{"status":"ok","message-type":"work","message-version":"1.0.0","message":{"indexed":{"date-parts":[[2024,7,11]],"date-time":"2024-07-11T18:48:46Z","timestamp":1720723726128},"reference-count":8,"publisher":"EDP Sciences","license":[{"start":{"date-parts":[[2019,4,3]],"date-time":"2019-04-03T00:00:00Z","timestamp":1554249600000},"content-version":"vor","delay-in-days":33,"URL":"https:\/\/www.edpsciences.org\/en\/authors\/copyright-and-licensing"}],"content-domain":{"domain":[],"crossmark-restriction":false},"short-container-title":["Med Sci (Paris)"],"published-print":{"date-parts":[[2019,3]]},"abstract":"<jats:p>Suivre les b\u00e9n\u00e9fices et la tol\u00e9rance d\u2019une th\u00e9rapie innovante constitue un exercice relativement r\u00e9cent dans le champ des maladies neuromusculaires. Fonction respiratoire, capacit\u00e9s musculaires et fonctionnelles, qualit\u00e9 de vie, effets ind\u00e9sirables, pour chaque param\u00e8tre \u00e0 \u00e9valuer s\u2019esquisse un panel de mesures id\u00e9ales.<\/jats:p>","DOI":"10.1051\/medsci\/2019053","type":"journal-article","created":{"date-parts":[[2019,4,3]],"date-time":"2019-04-03T09:35:04Z","timestamp":1554284104000},"page":"54-56","source":"Crossref","is-referenced-by-count":0,"special_numbering":"Hors s\u00e9rie n\u00b0 1","title":["Quel suivi pour les traitements innovants ?"],"prefix":"10.1051","volume":"35","author":[{"given":"Emmanuelle","family":"Campana-Salort","sequence":"first","affiliation":[],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"Caroline","family":"Espil-Taris","sequence":"additional","affiliation":[],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"H\u00e9l\u00e8ne","family":"Prigent","sequence":"additional","affiliation":[],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"Marie","family":"de Antonio","sequence":"additional","affiliation":[],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"B\u00e9n\u00e9dicte","family":"Lebrun-Vignes","sequence":"additional","affiliation":[],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"Vincent","family":"Tiffreau","sequence":"additional","affiliation":[],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"G\u00e9raldine","family":"Honnet","sequence":"additional","affiliation":[],"role":[{"role":"author","vocabulary":"crossref"}]}],"member":"250","published-online":{"date-parts":[[2019,4,3]]},"reference":[{"key":"R1","doi-asserted-by":"crossref","first-page":"1183","DOI":"10.1016\/j.rmr.2011.07.004","volume":"28","author":"Soci\u00e9t\u00e9 de Pneumologie de Langue Fran\u00e7aise","year":"2011","journal-title":"Rev Mal Respir"},{"key":"R2","doi-asserted-by":"crossref","first-page":"1396","DOI":"10.1056\/NEJMoa0909859","volume":"362","author":"van der Ploeg","year":"2010","journal-title":"N Engl J Med"},{"key":"R3","doi-asserted-by":"crossref","first-page":"1748","DOI":"10.1016\/S0140-6736(15)60025-3","volume":"385","author":"Buyse","year":"2015","journal-title":"Lancet"},{"key":"R4","doi-asserted-by":"crossref","first-page":"25","DOI":"10.3233\/JND-160195","volume":"4","author":"Jimenez-Moreno","year":"2017","journal-title":"J Neuromuscul Dis"},{"key":"R5","doi-asserted-by":"crossref","first-page":"101","DOI":"10.1212\/WNL.0000000000004061","volume":"89","author":"Bachasson","year":"2017","journal-title":"Neurology"},{"key":"R6","doi-asserted-by":"crossref","first-page":"2855","DOI":"10.1093\/brain\/awy231","volume":"141","author":"Bassez","year":"2018","journal-title":"Brain"},{"key":"R7","doi-asserted-by":"crossref","first-page":"595","DOI":"10.1016\/j.neurol.2013.07.002","volume":"169","author":"Lafor\u00eat","year":"2013","journal-title":"Rev Neurol (Paris)"},{"key":"R8","doi-asserted-by":"crossref","first-page":"80","DOI":"10.1016\/j.ymgme.2017.06.007","volume":"122","author":"Papadopoulos","year":"2017","journal-title":"Mol Genet Metab"}],"container-title":["m\u00e9decine\/sciences"],"original-title":[],"link":[{"URL":"https:\/\/www.medecinesciences.org\/10.1051\/medsci\/2019053\/pdf","content-type":"unspecified","content-version":"vor","intended-application":"similarity-checking"}],"deposited":{"date-parts":[[2020,3,19]],"date-time":"2020-03-19T16:07:49Z","timestamp":1584634069000},"score":1,"resource":{"primary":{"URL":"https:\/\/www.medecinesciences.org\/10.1051\/medsci\/2019053"}},"subtitle":[],"short-title":[],"issued":{"date-parts":[[2019,3]]},"references-count":8,"alternative-id":["medsci190053s"],"URL":"https:\/\/doi.org\/10.1051\/medsci\/2019053","relation":{},"ISSN":["0767-0974","1958-5381"],"issn-type":[{"value":"0767-0974","type":"print"},{"value":"1958-5381","type":"electronic"}],"subject":[],"published":{"date-parts":[[2019,3]]}}}