{"status":"ok","message-type":"work","message-version":"1.0.0","message":{"indexed":{"date-parts":[[2026,9,28]],"date-time":"2026-09-28T21:08:14Z","timestamp":1790629694997,"version":"4.1.0"},"reference-count":51,"publisher":"Oxford University Press (OUP)","issue":"8","content-domain":{"domain":[],"crossmark-restriction":false},"short-container-title":["Human Molecular Genetics"],"published-print":{"date-parts":[[2015,4,15]]},"DOI":"10.1093\/hmg\/ddu746","type":"journal-article","created":{"date-parts":[[2015,1,5]],"date-time":"2015-01-05T22:21:40Z","timestamp":1420496500000},"page":"2287-2296","source":"Crossref","is-referenced-by-count":25,"title":["Hepatic lentiviral gene transfer prevents the long-term onset of hepatic tumours of glycogen storage disease type 1a in mice"],"prefix":"10.1093","volume":"24","author":[{"given":"J.","family":"Clar","sequence":"first","affiliation":[],"role":[{"vocabulary":"crossref","role":"author"}]},{"given":"E.","family":"Mutel","sequence":"additional","affiliation":[],"role":[{"vocabulary":"crossref","role":"author"}]},{"given":"B.","family":"Gri","sequence":"additional","affiliation":[],"role":[{"vocabulary":"crossref","role":"author"}]},{"given":"A.","family":"Creneguy","sequence":"additional","affiliation":[],"role":[{"vocabulary":"crossref","role":"author"}]},{"given":"A.","family":"Stefanutti","sequence":"additional","affiliation":[],"role":[{"vocabulary":"crossref","role":"author"}]},{"given":"S.","family":"Gaillard","sequence":"additional","affiliation":[],"role":[{"vocabulary":"crossref","role":"author"}]},{"given":"N.","family":"Ferry","sequence":"additional","affiliation":[],"role":[{"vocabulary":"crossref","role":"author"}]},{"given":"O.","family":"Beuf","sequence":"additional","affiliation":[],"role":[{"vocabulary":"crossref","role":"author"}]},{"given":"G.","family":"Mithieux","sequence":"additional","affiliation":[],"role":[{"vocabulary":"crossref","role":"author"}]},{"given":"T. H.","family":"Nguyen","sequence":"additional","affiliation":[],"role":[{"vocabulary":"crossref","role":"author"}]},{"given":"F.","family":"Rajas","sequence":"additional","affiliation":[],"role":[{"vocabulary":"crossref","role":"author"}]}],"member":"286","published-online":{"date-parts":[[2015,1,5]]},"reference":[{"issue":"29","key":"1_14469998","doi-asserted-by":"crossref","first-page":"21482","DOI":"10.1016\/S0021-9258(20)80563-8","volume":"268","author":"Shelly","year":"1993","journal-title":"Journal of Biological Chemistry","ISSN":"https:\/\/id.crossref.org\/issn\/0021-9258","issn-type":"print"},{"issue":"2","key":"2_17003043","doi-asserted-by":"publisher","first-page":"121","DOI":"10.2174\/1566524024605798","volume":"2","author":"Chou","year":"2002","journal-title":"Current molecular medicine","ISSN":"https:\/\/id.crossref.org\/issn\/1566-5240","issn-type":"print"},{"key":"3_39991698","doi-asserted-by":"publisher","first-page":"27","DOI":"10.1186\/1750-1172-6-27","volume":"6","author":"Froissart","year":"2011","ISSN":"https:\/\/id.crossref.org\/issn\/1750-1172","issn-type":"print"},{"issue":"Pt 2","key":"4_6529565","doi-asserted-by":"publisher","first-page":"141","DOI":"10.1046\/j.1469-1809.1999.6320141.x","volume":"63","author":"Bruni","year":"1999","journal-title":"Annals of human genetics","ISSN":"https:\/\/id.crossref.org\/issn\/0003-4800","issn-type":"print"},{"issue":"5133","key":"5_14481251","doi-asserted-by":"publisher","first-page":"580","DOI":"10.1126\/science.8211187","volume":"262","author":"Lei","year":"1993","journal-title":"Science","ISSN":"https:\/\/id.crossref.org\/issn\/0036-8075","issn-type":"print"},{"issue":"43","key":"6_19570912","doi-asserted-by":"publisher","first-page":"44231","DOI":"10.1074\/jbc.R400011200","volume":"279","year":"2004","journal-title":"Journal of Biological Chemistry","ISSN":"https:\/\/id.crossref.org\/issn\/0021-9258","issn-type":"print"},{"issue":"3","key":"7_19633623","doi-asserted-by":"publisher","first-page":"E370","DOI":"10.1152\/ajpendo.00299.2003","volume":"286","year":"2004","journal-title":"American Journal of Physiology - Endocrinology And Metabolism","ISSN":"https:\/\/id.crossref.org\/issn\/0193-1849","issn-type":"print"},{"issue":"1","key":"8_10870304","doi-asserted-by":"publisher","first-page":"132","DOI":"10.1016\/S0016-5085(99)70559-7","volume":"117","author":"JAS","year":"1999","journal-title":"Gastroenterology","ISSN":"https:\/\/id.crossref.org\/issn\/0016-5085","issn-type":"print"},{"key":"9_30509143","doi-asserted-by":"crossref","first-page":"S20","DOI":"10.1007\/BF02679990","volume":"161","year":"2002","journal-title":"European journal of pediatrics","ISSN":"https:\/\/id.crossref.org\/issn\/0340-6199","issn-type":"print"},{"key":"10_49552101","doi-asserted-by":"crossref","first-page":"350","DOI":"10.1016\/j.jhep.2012.09.030","volume":"58","year":"2013","journal-title":"Journal of hepatology","ISSN":"https:\/\/id.crossref.org\/issn\/0168-8278","issn-type":"print"},{"issue":"2","key":"11_18844412","doi-asserted-by":"publisher","first-page":"153","DOI":"10.1007\/s10545-005-7500-2","volume":"28","author":"Franco","year":"2005","journal-title":"Journal of inherited metabolic disease","ISSN":"https:\/\/id.crossref.org\/issn\/0141-8955","issn-type":"print"},{"key":"12_30509144","doi-asserted-by":"crossref","first-page":"S112","DOI":"10.1007\/x00431-001-0876-6","volume":"161","year":"2002","journal-title":"European journal of pediatrics","ISSN":"https:\/\/id.crossref.org\/issn\/0340-6199","issn-type":"print"},{"key":"13_48382532","doi-asserted-by":"crossref","first-page":"595","DOI":"10.1016\/j.jhep.2013.04.004","volume":"59","year":"2013","journal-title":"Journal of hepatology","ISSN":"https:\/\/id.crossref.org\/issn\/0168-8278","issn-type":"print"},{"key":"14_34335801","doi-asserted-by":"crossref","first-page":"S76","DOI":"10.1038\/sj.gt.3302373","volume":"11","year":"2004","journal-title":"Gene therapy","ISSN":"https:\/\/id.crossref.org\/issn\/0969-7128","issn-type":"print"},{"issue":"2","key":"15_16231488","doi-asserted-by":"publisher","first-page":"203","DOI":"10.1038\/ng0696-203","volume":"13","author":"Lei","year":"1996","journal-title":"Nature genetics","ISSN":"https:\/\/id.crossref.org\/issn\/1061-4036","issn-type":"print"},{"issue":"1","key":"16_36415675","doi-asserted-by":"publisher","first-page":"83","DOI":"10.1354\/vp.38-1-83","volume":"38","author":"Kishnani","year":"2001","journal-title":"Veterinary Pathology","ISSN":"https:\/\/id.crossref.org\/issn\/0300-9858","issn-type":"print"},{"issue":"4","key":"17_41970771","doi-asserted-by":"publisher","first-page":"671","DOI":"10.1007\/s10545-012-9454-5","volume":"35","author":"Koeberl","year":"2012","journal-title":"Journal of inherited metabolic disease","ISSN":"https:\/\/id.crossref.org\/issn\/0141-8955","issn-type":"print"},{"issue":"8","key":"18_39764775","doi-asserted-by":"publisher","first-page":"1011","DOI":"10.1517\/14712598.2011.578067","volume":"11","author":"Chou","year":"2011","journal-title":"Expert opinion on biological therapy","ISSN":"https:\/\/id.crossref.org\/issn\/1471-2598","issn-type":"print"},{"issue":"5","key":"19_42169466","doi-asserted-by":"publisher","first-page":"1719","DOI":"10.1002\/hep.25717","volume":"56","author":"Lee","year":"2012","journal-title":"Hepatology (Baltimore, Md.)","ISSN":"https:\/\/id.crossref.org\/issn\/0270-9139","issn-type":"print"},{"issue":"4","key":"20_41798468","doi-asserted-by":"publisher","first-page":"407","DOI":"10.1089\/hum.2011.106","volume":"23","author":"Demaster","year":"2012","journal-title":"Human gene therapy","ISSN":"https:\/\/id.crossref.org\/issn\/1043-0342","issn-type":"print"},{"issue":"4","key":"21_21594485","doi-asserted-by":"publisher","first-page":"321","DOI":"10.1038\/sj.gt.3302650","volume":"13","author":"Ghosh","year":"2006","journal-title":"Gene therapy","ISSN":"https:\/\/id.crossref.org\/issn\/0969-7128","issn-type":"print"},{"issue":"3","key":"22_10388771","doi-asserted-by":"publisher","first-page":"186","DOI":"10.1002\/(SICI)1521-2254(200005\/06)2:3<186::AID-JGM100>3.0.CO;2-6","volume":"2","author":"Zahler","year":"2000","journal-title":"The journal of gene medicine","ISSN":"https:\/\/id.crossref.org\/issn\/1099-498X","issn-type":"print"},{"key":"23_49552102","doi-asserted-by":"crossref","first-page":"397","DOI":"10.1002\/hep.26204","volume":"58","year":"2013","journal-title":"Hepatology (Baltimore, Md.)","ISSN":"https:\/\/id.crossref.org\/issn\/0270-9139","issn-type":"print"},{"issue":"24","key":"24_40390002","doi-asserted-by":"publisher","first-page":"2516","DOI":"10.2174\/138161211797247587","volume":"17","author":"Ferry","year":"2011","journal-title":"Current pharmaceutical design","ISSN":"https:\/\/id.crossref.org\/issn\/1381-6128","issn-type":"print"},{"issue":"4","key":"25_19473308","doi-asserted-by":"publisher","first-page":"763","DOI":"10.1016\/j.ymthe.2005.07.358","volume":"12","author":"Themis","year":"2005","journal-title":"Molecular therapy : the journal of the American Society of Gene Therapy","ISSN":"https:\/\/id.crossref.org\/issn\/1525-0016","issn-type":"print"},{"key":"26_46677644","doi-asserted-by":"crossref","first-page":"132","DOI":"10.1089\/hum.2012.229","volume":"24","year":"2013","journal-title":"Human gene therapy","ISSN":"https:\/\/id.crossref.org\/issn\/1043-0342","issn-type":"print"},{"key":"27_49552103","doi-asserted-by":"crossref","first-page":"999","DOI":"10.1053\/j.gastro.2010.05.008","volume":"139","year":"2010","journal-title":"Gastroenterology","ISSN":"https:\/\/id.crossref.org\/issn\/0016-5085","issn-type":"print"},{"issue":"5","key":"28_19508584","doi-asserted-by":"publisher","first-page":"852","DOI":"10.1016\/j.ymthe.2005.06.482","volume":"12","author":"Nguyen","year":"2005","journal-title":"Molecular therapy : the journal of the American Society of Gene Therapy","ISSN":"https:\/\/id.crossref.org\/issn\/1525-0016","issn-type":"print"},{"issue":"8","key":"29_22341478","doi-asserted-by":"publisher","first-page":"974","DOI":"10.1080\/00365520600554790","volume":"41","author":"Merle","year":"2006","journal-title":"Scandinavian journal of gastroenterology","ISSN":"https:\/\/id.crossref.org\/issn\/0036-5521","issn-type":"print"},{"issue":"13","key":"30_29293354","doi-asserted-by":"publisher","first-page":"4144","DOI":"10.1182\/blood-2007-03-078493","volume":"110","year":"2007","journal-title":"Blood","ISSN":"https:\/\/id.crossref.org\/issn\/0006-4971","issn-type":"print"},{"issue":"4","key":"31_39153099","doi-asserted-by":"publisher","first-page":"723","DOI":"10.1038\/mt.2010.290","volume":"19","author":"Matsui","year":"2011","journal-title":"Molecular therapy : the journal of the American Society of Gene Therapy","ISSN":"https:\/\/id.crossref.org\/issn\/1525-0016","issn-type":"print"},{"key":"32_45985283","doi-asserted-by":"crossref","first-page":"529","DOI":"10.1016\/j.jhep.2010.08.014","volume":"54","year":"2011","journal-title":"Journal of hepatology","ISSN":"https:\/\/id.crossref.org\/issn\/0168-8278","issn-type":"print"},{"issue":"11","key":"33_31163268","doi-asserted-by":"publisher","first-page":"831","DOI":"10.1038\/gt.2008.64","volume":"15","author":"Alexander","year":"2008","journal-title":"Gene therapy","ISSN":"https:\/\/id.crossref.org\/issn\/0969-7128","issn-type":"print"},{"issue":"6","key":"34_22232239","doi-asserted-by":"publisher","first-page":"1085","DOI":"10.1016\/j.ymthe.2006.01.014","volume":"13","author":"Seppen","year":"2006","journal-title":"Molecular therapy : the journal of the American Society of Gene Therapy","ISSN":"https:\/\/id.crossref.org\/issn\/1525-0016","issn-type":"print"},{"issue":"6","key":"35_36493368","doi-asserted-by":"publisher","first-page":"704","DOI":"10.1089\/hum.2009.182","volume":"21","author":"Boutin","year":"2010","journal-title":"Human gene therapy","ISSN":"https:\/\/id.crossref.org\/issn\/1043-0342","issn-type":"print"},{"issue":"3","key":"36_11311134","doi-asserted-by":"publisher","first-page":"164","DOI":"10.1006\/mthe.2001.0450","volume":"4","author":"Park","year":"2001","journal-title":"Molecular therapy : the journal of the American Society of Gene Therapy","ISSN":"https:\/\/id.crossref.org\/issn\/1525-0016","issn-type":"print"},{"issue":"9","key":"37_37613528","doi-asserted-by":"publisher","first-page":"1592","DOI":"10.1038\/mt.2010.119","volume":"18","author":"Grinshpun","year":"2010","journal-title":"Molecular therapy : the journal of the American Society of Gene Therapy","ISSN":"https:\/\/id.crossref.org\/issn\/1525-0016","issn-type":"print"},{"key":"38_49552104","doi-asserted-by":"crossref","first-page":"1691","DOI":"10.2174\/1389557511313120001","volume":"13","year":"2013","journal-title":"Mini reviews in medicinal chemistry","ISSN":"https:\/\/id.crossref.org\/issn\/1389-5575","issn-type":"print"},{"key":"39_49552105","doi-asserted-by":"crossref","first-page":"230","DOI":"10.1016\/j.canlet.2013.07.033","volume":"345","year":"2014","journal-title":"Cancer letters","ISSN":"https:\/\/id.crossref.org\/issn\/0304-3835","issn-type":"print"},{"issue":"6","key":"40_37105710","doi-asserted-by":"publisher","first-page":"741","DOI":"10.2174\/138161210790883787","volume":"16","author":"Petta","year":"2010","journal-title":"Current pharmaceutical design","ISSN":"https:\/\/id.crossref.org\/issn\/1381-6128","issn-type":"print"},{"issue":"20","key":"41_47580733","doi-asserted-by":"publisher","first-page":"3195","DOI":"10.1182\/blood-2013-10-534032","volume":"123","year":"2014","journal-title":"Blood","ISSN":"https:\/\/id.crossref.org\/issn\/0006-4971","issn-type":"print"},{"key":"42_49552106","doi-asserted-by":"crossref","first-page":"1605","DOI":"10.1038\/mt.2014.114","volume":"22","year":"2014","journal-title":"Molecular therapy : the journal of the American Society of Gene Therapy","ISSN":"https:\/\/id.crossref.org\/issn\/1525-0016","issn-type":"print"},{"issue":"5","key":"43_22090915","doi-asserted-by":"publisher","first-page":"585","DOI":"10.1038\/nm1398","volume":"12","author":"Brown","year":"2006","journal-title":"Nature medicine","ISSN":"https:\/\/id.crossref.org\/issn\/1078-8956","issn-type":"print"},{"issue":"5","key":"44_21332927","doi-asserted-by":"publisher","first-page":"1727","DOI":"10.1182\/blood-2001-12-0249","volume":"101","year":"2003","journal-title":"Blood","ISSN":"https:\/\/id.crossref.org\/issn\/0006-4971","issn-type":"print"},{"issue":"2","key":"45_10338545","doi-asserted-by":"publisher","first-page":"217","DOI":"10.1038\/76095","volume":"25","author":"Follenzi","year":"2000","journal-title":"Nature genetics","ISSN":"https:\/\/id.crossref.org\/issn\/1061-4036","issn-type":"print"},{"issue":"2","key":"46_6569903","doi-asserted-by":"publisher","first-page":"173","DOI":"10.1016\/S0092-8674(00)80828-4","volume":"101","author":"Zennou","year":"2000","journal-title":"Cell","ISSN":"https:\/\/id.crossref.org\/issn\/0092-8674","issn-type":"print"},{"issue":"4","key":"47_10748414","doi-asserted-by":"crossref","first-page":"2886","DOI":"10.1128\/JVI.73.4.2886-2892.1999","volume":"73","author":"Zufferey","year":"1999","journal-title":"Journal of Virology","ISSN":"https:\/\/id.crossref.org\/issn\/0022-538X","issn-type":"print"},{"key":"48_50024597","first-page":"59","volume":"2","year":"1974","journal-title":"ENZYMATIC ANALYSIS"},{"key":"49_28010790","doi-asserted-by":"crossref","first-page":"911","DOI":"10.1139\/o59-099","volume":"37","year":"1959","journal-title":"CAN J BIOCHEM PHYSIOL"},{"issue":"2","key":"50_32134501","doi-asserted-by":"publisher","first-page":"616","DOI":"10.1210\/en.2008-0601","volume":"150","year":"2009","journal-title":"Endocrinology","ISSN":"https:\/\/id.crossref.org\/issn\/0013-7227","issn-type":"print"},{"issue":"5","key":"51_28410036","doi-asserted-by":"publisher","first-page":"555","DOI":"10.1007\/s00418-006-0263-5","volume":"127","author":"Rajas","year":"2007","journal-title":"Histochemistry and cell biology","ISSN":"https:\/\/id.crossref.org\/issn\/0948-6143","issn-type":"print"}],"container-title":["Human Molecular Genetics"],"original-title":[],"language":"en","link":[{"URL":"http:\/\/academic.oup.com\/hmg\/article-pdf\/24\/8\/2287\/1840700\/ddu746.pdf","content-type":"unspecified","content-version":"vor","intended-application":"similarity-checking"}],"deposited":{"date-parts":[[2022,4,25]],"date-time":"2022-04-25T20:45:13Z","timestamp":1650919513000},"score":1,"resource":{"primary":{"URL":"https:\/\/academic.oup.com\/hmg\/article-lookup\/doi\/10.1093\/hmg\/ddu746"}},"subtitle":[],"short-title":[],"issued":{"date-parts":[[2015,1,5]]},"references-count":51,"journal-issue":{"issue":"8","published-online":{"date-parts":[[2015,3,19]]},"published-print":{"date-parts":[[2015,4,15]]}},"URL":"https:\/\/doi.org\/10.1093\/hmg\/ddu746","relation":{},"ISSN":["0964-6906","1460-2083"],"issn-type":[{"value":"0964-6906","type":"print"},{"value":"1460-2083","type":"electronic"}],"subject":[],"published":{"date-parts":[[2015,1,5]]}}}