{"status":"ok","message-type":"work","message-version":"1.0.0","message":{"indexed":{"date-parts":[[2026,5,16]],"date-time":"2026-05-16T05:45:26Z","timestamp":1778910326088,"version":"3.51.4"},"reference-count":35,"publisher":"SAGE Publications","issue":"3","license":[{"start":{"date-parts":[[1996,2,10]],"date-time":"1996-02-10T00:00:00Z","timestamp":823910400000},"content-version":"tdm","delay-in-days":0,"URL":"http:\/\/www.liebertpub.com\/nv\/resources-tools\/text-and-data-mining-policy\/121\/"}],"content-domain":{"domain":[],"crossmark-restriction":false},"short-container-title":["Human Gene Therapy"],"published-print":{"date-parts":[[1996,2,10]]},"DOI":"10.1089\/hum.1996.7.3-283","type":"journal-article","created":{"date-parts":[[2008,3,20]],"date-time":"2008-03-20T08:37:58Z","timestamp":1206002278000},"page":"283-290","source":"Crossref","is-referenced-by-count":32,"title":["Preclinical Studies of Lymphocyte Gene Therapy for Mild Hunter Syndrome (Mucopolysaccharidosis Type II)"],"prefix":"10.1177","volume":"7","author":[{"given":"Stephen E.","family":"Braun","sequence":"first","affiliation":[],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"Dao","family":"Pan","sequence":"additional","affiliation":[],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"Elena L.","family":"Aronovich","sequence":"additional","affiliation":[],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"Jon J.","family":"Jonsson","sequence":"additional","affiliation":[],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"R. Scott","family":"McIvor","sequence":"additional","affiliation":[],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"Chester B.","family":"Whitley","sequence":"additional","affiliation":[],"role":[{"role":"author","vocabulary":"crossref"}]}],"member":"179","reference":[{"key":"p_14","doi-asserted-by":"crossref","first-page":"3081","DOI":"10.1182\/blood.V78.11.3081.3081","volume":"78","author":"BIRKENMEIER E.H.","year":"1991","journal-title":"Blood"},{"key":"p_15","doi-asserted-by":"publisher","DOI":"10.1203\/00006450-199304001-00010"},{"key":"p_16","doi-asserted-by":"publisher","DOI":"10.1016\/0003-2697(76)90527-3"},{"key":"p_17","doi-asserted-by":"publisher","DOI":"10.1073\/pnas.90.24.11830"},{"key":"p_21","doi-asserted-by":"publisher","DOI":"10.1073\/pnas.68.2.303"},{"key":"p_22","first-page":"363","volume":"21","author":"FENJVES E.S.","year":"1995","journal-title":"J. Cell. Biochem."},{"key":"p_23","doi-asserted-by":"publisher","DOI":"10.1126\/science.162.3853.570"},{"key":"p_24","doi-asserted-by":"publisher","DOI":"10.1038\/312467a0"},{"key":"p_25","doi-asserted-by":"publisher","DOI":"10.1016\/0006-291X(72)90310-5"},{"key":"p_26","doi-asserted-by":"publisher","DOI":"10.1016\/S0140-6736(81)91059-X"},{"key":"p_27","doi-asserted-by":"publisher","DOI":"10.1016\/S0140-6736(81)91046-1"},{"key":"p_28","first-page":"381","volume":"7","author":"MORRIS C P","year":"1990","journal-title":"Mol. Biol. Med."},{"key":"p_29","first-page":"409","volume":"53","author":"JONSSON J.J.","year":"1993","journal-title":"Am. J. Hum. Genet."},{"key":"p_30","first-page":"597","volume":"56","author":"JONSSON J.J.","year":"1995","journal-title":"Am. J. Hum. Genet."},{"key":"p_31","first-page":"1738","author":"DI FERRANTE N.","year":"1971","journal-title":"Proc. Nad. Acad. Sci. U S A"},{"key":"p_38","first-page":"980","volume":"7","author":"MILLER A.D.","year":"1989","journal-title":"Biotechniques"},{"key":"p_39","doi-asserted-by":"publisher","DOI":"10.1007\/BF01800340"},{"key":"p_40","first-page":"240","volume":"18","author":"SNITZER K.","year":"1994","journal-title":"J. Cell. Biochem."},{"key":"p_41","doi-asserted-by":"publisher","DOI":"10.1146\/annurev.bi.60.070191.001353"},{"key":"p_43","doi-asserted-by":"publisher","DOI":"10.1038\/291244a0"},{"key":"p_44","first-page":"412","volume":"21","author":"PAN D.","year":"1995","journal-title":"J. Cell. Biochem."},{"key":"p_45","first-page":"369","volume":"21","author":"BARRANTES B.","year":"1995","journal-title":"J. Cell. Biochem."},{"key":"p_47","doi-asserted-by":"publisher","DOI":"10.1089\/hum.1994.5.6-701"},{"key":"p_48","doi-asserted-by":"publisher","DOI":"10.1172\/JCI117237"},{"key":"p_49","doi-asserted-by":"publisher","DOI":"10.1097\/00004424-198802000-00008"},{"key":"p_51","doi-asserted-by":"publisher","DOI":"10.1203\/00006450-198809000-00015"},{"key":"p_52","doi-asserted-by":"crossref","first-page":"11977","DOI":"10.1016\/S0021-9258(19)68720-X","volume":"256","author":"VARKI A.","year":"1981","journal-title":"J. Biol. Chem."},{"key":"p_53","doi-asserted-by":"publisher","DOI":"10.1089\/hum.1995.6.4-481"},{"key":"p_54","first-page":"31","volume":"22","author":"WARKENTIN P.I.","year":"1986","journal-title":"Birth Defects"},{"key":"p_56","first-page":"7","volume":"22","author":"WHITLEY C.B.","year":"1986","journal-title":"Birth Defects"},{"key":"p_57","doi-asserted-by":"publisher","DOI":"10.1002\/ajmg.1320460222"},{"key":"p_58","first-page":"101","volume":"53","author":"WHITLEY C.B.","year":"1993","journal-title":"Am. J. Hum. Genet."},{"key":"p_59","doi-asserted-by":"publisher","DOI":"10.1136\/adc.57.11.828"},{"key":"p_60","doi-asserted-by":"crossref","first-page":"481","DOI":"10.1111\/j.1469-8749.1983.tb13747.x","volume":"25","author":"HARPER P.S.","year":"1983","journal-title":"Dev. Med. Child Neurol."},{"key":"p_61","doi-asserted-by":"publisher","DOI":"10.1136\/jmg.19.4.241"}],"container-title":["Human Gene Therapy"],"original-title":[],"language":"en","link":[{"URL":"http:\/\/www.liebertpub.com\/doi\/pdf\/10.1089\/hum.1996.7.3-283","content-type":"unspecified","content-version":"vor","intended-application":"similarity-checking"}],"deposited":{"date-parts":[[2026,1,13]],"date-time":"2026-01-13T08:16:35Z","timestamp":1768292195000},"score":1,"resource":{"primary":{"URL":"https:\/\/journals.sagepub.com\/doi\/full\/10.1089\/hum.1996.7.3-283"}},"subtitle":[],"short-title":[],"issued":{"date-parts":[[1996,2,10]]},"references-count":35,"journal-issue":{"issue":"3","published-print":{"date-parts":[[1996,2,10]]}},"alternative-id":["10.1089\/hum.1996.7.3-283"],"URL":"https:\/\/doi.org\/10.1089\/hum.1996.7.3-283","relation":{},"ISSN":["1043-0342","1557-7422"],"issn-type":[{"value":"1043-0342","type":"print"},{"value":"1557-7422","type":"electronic"}],"subject":[],"published":{"date-parts":[[1996,2,10]]}}}