{"status":"ok","message-type":"work","message-version":"1.0.0","message":{"indexed":{"date-parts":[[2026,5,14]],"date-time":"2026-05-14T21:15:48Z","timestamp":1778793348636,"version":"3.51.4"},"reference-count":29,"publisher":"SAGE Publications","issue":"11","license":[{"start":{"date-parts":[[2019,11,1]],"date-time":"2019-11-01T00:00:00Z","timestamp":1572566400000},"content-version":"tdm","delay-in-days":0,"URL":"https:\/\/www.liebertpub.com\/nv\/resources-tools\/text-and-data-mining-policy\/121\/"}],"content-domain":{"domain":[],"crossmark-restriction":false},"short-container-title":["Human Gene Therapy"],"published-print":{"date-parts":[[2019,11,1]]},"DOI":"10.1089\/hum.2019.047","type":"journal-article","created":{"date-parts":[[2019,6,10]],"date-time":"2019-06-10T07:22:26Z","timestamp":1560151346000},"page":"1395-1404","source":"Crossref","is-referenced-by-count":22,"title":["Hematopoietic Stem Cell-Targeted Neonatal Gene Therapy with a Clinically Applicable Lentiviral Vector Corrects Osteopetrosis in\n                    <i>oc\/oc<\/i>\n                    Mice"],"prefix":"10.1177","volume":"30","author":[{"given":"Henrik","family":"L\u00f6fvall","sequence":"first","affiliation":[{"name":"Department of Molecular Medicine and Gene Therapy, Lund Strategic Center for Stem Cell Biology, Lund University, Lund, Sweden."},{"name":"Department of Endocrinology, Nordic Bioscience, Herlev, Denmark."}],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"Michael","family":"Rothe","sequence":"additional","affiliation":[{"name":"Institute of Experimental Hematology, Hannover Medical School, Hannover, Germany."}],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"Axel","family":"Schambach","sequence":"additional","affiliation":[{"name":"Institute of Experimental Hematology, Hannover Medical School, Hannover, Germany."}],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"Kim","family":"Henriksen","sequence":"additional","affiliation":[{"name":"Department of Endocrinology, Nordic Bioscience, Herlev, Denmark."}],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"Johan","family":"Richter","sequence":"additional","affiliation":[{"name":"Department of Molecular Medicine and Gene Therapy, Lund Strategic Center for Stem Cell Biology, Lund University, Lund, Sweden."}],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"Ilana","family":"Moscatelli","sequence":"additional","affiliation":[{"name":"Department of Molecular Medicine and Gene Therapy, Lund Strategic Center for Stem Cell Biology, Lund University, Lund, Sweden."}],"role":[{"role":"author","vocabulary":"crossref"}]}],"member":"179","reference":[{"key":"B1","doi-asserted-by":"publisher","DOI":"10.1007\/s00439-008-0583-8"},{"key":"B2","doi-asserted-by":"publisher","DOI":"10.1056\/NEJMra040952"},{"key":"B3","doi-asserted-by":"publisher","DOI":"10.1016\/j.bone.2017.02.002"},{"key":"B4","doi-asserted-by":"publisher","DOI":"10.1034\/j.1399-3046.1999.00063.x"},{"key":"B5","doi-asserted-by":"publisher","DOI":"10.1007\/s11914-018-0415-2"},{"key":"B6","doi-asserted-by":"publisher","DOI":"10.1038\/77131"},{"key":"B7","doi-asserted-by":"publisher","DOI":"10.1038\/nrendo.2013.137"},{"key":"B8","doi-asserted-by":"publisher","DOI":"10.1016\/S0002-9440(10)63798-4"},{"key":"B9","doi-asserted-by":"publisher","DOI":"10.1136\/adc.83.5.449"},{"key":"B10","doi-asserted-by":"publisher","DOI":"10.1016\/j.bbmt.2012.10.026"},{"key":"B11","doi-asserted-by":"publisher","DOI":"10.1182\/blood.V99.9.3458"},{"key":"B12","doi-asserted-by":"publisher","DOI":"10.2174\/156652309788488613"},{"key":"B13","doi-asserted-by":"publisher","DOI":"10.1016\/S8756-3282(99)00278-1"},{"key":"B14","doi-asserted-by":"publisher","DOI":"10.1182\/blood-2006-12-061382"},{"key":"B15","doi-asserted-by":"publisher","DOI":"10.1016\/j.celrep.2013.09.040"},{"key":"B16","doi-asserted-by":"publisher","DOI":"10.1056\/NEJM200301163480314"},{"key":"B17","doi-asserted-by":"publisher","DOI":"10.1126\/science.1088547"},{"key":"B18","doi-asserted-by":"publisher","DOI":"10.1038\/mt.2013.265"},{"key":"B19","doi-asserted-by":"publisher","DOI":"10.1126\/scitranslmed.aad8856"},{"key":"B20","doi-asserted-by":"publisher","DOI":"10.1371\/journal.pone.0062333"},{"key":"B21","doi-asserted-by":"publisher","DOI":"10.1182\/blood-2009-10-250209"},{"key":"B22","doi-asserted-by":"publisher","DOI":"10.1089\/hum.2017.053"},{"key":"B23","doi-asserted-by":"publisher","DOI":"10.15252\/emmm.201707573"},{"key":"B24","doi-asserted-by":"publisher","DOI":"10.15252\/emmm.201809958"},{"key":"B25","doi-asserted-by":"publisher","DOI":"10.1006\/bbrc.2000.2229"},{"key":"B26","doi-asserted-by":"publisher","DOI":"10.1007\/s00223-016-0187-6"},{"key":"B27","doi-asserted-by":"publisher","DOI":"10.1038\/sj.leu.2403449"},{"key":"B28","doi-asserted-by":"publisher","DOI":"10.1016\/j.exphem.2005.11.010"},{"key":"B29","doi-asserted-by":"publisher","DOI":"10.1038\/sj.bmt.1704194"}],"container-title":["Human Gene Therapy"],"original-title":[],"language":"en","link":[{"URL":"https:\/\/www.liebertpub.com\/doi\/full-xml\/10.1089\/hum.2019.047","content-type":"application\/xml","content-version":"vor","intended-application":"text-mining"},{"URL":"https:\/\/www.liebertpub.com\/doi\/pdf\/10.1089\/hum.2019.047","content-type":"unspecified","content-version":"vor","intended-application":"similarity-checking"}],"deposited":{"date-parts":[[2026,4,29]],"date-time":"2026-04-29T07:54:45Z","timestamp":1777449285000},"score":1,"resource":{"primary":{"URL":"https:\/\/journals.sagepub.com\/doi\/full\/10.1089\/hum.2019.047"}},"subtitle":[],"short-title":[],"issued":{"date-parts":[[2019,11,1]]},"references-count":29,"journal-issue":{"issue":"11","published-print":{"date-parts":[[2019,11,1]]}},"alternative-id":["10.1089\/hum.2019.047"],"URL":"https:\/\/doi.org\/10.1089\/hum.2019.047","relation":{},"ISSN":["1043-0342","1557-7422"],"issn-type":[{"value":"1043-0342","type":"print"},{"value":"1557-7422","type":"electronic"}],"subject":[],"published":{"date-parts":[[2019,11,1]]}}}