{"status":"ok","message-type":"work","message-version":"1.0.0","message":{"indexed":{"date-parts":[[2026,10,5]],"date-time":"2026-10-05T04:06:27Z","timestamp":1791173187176,"version":"4.1.0"},"reference-count":42,"publisher":"Informa UK Limited","issue":"5","license":[{"start":{"date-parts":[[2020,2,13]],"date-time":"2020-02-13T00:00:00Z","timestamp":1581552000000},"content-version":"vor","delay-in-days":0,"URL":"http:\/\/creativecommons.org\/licenses\/by-nc-nd\/4.0\/"}],"content-domain":{"domain":["www.tandfonline.com"],"crossmark-restriction":true},"short-container-title":["Journal of Medical Economics"],"published-print":{"date-parts":[[2020,5,3]]},"DOI":"10.1080\/13696998.2020.1721508","type":"journal-article","created":{"date-parts":[[2020,1,23]],"date-time":"2020-01-23T11:46:14Z","timestamp":1579779974000},"page":"501-512","update-policy":"https:\/\/doi.org\/10.1080\/tandf_crossmark_01","source":"Crossref","is-referenced-by-count":51,"title":["Assessing the potential cost-effectiveness of a gene therapy for the treatment of hemophilia A"],"prefix":"10.1080","volume":"23","author":[{"given":"Keziah","family":"Cook","sequence":"first","affiliation":[{"name":"Analysis Group Inc, Health Care, Menlo Park, CA, USA;"}],"role":[{"vocabulary":"crossref","role":"author"}]},{"ORCID":"https:\/\/orcid.org\/0000-0002-4026-1817","authenticated-orcid":false,"given":"Shaun P.","family":"Forbes","sequence":"additional","affiliation":[{"name":"Department of Health Services, Policy & Practice, Brown University School of Public Health, RI, USA;"}],"role":[{"vocabulary":"crossref","role":"author"}]},{"given":"Kelly","family":"Adamski","sequence":"additional","affiliation":[{"name":"Analysis Group Inc, Health Care, Menlo Park, CA, USA;"}],"role":[{"vocabulary":"crossref","role":"author"}]},{"given":"Janice J.","family":"Ma","sequence":"additional","affiliation":[{"name":"Analysis Group Inc, Health Care, Menlo Park, CA, USA;"}],"role":[{"vocabulary":"crossref","role":"author"}]},{"given":"Anita","family":"Chawla","sequence":"additional","affiliation":[{"name":"Analysis Group Inc, Health Care, Menlo Park, CA, USA;"}],"role":[{"vocabulary":"crossref","role":"author"}]},{"ORCID":"https:\/\/orcid.org\/0000-0002-9468-4989","authenticated-orcid":false,"suffix":"Jr.","given":"Louis P.","family":"Garrison","sequence":"additional","affiliation":[{"name":"The Comparative Health Outcomes, Policy, and Economics (CHOICE) Institute, Department of Pharmacy, University of Washington, Seattle, WA, USA"}],"role":[{"vocabulary":"crossref","role":"author"}]}],"member":"301","published-online":{"date-parts":[[2020,2,13]]},"reference":[{"key":"CIT0001","doi-asserted-by":"publisher","DOI":"10.1111\/j.1365-2516.2012.02909.x"},{"key":"CIT0005","doi-asserted-by":"publisher","DOI":"10.3390\/jcm6070063"},{"key":"CIT0006","doi-asserted-by":"publisher","DOI":"10.15256\/joc.2011.1.2"},{"key":"CIT0007","doi-asserted-by":"publisher","DOI":"10.1186\/s13023-017-0660-y"},{"key":"CIT0008","doi-asserted-by":"publisher","DOI":"10.1002\/ajh.24218"},{"issue":"4","key":"CIT0009","doi-asserted-by":"crossref","first-page":"668","DOI":"10.1111\/hae.13758","volume":"25","author":"Croteau SE","year":"2019","journal-title":"Haemophilia"},{"key":"CIT0010","doi-asserted-by":"publisher","DOI":"10.1111\/j.1538-7836.2008.03270.x"},{"key":"CIT0011","doi-asserted-by":"publisher","DOI":"10.1111\/hae.13111"},{"key":"CIT0012","doi-asserted-by":"publisher","DOI":"10.1016\/j.jval.2014.03.1344"},{"key":"CIT0013","doi-asserted-by":"publisher","DOI":"10.1111\/hae.12533"},{"key":"CIT0014","doi-asserted-by":"publisher","DOI":"10.1111\/hae.13220"},{"key":"CIT0015","doi-asserted-by":"publisher","DOI":"10.3111\/13696998.2015.1016228"},{"key":"CIT0016","volume-title":"Prescribing information","author":"Hemlibra (emicizumab-kxwh) injection.","year":"2018"},{"key":"CIT0019","doi-asserted-by":"publisher","DOI":"10.1016\/j.jval.2015.02.001"},{"key":"CIT0020","doi-asserted-by":"publisher","DOI":"10.1056\/NEJMoa1908490"},{"key":"CIT0021","doi-asserted-by":"publisher","DOI":"10.1177\/0272989X18754513"},{"issue":"149","key":"CIT0022","first-page":"153","author":"Pettersson H","year":"1980","journal-title":"Clin Orthop Relat Res"},{"key":"CIT0023","doi-asserted-by":"publisher","DOI":"10.1001\/jama.2016.12195"},{"key":"CIT0024","doi-asserted-by":"crossref","unstructured":"Rangarajan S, Walsh L, Lester W, et al. AAV5\u2013factor VIII gene transfer in severe hemophilia A. N Engl J Med. 2017;377(26):2519\u20132530.","DOI":"10.1056\/NEJMoa1708483"},{"key":"CIT0025","doi-asserted-by":"publisher","DOI":"10.1182\/bloodadvances.2018021345"},{"key":"CIT0027","doi-asserted-by":"publisher","DOI":"10.1056\/NEJMoa1803550"},{"key":"CIT0028","doi-asserted-by":"publisher","DOI":"10.1111\/j.1365-2516.2011.02539.x"},{"key":"CIT0029","doi-asserted-by":"publisher","DOI":"10.1111\/j.1365-2516.2010.02383.x"},{"issue":"4","key":"CIT0030","first-page":"1","volume":"68","author":"Arias E","year":"2019","journal-title":"Natl Vital Stat Rep"},{"key":"CIT0031","doi-asserted-by":"publisher","DOI":"10.1111\/j.1538-7836.2006.01776.x"},{"key":"CIT0032","doi-asserted-by":"publisher","DOI":"10.1046\/j.1365-2796.1997.130135000.x"},{"key":"CIT0033","doi-asserted-by":"publisher","DOI":"10.1034\/j.1600-0455.2002.430514.x"},{"key":"CIT0034","doi-asserted-by":"publisher","DOI":"10.1111\/hae.12621"},{"key":"CIT0035","doi-asserted-by":"publisher","DOI":"10.3324\/haematol.2010.029868"},{"key":"CIT0036","doi-asserted-by":"publisher","DOI":"10.1056\/NEJMoa067659"},{"key":"CIT0037","first-page":"1","volume":"3","author":"Fryar CD","year":"2016","journal-title":"Vital Health Stat"},{"key":"CIT0040","unstructured":"America\u2019s Health Insurance Plans (AHIP). National Comparisons of Commercial and Medicare Fee-For-Service Payments to Hospitals. Data Brief. 2016."},{"key":"CIT0041","author":"Rosas S","year":"2019","journal-title":"J Knee Surg"},{"key":"CIT0042","doi-asserted-by":"publisher","DOI":"10.1111\/hae.13120"},{"key":"CIT0043","doi-asserted-by":"publisher","DOI":"10.1080\/13696998.2018.1468335"},{"key":"CIT0044","doi-asserted-by":"publisher","DOI":"10.1016\/j.jval.2016.09.1420"},{"key":"CIT0045","doi-asserted-by":"publisher","DOI":"10.1007\/s10198-014-0649-6"},{"key":"CIT0046","doi-asserted-by":"publisher","DOI":"10.1185\/030079908X273048"},{"key":"CIT0047","doi-asserted-by":"publisher","DOI":"10.18553\/jmcp.2018.24.7.632"},{"key":"CIT0049","doi-asserted-by":"publisher","DOI":"10.1111\/j.1365-2516.2008.01876.x"},{"key":"CIT0050","unstructured":"Eloctate (Antihemophilic factor (recombinant), FC fusion protein). Prescribing information. Cambridge, MA: Sanofi Genzyme; 2017."},{"key":"CIT0052","unstructured":"IBM Micromedex\u00ae. Red Book\u00ae Online 2019. 2019. Available from: http:\/\/www.micromedexsolutions.com\/micromedex2\/librarian\/"}],"container-title":["Journal of Medical Economics"],"original-title":[],"language":"en","link":[{"URL":"https:\/\/www.tandfonline.com\/doi\/pdf\/10.1080\/13696998.2020.1721508","content-type":"unspecified","content-version":"vor","intended-application":"similarity-checking"}],"deposited":{"date-parts":[[2023,9,25]],"date-time":"2023-09-25T11:21:27Z","timestamp":1695640887000},"score":1,"resource":{"primary":{"URL":"https:\/\/www.tandfonline.com\/doi\/full\/10.1080\/13696998.2020.1721508"}},"subtitle":[],"short-title":[],"issued":{"date-parts":[[2020,2,13]]},"references-count":42,"journal-issue":{"issue":"5","published-print":{"date-parts":[[2020,5,3]]}},"alternative-id":["10.1080\/13696998.2020.1721508"],"URL":"https:\/\/doi.org\/10.1080\/13696998.2020.1721508","relation":{},"ISSN":["1369-6998","1941-837X"],"issn-type":[{"value":"1369-6998","type":"print"},{"value":"1941-837X","type":"electronic"}],"subject":[],"published":{"date-parts":[[2020,2,13]]},"assertion":[{"value":"The publishing and review policy for this title is described in its Aims & Scope.","order":1,"name":"peerreview_statement","label":"Peer Review Statement"},{"value":"http:\/\/www.tandfonline.com\/action\/journalInformation?show=aimsScope&journalCode=ijme20","URL":"http:\/\/www.tandfonline.com\/action\/journalInformation?show=aimsScope&journalCode=ijme20","order":2,"name":"aims_and_scope_url","label":"Aim & Scope"},{"value":"2019-12-20","order":0,"name":"received","label":"Received","group":{"name":"publication_history","label":"Publication History"}},{"value":"2020-01-16","order":1,"name":"revised","label":"Revised","group":{"name":"publication_history","label":"Publication History"}},{"value":"2020-01-20","order":2,"name":"accepted","label":"Accepted","group":{"name":"publication_history","label":"Publication History"}},{"value":"2020-02-13","order":3,"name":"published","label":"Published","group":{"name":"publication_history","label":"Publication History"}}]}}