{"status":"ok","message-type":"work","message-version":"1.0.0","message":{"indexed":{"date-parts":[[2026,1,16]],"date-time":"2026-01-16T05:51:23Z","timestamp":1768542683650,"version":"3.49.0"},"reference-count":78,"publisher":"Oxford University Press (OUP)","issue":"12","content-domain":{"domain":[],"crossmark-restriction":false},"short-container-title":["Human Molecular Genetics"],"published-print":{"date-parts":[[2015,6,15]]},"DOI":"10.1093\/hmg\/ddv086","type":"journal-article","created":{"date-parts":[[2015,3,7]],"date-time":"2015-03-07T01:13:11Z","timestamp":1425690791000},"page":"3372-3389","source":"Crossref","is-referenced-by-count":61,"title":["Combined gene\/cell therapies provide long-term and pervasive rescue of multiple pathological symptoms in a murine model of globoid cell leukodystrophy"],"prefix":"10.1093","volume":"24","author":[{"given":"A.","family":"Ricca","sequence":"first","affiliation":[],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"N.","family":"Rufo","sequence":"additional","affiliation":[],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"S.","family":"Ungari","sequence":"additional","affiliation":[],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"F.","family":"Morena","sequence":"additional","affiliation":[],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"S.","family":"Martino","sequence":"additional","affiliation":[],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"W.","family":"Kulik","sequence":"additional","affiliation":[],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"V.","family":"Alberizzi","sequence":"additional","affiliation":[],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"A.","family":"Bolino","sequence":"additional","affiliation":[],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"F.","family":"Bianchi","sequence":"additional","affiliation":[],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"U.","family":"Del Carro","sequence":"additional","affiliation":[],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"A.","family":"Biffi","sequence":"additional","affiliation":[],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"A.","family":"Gritti","sequence":"additional","affiliation":[],"role":[{"role":"author","vocabulary":"crossref"}]}],"member":"286","published-online":{"date-parts":[[2015,3,5]]},"reference":[{"issue":"9","key":"1_17868672","doi-asserted-by":"publisher","first-page":"595","DOI":"10.1177\/08830738030180090201","volume":"18","author":"Suzuki","year":"2003","journal-title":"Journal of Child Neurology","ISSN":"https:\/\/id.crossref.org\/issn\/0883-0738","issn-type":"print"},{"issue":"2","key":"2_6533001","doi-asserted-by":"publisher","first-page":"231","DOI":"10.1002\/(SICI)1097-4547(20000415)60:2<231::AID-JNR12>3.0.CO;2-E","volume":"60","author":"LeVine","year":"2000","journal-title":"Journal of neuroscience research","ISSN":"https:\/\/id.crossref.org\/issn\/0360-4012","issn-type":"print"},{"issue":"10","key":"3_28017413","doi-asserted-by":"publisher","first-page":"2520","DOI":"10.1096\/fj.06-6169com","volume":"21","year":"2007","journal-title":"The FASEB Journal","ISSN":"https:\/\/id.crossref.org\/issn\/0892-6638","issn-type":"print"},{"issue":"4","key":"4_40030697","doi-asserted-by":"publisher","first-page":"367","DOI":"10.1016\/j.ymgme.2011.05.005","volume":"103","author":"Lin","year":"2011","journal-title":"Molecular genetics and metabolism","ISSN":"https:\/\/id.crossref.org\/issn\/1096-7192","issn-type":"print"},{"issue":"12","key":"5_47294576","doi-asserted-by":"publisher","first-page":"3250","DOI":"10.1093\/hmg\/ddu034","volume":"23","year":"2014","journal-title":"Human Molecular Genetics","ISSN":"https:\/\/id.crossref.org\/issn\/0964-6906","issn-type":"print"},{"issue":"3","key":"6_4867494","first-page":"302","volume":"58","author":"Suzuki","year":"1988","journal-title":"Laboratory investigation; a journal of technical methods and pathology","ISSN":"https:\/\/id.crossref.org\/issn\/0023-6837","issn-type":"print"},{"issue":"4843","key":"7_4861772","doi-asserted-by":"publisher","first-page":"1035","DOI":"10.1126\/science.3278379","volume":"239","author":"Hoogerbrugge","year":"1988","journal-title":"Science","ISSN":"https:\/\/id.crossref.org\/issn\/0036-8075","issn-type":"print"},{"issue":"7","key":"8_19283382","doi-asserted-by":"publisher","first-page":"565","DOI":"10.1097\/01.jnen.0000171646.01966.0c","volume":"64","author":"Yagi","year":"2005","journal-title":"Journal of neuropathology and experimental neurology","ISSN":"https:\/\/id.crossref.org\/issn\/0022-3069","issn-type":"print"},{"issue":"4666","key":"9_13304211","doi-asserted-by":"publisher","first-page":"1052","DOI":"10.1126\/science.6382609","volume":"225","author":"Yeager","year":"1984","journal-title":"Science","ISSN":"https:\/\/id.crossref.org\/issn\/0036-8075","issn-type":"print"},{"issue":"1-2","key":"10_19450856","doi-asserted-by":"publisher","first-page":"150","DOI":"10.1016\/j.ymgme.2005.06.023","volume":"86","author":"Luzi","year":"2005","journal-title":"Molecular genetics and metabolism","ISSN":"https:\/\/id.crossref.org\/issn\/1096-7192","issn-type":"print"},{"issue":"6","key":"12_22344324","doi-asserted-by":"publisher","first-page":"1585","DOI":"10.1111\/j.1471-4159.2006.03986.x","volume":"97","author":"Taylor","year":"2006","journal-title":"Journal of neurochemistry","ISSN":"https:\/\/id.crossref.org\/issn\/0022-3042","issn-type":"print"},{"issue":"2","key":"13_21526333","doi-asserted-by":"publisher","first-page":"314","DOI":"10.1016\/j.nbd.2005.07.016","volume":"21","author":"Pellegatta","year":"2006","journal-title":"Neurobiology of disease","ISSN":"https:\/\/id.crossref.org\/issn\/0969-9961","issn-type":"print"},{"key":"14_50162840","first-page":"67","volume":"29","year":"2010","journal-title":"Stem Cells","ISSN":"https:\/\/id.crossref.org\/issn\/0250-6793","issn-type":"print"},{"key":"15_47409810","doi-asserted-by":"crossref","first-page":"1523","DOI":"10.1002\/stem.1397","volume":"31","year":"2013","journal-title":"Stem Cells","ISSN":"https:\/\/id.crossref.org\/issn\/0250-6793","issn-type":"print"},{"issue":"11","key":"16_40725925","doi-asserted-by":"publisher","first-page":"1738","DOI":"10.1002\/stem.724","volume":"29","author":"Miranda","year":"2011","journal-title":"Stem Cells","ISSN":"https:\/\/id.crossref.org\/issn\/0250-6793","issn-type":"print"},{"issue":"4","key":"17_16101466","doi-asserted-by":"publisher","first-page":"385","DOI":"10.1016\/0963-6897(95)00021-O","volume":"4","author":"Krivit","year":"1995","journal-title":"Cell transplantation","ISSN":"https:\/\/id.crossref.org\/issn\/0963-6897","issn-type":"print"},{"issue":"R1","key":"18_39594499","doi-asserted-by":"publisher","first-page":"R42","DOI":"10.1093\/hmg\/ddr142","volume":"20","year":"2011","journal-title":"Human Molecular Genetics","ISSN":"https:\/\/id.crossref.org\/issn\/0964-6906","issn-type":"print"},{"issue":"2-3","key":"19_22258916","doi-asserted-by":"publisher","first-page":"413","DOI":"10.1007\/s10545-005-0258-8","volume":"29","author":"Boelens","year":"2006","journal-title":"Journal of inherited metabolic disease","ISSN":"https:\/\/id.crossref.org\/issn\/0141-8955","issn-type":"print"},{"issue":"20","key":"20_18868889","doi-asserted-by":"publisher","first-page":"2069","DOI":"10.1056\/NEJMoa042604","volume":"352","author":"Escolar","year":"2005","journal-title":"New England Journal of Medicine","ISSN":"https:\/\/id.crossref.org\/issn\/0028-4793","issn-type":"print"},{"issue":"6","key":"21_34538829","doi-asserted-by":"publisher","first-page":"450","DOI":"10.1097\/GIM.0b013e3181a16e04","volume":"11","author":"Duffner","year":"2009","journal-title":"Genetics in medicine : official journal of the American College of Medical Genetics","ISSN":"https:\/\/id.crossref.org\/issn\/1098-3600","issn-type":"print"},{"issue":"1","key":"22_11458864","doi-asserted-by":"publisher","first-page":"40","DOI":"10.1203\/00006450-200201000-00009","volume":"51","author":"BISWAS","year":"2002","journal-title":"Pediatric Research","ISSN":"https:\/\/id.crossref.org\/issn\/0031-3998","issn-type":"print"},{"issue":"1-2","key":"23_42871777","doi-asserted-by":"publisher","first-page":"186","DOI":"10.1016\/j.ymgme.2012.05.021","volume":"107","author":"Qin","year":"2012","journal-title":"Molecular genetics and metabolism","ISSN":"https:\/\/id.crossref.org\/issn\/1096-7192","issn-type":"print"},{"issue":"1","key":"24_23127143","doi-asserted-by":"publisher","first-page":"44","DOI":"10.1038\/sj.mt.6300026","volume":"15","author":"Lin","year":"2007","journal-title":"Molecular therapy : the journal of the American Society of Gene Therapy","ISSN":"https:\/\/id.crossref.org\/issn\/1525-0016","issn-type":"print"},{"issue":"27","key":"25_40270039","doi-asserted-by":"publisher","first-page":"9945","DOI":"10.1523\/JNEUROSCI.1802-11.2011","volume":"31","author":"Reddy","year":"2011","journal-title":"Journal of Neuroscience","ISSN":"https:\/\/id.crossref.org\/issn\/0270-6474","issn-type":"print"},{"issue":"8","key":"26_33870959","doi-asserted-by":"publisher","first-page":"1748","DOI":"10.1002\/jnr.22006","volume":"87","author":"Galbiati","year":"2009","journal-title":"Journal of neuroscience research","ISSN":"https:\/\/id.crossref.org\/issn\/0360-4012","issn-type":"print"},{"key":"27_50162841","doi-asserted-by":"crossref","first-page":"1","DOI":"10.3390\/jcm1010001","volume":"1","year":"2012","journal-title":"J CLIN MED"},{"issue":"11","key":"28_43346027","doi-asserted-by":"publisher","first-page":"2031","DOI":"10.1038\/mt.2012.153","volume":"20","author":"Rafi","year":"2012","journal-title":"Molecular therapy : the journal of the American Society of Gene Therapy","ISSN":"https:\/\/id.crossref.org\/issn\/1525-0016","issn-type":"print"},{"issue":"10","key":"29_40470997","doi-asserted-by":"publisher","first-page":"1559","DOI":"10.1002\/stem.701","volume":"29","author":"Neri","year":"2011","journal-title":"Stem Cells","ISSN":"https:\/\/id.crossref.org\/issn\/0250-6793","issn-type":"print"},{"issue":"6933","key":"30_17589402","doi-asserted-by":"publisher","first-page":"688","DOI":"10.1038\/nature01552","volume":"422","author":"Pluchino","year":"2003","journal-title":"Nature","ISSN":"https:\/\/id.crossref.org\/issn\/0028-0836","issn-type":"print"},{"issue":"11","key":"31_22897837","doi-asserted-by":"publisher","first-page":"3070","DOI":"10.1172\/JCI28873","volume":"116","author":"Biffi","year":"2006","journal-title":"Journal of Clinical Investigation","ISSN":"https:\/\/id.crossref.org\/issn\/0021-9738","issn-type":"print"},{"issue":"8","key":"32_18138038","doi-asserted-by":"publisher","first-page":"1118","DOI":"10.1172\/JCI200419205","volume":"113","author":"Biffi","year":"2004","journal-title":"Journal of Clinical Investigation","ISSN":"https:\/\/id.crossref.org\/issn\/0021-9738","issn-type":"print"},{"issue":"4","key":"33_38584667","doi-asserted-by":"publisher","first-page":"501","DOI":"10.1177\/34.4.3081625","volume":"34","author":"Alroy","year":"1986","journal-title":"Journal of Histochemistry &amp; Cytochemistry","ISSN":"https:\/\/id.crossref.org\/issn\/0022-1554","issn-type":"print"},{"issue":"1","key":"34_39407855","doi-asserted-by":"publisher","first-page":"35","DOI":"10.1007\/s00401-011-0814-2","volume":"122","author":"Castelvetri","year":"2011","journal-title":"Acta neuropathologica","ISSN":"https:\/\/id.crossref.org\/issn\/0001-6322","issn-type":"print"},{"key":"35_47409811","doi-asserted-by":"crossref","first-page":"1127","DOI":"10.1038\/jcbfm.2013.64","volume":"33","year":"2013","journal-title":"Journal of cerebral blood flow and metabolism : official journal of the International Society of Cerebral Blood Flow and Metabolism","ISSN":"https:\/\/id.crossref.org\/issn\/0271-678X","issn-type":"print"},{"issue":"3","key":"36_46540744","doi-asserted-by":"publisher","first-page":"730","DOI":"10.1093\/hmg\/ddt459","volume":"23","year":"2014","journal-title":"Human Molecular Genetics","ISSN":"https:\/\/id.crossref.org\/issn\/0964-6906","issn-type":"print"},{"key":"37_41941015","doi-asserted-by":"crossref","first-page":"7","DOI":"10.3389\/fnmol.2012.00007","volume":"5","author":"Hunt","year":"2012","ISSN":"https:\/\/id.crossref.org\/issn\/1662-5099","issn-type":"print"},{"issue":"4","key":"38_19308333","doi-asserted-by":"publisher","first-page":"597","DOI":"10.1002\/jnr.20574","volume":"81","author":"Dolcetta","year":"2005","journal-title":"Journal of neuroscience research","ISSN":"https:\/\/id.crossref.org\/issn\/0360-4012","issn-type":"print"},{"issue":"1","key":"40_34440136","doi-asserted-by":"publisher","first-page":"51","DOI":"10.1016\/j.nbd.2008.12.019","volume":"34","author":"Visigalli","year":"2009","journal-title":"Neurobiology of disease","ISSN":"https:\/\/id.crossref.org\/issn\/0969-9961","issn-type":"print"},{"key":"41_46714735","doi-asserted-by":"crossref","first-page":"643","DOI":"10.3171\/2013.3.PEDS12397","volume":"11","year":"2013","ISSN":"https:\/\/id.crossref.org\/issn\/1933-0715","issn-type":"print"},{"issue":"5","key":"42_31360508","doi-asserted-by":"publisher","first-page":"463","DOI":"10.1089\/hum.2008.022","volume":"19","author":"Worgall","year":"2008","journal-title":"Human gene therapy","ISSN":"https:\/\/id.crossref.org\/issn\/1043-0342","issn-type":"print"},{"key":"43_49522326","doi-asserted-by":"crossref","first-page":"506","DOI":"10.1089\/hum.2013.238","volume":"25","year":"2014","journal-title":"Human gene therapy","ISSN":"https:\/\/id.crossref.org\/issn\/1043-0342","issn-type":"print"},{"key":"44_49432488","doi-asserted-by":"crossref","first-page":"1138","DOI":"10.1016\/S0140-6736(13)61939-X","volume":"383","year":"2014","journal-title":"Lancet","ISSN":"https:\/\/id.crossref.org\/issn\/0140-6736","issn-type":"print"},{"issue":"1","key":"45_45655969","doi-asserted-by":"publisher","first-page":"23","DOI":"10.1182\/blood-2013-01-306647","volume":"122","year":"2013","journal-title":"Blood","ISSN":"https:\/\/id.crossref.org\/issn\/0006-4971","issn-type":"print"},{"issue":"4","key":"46_28748417","doi-asserted-by":"publisher","first-page":"439","DOI":"10.1038\/nm1548","volume":"13","author":"Lee","year":"2007","journal-title":"Nature medicine","ISSN":"https:\/\/id.crossref.org\/issn\/1078-8956","issn-type":"print"},{"issue":"7048","key":"47_19260779","doi-asserted-by":"publisher","first-page":"266","DOI":"10.1038\/nature03889","volume":"436","author":"Pluchino","year":"2005","journal-title":"Nature","ISSN":"https:\/\/id.crossref.org\/issn\/0028-0836","issn-type":"print"},{"issue":"3","key":"48_35559325","doi-asserted-by":"publisher","first-page":"310","DOI":"10.1016\/j.stem.2009.05.022","volume":"5","author":"Tamaki","year":"2009","ISSN":"https:\/\/id.crossref.org\/issn\/1875-9777","issn-type":"print"},{"key":"49_50162842","doi-asserted-by":"crossref","first-page":"193","DOI":"10.1016\/j.molcel.2014.08.020","volume":"56","year":"2014","journal-title":"Molecular cell","ISSN":"https:\/\/id.crossref.org\/issn\/1097-2765","issn-type":"print"},{"issue":"21","key":"50_43342035","doi-asserted-by":"publisher","first-page":"4732","DOI":"10.1093\/hmg\/dds313","volume":"21","year":"2012","journal-title":"Human Molecular Genetics","ISSN":"https:\/\/id.crossref.org\/issn\/0964-6906","issn-type":"print"},{"issue":"1","key":"51_18959473","doi-asserted-by":"publisher","first-page":"221","DOI":"10.1148\/radiol.2353040716","volume":"236","author":"McGraw","year":"2005","journal-title":"Radiology","ISSN":"https:\/\/id.crossref.org\/issn\/0033-8419","issn-type":"print"},{"issue":"5","key":"52_34637517","doi-asserted-by":"publisher","first-page":"1017","DOI":"10.3174\/ajnr.A1476","volume":"30","year":"2009","journal-title":"American Journal of Neuroradiology","ISSN":"https:\/\/id.crossref.org\/issn\/0195-6108","issn-type":"print"},{"issue":"50","key":"53_30048196","doi-asserted-by":"publisher","first-page":"13730","DOI":"10.1523\/JNEUROSCI.3379-07.2007","volume":"27","author":"Galbiati","year":"2007","journal-title":"Journal of Neuroscience","ISSN":"https:\/\/id.crossref.org\/issn\/0270-6474","issn-type":"print"},{"issue":"44","key":"54_43882642","doi-asserted-by":"publisher","first-page":"18150","DOI":"10.1073\/pnas.1210150109","volume":"109","year":"2012","journal-title":"PNAS","ISSN":"https:\/\/id.crossref.org\/issn\/0027-8424","issn-type":"print"},{"issue":"9","key":"55_40458143","doi-asserted-by":"publisher","first-page":"1142","DOI":"10.1038\/nn.2887","volume":"14","author":"Ajami","year":"2011","journal-title":"Nature neuroscience","ISSN":"https:\/\/id.crossref.org\/issn\/1097-6256","issn-type":"print"},{"issue":"4650","key":"56_13210787","doi-asserted-by":"publisher","first-page":"753","DOI":"10.1126\/science.6719111","volume":"224","author":"Igisu","year":"1984","journal-title":"Science","ISSN":"https:\/\/id.crossref.org\/issn\/0036-8075","issn-type":"print"},{"issue":"11","key":"57_11399622","doi-asserted-by":"crossref","first-page":"1062","DOI":"10.1093\/jnen\/60.11.1062","volume":"60","author":"Wu","year":"2001","journal-title":"Journal of neuropathology and experimental neurology","ISSN":"https:\/\/id.crossref.org\/issn\/0022-3069","issn-type":"print"},{"issue":"7","key":"58_35347780","doi-asserted-by":"publisher","first-page":"e1000113","DOI":"10.1371\/journal.pmed.1000113","volume":"6","author":"Shechter","year":"2009","ISSN":"https:\/\/id.crossref.org\/issn\/1549-1277","issn-type":"print"},{"key":"59_45781229","doi-asserted-by":"crossref","first-page":"263","DOI":"10.1212\/01.wnl.0000230153.34613.84","volume":"67","year":"2006","journal-title":"OGPL Neurology"},{"issue":"1","key":"60_5130565","doi-asserted-by":"publisher","first-page":"178","DOI":"10.1016\/0006-8993(88)91220-6","volume":"460","author":"Kondo","year":"1988","journal-title":"Brain research","ISSN":"https:\/\/id.crossref.org\/issn\/0006-8993","issn-type":"print"},{"key":"61_50162843","doi-asserted-by":"crossref","first-page":"268","DOI":"10.1212\/01.wnl.0000230156.01228.33","volume":"67","year":"2006","journal-title":"OGPL Neurology"},{"issue":"2","key":"62_7702286","doi-asserted-by":"publisher","first-page":"329","DOI":"10.1093\/brain\/92.2.329","volume":"92","author":"DUNN","year":"1969","journal-title":"Brain","ISSN":"https:\/\/id.crossref.org\/issn\/0006-8950","issn-type":"print"},{"issue":"5","key":"63_17166597","doi-asserted-by":"publisher","first-page":"284","DOI":"10.1016\/S0387-7604(02)00057-8","volume":"24","author":"Itoh","year":"2002","journal-title":"Brain &amp; development","ISSN":"https:\/\/id.crossref.org\/issn\/0387-7604","issn-type":"print"},{"key":"64_49636154","doi-asserted-by":"crossref","first-page":"92","DOI":"10.1016\/j.nbd.2014.02.012","volume":"66","year":"2014","journal-title":"Neurobiology of disease","ISSN":"https:\/\/id.crossref.org\/issn\/0969-9961","issn-type":"print"},{"issue":"2","key":"65_41964778","doi-asserted-by":"publisher","first-page":"325","DOI":"10.1016\/j.nbd.2012.01.013","volume":"46","author":"Cantuti-Castelvetri","year":"2012","journal-title":"Neurobiology of disease","ISSN":"https:\/\/id.crossref.org\/issn\/0969-9961","issn-type":"print"},{"issue":"8","key":"66_19529361","doi-asserted-by":"publisher","first-page":"1881","DOI":"10.1111\/j.1460-9568.2005.04389.x","volume":"22","author":"Vlug","year":"2005","journal-title":"The European journal of neuroscience","ISSN":"https:\/\/id.crossref.org\/issn\/0953-816X","issn-type":"print"},{"key":"67_47315337","doi-asserted-by":"crossref","first-page":"812","DOI":"10.1016\/j.neuroscience.2010.04.053","volume":"169","year":"2010","journal-title":"Neuroscience","ISSN":"https:\/\/id.crossref.org\/issn\/0306-4522","issn-type":"print"},{"issue":"13","key":"68_39568353","doi-asserted-by":"publisher","first-page":"4978","DOI":"10.1523\/JNEUROSCI.2672-10.2011","volume":"31","author":"Zhang","year":"2011","journal-title":"Journal of Neuroscience","ISSN":"https:\/\/id.crossref.org\/issn\/0270-6474","issn-type":"print"},{"issue":"11","key":"69_37370828","doi-asserted-by":"publisher","first-page":"1857","DOI":"10.1182\/blood-2009-12-256461","volume":"116","year":"2010","journal-title":"Blood","ISSN":"https:\/\/id.crossref.org\/issn\/0006-4971","issn-type":"print"},{"issue":"6148","key":"70_46130920","doi-asserted-by":"publisher","first-page":"1233158","DOI":"10.1126\/science.1233158","volume":"341","year":"2013","journal-title":"Science","ISSN":"https:\/\/id.crossref.org\/issn\/0036-8075","issn-type":"print"},{"key":"71_50162844","doi-asserted-by":"crossref","first-page":"8","DOI":"10.2217\/rme.12.81","volume":"7","year":"2012","ISSN":"https:\/\/id.crossref.org\/issn\/1746-076X","issn-type":"print"},{"issue":"3","key":"72_16060258","doi-asserted-by":"publisher","first-page":"249","DOI":"10.1111\/j.1750-3639.1995.tb00601.x","volume":"5","author":"Suzuki","year":"1995","journal-title":"Brain pathology (Zurich, Switzerland)","ISSN":"https:\/\/id.crossref.org\/issn\/1015-6305","issn-type":"print"},{"key":"73_50162845","doi-asserted-by":"crossref","first-page":"1228","DOI":"10.1002\/glia.21003","volume":"58","year":"2010","journal-title":"Glia","ISSN":"https:\/\/id.crossref.org\/issn\/0894-1491","issn-type":"print"},{"issue":"5","key":"74_22090915","doi-asserted-by":"publisher","first-page":"585","DOI":"10.1038\/nm1398","volume":"12","author":"Brown","year":"2006","journal-title":"Nature medicine","ISSN":"https:\/\/id.crossref.org\/issn\/1078-8956","issn-type":"print"},{"issue":"9","key":"75_29566420","doi-asserted-by":"publisher","first-page":"821","DOI":"10.1089\/hum.2007.048","volume":"18","author":"Capotondo","year":"2007","journal-title":"Human gene therapy","ISSN":"https:\/\/id.crossref.org\/issn\/1043-0342","issn-type":"print"},{"issue":"1","key":"76_18607556","doi-asserted-by":"publisher","first-page":"108","DOI":"10.1038\/nbt1049","volume":"23","author":"Amendola","year":"2005","journal-title":"Nature biotechnology","ISSN":"https:\/\/id.crossref.org\/issn\/1087-0156","issn-type":"print"},{"issue":"4","key":"77_37142449","doi-asserted-by":"publisher","first-page":"e10145","DOI":"10.1371\/journal.pone.0010145","volume":"5","author":"Neri","year":"2010","ISSN":"https:\/\/id.crossref.org\/issn\/1932-6203","issn-type":"print"},{"issue":"3","key":"78_35614846","doi-asserted-by":"publisher","first-page":"333","DOI":"10.1002\/cne.22153","volume":"517","author":"Gritti","year":"2009","journal-title":"The Journal of comparative neurology","ISSN":"https:\/\/id.crossref.org\/issn\/0021-9967","issn-type":"print"},{"issue":"3","key":"79_33483929","doi-asserted-by":"publisher","first-page":"541","DOI":"10.1373\/clinchem.2008.115873","volume":"55","year":"2009","journal-title":"Clinical Chemistry","ISSN":"https:\/\/id.crossref.org\/issn\/0009-9147","issn-type":"print"},{"issue":"5","key":"80_35890865","doi-asserted-by":"publisher","first-page":"1021","DOI":"10.1083\/jcb.148.5.1021","volume":"148","year":"2000","journal-title":"The Journal of Cell Biology","ISSN":"https:\/\/id.crossref.org\/issn\/0021-9525","issn-type":"print"}],"container-title":["Human Molecular Genetics"],"original-title":[],"language":"en","link":[{"URL":"http:\/\/academic.oup.com\/hmg\/article-pdf\/24\/12\/3372\/1722480\/ddv086.pdf","content-type":"unspecified","content-version":"vor","intended-application":"similarity-checking"}],"deposited":{"date-parts":[[2019,8,21]],"date-time":"2019-08-21T18:59:45Z","timestamp":1566413985000},"score":1,"resource":{"primary":{"URL":"https:\/\/academic.oup.com\/hmg\/article-lookup\/doi\/10.1093\/hmg\/ddv086"}},"subtitle":[],"short-title":[],"issued":{"date-parts":[[2015,3,5]]},"references-count":78,"journal-issue":{"issue":"12","published-online":{"date-parts":[[2015,5,19]]},"published-print":{"date-parts":[[2015,6,15]]}},"URL":"https:\/\/doi.org\/10.1093\/hmg\/ddv086","relation":{},"ISSN":["0964-6906","1460-2083"],"issn-type":[{"value":"0964-6906","type":"print"},{"value":"1460-2083","type":"electronic"}],"subject":[],"published":{"date-parts":[[2015,3,5]]}}}