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Urine glycosaminoglycans (GAGs) decreased post\u2010transplant and child has improved clinically and neurologically. Insignificant titers of the anti\u2010iduronidase antibodies which developed post\u2010transplant did not affect the transplant outcome or the endogenous recovery of the alpha\u2010L\u2010iduronidase enzyme.<\/jats:p>","DOI":"10.1111\/j.1399-3046.2007.00720.x","type":"journal-article","created":{"date-parts":[[2007,5,3]],"date-time":"2007-05-03T18:15:33Z","timestamp":1178216133000},"page":"563-567","source":"Crossref","is-referenced-by-count":10,"title":["Pre\u2010stem cell transplantation enzyme replacement therapy in Hurler syndrome does not lead to significant antibody formation or delayed recovery of the endogenous enzyme post\u2010transplant: A case report"],"prefix":"10.1111","volume":"11","author":[{"given":"Sandeep","family":"Soni","sequence":"first","affiliation":[],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"Monica","family":"Hente","sequence":"additional","affiliation":[],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"Nancy","family":"Breslin","sequence":"additional","affiliation":[],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"Joseph","family":"Hersh","sequence":"additional","affiliation":[],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"Chester","family":"Whitley","sequence":"additional","affiliation":[],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"Alexandra","family":"Cheerva","sequence":"additional","affiliation":[],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"Salvatore","family":"Bertolone","sequence":"additional","affiliation":[],"role":[{"role":"author","vocabulary":"crossref"}]}],"member":"311","published-online":{"date-parts":[[2007,4,19]]},"reference":[{"key":"e_1_2_6_2_2","first-page":"3421","volume-title":"The Metabolic and Molecular Bases of Inherited Diseases","author":"Neufeld EF","year":"2001"},{"key":"e_1_2_6_3_2","doi-asserted-by":"publisher","DOI":"10.1111\/j.1651-2227.1995.tb13640.x"},{"key":"e_1_2_6_4_2","doi-asserted-by":"publisher","DOI":"10.1007\/BF00710053"},{"key":"e_1_2_6_5_2","first-page":"S182","article-title":"Survival in Hurler\u2019s disease following bone marrow transplantation in 84 patients","volume":"15","author":"Kirvit W","year":"1995","journal-title":"Bone Marrow Transplant"},{"key":"e_1_2_6_6_2","doi-asserted-by":"publisher","DOI":"10.1056\/NEJMoa032613"},{"key":"e_1_2_6_7_2","doi-asserted-by":"crossref","first-page":"4894","DOI":"10.1182\/blood.V87.11.4894.bloodjournal87114894","article-title":"Outcome of unrelated donor bone marrow transplantation in 40 children with Hurler\u2019s syndrome","volume":"87","author":"Peters C","year":"1996","journal-title":"Blood"},{"key":"e_1_2_6_8_2","doi-asserted-by":"publisher","DOI":"10.1038\/sj.bmt.1704115"},{"key":"e_1_2_6_9_2","doi-asserted-by":"publisher","DOI":"10.1136\/adc.76.2.92"},{"key":"e_1_2_6_10_2","doi-asserted-by":"crossref","first-page":"732","DOI":"10.1182\/blood.V89.2.732b","article-title":"Developmental outcome of unrelated donor bone marrow transplantation in children with Hurler syndrome (letter)","volume":"89","author":"Phipps S","year":"1997","journal-title":"Blood"},{"key":"e_1_2_6_11_2","doi-asserted-by":"publisher","DOI":"10.1056\/NEJM200101183440304"},{"key":"e_1_2_6_12_2","doi-asserted-by":"publisher","DOI":"10.1097\/01.GIM.0000154299.22120.6A"},{"key":"e_1_2_6_13_2","doi-asserted-by":"publisher","DOI":"10.1038\/sj.bmt.1705401"}],"container-title":["Pediatric Transplantation"],"original-title":[],"language":"en","link":[{"URL":"https:\/\/api.wiley.com\/onlinelibrary\/tdm\/v1\/articles\/10.1111%2Fj.1399-3046.2007.00720.x","content-type":"unspecified","content-version":"vor","intended-application":"text-mining"},{"URL":"https:\/\/onlinelibrary.wiley.com\/doi\/pdf\/10.1111\/j.1399-3046.2007.00720.x","content-type":"unspecified","content-version":"vor","intended-application":"similarity-checking"}],"deposited":{"date-parts":[[2023,10,9]],"date-time":"2023-10-09T21:25:21Z","timestamp":1696886721000},"score":1,"resource":{"primary":{"URL":"https:\/\/onlinelibrary.wiley.com\/doi\/10.1111\/j.1399-3046.2007.00720.x"}},"subtitle":[],"short-title":[],"issued":{"date-parts":[[2007,4,19]]},"references-count":12,"journal-issue":{"issue":"5","published-print":{"date-parts":[[2007,8]]}},"alternative-id":["10.1111\/j.1399-3046.2007.00720.x"],"URL":"https:\/\/doi.org\/10.1111\/j.1399-3046.2007.00720.x","archive":["Portico"],"relation":{},"ISSN":["1397-3142","1399-3046"],"issn-type":[{"value":"1397-3142","type":"print"},{"value":"1399-3046","type":"electronic"}],"subject":[],"published":{"date-parts":[[2007,4,19]]}}}