{"status":"ok","message-type":"work","message-version":"1.0.0","message":{"indexed":{"date-parts":[[2026,10,18]],"date-time":"2026-10-18T02:51:17Z","timestamp":1792291877035,"version":"4.4.0"},"reference-count":242,"publisher":"SAGE Publications","issue":"17-18","license":[{"start":{"date-parts":[[2020,9,1]],"date-time":"2020-09-01T00:00:00Z","timestamp":1598918400000},"content-version":"tdm","delay-in-days":0,"URL":"https:\/\/www.liebertpub.com\/nv\/resources-tools\/text-and-data-mining-policy\/121\/"}],"content-domain":{"domain":[],"crossmark-restriction":false},"short-container-title":["Human Gene Therapy"],"published-print":{"date-parts":[[2020,9,1]]},"DOI":"10.1089\/hum.2020.166","type":"journal-article","created":{"date-parts":[[2020,8,20]],"date-time":"2020-08-20T01:05:34Z","timestamp":1597885534000},"page":"921-939","source":"Crossref","is-referenced-by-count":16,"title":["New Directions in Pulmonary Gene Therapy"],"prefix":"10.1177","volume":"31","author":[{"given":"Amber","family":"Vu","sequence":"first","affiliation":[{"name":"Stead Family Department of Pediatrics, Center for Gene Therapy, The University of Iowa, Iowa City, Iowa, USA."}],"role":[{"vocabulary":"crossref","role":"author"}]},{"suffix":", Jr.","given":"Paul B.","family":"McCray","sequence":"additional","affiliation":[{"name":"Stead Family Department of Pediatrics, Center for Gene Therapy, The University of Iowa, Iowa City, Iowa, USA."}],"role":[{"vocabulary":"crossref","role":"author"}]}],"member":"179","reference":[{"key":"B1","doi-asserted-by":"publisher","DOI":"10.1016\/j.copbio.2018.11.016"},{"key":"B2","doi-asserted-by":"publisher","DOI":"10.1016\/S0140-6736(17)31868-8"},{"key":"B3","doi-asserted-by":"publisher","DOI":"10.1038\/nbt.4068"},{"key":"B4","doi-asserted-by":"publisher","DOI":"10.3390\/genes9110538"},{"key":"B5","doi-asserted-by":"publisher","DOI":"10.1016\/j.gene.2020.144636"},{"key":"B6","doi-asserted-by":"publisher","DOI":"10.1128\/JB.169.12.5429-5433.1987"},{"key":"B7","doi-asserted-by":"publisher","DOI":"10.1126\/science.1138140"},{"key":"B8","doi-asserted-by":"publisher","DOI":"10.1038\/nature09523"},{"key":"B9","doi-asserted-by":"publisher","DOI":"10.1016\/j.sbi.2016.11.013"},{"key":"B10","doi-asserted-by":"publisher","DOI":"10.1016\/j.cell.2014.02.001"},{"key":"B11","doi-asserted-by":"publisher","DOI":"10.1073\/pnas.95.9.5172"},{"key":"B12","doi-asserted-by":"publisher","DOI":"10.1146\/annurev-genet-051710-150955"},{"key":"B13","doi-asserted-by":"publisher","DOI":"10.1146\/annurev.biochem.77.061306.125255"},{"key":"B14","doi-asserted-by":"publisher","DOI":"10.1016\/j.cell.2015.09.038"},{"key":"B15","doi-asserted-by":"publisher","DOI":"10.1038\/s41467-018-06129-w"},{"key":"B16","doi-asserted-by":"publisher","DOI":"10.1038\/nbt.3609"},{"key":"B17","doi-asserted-by":"publisher","DOI":"10.1038\/s41467-019-12922-y"},{"key":"B18","doi-asserted-by":"publisher","DOI":"10.1038\/s41587-018-0011-0"},{"key":"B19","doi-asserted-by":"publisher","DOI":"10.1038\/s41467-019-10735-7"},{"key":"B20","doi-asserted-by":"publisher","DOI":"10.1038\/nature09929"},{"key":"B21","doi-asserted-by":"publisher","DOI":"10.1038\/nature26155"},{"key":"B22","doi-asserted-by":"publisher","DOI":"10.1038\/s41587-020-0412-8"},{"key":"B23","doi-asserted-by":"publisher","DOI":"10.1038\/s41477-018-0321-8"},{"key":"B24","doi-asserted-by":"publisher","DOI":"10.1016\/j.molp.2019.03.010"},{"key":"B25","doi-asserted-by":"publisher","DOI":"10.1016\/j.molp.2019.03.009"},{"key":"B26","doi-asserted-by":"publisher","DOI":"10.1038\/s41587-019-0134-y"},{"key":"B27","doi-asserted-by":"publisher","DOI":"10.1038\/s41586-019-0908-x"},{"key":"B28","doi-asserted-by":"publisher","DOI":"10.1016\/j.molmet.2017.07.001"},{"key":"B29","doi-asserted-by":"publisher","DOI":"10.1016\/j.cell.2013.02.022"},{"key":"B30","doi-asserted-by":"publisher","DOI":"10.12688\/f1000research.11113.1"},{"key":"B31","doi-asserted-by":"publisher","DOI":"10.1080\/21655979.2018.1470720"},{"key":"B32","doi-asserted-by":"publisher","DOI":"10.1038\/s41586-019-1430-x"},{"key":"B33","doi-asserted-by":"publisher","DOI":"10.1038\/s41576-018-0059-1"},{"key":"B34","doi-asserted-by":"publisher","DOI":"10.1038\/nature24644"},{"key":"B35","doi-asserted-by":"publisher","DOI":"10.1038\/nature17946"},{"key":"B36","doi-asserted-by":"publisher","DOI":"10.1093\/nar\/gkv1222"},{"key":"B37","doi-asserted-by":"publisher","DOI":"10.1038\/s41587-020-0453-z"},{"key":"B38","doi-asserted-by":"crossref","first-page":"289","DOI":"10.1126\/science.aav9973","volume":"364","author":"Zuo E","year":"2019","journal-title":"Science"},{"key":"B39","doi-asserted-by":"publisher","DOI":"10.1038\/s41467-019-10421-8"},{"key":"B40","doi-asserted-by":"publisher","DOI":"10.1038\/s41467-020-15892-8"},{"key":"B41","doi-asserted-by":"publisher","DOI":"10.1096\/fj.201901587R"},{"key":"B42","doi-asserted-by":"publisher","DOI":"10.3389\/fgene.2019.00215"},{"key":"B43","doi-asserted-by":"publisher","DOI":"10.1038\/s41467-018-07322-7"},{"key":"B44","doi-asserted-by":"publisher","DOI":"10.1038\/s41591-018-0209-1"},{"key":"B45","doi-asserted-by":"publisher","DOI":"10.1038\/nbt.4148"},{"key":"B46","doi-asserted-by":"publisher","DOI":"10.1038\/s41586-019-1711-4"},{"key":"B47","doi-asserted-by":"publisher","DOI":"10.1016\/j.addr.2008.09.008"},{"key":"B48","doi-asserted-by":"publisher","DOI":"10.1016\/j.addr.2008.09.011"},{"key":"B49","doi-asserted-by":"publisher","DOI":"10.1016\/j.jconrel.2016.05.031"},{"key":"B50","doi-asserted-by":"publisher","DOI":"10.1016\/S0006-3495(94)80802-1"},{"key":"B51","doi-asserted-by":"publisher","DOI":"10.1016\/S0006-3495(01)75844-4"},{"key":"B52","doi-asserted-by":"publisher","DOI":"10.1086\/595830"},{"key":"B53","doi-asserted-by":"publisher","DOI":"10.1089\/hum.2006.17.440"},{"key":"B54","doi-asserted-by":"publisher","DOI":"10.1038\/sj.gt.3300994"},{"key":"B55","doi-asserted-by":"publisher","DOI":"10.1378\/chest.125.2.509"},{"key":"B56","doi-asserted-by":"publisher","DOI":"10.1172\/JCI118573"},{"key":"B57","doi-asserted-by":"publisher","DOI":"10.1128\/JVI.00227-08"},{"key":"B58","doi-asserted-by":"publisher","DOI":"10.1164\/rccm.201206-1056OC"},{"key":"B59","doi-asserted-by":"publisher","DOI":"10.1016\/j.ymthe.2020.05.007"},{"key":"B60","doi-asserted-by":"publisher","DOI":"10.1038\/nmeth.3993"},{"key":"B61","doi-asserted-by":"publisher","DOI":"10.1038\/s41591-019-0344-3"},{"key":"B62","doi-asserted-by":"publisher","DOI":"10.1038\/s41551-019-0431-2"},{"key":"B63","doi-asserted-by":"publisher","DOI":"10.1016\/j.ymthe.2020.04.017"},{"key":"B64","doi-asserted-by":"publisher","DOI":"10.1038\/s41591-018-0326-x"},{"key":"B65","doi-asserted-by":"publisher","DOI":"10.1016\/j.omtm.2018.06.006"},{"key":"B66","doi-asserted-by":"publisher","DOI":"10.1038\/s41591-018-0204-6"},{"key":"B67","doi-asserted-by":"publisher","DOI":"10.1038\/s41467-019-09693-x"},{"key":"B68","doi-asserted-by":"publisher","DOI":"10.1002\/(SICI)1521-2254(199909\/10)1:5<331::AID-JGM60>3.0.CO;2-8"},{"key":"B69","doi-asserted-by":"publisher","DOI":"10.1089\/hum.1997.8.7-817"},{"key":"B70","doi-asserted-by":"publisher","DOI":"10.1089\/hum.1997.8.4-431"},{"key":"B71","doi-asserted-by":"publisher","DOI":"10.1080\/10611860600834375"},{"key":"B72","doi-asserted-by":"publisher","DOI":"10.1093\/toxsci\/kfv005"},{"key":"B73","doi-asserted-by":"publisher","DOI":"10.1006\/mthe.2002.0698"},{"key":"B74","doi-asserted-by":"publisher","DOI":"10.1128\/JVI.72.7.6014-6023.1998"},{"key":"B75","doi-asserted-by":"publisher","DOI":"10.1513\/AnnalsATS.201506-344KV"},{"key":"B76","doi-asserted-by":"publisher","DOI":"10.1111\/j.1365-2796.2006.01744.x"},{"key":"B77","doi-asserted-by":"publisher","DOI":"10.1038\/mt.2016.182"},{"key":"B78","doi-asserted-by":"publisher","DOI":"10.1126\/scitranslmed.3010525"},{"key":"B79","doi-asserted-by":"publisher","DOI":"10.2217\/nnm.10.123"},{"key":"B80","doi-asserted-by":"publisher","DOI":"10.1371\/journal.pone.0019919"},{"key":"B81","doi-asserted-by":"publisher","DOI":"10.1038\/mt.2014.89"},{"key":"B82","doi-asserted-by":"publisher","DOI":"10.1038\/mt.2011.160"},{"key":"B83","doi-asserted-by":"publisher","DOI":"10.1002\/anie.201208556"},{"key":"B84","doi-asserted-by":"publisher","DOI":"10.1016\/j.jconrel.2014.01.007"},{"key":"B85","doi-asserted-by":"publisher","DOI":"10.1073\/pnas.182412299"},{"key":"B86","doi-asserted-by":"publisher","DOI":"10.1016\/j.ymthe.2003.08.015"},{"key":"B87","doi-asserted-by":"publisher","DOI":"10.1073\/pnas.0409845102"},{"key":"B88","doi-asserted-by":"publisher","DOI":"10.1038\/mt.2009.230"},{"key":"B89","doi-asserted-by":"publisher","DOI":"10.1038\/mt.2008.261"},{"key":"B90","doi-asserted-by":"publisher","DOI":"10.1089\/104303403322124792"},{"key":"B91","doi-asserted-by":"publisher","DOI":"10.1089\/hum.1998.9.6-889"},{"key":"B92","doi-asserted-by":"publisher","DOI":"10.1089\/hum.2007.022"},{"key":"B93","doi-asserted-by":"publisher","DOI":"10.1089\/104303401753153956"},{"key":"B94","doi-asserted-by":"publisher","DOI":"10.1097\/00005537-199902000-00017"},{"key":"B95","doi-asserted-by":"publisher","DOI":"10.1038\/nature16465"},{"key":"B96","doi-asserted-by":"publisher","DOI":"10.1073\/pnas.0813365106"},{"key":"B97","doi-asserted-by":"publisher","DOI":"10.1038\/s41434-019-0078-3"},{"key":"B98","doi-asserted-by":"publisher","DOI":"10.1128\/JVI.00254-08"},{"key":"B99","doi-asserted-by":"publisher","DOI":"10.1038\/mt.2016.62"},{"key":"B100","doi-asserted-by":"publisher","DOI":"10.1172\/jci.insight.131610"},{"key":"B101","doi-asserted-by":"publisher","DOI":"10.1089\/hum.2019.339"},{"key":"B102","doi-asserted-by":"publisher","DOI":"10.1038\/nature12875"},{"key":"B103","doi-asserted-by":"publisher","DOI":"10.1016\/j.ymthe.2017.09.021"},{"key":"B104","doi-asserted-by":"publisher","DOI":"10.1016\/j.ymthe.2006.05.009"},{"key":"B105","doi-asserted-by":"publisher","DOI":"10.1016\/j.omtm.2019.01.008"},{"key":"B106","doi-asserted-by":"publisher","DOI":"10.1038\/nbt.3440"},{"key":"B107","doi-asserted-by":"publisher","DOI":"10.1038\/ncomms7246"},{"key":"B108","doi-asserted-by":"publisher","DOI":"10.1016\/j.omtm.2018.03.006"},{"key":"B109","doi-asserted-by":"publisher","DOI":"10.1038\/mt.2009.255"},{"key":"B110","doi-asserted-by":"publisher","DOI":"10.1089\/hum.2015.001"},{"key":"B111","doi-asserted-by":"publisher","DOI":"10.1073\/pnas.261714599"},{"key":"B112","doi-asserted-by":"publisher","DOI":"10.1093\/nar\/gkv601"},{"key":"B113","doi-asserted-by":"publisher","DOI":"10.1073\/pnas.1701083114"},{"key":"B114","doi-asserted-by":"publisher","DOI":"10.1038\/s41551-019-0501-5"},{"key":"B115","doi-asserted-by":"publisher","DOI":"10.1126\/scitranslmed.aay9101"},{"key":"B116","doi-asserted-by":"publisher","DOI":"10.1165\/rcmb.2019-0006OC"},{"key":"B117","doi-asserted-by":"publisher","DOI":"10.1038\/nbt0702-697"},{"key":"B118","doi-asserted-by":"publisher","DOI":"10.1128\/JVI.72.6.5224-5230.1998"},{"key":"B119","doi-asserted-by":"publisher","DOI":"10.1016\/j.omtm.2019.01.003"},{"key":"B120","doi-asserted-by":"publisher","DOI":"10.1089\/hum.2017.060"},{"key":"B121","doi-asserted-by":"publisher","DOI":"10.1038\/mt.2013.92"},{"key":"B122","doi-asserted-by":"publisher","DOI":"10.1128\/JVI.02964-15"},{"key":"B123","doi-asserted-by":"publisher","DOI":"10.1089\/hum.2018.173"},{"key":"B124","doi-asserted-by":"publisher","DOI":"10.3390\/genes11040439"},{"key":"B125","doi-asserted-by":"publisher","DOI":"10.1089\/10430340260355347"},{"key":"B126","doi-asserted-by":"publisher","DOI":"10.1089\/hum.2009.092"},{"key":"B127","doi-asserted-by":"publisher","DOI":"10.1093\/hmg\/ddr141"},{"key":"B128","doi-asserted-by":"publisher","DOI":"10.1128\/JVI.80.4.1874-1885.2006"},{"key":"B129","first-page":"94","author":"Fakhiri J","year":"2020","journal-title":"J Virol"},{"key":"B130","doi-asserted-by":"publisher","DOI":"10.1128\/JVI.02721-07"},{"key":"B131","doi-asserted-by":"publisher","DOI":"10.1093\/nar\/gku749"},{"key":"B132","doi-asserted-by":"publisher","DOI":"10.1038\/mtna.2012.47"},{"key":"B133","doi-asserted-by":"publisher","DOI":"10.1128\/JVI.75.23.11747-11754.2001"},{"key":"B134","doi-asserted-by":"publisher","DOI":"10.1002\/jgm.1025"},{"key":"B135","doi-asserted-by":"publisher","DOI":"10.1128\/JVI.72.12.9818-9826.1998"},{"key":"B136","doi-asserted-by":"publisher","DOI":"10.1165\/ajrcmb.22.2.3938"},{"key":"B137","doi-asserted-by":"publisher","DOI":"10.1038\/sj.gt.3301138"},{"key":"B138","doi-asserted-by":"publisher","DOI":"10.1080\/01902148.2017.1395931"},{"key":"B139","doi-asserted-by":"publisher","DOI":"10.1038\/gt.2017.78"},{"key":"B140","doi-asserted-by":"publisher","DOI":"10.1128\/JVI.77.10.5902-5910.2003"},{"key":"B141","doi-asserted-by":"publisher","DOI":"10.1128\/JVI.79.20.12818-12827.2005"},{"key":"B142","doi-asserted-by":"publisher","DOI":"10.1089\/hum.2005.16.479"},{"key":"B143","doi-asserted-by":"publisher","DOI":"10.1128\/JVI.76.18.9378-9388.2002"},{"key":"B144","doi-asserted-by":"publisher","DOI":"10.1038\/85664"},{"key":"B145","doi-asserted-by":"publisher","DOI":"10.1038\/mt.2010.13"},{"key":"B146","doi-asserted-by":"publisher","DOI":"10.1038\/sj.gt.3302991"},{"key":"B147","doi-asserted-by":"publisher","DOI":"10.1038\/s41592-020-0771-6"},{"key":"B148","doi-asserted-by":"publisher","DOI":"10.1073\/pnas.1917668117"},{"key":"B149","doi-asserted-by":"publisher","DOI":"10.1093\/nar\/gkaa219"},{"key":"B150","doi-asserted-by":"publisher","DOI":"10.1016\/j.omtm.2018.04.008"},{"key":"B151","doi-asserted-by":"publisher","DOI":"10.1261\/rna.071704.119"},{"key":"B152","doi-asserted-by":"publisher","DOI":"10.2174\/1566523214666140825124311"},{"key":"B155","doi-asserted-by":"publisher","DOI":"10.1186\/s13059-020-01956-x"},{"key":"B156","doi-asserted-by":"publisher","DOI":"10.1038\/s41467-020-16542-9"},{"key":"B157","doi-asserted-by":"publisher","DOI":"10.1016\/j.ymthe.2019.09.006"},{"key":"B158","doi-asserted-by":"publisher","DOI":"10.1074\/jbc.274.15.10219"},{"key":"B159","doi-asserted-by":"publisher","DOI":"10.1089\/hum.2009.056"},{"key":"B160","doi-asserted-by":"publisher","DOI":"10.1089\/hum.1993.4.6-771"},{"key":"B161","doi-asserted-by":"publisher","DOI":"10.1089\/hum.1993.4.6-759"},{"key":"B162","doi-asserted-by":"publisher","DOI":"10.1023\/A:1005369926784"},{"key":"B163","doi-asserted-by":"publisher","DOI":"10.1126\/science.286.5448.2244"},{"key":"B164","doi-asserted-by":"publisher","DOI":"10.1002\/1873-3468.13696"},{"key":"B165","doi-asserted-by":"publisher","DOI":"10.1038\/s41598-020-61730-8"},{"key":"B167","doi-asserted-by":"publisher","DOI":"10.1038\/mt.2013.142"},{"key":"B168","doi-asserted-by":"publisher","DOI":"10.1128\/JVI.00265-20"},{"key":"B169","doi-asserted-by":"publisher","DOI":"10.2174\/156652321305131212125338"},{"key":"B170","doi-asserted-by":"publisher","DOI":"10.1089\/hum.2017.201"},{"key":"B171","doi-asserted-by":"publisher","DOI":"10.1016\/j.omtm.2020.01.014"},{"key":"B172","doi-asserted-by":"publisher","DOI":"10.1016\/j.omtn.2018.10.015"},{"key":"B174","doi-asserted-by":"publisher","DOI":"10.3389\/fbioe.2019.00406"},{"key":"B175","doi-asserted-by":"publisher","DOI":"10.1056\/NEJMra1300109"},{"key":"B176","doi-asserted-by":"publisher","DOI":"10.1093\/hmg\/ddz139"},{"key":"B177","doi-asserted-by":"publisher","DOI":"10.1016\/j.jcf.2018.05.004"},{"key":"B178","doi-asserted-by":"publisher","DOI":"10.1016\/S2213-2600(14)70132-8"},{"key":"B179","doi-asserted-by":"publisher","DOI":"10.1056\/NEJMoa1409547"},{"key":"B180","doi-asserted-by":"publisher","DOI":"10.3389\/fphar.2019.01662"},{"key":"B181","doi-asserted-by":"publisher","DOI":"10.1016\/j.cell.2019.12.032"},{"key":"B182","doi-asserted-by":"publisher","DOI":"10.1038\/ng0992-21"},{"key":"B183","doi-asserted-by":"publisher","DOI":"10.1038\/ng0295-126"},{"key":"B184","doi-asserted-by":"publisher","DOI":"10.1152\/ajplung.00049.2005"},{"key":"B185","doi-asserted-by":"publisher","DOI":"10.1371\/journal.pbio.1000155"},{"key":"B186","doi-asserted-by":"publisher","DOI":"10.1165\/rcmb.2008-0018OC"},{"key":"B187","doi-asserted-by":"publisher","DOI":"10.1073\/pnas.1604905113"},{"key":"B188","doi-asserted-by":"publisher","DOI":"10.1172\/JCI8390"},{"key":"B189","doi-asserted-by":"publisher","DOI":"10.1172\/jci.insight.88730"},{"key":"B190","doi-asserted-by":"publisher","DOI":"10.1089\/10430340260355365"},{"key":"B191","doi-asserted-by":"publisher","DOI":"10.1136\/thoraxjnl-2016-208406"},{"key":"B192","doi-asserted-by":"publisher","DOI":"10.1128\/JVI.70.5.3235-3241.1996"},{"key":"B193","doi-asserted-by":"publisher","DOI":"10.1128\/JVI.71.8.5932-5941.1997"},{"key":"B194","doi-asserted-by":"publisher","DOI":"10.1089\/hum.2005.16.921"},{"key":"B195","doi-asserted-by":"publisher","DOI":"10.1089\/104303402760128577"},{"key":"B196","doi-asserted-by":"publisher","DOI":"10.1016\/S2213-2600(15)00245-3"},{"key":"B197","doi-asserted-by":"publisher","DOI":"10.1073\/pnas.93.24.13565"},{"key":"B198","doi-asserted-by":"publisher","DOI":"10.1038\/gt.2008.14"},{"key":"B199","doi-asserted-by":"publisher","DOI":"10.1093\/nar\/gky773"},{"key":"B200","doi-asserted-by":"publisher","DOI":"10.1089\/hum.2019.074"},{"key":"B201","doi-asserted-by":"publisher","DOI":"10.1038\/nbt.3241"},{"key":"B202","doi-asserted-by":"publisher","DOI":"10.1038\/nature13864"},{"key":"B203","doi-asserted-by":"publisher","DOI":"10.15252\/emmm.201707601"},{"key":"B204","doi-asserted-by":"publisher","DOI":"10.1172\/jci.insight.128863"},{"key":"B205","doi-asserted-by":"publisher","DOI":"10.1080\/10717544.2018.1474964"},{"key":"B206","doi-asserted-by":"publisher","DOI":"10.1038\/srep32301"},{"key":"B207","doi-asserted-by":"publisher","DOI":"10.3390\/ph5111177"},{"key":"B208","doi-asserted-by":"publisher","DOI":"10.1016\/j.bbamem.2006.02.021"},{"key":"B209","doi-asserted-by":"publisher","DOI":"10.1039\/C7SC03918B"},{"key":"B210","doi-asserted-by":"publisher","DOI":"10.1371\/journal.pone.0161072"},{"key":"B212","doi-asserted-by":"publisher","DOI":"10.1016\/j.celrep.2015.07.062"},{"key":"B213","doi-asserted-by":"publisher","DOI":"10.1016\/j.stem.2013.11.002"},{"key":"B214","doi-asserted-by":"publisher","DOI":"10.1016\/j.omtn.2019.02.006"},{"key":"B215","doi-asserted-by":"publisher","DOI":"10.1016\/j.cell.2014.09.014"},{"key":"B216","doi-asserted-by":"publisher","DOI":"10.1016\/S0140-6736(16)00576-6"},{"key":"B217","doi-asserted-by":"publisher","DOI":"10.1371\/journal.pone.0184009"},{"key":"B218","first-page":"623","volume":"56","author":"Chillon M","year":"1995","journal-title":"Am J Hum Genet"},{"key":"B219","doi-asserted-by":"publisher","DOI":"10.1002\/(SICI)1098-1004(1999)14:2<133::AID-HUMU5>3.0.CO;2-T"},{"key":"B220","doi-asserted-by":"publisher","DOI":"10.1056\/NEJM199410133311503"},{"key":"B221","doi-asserted-by":"publisher","DOI":"10.1038\/srep32230"},{"key":"B223","first-page":"23","author":"Ricciardi AS","year":"2018","journal-title":"Molecules"},{"key":"B224","doi-asserted-by":"publisher","DOI":"10.1016\/j.chembiol.2011.07.010"},{"key":"B225","doi-asserted-by":"publisher","DOI":"10.1038\/gt.2012.82"},{"key":"B226","doi-asserted-by":"publisher","DOI":"10.1038\/mtna.2013.59"},{"key":"B227","doi-asserted-by":"publisher","DOI":"10.1038\/ncomms13304"},{"key":"B228","doi-asserted-by":"publisher","DOI":"10.1038\/ncomms7952"},{"key":"B229","doi-asserted-by":"publisher","DOI":"10.1016\/j.ymthe.2019.07.002"},{"key":"B230","doi-asserted-by":"publisher","DOI":"10.1038\/mt.2016.112"},{"key":"B231","doi-asserted-by":"publisher","DOI":"10.1073\/pnas.1306243110"},{"key":"B232","doi-asserted-by":"publisher","DOI":"10.1016\/j.ymgme.2009.01.015"},{"key":"B233","doi-asserted-by":"publisher","DOI":"10.1513\/AnnalsATS.201411-507FR"},{"key":"B234","doi-asserted-by":"publisher","DOI":"10.1165\/ajrcmb.11.3.8086169"},{"key":"B235","doi-asserted-by":"publisher","DOI":"10.1177\/1535370217713000"},{"key":"B237","doi-asserted-by":"publisher","DOI":"10.1038\/s41598-019-49696-8"},{"key":"B238","doi-asserted-by":"publisher","DOI":"10.1126\/scitranslmed.aav8375"},{"key":"B239","doi-asserted-by":"publisher","DOI":"10.1073\/pnas.101500298"},{"key":"B240","doi-asserted-by":"publisher","DOI":"10.1089\/hum.2018.29070.trf"},{"key":"B241","doi-asserted-by":"publisher","DOI":"10.1186\/1750-1172-3-16"},{"key":"B242","doi-asserted-by":"publisher","DOI":"10.1172\/JCI110360"},{"key":"B243","first-page":"244","volume":"5","author":"Stiles KM","year":"2018","journal-title":"Chronic Obstr Pulm Dis"},{"key":"B244","doi-asserted-by":"publisher","DOI":"10.1016\/j.ymthe.2004.08.022"},{"key":"B245","doi-asserted-by":"publisher","DOI":"10.1089\/humc.2014.2513"},{"key":"B246","doi-asserted-by":"publisher","DOI":"10.1089\/hum.2017.227"},{"key":"B247","doi-asserted-by":"publisher","DOI":"10.1089\/hum.2017.225"},{"key":"B248","doi-asserted-by":"publisher","DOI":"10.1038\/s41434-018-0003-1"},{"key":"B249","doi-asserted-by":"publisher","DOI":"10.1016\/j.ebiom.2018.02.015"}],"container-title":["Human Gene Therapy"],"original-title":[],"language":"en","link":[{"URL":"https:\/\/www.liebertpub.com\/doi\/full-xml\/10.1089\/hum.2020.166","content-type":"application\/xml","content-version":"vor","intended-application":"text-mining"},{"URL":"https:\/\/www.liebertpub.com\/doi\/pdf\/10.1089\/hum.2020.166","content-type":"unspecified","content-version":"vor","intended-application":"similarity-checking"}],"deposited":{"date-parts":[[2026,4,29]],"date-time":"2026-04-29T07:55:18Z","timestamp":1777449318000},"score":1,"resource":{"primary":{"URL":"https:\/\/journals.sagepub.com\/doi\/full\/10.1089\/hum.2020.166"}},"subtitle":[],"short-title":[],"issued":{"date-parts":[[2020,9,1]]},"references-count":242,"journal-issue":{"issue":"17-18","published-print":{"date-parts":[[2020,9,1]]}},"alternative-id":["10.1089\/hum.2020.166"],"URL":"https:\/\/doi.org\/10.1089\/hum.2020.166","relation":{},"ISSN":["1043-0342","1557-7422"],"issn-type":[{"value":"1043-0342","type":"print"},{"value":"1557-7422","type":"electronic"}],"subject":[],"published":{"date-parts":[[2020,9,1]]}}}