{"status":"ok","message-type":"work","message-version":"1.0.0","message":{"indexed":{"date-parts":[[2025,11,3]],"date-time":"2025-11-03T08:48:21Z","timestamp":1762159701767},"reference-count":40,"publisher":"Elsevier BV","issue":"46","license":[{"start":{"date-parts":[[2001,11,1]],"date-time":"2001-11-01T00:00:00Z","timestamp":1004572800000},"content-version":"tdm","delay-in-days":0,"URL":"https:\/\/www.elsevier.com\/tdm\/userlicense\/1.0\/"},{"start":{"date-parts":[[2020,10,16]],"date-time":"2020-10-16T00:00:00Z","timestamp":1602806400000},"content-version":"vor","delay-in-days":6924,"URL":"http:\/\/creativecommons.org\/licenses\/by\/4.0\/"}],"content-domain":{"domain":[],"crossmark-restriction":false},"short-container-title":["Journal of Biological Chemistry"],"published-print":{"date-parts":[[2001,11]]},"DOI":"10.1074\/jbc.m107778200","type":"journal-article","created":{"date-parts":[[2002,7,26]],"date-time":"2002-07-26T14:56:15Z","timestamp":1027695375000},"page":"43160-43165","source":"Crossref","is-referenced-by-count":64,"title":["Biodistribution, Kinetics, and Efficacy of Highly Phosphorylated and Non-phosphorylated \u03b2-Glucuronidase in the Murine Model of Mucopolysaccharidosis VII"],"prefix":"10.1016","volume":"276","author":[{"given":"Mark S.","family":"Sands","sequence":"first","affiliation":[],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"Carole A.","family":"Vogler","sequence":"additional","affiliation":[],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"Kevin K.","family":"Ohlemiller","sequence":"additional","affiliation":[],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"Marie S.","family":"Roberts","sequence":"additional","affiliation":[],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"Jeffrey H.","family":"Grubb","sequence":"additional","affiliation":[],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"Beth","family":"Levy","sequence":"additional","affiliation":[],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"William S.","family":"Sly","sequence":"additional","affiliation":[],"role":[{"role":"author","vocabulary":"crossref"}]}],"member":"78","reference":[{"key":"10.1074\/jbc.M107778200_bib1","doi-asserted-by":"crossref","first-page":"257","DOI":"10.1146\/annurev.bi.60.070191.001353","volume":"60","author":"Neufeld","year":"1991","journal-title":"Annu. Rev. Biochem."},{"key":"10.1074\/jbc.M107778200_bib2","doi-asserted-by":"crossref","first-page":"141","DOI":"10.1126\/science.169.3941.141","volume":"169","author":"Neufeld","year":"1970","journal-title":"Science"},{"key":"10.1074\/jbc.M107778200_bib3","doi-asserted-by":"crossref","first-page":"307","DOI":"10.1146\/annurev.bi.61.070192.001515","volume":"61","author":"Kornfeld","year":"1992","journal-title":"Annu. Rev. Biochem."},{"key":"10.1074\/jbc.M107778200_bib4","doi-asserted-by":"crossref","first-page":"269","DOI":"10.1016\/0092-8674(78)90102-2","volume":"15","author":"Achord","year":"1978","journal-title":"Cell"},{"key":"10.1074\/jbc.M107778200_bib5","doi-asserted-by":"crossref","first-page":"67","DOI":"10.1242\/dev.109.1.67","volume":"109","author":"Senior","year":"1990","journal-title":"Development"},{"key":"10.1074\/jbc.M107778200_bib6","doi-asserted-by":"crossref","first-page":"965","DOI":"10.1242\/dev.114.4.965","volume":"114","author":"Matzner","year":"1992","journal-title":"Development"},{"key":"10.1074\/jbc.M107778200_bib7","doi-asserted-by":"crossref","first-page":"311","DOI":"10.1007\/s004410051062","volume":"292","author":"Takahashi","year":"1998","journal-title":"Cell Tissue Res."},{"key":"10.1074\/jbc.M107778200_bib8","doi-asserted-by":"crossref","first-page":"1464","DOI":"10.1056\/NEJM199105233242104","volume":"324","author":"Barton","year":"1991","journal-title":"N. Engl. J. Med."},{"key":"10.1074\/jbc.M107778200_bib9","doi-asserted-by":"crossref","first-page":"1183","DOI":"10.1182\/blood.V78.5.1183.1183","volume":"78","author":"Beutler","year":"1991","journal-title":"Blood"},{"key":"10.1074\/jbc.M107778200_bib10","doi-asserted-by":"crossref","first-page":"182","DOI":"10.1056\/NEJM200101183440304","volume":"344","author":"Kakkis","year":"2001","journal-title":"N. Engl. J. Med."},{"key":"10.1074\/jbc.M107778200_bib11","doi-asserted-by":"crossref","first-page":"12937","DOI":"10.1073\/pnas.91.26.12937","volume":"91","author":"Shull","year":"1994","journal-title":"Proc. Natl. Acad. Sci."},{"key":"10.1074\/jbc.M107778200_bib12","doi-asserted-by":"crossref","first-page":"2324","DOI":"10.1172\/JCI117237","volume":"93","author":"Sands","year":"1994","journal-title":"J. Clin. Invest."},{"key":"10.1074\/jbc.M107778200_bib13","doi-asserted-by":"crossref","first-page":"1864","DOI":"10.1172\/JCI118617","volume":"97","author":"Crawley","year":"1996","journal-title":"J. Clin. Invest."},{"key":"10.1074\/jbc.M107778200_bib14","doi-asserted-by":"crossref","first-page":"827","DOI":"10.1172\/JCI1722","volume":"101","author":"Kikuchi","year":"1998","journal-title":"J. Clin. Invest."},{"key":"10.1074\/jbc.M107778200_bib15","doi-asserted-by":"crossref","first-page":"1988","DOI":"10.1096\/fj.00-0014com","volume":"14","author":"Miranda","year":"1999","journal-title":"FASEB J."},{"key":"10.1074\/jbc.M107778200_bib16","doi-asserted-by":"crossref","first-page":"361","DOI":"10.1096\/fasebj.14.2.361","volume":"14","author":"Dunder","year":"2000","journal-title":"FASEB J."},{"key":"10.1074\/jbc.M107778200_bib17","doi-asserted-by":"crossref","first-page":"9","DOI":"10.1056\/NEJM200107053450102","volume":"345","author":"Eng","year":"2001","journal-title":"N. Engl. J. Med."},{"key":"10.1074\/jbc.M107778200_bib18","doi-asserted-by":"crossref","first-page":"837","DOI":"10.1203\/00006450-199312000-00028","volume":"34","author":"Vogler","year":"1993","journal-title":"Pediatr. Res."},{"key":"10.1074\/jbc.M107778200_bib19","doi-asserted-by":"crossref","first-page":"249","DOI":"10.1016\/S0022-3476(73)80162-3","volume":"82","author":"Sly","year":"1973","journal-title":"J. Pediatr."},{"key":"10.1074\/jbc.M107778200_bib20","doi-asserted-by":"crossref","first-page":"1258","DOI":"10.1172\/JCI114010","volume":"83","author":"Birkenmeier","year":"1989","journal-title":"J. Clin. Invest."},{"key":"10.1074\/jbc.M107778200_bib21","first-page":"207","volume":"136","author":"Vogler","year":"1990","journal-title":"Am. J. Pathol."},{"key":"10.1074\/jbc.M107778200_bib22","doi-asserted-by":"crossref","first-page":"6567","DOI":"10.1073\/pnas.90.14.6567","volume":"90","author":"Sands","year":"1993","journal-title":"Proc. Natl. Acad. Sci."},{"key":"10.1074\/jbc.M107778200_bib23","doi-asserted-by":"crossref","first-page":"2033","DOI":"10.1182\/blood.V86.5.2033.bloodjournal8652033","volume":"86","author":"Sands","year":"1995","journal-title":"Blood"},{"key":"10.1074\/jbc.M107778200_bib24","first-page":"507","volume":"4","author":"Chang","year":"1993","journal-title":"Neuro. Rep."},{"key":"10.1074\/jbc.M107778200_bib25","doi-asserted-by":"crossref","first-page":"469","DOI":"10.1006\/exer.2000.0897","volume":"71","author":"Ohlemiller","year":"2000","journal-title":"Exp. Eye Res."},{"key":"10.1074\/jbc.M107778200_bib26","doi-asserted-by":"crossref","first-page":"1394","DOI":"10.1172\/JCI1773","volume":"101","author":"O'Connor","year":"1998","journal-title":"J. Clin. Invest."},{"key":"10.1074\/jbc.M107778200_bib27","doi-asserted-by":"crossref","first-page":"1596","DOI":"10.1172\/JCI119322","volume":"99","author":"Sands","year":"1997","journal-title":"J. Clin. Invest."},{"key":"10.1074\/jbc.M107778200_bib28","doi-asserted-by":"crossref","first-page":"1050","DOI":"10.1203\/00006450-199606000-00019","volume":"39","author":"Vogler","year":"1996","journal-title":"Pediatr. Res."},{"key":"10.1074\/jbc.M107778200_bib29","doi-asserted-by":"crossref","first-page":"757","DOI":"10.1203\/00006450-200006000-00012","volume":"47","author":"Daly","year":"2000","journal-title":"Pediatr. Res."},{"key":"10.1074\/jbc.M107778200_bib30","first-page":"1255a","volume":"7","author":"Grubb","year":"1993","journal-title":"FASEB J."},{"key":"10.1074\/jbc.M107778200_bib31","first-page":"969","volume":"82","author":"Glaser","year":"1973","journal-title":"J. Lab. Clin. Med."},{"key":"10.1074\/jbc.M107778200_bib32","first-page":"328","volume":"49","author":"Sands","year":"1999","journal-title":"Lab. Anim. Sci."},{"key":"10.1074\/jbc.M107778200_bib33","series-title":"Gene Transfer into Neurones, Towards Gene Therapy of Neurological Disorders","author":"Wolfe","year":"1996"},{"key":"10.1074\/jbc.M107778200_bib34","doi-asserted-by":"crossref","first-page":"237","DOI":"10.1159\/000013847","volume":"4","author":"Ohlemiller","year":"1999","journal-title":"Audiol. Neurootol."},{"key":"10.1074\/jbc.M107778200_bib35","doi-asserted-by":"crossref","first-page":"111","DOI":"10.1016\/1046-5928(90)90003-H","volume":"1","author":"Boose","year":"1990","journal-title":"Prot. Exp. Purif."},{"key":"10.1074\/jbc.M107778200_bib36","doi-asserted-by":"crossref","first-page":"8793","DOI":"10.1021\/bi00195a022","volume":"33","author":"Aeed","year":"1994","journal-title":"Biochemistry"},{"key":"10.1074\/jbc.M107778200_bib37","doi-asserted-by":"crossref","first-page":"197","DOI":"10.1016\/0378-1119(94)90378-6","volume":"144","author":"Coppola","year":"1994","journal-title":"Gene"},{"key":"10.1074\/jbc.M107778200_bib38","doi-asserted-by":"crossref","first-page":"4322","DOI":"10.1073\/pnas.76.9.4322","volume":"76","author":"Natowicz","year":"1979","journal-title":"Proc. Natl. Acad. Sci."},{"key":"10.1074\/jbc.M107778200_bib39","doi-asserted-by":"crossref","first-page":"4412","DOI":"10.1016\/S0021-9258(18)34738-0","volume":"257","author":"Natowicz","year":"1982","journal-title":"J. Biol. Chem."},{"key":"10.1074\/jbc.M107778200_bib40","doi-asserted-by":"crossref","first-page":"838","DOI":"10.1203\/00006450-199906000-00010","volume":"45","author":"Vogler","year":"1999","journal-title":"Pediatr. Res."}],"container-title":["Journal of Biological Chemistry"],"original-title":[],"language":"en","link":[{"URL":"https:\/\/api.elsevier.com\/content\/article\/PII:S0021925819829496?httpAccept=text\/xml","content-type":"text\/xml","content-version":"vor","intended-application":"text-mining"},{"URL":"https:\/\/api.elsevier.com\/content\/article\/PII:S0021925819829496?httpAccept=text\/plain","content-type":"text\/plain","content-version":"vor","intended-application":"text-mining"},{"URL":"https:\/\/syndication.highwire.org\/content\/doi\/10.1074\/jbc.M107778200","content-type":"unspecified","content-version":"vor","intended-application":"similarity-checking"}],"deposited":{"date-parts":[[2022,1,4]],"date-time":"2022-01-04T00:59:07Z","timestamp":1641257947000},"score":1,"resource":{"primary":{"URL":"https:\/\/linkinghub.elsevier.com\/retrieve\/pii\/S0021925819829496"}},"subtitle":[],"short-title":[],"issued":{"date-parts":[[2001,11]]},"references-count":40,"journal-issue":{"issue":"46","published-print":{"date-parts":[[2001,11]]}},"alternative-id":["S0021925819829496"],"URL":"https:\/\/doi.org\/10.1074\/jbc.m107778200","relation":{},"ISSN":["0021-9258"],"issn-type":[{"value":"0021-9258","type":"print"}],"subject":[],"published":{"date-parts":[[2001,11]]}}}