{"status":"ok","message-type":"work","message-version":"1.0.0","message":{"indexed":{"date-parts":[[2026,3,12]],"date-time":"2026-03-12T06:36:14Z","timestamp":1773297374823,"version":"3.50.1"},"reference-count":55,"publisher":"SAGE Publications","issue":"3","license":[{"start":{"date-parts":[[2014,9,1]],"date-time":"2014-09-01T00:00:00Z","timestamp":1409529600000},"content-version":"tdm","delay-in-days":0,"URL":"http:\/\/www.liebertpub.com\/nv\/resources-tools\/text-and-data-mining-policy\/121\/"}],"content-domain":{"domain":[],"crossmark-restriction":false},"short-container-title":["Human Gene Therapy Clinical Development"],"published-print":{"date-parts":[[2014,9]]},"DOI":"10.1089\/humc.2013.239","type":"journal-article","created":{"date-parts":[[2014,8,21]],"date-time":"2014-08-21T14:38:39Z","timestamp":1408631919000},"page":"164-177","source":"Crossref","is-referenced-by-count":53,"title":["Comparative Efficacy and Safety of Multiple Routes of Direct CNS Administration of Adeno-Associated Virus Gene Transfer Vector Serotype rh.10 Expressing the Human Arylsulfatase A cDNA to Nonhuman Primates"],"prefix":"10.1177","volume":"25","author":[{"given":"Jonathan B.","family":"Rosenberg","sequence":"first","affiliation":[{"name":"Department of Genetic Medicine, Weill Medical College of Cornell University, New York, NY 10065."}],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"Dolan","family":"Sondhi","sequence":"additional","affiliation":[{"name":"Department of Genetic Medicine, Weill Medical College of Cornell University, New York, NY 10065."}],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"David G.","family":"Rubin","sequence":"additional","affiliation":[{"name":"Department of Genetic Medicine, Weill Medical College of Cornell University, New York, NY 10065."}],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"S\u00e9bastien","family":"Monette","sequence":"additional","affiliation":[{"name":"Tri-Institutional Laboratory of Comparative Pathology, Weill Cornell Medical College, Memorial Sloan-Kettering Cancer Center, and Rockefeller University, New York, NY 10065."}],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"Alvin","family":"Chen","sequence":"additional","affiliation":[{"name":"Department of Genetic Medicine, Weill Medical College of Cornell University, New York, NY 10065."}],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"Sara","family":"Cram","sequence":"additional","affiliation":[{"name":"Department of Genetic Medicine, Weill Medical College of Cornell University, New York, NY 10065."}],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"Bishnu P.","family":"De","sequence":"additional","affiliation":[{"name":"Department of Genetic Medicine, Weill Medical College of Cornell University, New York, NY 10065."}],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"Stephen M.","family":"Kaminsky","sequence":"additional","affiliation":[{"name":"Department of Genetic Medicine, Weill Medical College of Cornell University, New York, NY 10065."}],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"Caroline","family":"Sevin","sequence":"additional","affiliation":[{"name":"INSERM U986, University Paris-Descartes, 75005 Paris, France."},{"name":"Neuropediatrics Unit, Bic\u00eatre Hospital, Le Kremlin Bic\u00eatre, 94275 Paris, France."}],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"Patrick","family":"Aubourg","sequence":"additional","affiliation":[{"name":"INSERM U986, University Paris-Descartes, 75005 Paris, France."},{"name":"Neuropediatrics Unit, Bic\u00eatre Hospital, Le Kremlin Bic\u00eatre, 94275 Paris, France."}],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"Ronald G.","family":"Crystal","sequence":"additional","affiliation":[{"name":"Department of Genetic Medicine, Weill Medical College of Cornell University, New York, NY 10065."}],"role":[{"role":"author","vocabulary":"crossref"}]}],"member":"179","reference":[{"key":"B1","doi-asserted-by":"publisher","DOI":"10.1073\/pnas.0306431101"},{"key":"B2","doi-asserted-by":"publisher","DOI":"10.1007\/978-1-60761-898-0_26"},{"key":"B3","doi-asserted-by":"publisher","DOI":"10.1007\/978-1-4614-9105-7_18"},{"key":"B4","doi-asserted-by":"publisher","DOI":"10.1016\/j.ymgme.2011.10.002"},{"key":"B5","doi-asserted-by":"publisher","DOI":"10.1016\/S0140-6736(85)90402-7"},{"key":"B6","doi-asserted-by":"publisher","DOI":"10.1007\/s00439-006-0280-4"},{"key":"B7","doi-asserted-by":"publisher","DOI":"10.1172\/JCI200419205"},{"key":"B8","doi-asserted-by":"publisher","DOI":"10.1172\/JCI28873"},{"key":"B9","doi-asserted-by":"publisher","DOI":"10.1126\/science.1233158"},{"key":"B10","doi-asserted-by":"publisher","DOI":"10.1038\/sj.bmt.1705581"},{"key":"B11","doi-asserted-by":"publisher","DOI":"10.1016\/j.brainresrev.2006.11.002"},{"key":"B12","doi-asserted-by":"publisher","DOI":"10.1093\/hmg\/ddp475"},{"key":"B13","doi-asserted-by":"publisher","DOI":"10.1016\/j.ymthe.2005.09.003"},{"key":"B14","doi-asserted-by":"publisher","DOI":"10.1210\/jc.75.2.424"},{"key":"B15","doi-asserted-by":"publisher","DOI":"10.1038\/nrm1050"},{"key":"B16","doi-asserted-by":"publisher","DOI":"10.1055\/s-0030-1253412"},{"key":"B17","doi-asserted-by":"publisher","DOI":"10.1111\/j.1651-2227.2003.tb00225.x"},{"key":"B18","volume-title":"Lippincott's Pocket Neuroanatomy","author":"Gould D.J.","year":"2013"},{"key":"B19","doi-asserted-by":"publisher","DOI":"10.1016\/j.neuropharm.2012.06.024"},{"key":"B20","doi-asserted-by":"publisher","DOI":"10.1089\/hum.2005.16.1484"},{"key":"B21","doi-asserted-by":"publisher","DOI":"10.1182\/blood-2012-05-423210"},{"key":"B22","doi-asserted-by":"publisher","DOI":"10.1089\/104303402760128612"},{"key":"B23","doi-asserted-by":"publisher","DOI":"10.1016\/S0140-6736(07)60982-9"},{"key":"B24","doi-asserted-by":"publisher","DOI":"10.1016\/j.nbd.2011.10.004"},{"key":"B25","doi-asserted-by":"crossref","first-page":"986","DOI":"10.1182\/blood.V90.3.986","volume":"90","author":"Kennedy D.W.","year":"1997","journal-title":"Blood"},{"key":"B26","doi-asserted-by":"publisher","DOI":"10.3171\/jns.2005.103.5.0923"},{"key":"B27","doi-asserted-by":"publisher","DOI":"10.1177\/096368979500400409"},{"key":"B28","doi-asserted-by":"publisher","DOI":"10.1097\/00062752-199911000-00004"},{"key":"B29","doi-asserted-by":"publisher","DOI":"10.1111\/j.1600-0684.2010.00422.x"},{"key":"B30","doi-asserted-by":"publisher","DOI":"10.1038\/mt.2013.95"},{"key":"B31","first-page":"240","volume":"12","author":"Mandel R.J.","year":"2010","journal-title":"Curr. Opin. Mol. Ther."},{"key":"B32","doi-asserted-by":"publisher","DOI":"10.1093\/hmg\/dds086"},{"key":"B33","doi-asserted-by":"publisher","DOI":"10.1038\/sj.gt.3301232"},{"key":"B34","doi-asserted-by":"publisher","DOI":"10.1093\/hmg\/ddi126"},{"key":"B35","doi-asserted-by":"publisher","DOI":"10.1002\/jgm.885"},{"key":"B36","doi-asserted-by":"publisher","DOI":"10.1182\/blood-2013-01-306647"},{"key":"B37","doi-asserted-by":"publisher","DOI":"10.3727\/096368912X656117"},{"key":"B38","doi-asserted-by":"publisher","DOI":"10.1023\/B:NEUR.0000046572.53905.2c"},{"key":"B39","first-page":"729","volume":"7","author":"Patil S.A.","year":"2013","journal-title":"Drug Des. Devel. Ther."},{"key":"B40","doi-asserted-by":"publisher","DOI":"10.1089\/hum.2012.015"},{"key":"B41","doi-asserted-by":"publisher","DOI":"10.1212\/01.wnl.0000234129.97727.4d"},{"key":"B42","doi-asserted-by":"publisher","DOI":"10.1038\/mt.2013.266"},{"key":"B43","doi-asserted-by":"publisher","DOI":"10.1089\/hum.2011.162"},{"key":"B44","doi-asserted-by":"publisher","DOI":"10.1093\/hmg\/ddi425"},{"key":"B45","doi-asserted-by":"publisher","DOI":"10.1038\/sj.gt.3302883"},{"key":"B46","doi-asserted-by":"publisher","DOI":"10.1038\/sj.mt.6300049"},{"key":"B47","doi-asserted-by":"publisher","DOI":"10.1016\/j.expneurol.2008.04.022"},{"key":"B48","doi-asserted-by":"publisher","DOI":"10.3171\/2010.4.PEDS09507"},{"key":"B49","doi-asserted-by":"publisher","DOI":"10.1194\/jlr.R026682"},{"key":"B50","first-page":"441","volume":"146","author":"Tuszynski M.H.","year":"2004","journal-title":"Prog. Brain Res."},{"key":"B51","first-page":"3695","volume-title":"The Metabolic and Molecular Bases of Inherited Disease","author":"von Figura K.","year":"2001"},{"key":"B52","doi-asserted-by":"publisher","DOI":"10.1073\/pnas.78.11.6967"},{"key":"B53","doi-asserted-by":"publisher","DOI":"10.1007\/s00401-004-0883-6"},{"key":"B54","doi-asserted-by":"publisher","DOI":"10.1089\/hum.2008.022"},{"key":"B55","doi-asserted-by":"publisher","DOI":"10.1038\/gt.2008.54"}],"container-title":["Human Gene Therapy Clinical Development"],"original-title":[],"language":"en","link":[{"URL":"http:\/\/www.liebertpub.com\/doi\/full-xml\/10.1089\/humc.2013.239","content-type":"application\/xml","content-version":"vor","intended-application":"text-mining"},{"URL":"http:\/\/www.liebertpub.com\/doi\/pdf\/10.1089\/humc.2013.239","content-type":"unspecified","content-version":"vor","intended-application":"similarity-checking"}],"deposited":{"date-parts":[[2026,3,2]],"date-time":"2026-03-02T03:59:05Z","timestamp":1772423945000},"score":1,"resource":{"primary":{"URL":"https:\/\/journals.sagepub.com\/doi\/full\/10.1089\/humc.2013.239"}},"subtitle":[],"short-title":[],"issued":{"date-parts":[[2014,9]]},"references-count":55,"journal-issue":{"issue":"3","published-print":{"date-parts":[[2014,9]]}},"alternative-id":["10.1089\/humc.2013.239"],"URL":"https:\/\/doi.org\/10.1089\/humc.2013.239","relation":{},"ISSN":["2324-8637","2324-8645"],"issn-type":[{"value":"2324-8637","type":"print"},{"value":"2324-8645","type":"electronic"}],"subject":[],"published":{"date-parts":[[2014,9]]}}}