{"status":"ok","message-type":"work","message-version":"1.0.0","message":{"indexed":{"date-parts":[[2025,10,23]],"date-time":"2025-10-23T16:49:05Z","timestamp":1761238145159,"version":"build-2065373602"},"reference-count":117,"publisher":"Informa UK Limited","issue":"10","funder":[{"DOI":"10.13039\/100005202","name":"Muscular Dystrophy Association","doi-asserted-by":"crossref","award":["964509"],"award-info":[{"award-number":["964509"]}],"id":[{"id":"10.13039\/100005202","id-type":"DOI","asserted-by":"crossref"}]}],"content-domain":{"domain":["www.tandfonline.com"],"crossmark-restriction":true},"short-container-title":["Regenerative Medicine"],"published-print":{"date-parts":[[2025,10,3]]},"DOI":"10.1080\/17460751.2025.2571355","type":"journal-article","created":{"date-parts":[[2025,10,8]],"date-time":"2025-10-08T11:45:43Z","timestamp":1759923943000},"page":"489-500","update-policy":"https:\/\/doi.org\/10.1080\/tandf_crossmark_01","source":"Crossref","is-referenced-by-count":0,"title":["Translational progress in the development of pharmacotherapies for Duchenne muscular dystrophy"],"prefix":"10.1080","volume":"20","author":[{"given":"Kristy","family":"Swiderski","sequence":"first","affiliation":[{"name":"The University of Melbourne","place":["Melbourne, Australia"]}],"role":[{"role":"author","vocabulary":"crossref"}]},{"ORCID":"https:\/\/orcid.org\/0000-0001-9220-9810","authenticated-orcid":false,"given":"Gordon S.","family":"Lynch","sequence":"additional","affiliation":[{"name":"The University of Melbourne","place":["Melbourne, Australia"]}],"role":[{"role":"author","vocabulary":"crossref"}]}],"member":"301","published-online":{"date-parts":[[2025,10,8]]},"reference":[{"key":"e_1_3_5_3_1","doi-asserted-by":"publisher","DOI":"10.1016\/S1474-4422(18)30024-3"},{"key":"e_1_3_5_4_1","doi-asserted-by":"publisher","DOI":"10.3390\/biomedicines12040912"},{"key":"e_1_3_5_5_1","doi-asserted-by":"publisher","DOI":"10.1002\/mus.27347"},{"key":"e_1_3_5_6_1","doi-asserted-by":"publisher","DOI":"10.1016\/j.nmd.2022.07.248"},{"key":"e_1_3_5_7_1","doi-asserted-by":"publisher","DOI":"10.7759\/cureus.51237"},{"key":"e_1_3_5_8_1","doi-asserted-by":"publisher","DOI":"10.1097\/MD.0000000000015858"},{"key":"e_1_3_5_9_1","doi-asserted-by":"publisher","DOI":"10.1212\/WNL.0000000000005680"},{"key":"e_1_3_5_10_1","doi-asserted-by":"publisher","DOI":"10.3233\/JND-170272"},{"key":"e_1_3_5_11_1","doi-asserted-by":"publisher","DOI":"10.3233\/JND-210643"},{"key":"e_1_3_5_12_1","doi-asserted-by":"publisher","DOI":"10.1002\/ana.24555"},{"key":"e_1_3_5_13_1","doi-asserted-by":"publisher","DOI":"10.1002\/ana.23982"},{"key":"e_1_3_5_14_1","doi-asserted-by":"publisher","DOI":"10.3233\/JND-210665"},{"key":"e_1_3_5_15_1","doi-asserted-by":"publisher","DOI":"10.3233\/JND-220811"},{"key":"e_1_3_5_16_1","doi-asserted-by":"publisher","DOI":"10.3233\/JND-221656"},{"key":"e_1_3_5_17_1","doi-asserted-by":"publisher","DOI":"10.1001\/jamaneurol.2020.1264"},{"key":"e_1_3_5_18_1","doi-asserted-by":"publisher","DOI":"10.1038\/s41598-024-70783-y"},{"key":"e_1_3_5_19_1","doi-asserted-by":"publisher","DOI":"10.1002\/acn3.51235"},{"key":"e_1_3_5_20_1","doi-asserted-by":"publisher","DOI":"10.1212\/WNL.0000000000009233"},{"key":"e_1_3_5_21_1","doi-asserted-by":"publisher","DOI":"10.1186\/s40478-020-01106-1"},{"key":"e_1_3_5_22_1","doi-asserted-by":"publisher","DOI":"10.1089\/nat.2021.0043"},{"key":"e_1_3_5_23_1","doi-asserted-by":"publisher","DOI":"10.1038\/s41591-024-03304-z"},{"key":"e_1_3_5_24_1","doi-asserted-by":"publisher","DOI":"10.1007\/s00439-025-02758-6"},{"key":"e_1_3_5_25_1","doi-asserted-by":"publisher","DOI":"10.1089\/hum.2019.255"},{"key":"e_1_3_5_26_1","doi-asserted-by":"publisher","DOI":"10.1089\/hum.2024.013"},{"key":"e_1_3_5_27_1","doi-asserted-by":"publisher","DOI":"10.1002\/(SICI)1097-4598(199612)19:12<1576::AID-MUS7>3.0.CO;2-7"},{"key":"e_1_3_5_28_1","doi-asserted-by":"publisher","DOI":"10.1002\/mus.21341"},{"key":"e_1_3_5_29_1","doi-asserted-by":"publisher","DOI":"10.3390\/ijms21228763"},{"key":"e_1_3_5_30_1","doi-asserted-by":"publisher","DOI":"10.1002\/mus.26191"},{"key":"e_1_3_5_31_1","doi-asserted-by":"publisher","DOI":"10.1001\/jamaneurol.2022.2480"},{"key":"e_1_3_5_32_1","doi-asserted-by":"publisher","DOI":"10.1007\/s40272-024-00655-5"},{"key":"e_1_3_5_33_1","doi-asserted-by":"publisher","DOI":"10.1007\/s10072-024-07939-1"},{"key":"e_1_3_5_34_1","doi-asserted-by":"publisher","DOI":"10.1212\/WNL.0000000000208112"},{"key":"e_1_3_5_35_1","doi-asserted-by":"publisher","DOI":"10.2119\/molmed.2013.00011"},{"key":"e_1_3_5_36_1","doi-asserted-by":"publisher","DOI":"10.1186\/s13395-021-00273-6"},{"key":"e_1_3_5_37_1","doi-asserted-by":"publisher","DOI":"10.1016\/S1474-4422(24)00036-X"},{"key":"e_1_3_5_38_1","doi-asserted-by":"publisher","DOI":"10.1016\/j.lanwpc.2025.101568"},{"key":"e_1_3_5_39_1","doi-asserted-by":"publisher","DOI":"10.1007\/s10654-020-00613-8"},{"key":"e_1_3_5_40_1","doi-asserted-by":"publisher","DOI":"10.1016\/0092-8674(87)90579-4"},{"key":"e_1_3_5_41_1","doi-asserted-by":"publisher","DOI":"10.3390\/genes15111489"},{"key":"e_1_3_5_42_1","doi-asserted-by":"publisher","DOI":"10.1007\/s10974-024-09688-2"},{"key":"e_1_3_5_43_1","doi-asserted-by":"publisher","DOI":"10.1371\/journal.pone.0294847"},{"key":"e_1_3_5_44_1","doi-asserted-by":"publisher","DOI":"10.1038\/ncomms14454"},{"key":"e_1_3_5_45_1","doi-asserted-by":"publisher","DOI":"10.1126\/science.aad5725"},{"key":"e_1_3_5_46_1","doi-asserted-by":"publisher","DOI":"10.1126\/science.1254445"},{"key":"e_1_3_5_47_1","doi-asserted-by":"publisher","DOI":"10.1126\/science.aad5143"},{"key":"e_1_3_5_48_1","doi-asserted-by":"publisher","DOI":"10.1126\/science.aad5177"},{"key":"e_1_3_5_49_1","doi-asserted-by":"publisher","DOI":"10.1038\/mt.2015.192"},{"key":"e_1_3_5_50_1","doi-asserted-by":"publisher","DOI":"10.1016\/j.omtn.2025.102569"},{"key":"e_1_3_5_51_1","doi-asserted-by":"publisher","DOI":"10.1038\/nm0302-253"},{"key":"e_1_3_5_52_1","doi-asserted-by":"publisher","DOI":"10.1016\/j.ymthe.2004.07.016"},{"key":"e_1_3_5_53_1","doi-asserted-by":"publisher","DOI":"10.1038\/nm1439"},{"key":"e_1_3_5_54_1","doi-asserted-by":"publisher","DOI":"10.1212\/WNL.0000000000213604"},{"key":"e_1_3_5_55_1","doi-asserted-by":"publisher","DOI":"10.1016\/j.ymthe.2025.03.065"},{"key":"e_1_3_5_56_1","doi-asserted-by":"publisher","DOI":"10.1016\/j.ymthe.2025.06.032"},{"key":"e_1_3_5_57_1","doi-asserted-by":"publisher","DOI":"10.1172\/JCI173510"},{"key":"e_1_3_5_58_1","doi-asserted-by":"publisher","DOI":"10.1016\/j.nmd.2025.106208"},{"key":"e_1_3_5_59_1","doi-asserted-by":"publisher","DOI":"10.1517\/21678707.2015.1085858"},{"key":"e_1_3_5_60_1","doi-asserted-by":"publisher","DOI":"10.1016\/j.nmd.2009.06.368"},{"key":"e_1_3_5_61_1","doi-asserted-by":"publisher","DOI":"10.1177\/22143602251360664"},{"key":"e_1_3_5_62_1","doi-asserted-by":"publisher","DOI":"10.1152\/ajpheart.01253.2007"},{"key":"e_1_3_5_63_1","doi-asserted-by":"publisher","DOI":"10.1016\/j.nmd.2008.06.386"},{"key":"e_1_3_5_64_1","doi-asserted-by":"publisher","DOI":"10.1016\/j.bbadis.2015.10.007"},{"key":"e_1_3_5_65_1","doi-asserted-by":"publisher","DOI":"10.1016\/j.bbamcr.2014.03.025"},{"key":"e_1_3_5_66_1","doi-asserted-by":"publisher","DOI":"10.3390\/ijms22137063"},{"key":"e_1_3_5_67_1","doi-asserted-by":"publisher","DOI":"10.14670\/HH-18-083"},{"key":"e_1_3_5_68_1","doi-asserted-by":"publisher","DOI":"10.1172\/jci.insight.90341"},{"key":"e_1_3_5_69_1","doi-asserted-by":"publisher","DOI":"10.1016\/s0960-8966(99)00126-1"},{"key":"e_1_3_5_70_1","doi-asserted-by":"publisher","DOI":"10.1038\/s41598-019-49140-x"},{"key":"e_1_3_5_71_1","doi-asserted-by":"publisher","DOI":"10.1056\/NEJM198906153202405"},{"key":"e_1_3_5_72_1","doi-asserted-by":"publisher","DOI":"10.1001\/archneur.1991.00530160047012"},{"key":"e_1_3_5_73_1","doi-asserted-by":"publisher","DOI":"10.1002\/mus.24665"},{"key":"e_1_3_5_74_1","doi-asserted-by":"publisher","DOI":"10.1172\/JCI153837"},{"key":"e_1_3_5_75_1","doi-asserted-by":"publisher","DOI":"10.1002\/mus.28444"},{"key":"e_1_3_5_76_1","doi-asserted-by":"publisher","DOI":"10.1152\/ajpcell.00183.2011"},{"key":"e_1_3_5_77_1","doi-asserted-by":"publisher","DOI":"10.1093\/hmg\/ddr265"},{"key":"e_1_3_5_78_1","doi-asserted-by":"publisher","DOI":"10.1186\/2044-5040-2-16"},{"key":"e_1_3_5_79_1","doi-asserted-by":"publisher","DOI":"10.3389\/fphys.2021.642908"},{"key":"e_1_3_5_80_1","doi-asserted-by":"publisher","DOI":"10.1016\/j.bcp.2018.04.022"},{"key":"e_1_3_5_81_1","doi-asserted-by":"publisher","DOI":"10.1371\/journal.pone.0147634"},{"key":"e_1_3_5_82_1","doi-asserted-by":"publisher","DOI":"10.1096\/fj.202201846RR"},{"key":"e_1_3_5_83_1","doi-asserted-by":"publisher","DOI":"10.1096\/fasebj.2021.35.S1.00406"},{"key":"e_1_3_5_84_1","doi-asserted-by":"publisher","DOI":"10.1093\/hmg\/ddt514"},{"key":"e_1_3_5_85_1","doi-asserted-by":"publisher","DOI":"10.1016\/j.phrs.2020.104999"},{"key":"e_1_3_5_86_1","doi-asserted-by":"publisher","DOI":"10.1016\/j.ijcard.2020.03.031"},{"key":"e_1_3_5_87_1","doi-asserted-by":"publisher","DOI":"10.1152\/ajpheart.00729.2023"},{"key":"e_1_3_5_88_1","doi-asserted-by":"publisher","DOI":"10.1152\/ajpheart.00180.2021"},{"key":"e_1_3_5_89_1","doi-asserted-by":"publisher","DOI":"10.1161\/JAHA.118.011902"},{"key":"e_1_3_5_90_1","doi-asserted-by":"publisher","DOI":"10.1093\/eurheartj\/ehad655.763"},{"key":"e_1_3_5_91_1","doi-asserted-by":"publisher","DOI":"10.1212\/WNL.0000000000006950"},{"key":"e_1_3_5_92_1","doi-asserted-by":"publisher","DOI":"10.1016\/S0140-6736(22)00012-5"},{"key":"e_1_3_5_93_1","doi-asserted-by":"publisher","DOI":"10.1016\/j.stemcr.2018.01.023"},{"key":"e_1_3_5_94_1","doi-asserted-by":"publisher","DOI":"10.1016\/j.stemcr.2025.102468"},{"key":"e_1_3_5_95_1","doi-asserted-by":"publisher","DOI":"10.1172\/jci.insight.130202"},{"key":"e_1_3_5_96_1","doi-asserted-by":"publisher","DOI":"10.3233\/JND-210689"},{"key":"e_1_3_5_97_1","doi-asserted-by":"publisher","DOI":"10.1002\/psp4.13087"},{"key":"e_1_3_5_98_1","doi-asserted-by":"publisher","DOI":"10.3233\/JND-210776"},{"key":"e_1_3_5_99_1","doi-asserted-by":"publisher","DOI":"10.1093\/hmg\/ddad173"},{"key":"e_1_3_5_100_1","doi-asserted-by":"publisher","DOI":"10.1002\/mus.20812"},{"key":"e_1_3_5_101_1","doi-asserted-by":"publisher","DOI":"10.3892\/etm.2021.9875"},{"key":"e_1_3_5_102_1","doi-asserted-by":"publisher","DOI":"10.1002\/1097-4598(200009)23:9<1344::AID-MUS4>3.0.CO;2-F"},{"key":"e_1_3_5_103_1","doi-asserted-by":"publisher","DOI":"10.1212\/WNL.0000000000207948"},{"key":"e_1_3_5_104_1","doi-asserted-by":"publisher","DOI":"10.1177\/22143602241303370"},{"key":"e_1_3_5_105_1","doi-asserted-by":"publisher","DOI":"10.1097\/MS9.0000000000003049"},{"key":"e_1_3_5_106_1","doi-asserted-by":"publisher","DOI":"10.1210\/clinem\/dgae521"},{"key":"e_1_3_5_107_1","doi-asserted-by":"publisher","DOI":"10.1371\/journal.pone.0139483"},{"key":"e_1_3_5_108_1","doi-asserted-by":"publisher","DOI":"10.1016\/j.molmed.2023.03.008"},{"key":"e_1_3_5_109_1","doi-asserted-by":"publisher","DOI":"10.3390\/cells10051095"},{"key":"e_1_3_5_110_1","doi-asserted-by":"publisher","DOI":"10.1001\/jamanetworkopen.2019.14171"},{"key":"e_1_3_5_111_1","doi-asserted-by":"publisher","DOI":"10.1002\/ppul.25261"},{"key":"e_1_3_5_112_1","doi-asserted-by":"publisher","DOI":"10.1016\/S1474-4422(18)30025-5"},{"key":"e_1_3_5_113_1","doi-asserted-by":"publisher","DOI":"10.1111\/ene.70097"},{"key":"e_1_3_5_114_1","doi-asserted-by":"publisher","DOI":"10.18773\/austprescr.2015.024"},{"key":"e_1_3_5_115_1","doi-asserted-by":"publisher","DOI":"10.1056\/NEJMoa2107038"},{"key":"e_1_3_5_116_1","doi-asserted-by":"publisher","DOI":"10.1016\/j.stem.2019.01.002"},{"key":"e_1_3_5_117_1","doi-asserted-by":"publisher","DOI":"10.1016\/j.redox.2025.103676"},{"key":"e_1_3_5_118_1","doi-asserted-by":"publisher","DOI":"10.1016\/j.isci.2025.112335"},{"key":"e_1_3_5_119_1","doi-asserted-by":"publisher","DOI":"10.1016\/j.omtn.2022.11.017"}],"container-title":["Regenerative Medicine"],"original-title":[],"language":"en","link":[{"URL":"https:\/\/www.tandfonline.com\/doi\/pdf\/10.1080\/17460751.2025.2571355","content-type":"unspecified","content-version":"vor","intended-application":"similarity-checking"}],"deposited":{"date-parts":[[2025,10,23]],"date-time":"2025-10-23T16:44:20Z","timestamp":1761237860000},"score":1,"resource":{"primary":{"URL":"https:\/\/www.tandfonline.com\/doi\/full\/10.1080\/17460751.2025.2571355"}},"subtitle":[],"short-title":[],"issued":{"date-parts":[[2025,10,3]]},"references-count":117,"journal-issue":{"issue":"10","published-print":{"date-parts":[[2025,10,3]]}},"alternative-id":["10.1080\/17460751.2025.2571355"],"URL":"https:\/\/doi.org\/10.1080\/17460751.2025.2571355","relation":{},"ISSN":["1746-0751","1746-076X"],"issn-type":[{"type":"print","value":"1746-0751"},{"type":"electronic","value":"1746-076X"}],"subject":[],"published":{"date-parts":[[2025,10,3]]},"assertion":[{"value":"The publishing and review policy for this title is described in its Aims & Scope.","order":1,"name":"peerreview_statement","label":"Peer Review Statement"},{"value":"http:\/\/www.tandfonline.com\/action\/journalInformation?show=aimsScope&journalCode=irme20","URL":"http:\/\/www.tandfonline.com\/action\/journalInformation?show=aimsScope&journalCode=irme20","order":2,"name":"aims_and_scope_url","label":"Aim & Scope"},{"value":"2025-06-29","order":0,"name":"received","label":"Received","group":{"name":"publication_history","label":"Publication History"}},{"value":"2025-10-03","order":2,"name":"accepted","label":"Accepted","group":{"name":"publication_history","label":"Publication History"}},{"value":"2025-10-08","order":3,"name":"published","label":"Published","group":{"name":"publication_history","label":"Publication History"}}]}}