{"status":"ok","message-type":"work","message-version":"1.0.0","message":{"indexed":{"date-parts":[[2026,9,29]],"date-time":"2026-09-29T14:16:28Z","timestamp":1790691388742,"version":"4.1.0"},"reference-count":14,"publisher":"Ovid Technologies (Wolters Kluwer Health)","issue":"5","content-domain":{"domain":[],"crossmark-restriction":false},"short-container-title":[],"published-print":{"date-parts":[[2007,5]]},"DOI":"10.1097\/phm.0b013e31804a8505","type":"journal-article","created":{"date-parts":[[2007,4,18]],"date-time":"2007-04-18T04:04:09Z","timestamp":1176869049000},"page":"339-345","source":"Crossref","is-referenced-by-count":67,"title":["Long-Term Survival in Werdnig\u2013Hoffmann Disease"],"prefix":"10.1097","volume":"86","author":[{"given":"John R.","family":"Bach","sequence":"first","affiliation":[],"role":[{"vocabulary":"crossref","role":"author"}]},{"given":"Katherine","family":"Saltstein","sequence":"additional","affiliation":[],"role":[{"vocabulary":"crossref","role":"author"}]},{"given":"Diane","family":"Sinquee","sequence":"additional","affiliation":[],"role":[{"vocabulary":"crossref","role":"author"}]},{"given":"Brian","family":"Weaver","sequence":"additional","affiliation":[],"role":[{"vocabulary":"crossref","role":"author"}]},{"given":"Eugene","family":"Komaroff","sequence":"additional","affiliation":[],"role":[{"vocabulary":"crossref","role":"author"}]}],"member":"276","reference":[{"key":"R1-2-20210202","doi-asserted-by":"crossref","first-page":"19","DOI":"10.1055\/s-2008-1040858","article-title":"Spinal muscular atrophy.","volume":"18","author":"Iannaccone","year":"1998","journal-title":"Semin Neurol"},{"key":"R2-2-20210202","doi-asserted-by":"crossref","first-page":"2061","DOI":"10.1097\/00003246-199812000-00042","article-title":"Noninvasive management of pediatric neuromuscular ventilatory failure.","volume":"26","author":"Niranjan","year":"1998","journal-title":"Crit Care Med"},{"key":"R3-2-20210202","doi-asserted-by":"crossref","first-page":"49","DOI":"10.1016\/S1090-3798(99)80012-9","article-title":"Very severe spinal muscular atrophy: an expanding clinical phenotype.","volume":"3","author":"Dubowitz","year":"1999","journal-title":"Eur J Paediatr Neurol"},{"key":"R4-2-20210202","doi-asserted-by":"crossref","first-page":"8","DOI":"10.1097\/00002060-199801000-00003","article-title":"Neuromuscular ventilatory insufficiency: the effect of home mechanical ventilator use vs. oxygen therapy on pneumonia and hospitalization rates.","volume":"77","author":"Bach","year":"1998","journal-title":"Am J Phys Med Rehabil"},{"key":"R5-2-20210202","doi-asserted-by":"crossref","first-page":"16","DOI":"10.1002\/ppul.10110","article-title":"Spinal muscular atrophy type 1: management and outcomes.","volume":"34","author":"Bach","year":"2002","journal-title":"Pediatr Pulmonol"},{"key":"R6-2-20210202","doi-asserted-by":"crossref","first-page":"815","DOI":"10.1097\/01.PHM.0000083669.22483.04","article-title":"Prevention of pectus excavatum for children with spinal muscular atrophy type 1.","volume":"82","author":"Bach","year":"2003","journal-title":"Am J Phys Med Rehabil"},{"key":"R7-2-20210202","first-page":"309","article-title":"The Management of Patients with Neuromuscular Disease.","author":"Bach","year":"2004"},{"key":"R8-2-20210202","first-page":"211","article-title":"The Management of Patients with Neuromuscular Disease.","author":"Bach","year":"2004"},{"key":"R9-2-20210202","first-page":"000","article-title":"Medical considerations of long-term survival of Werdnig\u2013Hoffmann disease.","volume":"86","author":"Bach","year":"2007","journal-title":"Am J Phys Med Rehabil"},{"key":"R10-2-20210202","doi-asserted-by":"crossref","first-page":"411","DOI":"10.1097\/00002060-200206000-00003","article-title":"Duchenne muscular dystrophy: prolongation of life by noninvasive respiratory muscle aids.","volume":"81","author":"Gomez-Merino","year":"2002","journal-title":"Am J Phys Med Rehabil"},{"key":"R11-2-20210202","doi-asserted-by":"crossref","first-page":"359","DOI":"10.1046\/j.1442-200x.2000.01241.x","article-title":"Long-term ventilator support in patients with Werdnig-Hoffmann disease.","volume":"42","author":"Sakakihara","year":"2000","journal-title":"Pediatr Int"},{"key":"R12-2-20210202","doi-asserted-by":"crossref","first-page":"193","DOI":"10.1097\/00002060-200003000-00013","article-title":"Management approaches in muscular dystrophy association clinics.","volume":"79","author":"Bach","year":"2000","journal-title":"Am J Phys Med Rehabil"},{"key":"R13-2-20210202","doi-asserted-by":"crossref","first-page":"137","DOI":"10.1097\/00002060-200302000-00009","article-title":"Spinal muscular atrophy type 1 quality of life.","volume":"82","author":"Bach","year":"2003","journal-title":"Am J Phys Med Rehabil"},{"key":"R14-2-20210202","first-page":"109","article-title":"Quality of life: the physician\u2019s dilemma.","volume":"65","author":"Freed","year":"1984","journal-title":"Arch Phys Med Rehabil"}],"container-title":["American Journal of Physical Medicine &amp; Rehabilitation"],"original-title":[],"language":"en","link":[{"URL":"https:\/\/www.ovid.com\/00002060-200705000-00002","content-type":"unspecified","content-version":"vor","intended-application":"similarity-checking"}],"deposited":{"date-parts":[[2026,8,6]],"date-time":"2026-08-06T16:34:39Z","timestamp":1786034079000},"score":1,"resource":{"primary":{"URL":"https:\/\/www.ovid.com\/00002060-200705000-00002"}},"subtitle":[],"short-title":[],"issued":{"date-parts":[[2007,5]]},"references-count":14,"journal-issue":{"issue":"5","published-print":{"date-parts":[[2007]]}},"URL":"https:\/\/doi.org\/10.1097\/phm.0b013e31804a8505","relation":{},"ISSN":["0894-9115"],"issn-type":[{"value":"0894-9115","type":"print"}],"subject":[],"published":{"date-parts":[[2007,5]]}}}