{"status":"ok","message-type":"work","message-version":"1.0.0","message":{"indexed":{"date-parts":[[2026,10,4]],"date-time":"2026-10-04T08:46:55Z","timestamp":1791103615074,"version":"4.1.0"},"reference-count":30,"publisher":"SAGE Publications","issue":"7","license":[{"start":{"date-parts":[[2010,7,1]],"date-time":"2010-07-01T00:00:00Z","timestamp":1277942400000},"content-version":"tdm","delay-in-days":0,"URL":"http:\/\/www.liebertpub.com\/nv\/resources-tools\/text-and-data-mining-policy\/121\/"}],"content-domain":{"domain":[],"crossmark-restriction":false},"short-container-title":["Human Gene Therapy"],"published-print":{"date-parts":[[2010,7]]},"DOI":"10.1089\/hum.2009.157","type":"journal-article","created":{"date-parts":[[2010,2,17]],"date-time":"2010-02-17T15:00:37Z","timestamp":1266418837000},"page":"903-910","source":"Crossref","is-referenced-by-count":53,"title":["Adeno-Associated Virus-Mediated Correction of a Canine Model of Glycogen Storage Disease Type Ia"],"prefix":"10.1177","volume":"21","author":[{"given":"David A.","family":"Weinstein","sequence":"first","affiliation":[{"name":"Glycogen Storage Disease Program, Division of Pediatric Endocrinology, Department of Pediatrics, University of Florida, Gainesville, FL 32610."}],"role":[{"vocabulary":"crossref","role":"author"}]},{"given":"Catherine E.","family":"Correia","sequence":"additional","affiliation":[{"name":"Glycogen Storage Disease Program, Division of Pediatric Endocrinology, Department of Pediatrics, University of Florida, Gainesville, FL 32610."}],"role":[{"vocabulary":"crossref","role":"author"}]},{"given":"Thomas","family":"Conlon","sequence":"additional","affiliation":[{"name":"Powell Gene Therapy Center, University of Florida, Gainesville, FL 32610."}],"role":[{"vocabulary":"crossref","role":"author"}]},{"given":"Andrew","family":"Specht","sequence":"additional","affiliation":[{"name":"Division of Small Animal Medicine, Department of Small Animal Clinical Sciences, University of Florida, Gainesville, FL 32610."}],"role":[{"vocabulary":"crossref","role":"author"}]},{"given":"John","family":"Verstegen","sequence":"additional","affiliation":[{"name":"Division of Theriogenology, Department of Large Animal Clinical Sciences, University of Florida, Gainesville, FL 32610."}],"role":[{"vocabulary":"crossref","role":"author"}]},{"given":"Karine","family":"Onclin-Verstegen","sequence":"additional","affiliation":[{"name":"Division of Theriogenology, Department of Large Animal Clinical Sciences, University of Florida, Gainesville, FL 32610."}],"role":[{"vocabulary":"crossref","role":"author"}]},{"given":"Martha","family":"Campbell-Thompson","sequence":"additional","affiliation":[{"name":"Department of Pathology, Immunology, and Laboratory Medicine, University of Florida, Gainesville, FL 32610."}],"role":[{"vocabulary":"crossref","role":"author"}]},{"given":"Gurmeet","family":"Dhaliwal","sequence":"additional","affiliation":[{"name":"Division of Theriogenology, Department of Large Animal Clinical Sciences, University of Florida, Gainesville, FL 32610."}],"role":[{"vocabulary":"crossref","role":"author"}]},{"given":"Layla","family":"Mirian","sequence":"additional","affiliation":[{"name":"Division of Theriogenology, Department of Large Animal Clinical Sciences, University of Florida, Gainesville, FL 32610."}],"role":[{"vocabulary":"crossref","role":"author"}]},{"given":"Holly","family":"Cossette","sequence":"additional","affiliation":[{"name":"Powell Gene Therapy Center, University of Florida, Gainesville, FL 32610."}],"role":[{"vocabulary":"crossref","role":"author"}]},{"given":"Darin J.","family":"Falk","sequence":"additional","affiliation":[{"name":"Powell Gene Therapy Center, University of Florida, Gainesville, FL 32610."}],"role":[{"vocabulary":"crossref","role":"author"}]},{"given":"Sean","family":"Germain","sequence":"additional","affiliation":[{"name":"Powell Gene Therapy Center, University of Florida, Gainesville, FL 32610."}],"role":[{"vocabulary":"crossref","role":"author"}]},{"given":"Nathalie","family":"Clement","sequence":"additional","affiliation":[{"name":"Powell Gene Therapy Center, University of Florida, Gainesville, FL 32610."}],"role":[{"vocabulary":"crossref","role":"author"}]},{"given":"Stacy","family":"Porvasnik","sequence":"additional","affiliation":[{"name":"Powell Gene Therapy Center, University of Florida, Gainesville, FL 32610."}],"role":[{"vocabulary":"crossref","role":"author"}]},{"given":"Laurie","family":"Fiske","sequence":"additional","affiliation":[{"name":"Glycogen Storage Disease Program, Division of Pediatric Endocrinology, Department of Pediatrics, University of Florida, Gainesville, FL 32610."}],"role":[{"vocabulary":"crossref","role":"author"}]},{"given":"Maggie","family":"Struck","sequence":"additional","affiliation":[{"name":"Animal Care Services, University of Florida, Gainesville, FL 32610."}],"role":[{"vocabulary":"crossref","role":"author"}]},{"given":"Harvey E.","family":"Ramirez","sequence":"additional","affiliation":[{"name":"Animal Care Services, University of Florida, Gainesville, FL 32610."}],"role":[{"vocabulary":"crossref","role":"author"}]},{"given":"Juan","family":"Jordan","sequence":"additional","affiliation":[{"name":"Animal Care Services, University of Florida, Gainesville, FL 32610."}],"role":[{"vocabulary":"crossref","role":"author"}]},{"given":"Karl","family":"Andrutis","sequence":"additional","affiliation":[{"name":"Animal Care Services, University of Florida, Gainesville, FL 32610."}],"role":[{"vocabulary":"crossref","role":"author"}]},{"given":"Janice Y.","family":"Chou","sequence":"additional","affiliation":[{"name":"Section on Cellular Differentiation, Program in Developmental Endocrinology and Genetics, National Institute of Child Health and Human Development, National Institutes of Health, Bethesda, MD 20892."}],"role":[{"vocabulary":"crossref","role":"author"}]},{"given":"Barry J.","family":"Byrne","sequence":"additional","affiliation":[{"name":"Powell Gene Therapy Center, University of Florida, Gainesville, FL 32610."},{"name":"Division of Cellular and Molecular Therapy, Department of Pediatrics, University of Florida, Gainesville, FL 32610."}],"role":[{"vocabulary":"crossref","role":"author"}]},{"given":"Cathryn S.","family":"Mah","sequence":"additional","affiliation":[{"name":"Powell Gene Therapy Center, University of Florida, Gainesville, FL 32610."},{"name":"Division of Cellular and Molecular Therapy, Department of Pediatrics, University of Florida, Gainesville, FL 32610."}],"role":[{"vocabulary":"crossref","role":"author"}]}],"member":"179","reference":[{"key":"B1","doi-asserted-by":"publisher","DOI":"10.1007\/s10545-007-0479-0"},{"key":"B2","doi-asserted-by":"publisher","DOI":"10.1177\/030098589503200502"},{"key":"B3","first-page":"905","volume-title":"The Metabolic and Molecular Bases of Inherited Disease","author":"Chen Y.T.","year":"1995","edition":"7"},{"key":"B4","doi-asserted-by":"publisher","DOI":"10.1056\/NEJM198401193100306"},{"key":"B5","doi-asserted-by":"publisher","DOI":"10.2174\/1566524024605798"},{"key":"B6","doi-asserted-by":"publisher","DOI":"10.1016\/j.ymthe.2005.05.016"},{"key":"B7","doi-asserted-by":"publisher","DOI":"10.1038\/mt.2008.72"},{"key":"B8","doi-asserted-by":"publisher","DOI":"10.1038\/mt.2009.88"},{"key":"B9","doi-asserted-by":"publisher","DOI":"10.1007\/BF00442683"},{"key":"B10","doi-asserted-by":"publisher","DOI":"10.1038\/sj.gt.3302650"},{"key":"B11","doi-asserted-by":"publisher","DOI":"10.1016\/j.febslet.2007.07.013"},{"key":"B12","doi-asserted-by":"publisher","DOI":"10.1006\/bmme.1997.2600"},{"key":"B13","doi-asserted-by":"publisher","DOI":"10.1354\/vp.38-1-83"},{"key":"B14","doi-asserted-by":"publisher","DOI":"10.1038\/sj.gt.3302774"},{"key":"B15","doi-asserted-by":"publisher","DOI":"10.1007\/s10545-007-0519-9"},{"key":"B16","doi-asserted-by":"publisher","DOI":"10.1038\/sj.mt.6300188"},{"key":"B17","doi-asserted-by":"publisher","DOI":"10.1038\/mt.2008.15"},{"key":"B18","doi-asserted-by":"publisher","DOI":"10.1038\/ng0696-203"},{"key":"B19","doi-asserted-by":"publisher","DOI":"10.1038\/sj.mt.6300100"},{"key":"B20","doi-asserted-by":"publisher","DOI":"10.1046\/j.1365-2265.2003.01717.x"},{"key":"B21","doi-asserted-by":"publisher","DOI":"10.1210\/jc.2004-0890"},{"key":"B22","doi-asserted-by":"publisher","DOI":"10.3748\/wjg.v13.i18.2541"},{"key":"B23","doi-asserted-by":"publisher","DOI":"10.1203\/00006450-198409000-00015"},{"key":"B24","doi-asserted-by":"crossref","first-page":"95","DOI":"10.1093\/ajcn\/48.1.95","volume":"48","author":"Smit G.P.","year":"1988","journal-title":"Am. J. Clin. Nutr."},{"key":"B25","doi-asserted-by":"publisher","DOI":"10.1007\/BF01799498"},{"key":"B26","doi-asserted-by":"publisher","DOI":"10.1093\/hmg\/11.18.2155"},{"key":"B27","doi-asserted-by":"publisher","DOI":"10.1016\/S0079-6336(81)80001-0"},{"key":"B28","doi-asserted-by":"publisher","DOI":"10.1038\/nbt1073"},{"key":"B29","doi-asserted-by":"publisher","DOI":"10.1023\/A:1021831621210"},{"key":"B30","doi-asserted-by":"publisher","DOI":"10.1016\/S1046-2023(02)00220-7"}],"container-title":["Human Gene Therapy"],"original-title":[],"language":"en","link":[{"URL":"http:\/\/www.liebertpub.com\/doi\/full-xml\/10.1089\/hum.2009.157","content-type":"application\/xml","content-version":"vor","intended-application":"text-mining"},{"URL":"http:\/\/www.liebertpub.com\/doi\/pdf\/10.1089\/hum.2009.157","content-type":"unspecified","content-version":"vor","intended-application":"similarity-checking"}],"deposited":{"date-parts":[[2026,4,29]],"date-time":"2026-04-29T07:53:54Z","timestamp":1777449234000},"score":1,"resource":{"primary":{"URL":"https:\/\/journals.sagepub.com\/doi\/full\/10.1089\/hum.2009.157"}},"subtitle":[],"short-title":[],"issued":{"date-parts":[[2010,7]]},"references-count":30,"journal-issue":{"issue":"7","published-print":{"date-parts":[[2010,7]]}},"alternative-id":["10.1089\/hum.2009.157"],"URL":"https:\/\/doi.org\/10.1089\/hum.2009.157","relation":{},"ISSN":["1043-0342","1557-7422"],"issn-type":[{"value":"1043-0342","type":"print"},{"value":"1557-7422","type":"electronic"}],"subject":[],"published":{"date-parts":[[2010,7]]}}}