120","author":"Moser","year":"1997","journal-title":"Brain"},{"key":"10.1016\/j.ymgmr.2018.11.001_bb0010","doi-asserted-by":"crossref","first-page":"369","DOI":"10.1007\/978-1-4419-9072-3_47","article-title":"Evaluation of the preventive effect of glyceryl trioleate-trierucate (\"Lorenzo's oil\") therapy in X-linked adrenoleukodystrophy: results of two concurrent trials","volume":"544","author":"Moser","year":"2003","journal-title":"Adv. Exp. Med. Biol."},{"key":"10.1016\/j.ymgmr.2018.11.001_bb0015","doi-asserted-by":"crossref","first-page":"276","DOI":"10.1056\/NEJMc0907735","article-title":"Lovastatin in X-linked adrenoleukodystrophy","volume":"362","author":"Engelen","year":"2010","journal-title":"N. Engl. J. Med."},{"key":"10.1016\/j.ymgmr.2018.11.001_bb0020","doi-asserted-by":"crossref","first-page":"1410","DOI":"10.1212\/WNL.34.11.1410","article-title":"Bone marrow transplant in adrenoleukodystrophy","volume":"34","author":"Moser","year":"1984","journal-title":"Neurology"},{"key":"10.1016\/j.ymgmr.2018.11.001_bb0025","doi-asserted-by":"crossref","first-page":"881","DOI":"10.1182\/blood-2003-10-3402","article-title":"Cerebral X-linked adrenoleukodystrophy: the international hematopoietic cell transplantation experience from 1982 to 1999","volume":"104","author":"Peters","year":"2004","journal-title":"Blood"},{"key":"10.1016\/j.ymgmr.2018.11.001_bb0030","doi-asserted-by":"crossref","first-page":"E63","DOI":"10.1111\/j.1399-3046.2011.01539.x","article-title":"Successful cord blood transplantation with reduced-intensity conditioning for childhood cerebral X-linked adrenoleukodystrophy at advanced and early stages","volume":"16","author":"Niizuma","year":"2012","journal-title":"Pediatr. Transplant."},{"key":"10.1016\/j.ymgmr.2018.11.001_bb0035","doi-asserted-by":"crossref","first-page":"E116","DOI":"10.1111\/j.1399-3046.2009.01188.x","article-title":"Successful cord blood transplantation using a reduced-intensity conditioning regimen for advanced childhood-onset cerebral adrenoleukodystrophy","volume":"15","author":"Awaya","year":"2011","journal-title":"Pediatr. Transplant."},{"key":"10.1016\/j.ymgmr.2018.11.001_bb0040","doi-asserted-by":"crossref","first-page":"130","DOI":"10.1111\/j.1399-3046.2008.00962.x","article-title":"Successful allogeneic unrelated bone marrow transplantation using reduced-intensity conditioning for the treatment of X-linked adrenoleukodystrophy in a one-yr-old boy","volume":"13","author":"Okamura","year":"2009","journal-title":"Pediatr. Transplant."},{"key":"10.1016\/j.ymgmr.2018.11.001_bb0045","doi-asserted-by":"crossref","first-page":"1118","DOI":"10.1002\/pbc.22645","article-title":"Danaparoid as the prophylaxis for hepatic veno-occlusive disease after allogeneic hematopoietic stem cell transplantation in childhood hematological malignancy","volume":"55","author":"Sakaguchi","year":"2010","journal-title":"Pediatr. Blood Cancer"},{"key":"10.1016\/j.ymgmr.2018.11.001_bb0050","doi-asserted-by":"crossref","DOI":"10.1111\/petr.13099","article-title":"Danaparoid reduces transplant-related mortality in stem cell transplantation for children","volume":"22","author":"Kato","year":"2018","journal-title":"Pediatr. Transplant."},{"key":"10.1016\/j.ymgmr.2018.11.001_bb0055","first-page":"1761","article-title":"Adrenoleukodystrophy: a scoring method for brain MR observations","volume":"15","author":"Loes","year":"1994","journal-title":"Am. J. Neuroradiol."},{"key":"10.1016\/j.ymgmr.2018.11.001_bb0060","doi-asserted-by":"crossref","first-page":"1073","DOI":"10.1001\/archneur.62.7.1073","article-title":"Follow-up of 89 asymptomatic patients with adrenoleukodystrophy treated with Lorenzo's oil","volume":"62","author":"Moser","year":"2005","journal-title":"Arch. Neurol."},{"key":"10.1016\/j.ymgmr.2018.11.001_bb0065","first-page":"825","article-title":"1994 Consensus conference on acute GVHD grading","volume":"15","author":"Przepiorka","year":"1995","journal-title":"Bone Marrow Transplant."},{"key":"10.1016\/j.ymgmr.2018.11.001_bb0070","doi-asserted-by":"crossref","first-page":"204","DOI":"10.1016\/0002-9343(80)90380-0","article-title":"Chronic graft-versus-host syndrome in man. A long-term clinicopathologic study of 20 Seattle patients","volume":"69","author":"Shulman","year":"1980","journal-title":"Am. J. Med."},{"key":"10.1016\/j.ymgmr.2018.11.001_bb0075","doi-asserted-by":"crossref","first-page":"452","DOI":"10.1038\/bmt.2012.244","article-title":"Investigation of the freely available easy-to-use software 'EZR' for medical statistics","volume":"48","author":"Kanda","year":"2013","journal-title":"Bone Marrow Transplant."},{"key":"10.1016\/j.ymgmr.2018.11.001_bb0080","doi-asserted-by":"crossref","first-page":"1630","DOI":"10.1056\/NEJMoa1700554","article-title":"Hematopoietic stem-cell gene therapy for cerebral adrenoleukodystrophy","volume":"377","author":"Eichler","year":"2017","journal-title":"N. Engl. J. Med."},{"key":"10.1016\/j.ymgmr.2018.11.001_bb0085","doi-asserted-by":"crossref","first-page":"1971","DOI":"10.1182\/blood-2011-01-329235","article-title":"Outcomes after allogeneic hematopoietic cell transplantation for childhood cerebral adrenoleukodystrophy: the largest single-institution cohort report","volume":"118","author":"Miller","year":"2011","journal-title":"Blood"},{"key":"10.1016\/j.ymgmr.2018.11.001_bb0090","doi-asserted-by":"crossref","first-page":"665","DOI":"10.1016\/j.bbmt.2007.01.082","article-title":"Outcomes of unrelated umbilical cord blood transplantation for X-linked adrenoleukodystrophy","volume":"13","author":"Beam","year":"2007","journal-title":"Biol. Blood Marrow Transplant."},{"key":"10.1016\/j.ymgmr.2018.11.001_bb0095","doi-asserted-by":"crossref","first-page":"79","DOI":"10.1038\/sj.bmt.1704069","article-title":"Incidence, survival and risk factors for the development of veno-occlusive disease in pediatric hematopoietic stem cell transplant recipients","volume":"32","author":"Barker","year":"2003","journal-title":"Bone Marrow Transplant."},{"key":"10.1016\/j.ymgmr.2018.11.001_bb0100","doi-asserted-by":"crossref","first-page":"166","DOI":"10.1007\/BF02906128","article-title":"The role of busulfan in bone marrow transplantation","volume":"16","author":"Hassan","year":"1999","journal-title":"Med. Oncol."},{"key":"10.1016\/j.ymgmr.2018.11.001_bb0105","first-page":"6203","article-title":"Dose-dependent neurotoxicity of high-dose busulfan in children: a clinical and pharmacological study","volume":"50","author":"Vassal","year":"1990","journal-title":"Cancer Res."},{"key":"10.1016\/j.ymgmr.2018.11.001_bb0110","doi-asserted-by":"crossref","first-page":"491","DOI":"10.1182\/blood-2013-02-453175","article-title":"Umbilical cord blood transplantation: the first 25 ye2rs and beyond","volume":"122","author":"Ballen","year":"2013","journal-title":"Blood"},{"key":"10.1016\/j.ymgmr.2018.11.001_bb0115","doi-asserted-by":"crossref","first-page":"119","DOI":"10.1016\/j.bbmt.2016.10.019","article-title":"Allele-level HLA matching impacts key outcomes following umbilical cord blood transplantation for inherited metabolic disorders","volume":"23","author":"Mallhi","year":"2017","journal-title":"Biol. Blood Marrow Transplant."},{"key":"10.1016\/j.ymgmr.2018.11.001_bb0120","doi-asserted-by":"crossref","first-page":"617","DOI":"10.1038\/bmt.2009.69","article-title":"Successful engraftment of cord blood following a one-day reduced-intensity conditioning regimen in two patients suffering primary graft failure and sepsis","volume":"44","author":"Shimizu","year":"2009","journal-title":"Bone Marrow Transplant."},{"key":"10.1016\/j.ymgmr.2018.11.001_bb0125","doi-asserted-by":"crossref","first-page":"953","DOI":"10.1093\/brain\/awx016","article-title":"Long-term outcomes of allogeneic haematopoietic stem cell transplantation for adult cerebral X-linked adrenoleukodystrophy","volume":"140","author":"K\u00fchl","year":"2017","journal-title":"Brain"},{"key":"10.1016\/j.ymgmr.2018.11.001_bb0130","doi-asserted-by":"crossref","first-page":"1860","DOI":"10.1056\/NEJM199006283222607","article-title":"Reversal of early neurologic and neuroradiologic manifestations of X-linked adrenoleukodystrophy by bone marrow transplantation","volume":"322","author":"Aubourg","year":"1990","journal-title":"N. Engl. J. Med."},{"key":"10.1016\/j.ymgmr.2018.11.001_bb0135","doi-asserted-by":"crossref","first-page":"136","DOI":"10.14336\/AD.2015.0823","article-title":"Brain lipotoxicity of phytanic acid and very long-chain fatty acids. Harmful cellular\/mitochondrial activities in refsum disease and X-linked adrenoleukodystrophy","volume":"7","author":"Sch\u00f6nfeld","year":"2016","journal-title":"Aging Dis."},{"key":"10.1016\/j.ymgmr.2018.11.001_bb0140","first-page":"109","article-title":"The genetic landscape of X-linked adrenoleukodystrophy: inheritance, mutations, modifier genes, and diagnosis","volume":"8","author":"Wiesinger","year":"2015","journal-title":"Appl. Clin. Genet."},{"key":"10.1016\/j.ymgmr.2018.11.001_bb0145","first-page":"115","article-title":"Application of a diagnostic methodology by quantification of 26:0 lysophosphatidylcholine in dried blood spots for Japanese newborn screening of X-linked adrenoleukodystrophy","volume":"12","author":"Wu","year":"2017","journal-title":"Mol. Genet. Metab. Rep."},{"key":"10.1016\/j.ymgmr.2018.11.001_bb0150","doi-asserted-by":"crossref","first-page":"599","DOI":"10.1016\/j.ymgme.2015.02.002","article-title":"Newborn screening for X-linked adrenoleukodystrophy in New York State: diagnostic protocol, surveillance protocol and treatment guidelines","volume":"114","author":"Vogel","year":"2015","journal-title":"Mol. Genet. Metab."}],"container-title":["Molecular Genetics and Metabolism Reports"],"original-title":[],"language":"en","link":[{"URL":"https:\/\/api.elsevier.com\/content\/article\/PII:S2214426918300570?httpAccept=text\/xml","content-type":"text\/xml","content-version":"vor","intended-application":"text-mining"},{"URL":"https:\/\/api.elsevier.com\/content\/article\/PII:S2214426918300570?httpAccept=text\/plain","content-type":"text\/plain","content-version":"vor","intended-application":"text-mining"}],"deposited":{"date-parts":[[2025,11,1]],"date-time":"2025-11-01T12:50:14Z","timestamp":1762001414000},"score":1,"resource":{"primary":{"URL":"https:\/\/linkinghub.elsevier.com\/retrieve\/pii\/S2214426918300570"}},"subtitle":[],"short-title":[],"issued":{"date-parts":[[2019,3]]},"references-count":30,"alternative-id":["S2214426918300570"],"URL":"https:\/\/doi.org\/10.1016\/j.ymgmr.2018.11.001","relation":{},"ISSN":["2214-4269"],"issn-type":[{"type":"print","value":"2214-4269"}],"subject":[],"published":{"date-parts":[[2019,3]]},"assertion":[{"value":"Elsevier","name":"publisher","label":"This article is maintained by"},{"value":"Allogeneic stem cell transplantation with reduced intensity conditioning for patients with adrenoleukodystrophy","name":"articletitle","label":"Article Title"},{"value":"Molecular Genetics and Metabolism Reports","name":"journaltitle","label":"Journal Title"},{"value":"https:\/\/doi.org\/10.1016\/j.ymgmr.2018.11.001","name":"articlelink","label":"CrossRef DOI link to publisher maintained version"},{"value":"article","name":"content_type","label":"Content Type"},{"value":"\u00a9 2018 The Authors. Published by Elsevier Inc.","name":"copyright","label":"Copyright"}]}}