{"status":"ok","message-type":"work","message-version":"1.0.0","message":{"indexed":{"date-parts":[[2026,1,13]],"date-time":"2026-01-13T12:51:35Z","timestamp":1768308695482,"version":"3.49.0"},"reference-count":44,"publisher":"SAGE Publications","issue":"13","license":[{"start":{"date-parts":[[1999,9,1]],"date-time":"1999-09-01T00:00:00Z","timestamp":936144000000},"content-version":"tdm","delay-in-days":0,"URL":"http:\/\/www.liebertpub.com\/nv\/resources-tools\/text-and-data-mining-policy\/121\/"}],"content-domain":{"domain":[],"crossmark-restriction":false},"short-container-title":["Human Gene Therapy"],"published-print":{"date-parts":[[1999,9]]},"DOI":"10.1089\/10430349950017158","type":"journal-article","created":{"date-parts":[[2002,7,26]],"date-time":"2002-07-26T18:05:44Z","timestamp":1027706744000},"page":"2163-2172","source":"Crossref","is-referenced-by-count":15,"title":["Enzymatic Correction and Cross-Correction of Mucopolysaccharidosis Type I Fibroblasts by Adeno-Associated Virus-Mediated Transduction of the alpha-L-Iduronidase Gene"],"prefix":"10.1177","volume":"10","author":[{"given":"Seth D.","family":"Hartung","sequence":"first","affiliation":[],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"Rukmini G.","family":"Reddy","sequence":"additional","affiliation":[],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"Chester B.","family":"Whitley","sequence":"additional","affiliation":[],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"R. Scott","family":"Mcivor","sequence":"additional","affiliation":[],"role":[{"role":"author","vocabulary":"crossref"}]}],"member":"179","reference":[{"key":"p_174","doi-asserted-by":"publisher","DOI":"10.1089\/hum.1992.3.4-371"},{"key":"p_175","first-page":"75","volume":"58","author":"ARONOVICH E.L.","year":"1996","journal-title":"Am. J. Hum. Genet."},{"key":"p_176","doi-asserted-by":"publisher","DOI":"10.1089\/hum.1996.7.16-1965"},{"key":"p_177","doi-asserted-by":"publisher","DOI":"10.1073\/pnas.90.24.11830"},{"key":"p_178","doi-asserted-by":"publisher","DOI":"10.1093\/hmg\/6.4.503"},{"key":"p_179","doi-asserted-by":"publisher","DOI":"10.1073\/pnas.96.5.2296"},{"key":"p_180","doi-asserted-by":"publisher","DOI":"10.1038\/sj.gt.3300411"},{"key":"p_181","doi-asserted-by":"publisher","DOI":"10.1073\/pnas.93.5.2025"},{"key":"p_182","doi-asserted-by":"crossref","first-page":"492","DOI":"10.1182\/blood.V88.2.492.bloodjournal882492","volume":"88","author":"FISHER-ADAMS G.","year":"1996","journal-title":"Blood"},{"key":"p_183","doi-asserted-by":"publisher","DOI":"10.1126\/science.162.3853.570"},{"key":"p_184","doi-asserted-by":"crossref","first-page":"1492","DOI":"10.1182\/blood.V84.5.1492.1492","volume":"84","author":"GOODMAN S.","year":"1994","journal-title":"Blood"},{"key":"p_185","doi-asserted-by":"crossref","first-page":"1294","DOI":"10.1203\/00006450-197911000-00018","volume":"13","author":"HASKINS M.E.","year":"1979","journal-title":"Pediatr. Res."},{"key":"p_186","doi-asserted-by":"publisher","DOI":"10.1016\/0304-4157(95)00004-B"},{"key":"p_187","doi-asserted-by":"publisher","DOI":"10.1016\/S0140-6736(81)91046-1"},{"key":"p_188","doi-asserted-by":"publisher","DOI":"10.1038\/sj.gt.3300504"},{"key":"p_189","doi-asserted-by":"publisher","DOI":"10.1006\/bmme.1996.0044"},{"key":"p_190","doi-asserted-by":"publisher","DOI":"10.1038\/ng1094-148"},{"key":"p_191","doi-asserted-by":"publisher","DOI":"10.1006\/exnr.1997.6736"},{"key":"p_192","first-page":"54","volume":"107","author":"KOHN D.B.","year":"1997","journal-title":"Clin. Exp. Immunol."},{"key":"p_193","doi-asserted-by":"crossref","first-page":"1776","DOI":"10.1128\/JVI.71.3.1776-1783.1997","volume":"71","author":"MALIK P.","year":"1997","journal-title":"J. Virol."},{"key":"p_194","doi-asserted-by":"crossref","first-page":"1358","DOI":"10.1182\/blood.V82.4.1358.1358","volume":"4","author":"MARECHAL V.","year":"1993","journal-title":"Blood"},{"key":"p_195","doi-asserted-by":"publisher","DOI":"10.1038\/ng0598-13"},{"key":"p_196","first-page":"194","volume":"140","author":"NISHIOKA J.","year":"1979","journal-title":"Clin. Orthopaed. Rel. Res."},{"key":"p_197","doi-asserted-by":"publisher","DOI":"10.1073\/pnas.94.4.1287"},{"key":"p_198","first-page":"A248","volume":"57","author":"PAN D.","year":"1995","journal-title":"Am. J. Hum. Genet."},{"key":"p_200","doi-asserted-by":"crossref","first-page":"4894","DOI":"10.1182\/blood.V87.11.4894.bloodjournal87114894","volume":"87","author":"PETERS C.","year":"1996","journal-title":"Blood"},{"key":"p_201","doi-asserted-by":"crossref","first-page":"2601","DOI":"10.1182\/blood.V91.7.2601","volume":"91","author":"PETERS C.","year":"1998","journal-title":"Blood"},{"key":"p_202","doi-asserted-by":"crossref","first-page":"8262","DOI":"10.1128\/JVI.71.11.8262-8267.1997","volume":"71","author":"PONNAZHAGAN S.","year":"1997","journal-title":"J. Virol."},{"key":"p_203","doi-asserted-by":"publisher","DOI":"10.1073\/pnas.76.5.2331"},{"key":"p_205","first-page":"973","volume":"53","author":"SCOTT H.","year":"1993","journal-title":"Am. J. Hum. Genet."},{"key":"p_206","doi-asserted-by":"publisher","DOI":"10.1002\/humu.1380060403"},{"key":"p_207","doi-asserted-by":"publisher","DOI":"10.1038\/ng0797-270"},{"key":"p_208","doi-asserted-by":"publisher","DOI":"10.1073\/pnas.95.24.14384"},{"key":"p_209","doi-asserted-by":"publisher","DOI":"10.1073\/pnas.80.19.6091"},{"key":"p_210","doi-asserted-by":"publisher","DOI":"10.1038\/sj.gt.3300364"},{"key":"p_211","doi-asserted-by":"publisher","DOI":"10.1038\/nm0797-771"},{"key":"p_212","doi-asserted-by":"crossref","first-page":"5472","DOI":"10.1128\/JVI.72.7.5472-5480.1998","volume":"72","author":"WANG X.S.","year":"1998","journal-title":"J. Virol."},{"key":"p_213","doi-asserted-by":"publisher","DOI":"10.1038\/sj.gt.3300775"},{"key":"p_215","doi-asserted-by":"publisher","DOI":"10.1002\/ajmg.1320460222"},{"key":"p_216","doi-asserted-by":"publisher","DOI":"10.1038\/360749a0"},{"key":"p_217","doi-asserted-by":"crossref","first-page":"8098","DOI":"10.1128\/JVI.70.11.8098-8108.1996","volume":"70","author":"XIAO X.","year":"1996","journal-title":"J. Virol."},{"key":"p_218","first-page":"12","volume":"10","author":"XIAO X.","year":"1996","journal-title":"Supplement"},{"key":"p_219","doi-asserted-by":"publisher","DOI":"10.1084\/jem.179.6.1867"},{"key":"p_220","doi-asserted-by":"crossref","first-page":"4646","DOI":"10.1128\/JVI.70.7.4646-4654.1996","volume":"70","author":"ZOLOTUKHIN S.","year":"1996","journal-title":"J. Virol."}],"container-title":["Human Gene Therapy"],"original-title":[],"language":"en","link":[{"URL":"http:\/\/www.liebertpub.com\/doi\/pdf\/10.1089\/10430349950017158","content-type":"unspecified","content-version":"vor","intended-application":"similarity-checking"}],"deposited":{"date-parts":[[2026,1,13]],"date-time":"2026-01-13T07:56:11Z","timestamp":1768290971000},"score":1,"resource":{"primary":{"URL":"https:\/\/journals.sagepub.com\/doi\/full\/10.1089\/10430349950017158"}},"subtitle":[],"short-title":[],"issued":{"date-parts":[[1999,9]]},"references-count":44,"journal-issue":{"issue":"13","published-print":{"date-parts":[[1999,9]]}},"alternative-id":["10.1089\/10430349950017158"],"URL":"https:\/\/doi.org\/10.1089\/10430349950017158","relation":{},"ISSN":["1043-0342","1557-7422"],"issn-type":[{"value":"1043-0342","type":"print"},{"value":"1557-7422","type":"electronic"}],"subject":[],"published":{"date-parts":[[1999,9]]}}}