{"status":"ok","message-type":"work","message-version":"1.0.0","message":{"indexed":{"date-parts":[[2026,9,23]],"date-time":"2026-09-23T08:28:54Z","timestamp":1790152134236,"version":"4.0.1"},"reference-count":16,"publisher":"SAGE Publications","issue":"8","license":[{"start":{"date-parts":[[2001,5,20]],"date-time":"2001-05-20T00:00:00Z","timestamp":990316800000},"content-version":"tdm","delay-in-days":0,"URL":"http:\/\/www.liebertpub.com\/nv\/resources-tools\/text-and-data-mining-policy\/121\/"}],"content-domain":{"domain":[],"crossmark-restriction":false},"short-container-title":["Human Gene Therapy"],"published-print":{"date-parts":[[2001,5,20]]},"DOI":"10.1089\/104303401750195917","type":"journal-article","created":{"date-parts":[[2002,7,26]],"date-time":"2002-07-26T18:08:56Z","timestamp":1027706936000},"page":"955-965","source":"Crossref","is-referenced-by-count":51,"title":["Long-Term Efficacy after [E1\n                    <sup>-<\/sup>\n                    , polymerase\n                    <sup>-<\/sup>\n                    ] Adenovirus-Mediated Transfer of Human Acid-\u03b1-Glucosidase Gene into Glycogen Storage Disease Type II Knockout Mice"],"prefix":"10.1177","volume":"12","author":[{"given":"E.Y.","family":"Ding","sequence":"first","affiliation":[{"name":"Division of Medical Genetics, Department of Pediatrics, Duke University Medical Center, Durham, NC 27710."}],"role":[{"vocabulary":"crossref","role":"author"}]},{"given":"B.L.","family":"Hodges","sequence":"additional","affiliation":[{"name":"Division of Medical Genetics, Department of Pediatrics, Duke University Medical Center, Durham, NC 27710."}],"role":[{"vocabulary":"crossref","role":"author"}]},{"given":"H.","family":"Hu","sequence":"additional","affiliation":[{"name":"Division of Medical Genetics, Department of Pediatrics, Duke University Medical Center, Durham, NC 27710."}],"role":[{"vocabulary":"crossref","role":"author"}]},{"given":"A.J.","family":"McVie-Wylie","sequence":"additional","affiliation":[{"name":"Division of Medical Genetics, Department of Pediatrics, Duke University Medical Center, Durham, NC 27710."}],"role":[{"vocabulary":"crossref","role":"author"}]},{"given":"D.","family":"Serra","sequence":"additional","affiliation":[{"name":"Division of Medical Genetics, Department of Pediatrics, Duke University Medical Center, Durham, NC 27710."}],"role":[{"vocabulary":"crossref","role":"author"}]},{"given":"F.K.","family":"Migone","sequence":"additional","affiliation":[{"name":"Division of Medical Genetics, Department of Pediatrics, Duke University Medical Center, Durham, NC 27710."}],"role":[{"vocabulary":"crossref","role":"author"}]},{"given":"D.","family":"Pressley","sequence":"additional","affiliation":[{"name":"Division of Medical Genetics, Department of Pediatrics, Duke University Medical Center, Durham, NC 27710."}],"role":[{"vocabulary":"crossref","role":"author"}]},{"given":"Y.T.","family":"Chen","sequence":"additional","affiliation":[{"name":"Division of Medical Genetics, Department of Pediatrics, Duke University Medical Center, Durham, NC 27710."}],"role":[{"vocabulary":"crossref","role":"author"}]},{"given":"A.","family":"Amalfitano","sequence":"additional","affiliation":[{"name":"Division of Medical Genetics, Department of Pediatrics, Duke University Medical Center, Durham, NC 27710."}],"role":[{"vocabulary":"crossref","role":"author"}]}],"member":"179","reference":[{"key":"p_97","doi-asserted-by":"crossref","first-page":"926","DOI":"10.1128\/JVI.72.2.926-933.1998","volume":"72","author":"AMALFITANO A.","year":"1998","journal-title":"J. Virol."},{"key":"p_98","doi-asserted-by":"publisher","DOI":"10.1073\/pnas.96.16.8861"},{"key":"p_99","doi-asserted-by":"publisher","DOI":"10.1097\/00125817-200103000-00008"},{"key":"p_100","first-page":"A397","volume":"63","author":"BIJVOET A.G.","year":"1998","journal-title":"Am. J. Hum. Genet."},{"key":"p_101","doi-asserted-by":"publisher","DOI":"10.1016\/S1357-4310(00)01713-5"},{"key":"p_102","doi-asserted-by":"publisher","DOI":"10.1210\/jc.75.2.424"},{"key":"p_103","doi-asserted-by":"publisher","DOI":"10.1073\/pnas.95.5.2509"},{"key":"p_105","doi-asserted-by":"publisher","DOI":"10.1002\/1521-2254(200007\/08)2:4<250::AID-JGM113>3.0.CO;2-3"},{"key":"p_106","doi-asserted-by":"publisher","DOI":"10.1089\/10430349950018805"},{"key":"p_107","doi-asserted-by":"publisher","DOI":"10.1172\/JCI1722"},{"key":"p_108","doi-asserted-by":"publisher","DOI":"10.1093\/hmg\/7.11.1695"},{"key":"p_109","doi-asserted-by":"publisher","DOI":"10.1038\/sj.gt.3300609"},{"key":"p_110","doi-asserted-by":"publisher","DOI":"10.1074\/jbc.273.30.19086"},{"key":"p_111","doi-asserted-by":"crossref","first-page":"16733","DOI":"10.1016\/S0021-9258(19)84766-X","volume":"264","author":"SKLAR M.M.","year":"1989","journal-title":"J. Biol. Chem."},{"key":"p_112","doi-asserted-by":"publisher","DOI":"10.1089\/hum.1998.9.11-1609"},{"key":"p_113","doi-asserted-by":"publisher","DOI":"10.1073\/pnas.93.1.65"}],"container-title":["Human Gene Therapy"],"original-title":[],"language":"en","link":[{"URL":"http:\/\/www.liebertpub.com\/doi\/pdf\/10.1089\/104303401750195917","content-type":"unspecified","content-version":"vor","intended-application":"similarity-checking"}],"deposited":{"date-parts":[[2026,1,13]],"date-time":"2026-01-13T07:58:10Z","timestamp":1768291090000},"score":1,"resource":{"primary":{"URL":"https:\/\/journals.sagepub.com\/doi\/full\/10.1089\/104303401750195917"}},"subtitle":[],"short-title":[],"issued":{"date-parts":[[2001,5,20]]},"references-count":16,"journal-issue":{"issue":"8","published-print":{"date-parts":[[2001,5,20]]}},"alternative-id":["10.1089\/104303401750195917"],"URL":"https:\/\/doi.org\/10.1089\/104303401750195917","relation":{},"ISSN":["1043-0342","1557-7422"],"issn-type":[{"value":"1043-0342","type":"print"},{"value":"1557-7422","type":"electronic"}],"subject":[],"published":{"date-parts":[[2001,5,20]]}}}