{"status":"ok","message-type":"work","message-version":"1.0.0","message":{"indexed":{"date-parts":[[2026,9,18]],"date-time":"2026-09-18T20:42:50Z","timestamp":1789764170498,"version":"4.0.1"},"reference-count":75,"publisher":"Informa UK Limited","issue":"7","funder":[{"name":"not funded"}],"content-domain":{"domain":["www.tandfonline.com"],"crossmark-restriction":true},"short-container-title":["Expert Opinion on Biological Therapy"],"published-print":{"date-parts":[[2018,7,3]]},"DOI":"10.1080\/14712598.2018.1492544","type":"journal-article","created":{"date-parts":[[2018,6,23]],"date-time":"2018-06-23T12:18:17Z","timestamp":1529756297000},"page":"755-764","update-policy":"https:\/\/doi.org\/10.1080\/tandf_crossmark_01","source":"Crossref","is-referenced-by-count":13,"title":["Progress in gene and cell therapies for the neuronal ceroid lipofuscinoses"],"prefix":"10.1080","volume":"18","author":[{"ORCID":"https:\/\/orcid.org\/0000-0002-7591-7417","authenticated-orcid":false,"given":"Anthony","family":"Donsante","sequence":"first","affiliation":[{"name":"Department of Neurosurgery, Emory University, Atlanta, GA, USA"}],"role":[{"vocabulary":"crossref","role":"author"}]},{"given":"Nicholas M","family":"Boulis","sequence":"additional","affiliation":[{"name":"Department of Neurosurgery, Emory University, Atlanta, GA, USA"}],"role":[{"vocabulary":"crossref","role":"author"}]}],"member":"301","published-online":{"date-parts":[[2018,7,2]]},"reference":[{"key":"CIT0001","doi-asserted-by":"publisher","DOI":"10.1016\/j.bbadis.2013.05.014"},{"issue":"2","key":"CIT0002","first-page":"73","volume":"18","author":"Nita DA","year":"2016","journal-title":"Epileptic Disord"},{"key":"CIT0003","doi-asserted-by":"publisher","DOI":"10.1016\/j.gene.2016.08.031"},{"key":"CIT0004","doi-asserted-by":"publisher","DOI":"10.3233\/TRD-160005"},{"key":"CIT0005","doi-asserted-by":"publisher","DOI":"10.1016\/j.bbamcr.2008.10.016"},{"key":"CIT0006","doi-asserted-by":"publisher","DOI":"10.1126\/science.162.3853.570"},{"key":"CIT0007","doi-asserted-by":"publisher","DOI":"10.1080\/21678707.2017.1360182"},{"key":"CIT0008","doi-asserted-by":"publisher","DOI":"10.1016\/j.nbd.2017.08.017"},{"key":"CIT0009","doi-asserted-by":"publisher","DOI":"10.1177\/0883073813493666"},{"key":"CIT0010","doi-asserted-by":"publisher","DOI":"10.1016\/j.bbadis.2013.01.009"},{"key":"CIT0011","doi-asserted-by":"publisher","DOI":"10.1111\/j.1399-0004.1990.tb04188.x"},{"key":"CIT0012","doi-asserted-by":"publisher","DOI":"10.1080\/00480169.1976.34298"},{"key":"CIT0013","doi-asserted-by":"publisher","DOI":"10.1002\/ajmg.1320570252"},{"key":"CIT0014","doi-asserted-by":"publisher","DOI":"10.1016\/j.bbrc.2004.12.038"},{"key":"CIT0015","doi-asserted-by":"publisher","DOI":"10.1016\/j.bbadis.2006.09.004"},{"key":"CIT0016","doi-asserted-by":"publisher","DOI":"10.1002\/ajmg.1320570253"},{"key":"CIT0017","doi-asserted-by":"publisher","DOI":"10.1055\/s-2007-973677"},{"key":"CIT0018","doi-asserted-by":"publisher","DOI":"10.1111\/j.1442-200x.2005.02126.x"},{"key":"CIT0019","doi-asserted-by":"publisher","DOI":"10.1212\/WNL.57.8.1411"},{"key":"CIT0020","doi-asserted-by":"publisher","DOI":"10.1073\/pnas.97.26.14720"},{"key":"CIT0021","doi-asserted-by":"publisher","DOI":"10.1016\/j.stem.2009.05.022"},{"key":"CIT0022","doi-asserted-by":"publisher","DOI":"10.3171\/2013.3.PEDS12397"},{"key":"CIT0023","doi-asserted-by":"publisher","DOI":"10.1016\/j.exer.2016.09.003"},{"key":"CIT0024","doi-asserted-by":"publisher","DOI":"10.1007\/s40259-017-0234-5"},{"key":"CIT0025","doi-asserted-by":"publisher","DOI":"10.2165\/00063030-200519020-00003"},{"key":"CIT0026","doi-asserted-by":"publisher","DOI":"10.1634\/stemcells.2005-0059"},{"key":"CIT0027","doi-asserted-by":"publisher","DOI":"10.1371\/journal.pone.0127204"},{"key":"CIT0028","doi-asserted-by":"publisher","DOI":"10.1016\/j.nbd.2004.03.005"},{"key":"CIT0029","doi-asserted-by":"publisher","DOI":"10.1016\/j.ymthe.2005.11.008"},{"key":"CIT0030","doi-asserted-by":"publisher","DOI":"10.1016\/j.ymthe.2005.04.018"},{"key":"CIT0031","doi-asserted-by":"publisher","DOI":"10.1016\/j.ymthe.2004.05.024"},{"key":"CIT0032","doi-asserted-by":"publisher","DOI":"10.1002\/ana.23545"},{"issue":"12","key":"CIT0033","doi-asserted-by":"crossref","first-page":"8282","DOI":"10.1128\/JVI.68.12.8282-8287.1994","volume":"68","author":"Alexander IE","year":"1994","journal-title":"J Virol"},{"issue":"11","key":"CIT0034","first-page":"3123","volume":"48","author":"Yalkinoglu AO","year":"1988","journal-title":"Cancer Res"},{"key":"CIT0035","doi-asserted-by":"publisher","DOI":"10.1038\/86554"},{"key":"CIT0036","doi-asserted-by":"publisher","DOI":"10.1007\/s10545-011-9446-x"},{"key":"CIT0037","doi-asserted-by":"publisher","DOI":"10.1523\/JNEUROSCI.2518-14.2014"},{"key":"CIT0038","doi-asserted-by":"publisher","DOI":"10.1073\/pnas.1701832114"},{"key":"CIT0039","doi-asserted-by":"publisher","DOI":"10.1038\/nbt.1515"},{"key":"CIT0040","doi-asserted-by":"publisher","DOI":"10.1056\/NEJMoa1706198"},{"key":"CIT0041","doi-asserted-by":"publisher","DOI":"10.1042\/bj3570049"},{"key":"CIT0042","doi-asserted-by":"publisher","DOI":"10.1038\/sj.gt.3301843"},{"key":"CIT0043","doi-asserted-by":"publisher","DOI":"10.1038\/sj.gt.3302549"},{"key":"CIT0044","doi-asserted-by":"publisher","DOI":"10.1089\/hum.2008.022"},{"key":"CIT0045","doi-asserted-by":"publisher","DOI":"10.1523\/JNEUROSCI.2676-05.2006"},{"key":"CIT0046","doi-asserted-by":"publisher","DOI":"10.1038\/sj.mt.6300049"},{"key":"CIT0047","doi-asserted-by":"publisher","DOI":"10.1016\/j.expneurol.2008.04.022"},{"key":"CIT0048","doi-asserted-by":"publisher","DOI":"10.1038\/sj.mt.6300249"},{"key":"CIT0049","doi-asserted-by":"publisher","DOI":"10.1126\/scitranslmed.aac6191"},{"key":"CIT0050","doi-asserted-by":"publisher","DOI":"10.1016\/j.exer.2016.03.023"},{"key":"CIT0051","doi-asserted-by":"publisher","DOI":"10.1038\/gt.2017.4"},{"key":"CIT0052","doi-asserted-by":"publisher","DOI":"10.1016\/j.nbd.2013.11.011"},{"key":"CIT0053","doi-asserted-by":"publisher","DOI":"10.1016\/j.bbadis.2015.06.013"},{"key":"CIT0054","doi-asserted-by":"publisher","DOI":"10.2353\/ajpath.2010.091267"},{"key":"CIT0055","doi-asserted-by":"publisher","DOI":"10.1038\/nrn.2017.36"},{"key":"CIT0056","doi-asserted-by":"publisher","DOI":"10.1523\/JNEUROSCI.3081-17.2018"},{"key":"CIT0057","doi-asserted-by":"publisher","DOI":"10.1089\/hum.2012.253"},{"key":"CIT0058","doi-asserted-by":"publisher","DOI":"10.1093\/hmg\/ddn396"},{"key":"CIT0059","doi-asserted-by":"publisher","DOI":"10.1523\/JNEUROSCI.1635-16.2016"},{"key":"CIT0060","doi-asserted-by":"publisher","DOI":"10.1016\/j.ymthe.2018.02.027"},{"key":"CIT0061","doi-asserted-by":"publisher","DOI":"10.1016\/j.bbadis.2014.07.009"},{"key":"CIT0062","doi-asserted-by":"publisher","DOI":"10.1016\/S0896-6273(04)00190-4"},{"key":"CIT0063","doi-asserted-by":"publisher","DOI":"10.1186\/s40035-017-0077-5"},{"key":"CIT0064","doi-asserted-by":"publisher","DOI":"10.1007\/s00401-015-1512-2"},{"key":"CIT0065","doi-asserted-by":"publisher","DOI":"10.1089\/hum.2016.190"},{"key":"CIT0066","doi-asserted-by":"publisher","DOI":"10.3389\/fnmol.2016.00056"},{"key":"CIT0067","doi-asserted-by":"publisher","DOI":"10.1016\/j.nbd.2007.08.007"},{"key":"CIT0068","doi-asserted-by":"publisher","DOI":"10.1212\/01.WNL.0000151973.08426.7E"},{"key":"CIT0069","doi-asserted-by":"publisher","DOI":"10.1111\/j.1365-2990.2006.00738.x"},{"key":"CIT0070","doi-asserted-by":"publisher","DOI":"10.1093\/hmg\/11.12.1421"},{"key":"CIT0071","doi-asserted-by":"publisher","DOI":"10.1212\/01.WNL.0000041913.97883.8B"},{"key":"CIT0072","doi-asserted-by":"publisher","DOI":"10.1016\/j.jneuroim.2010.08.024"},{"issue":"119","key":"CIT0073","first-page":"73","volume":"22","author":"Arellano B","year":"2016","journal-title":"Discov Med"},{"key":"CIT0074","doi-asserted-by":"publisher","DOI":"10.1038\/mt.2014.68"},{"key":"CIT0075","doi-asserted-by":"publisher","DOI":"10.1371\/journal.pone.0061618"}],"container-title":["Expert Opinion on Biological Therapy"],"original-title":[],"language":"en","link":[{"URL":"https:\/\/www.tandfonline.com\/doi\/pdf\/10.1080\/14712598.2018.1492544","content-type":"unspecified","content-version":"vor","intended-application":"similarity-checking"}],"deposited":{"date-parts":[[2020,9,7]],"date-time":"2020-09-07T00:54:08Z","timestamp":1599440048000},"score":1,"resource":{"primary":{"URL":"https:\/\/www.tandfonline.com\/doi\/full\/10.1080\/14712598.2018.1492544"}},"subtitle":[],"short-title":[],"issued":{"date-parts":[[2018,7,2]]},"references-count":75,"journal-issue":{"issue":"7","published-print":{"date-parts":[[2018,7,3]]}},"alternative-id":["10.1080\/14712598.2018.1492544"],"URL":"https:\/\/doi.org\/10.1080\/14712598.2018.1492544","relation":{},"ISSN":["1471-2598","1744-7682"],"issn-type":[{"value":"1471-2598","type":"print"},{"value":"1744-7682","type":"electronic"}],"subject":[],"published":{"date-parts":[[2018,7,2]]},"assertion":[{"value":"The publishing and review policy for this title is described in its Aims & Scope.","order":1,"name":"peerreview_statement","label":"Peer Review Statement"},{"value":"http:\/\/www.tandfonline.com\/action\/journalInformation?show=aimsScope&journalCode=iebt20","URL":"http:\/\/www.tandfonline.com\/action\/journalInformation?show=aimsScope&journalCode=iebt20","order":2,"name":"aims_and_scope_url","label":"Aim & Scope"},{"value":"2018-04-06","order":0,"name":"received","label":"Received","group":{"name":"publication_history","label":"Publication History"}},{"value":"2018-06-20","order":2,"name":"accepted","label":"Accepted","group":{"name":"publication_history","label":"Publication History"}},{"value":"2018-07-02","order":3,"name":"published","label":"Published","group":{"name":"publication_history","label":"Publication History"}}]}}