{"status":"ok","message-type":"work","message-version":"1.0.0","message":{"indexed":{"date-parts":[[2025,5,15]],"date-time":"2025-05-15T13:40:06Z","timestamp":1747316406344,"version":"3.40.5"},"reference-count":26,"publisher":"Informa UK Limited","issue":"7","content-domain":{"domain":["www.tandfonline.com"],"crossmark-restriction":true},"short-container-title":["Expert Opinion on Investigational Drugs"],"published-print":{"date-parts":[[2024,7,2]]},"DOI":"10.1080\/13543784.2024.2352635","type":"journal-article","created":{"date-parts":[[2024,5,7]],"date-time":"2024-05-07T08:21:20Z","timestamp":1715070080000},"page":"653-656","update-policy":"https:\/\/doi.org\/10.1080\/tandf_crossmark_01","source":"Crossref","is-referenced-by-count":1,"title":["Will new investigational drugs change the way we treat Charcot-Marie-Tooth disease?"],"prefix":"10.1080","volume":"33","author":[{"ORCID":"https:\/\/orcid.org\/0009-0003-2342-8827","authenticated-orcid":false,"given":"Amedeo","family":"De Grado","sequence":"first","affiliation":[{"name":"Fondazione IRCCS Istituto Neurologico Carlo Besta","place":["Milan, Italy"]}],"role":[{"role":"author","vocabulary":"crossref"}]},{"ORCID":"https:\/\/orcid.org\/0000-0002-3850-076X","authenticated-orcid":false,"given":"Chiara","family":"Pisciotta","sequence":"additional","affiliation":[{"name":"Fondazione IRCCS Istituto Neurologico Carlo Besta","place":["Milan, Italy"]}],"role":[{"role":"author","vocabulary":"crossref"}]},{"ORCID":"https:\/\/orcid.org\/0000-0002-5396-997X","authenticated-orcid":false,"given":"Paola","family":"Saveri","sequence":"additional","affiliation":[{"name":"Fondazione IRCCS Istituto Neurologico Carlo Besta","place":["Milan, Italy"]}],"role":[{"role":"author","vocabulary":"crossref"}]},{"ORCID":"https:\/\/orcid.org\/0001-6854-0000-765X","authenticated-orcid":false,"given":"Davide","family":"Pareyson","sequence":"additional","affiliation":[{"name":"Fondazione IRCCS Istituto Neurologico Carlo Besta","place":["Milan, Italy"]}],"role":[{"role":"author","vocabulary":"crossref"}]}],"member":"301","published-online":{"date-parts":[[2024,5,8]]},"reference":[{"doi-asserted-by":"publisher","key":"e_1_3_3_3_1","DOI":"10.1016\/j.nmd.2023.07.001"},{"doi-asserted-by":"publisher","key":"e_1_3_3_4_1","DOI":"10.1111\/jns.12539"},{"doi-asserted-by":"publisher","key":"e_1_3_3_5_1","DOI":"10.1111\/jns.12543"},{"doi-asserted-by":"publisher","key":"e_1_3_3_6_1","DOI":"10.1172\/JCI96499"},{"doi-asserted-by":"publisher","key":"e_1_3_3_7_1","DOI":"10.1038\/s42003-021-01839-2"},{"doi-asserted-by":"publisher","key":"e_1_3_3_8_1","DOI":"10.1111\/jns.12585"},{"doi-asserted-by":"publisher","key":"e_1_3_3_9_1","DOI":"10.1038\/s41467-021-22593-3"},{"doi-asserted-by":"publisher","key":"e_1_3_3_10_1","DOI":"10.5607\/en.2019.28.2.279"},{"doi-asserted-by":"publisher","key":"e_1_3_3_11_1","DOI":"10.1172\/JCI159814"},{"doi-asserted-by":"publisher","key":"e_1_3_3_12_1","DOI":"10.1093\/nar\/gkz1070"},{"doi-asserted-by":"publisher","key":"e_1_3_3_13_1","DOI":"10.1111\/jns.12585"},{"doi-asserted-by":"publisher","key":"e_1_3_3_14_1","DOI":"10.1186\/s13023-021-02040-8"},{"unstructured":"Pharnext reports topline results from the pivotal phase III clinical trial (PREMIER trial) of PXT3003 in Charcot-Marie-tooth disease. Available from: https:\/\/pharnext.com\/en\/press-releases\/pharnext-reports-topline-results-from-the-pivotal-phase-iii-clinical-trial-premier-trial-of-pxt3003-in-charcot-marie-tooth-disease-type-1a","key":"e_1_3_3_15_1"},{"doi-asserted-by":"publisher","key":"e_1_3_3_16_1","DOI":"10.1038\/s41588-020-0615-4"},{"doi-asserted-by":"publisher","key":"e_1_3_3_17_1","DOI":"10.1172\/jci.insight.e164954"},{"doi-asserted-by":"publisher","key":"e_1_3_3_18_1","DOI":"10.1111\/jns.12585"},{"doi-asserted-by":"publisher","key":"e_1_3_3_19_1","DOI":"10.1212\/WNL.0000000000006811"},{"doi-asserted-by":"publisher","key":"e_1_3_3_20_1","DOI":"10.1038\/s41586-022-05637-6"},{"doi-asserted-by":"publisher","key":"e_1_3_3_21_1","DOI":"10.1056\/NEJMoa2307952"},{"doi-asserted-by":"publisher","key":"e_1_3_3_22_1","DOI":"10.1172\/JCI161566"},{"doi-asserted-by":"publisher","key":"e_1_3_3_23_1","DOI":"10.1038\/nm.2396"},{"doi-asserted-by":"publisher","key":"e_1_3_3_24_1","DOI":"10.1007\/s13311-016-0501-z"},{"doi-asserted-by":"publisher","key":"e_1_3_3_25_1","DOI":"10.1093\/brain\/awx375"},{"doi-asserted-by":"publisher","key":"e_1_3_3_26_1","DOI":"10.1016\/j.expneurol.2020.113281"},{"doi-asserted-by":"publisher","key":"e_1_3_3_27_1","DOI":"10.1111\/bph.15231"},{"doi-asserted-by":"publisher","key":"e_1_3_3_28_1","DOI":"10.1002\/ana.26633"}],"container-title":["Expert Opinion on Investigational Drugs"],"original-title":[],"language":"en","link":[{"URL":"https:\/\/www.tandfonline.com\/doi\/pdf\/10.1080\/13543784.2024.2352635","content-type":"unspecified","content-version":"vor","intended-application":"similarity-checking"}],"deposited":{"date-parts":[[2025,5,15]],"date-time":"2025-05-15T13:07:09Z","timestamp":1747314429000},"score":1,"resource":{"primary":{"URL":"https:\/\/www.tandfonline.com\/doi\/full\/10.1080\/13543784.2024.2352635"}},"subtitle":[],"short-title":[],"issued":{"date-parts":[[2024,5,8]]},"references-count":26,"journal-issue":{"issue":"7","published-print":{"date-parts":[[2024,7,2]]}},"alternative-id":["10.1080\/13543784.2024.2352635"],"URL":"https:\/\/doi.org\/10.1080\/13543784.2024.2352635","relation":{},"ISSN":["1354-3784","1744-7658"],"issn-type":[{"type":"print","value":"1354-3784"},{"type":"electronic","value":"1744-7658"}],"subject":[],"published":{"date-parts":[[2024,5,8]]},"assertion":[{"value":"The publishing and review policy for this title is described in its Aims & Scope.","order":1,"name":"peerreview_statement","label":"Peer Review Statement"},{"value":"http:\/\/www.tandfonline.com\/action\/journalInformation?show=aimsScope&journalCode=ieid20","URL":"http:\/\/www.tandfonline.com\/action\/journalInformation?show=aimsScope&journalCode=ieid20","order":2,"name":"aims_and_scope_url","label":"Aim & Scope"},{"value":"2024-01-17","order":0,"name":"received","label":"Received","group":{"name":"publication_history","label":"Publication History"}},{"value":"2024-05-03","order":2,"name":"accepted","label":"Accepted","group":{"name":"publication_history","label":"Publication History"}},{"value":"2024-05-08","order":3,"name":"published","label":"Published","group":{"name":"publication_history","label":"Publication History"}}]}}