{"status":"ok","message-type":"work","message-version":"1.0.0","message":{"indexed":{"date-parts":[[2025,8,27]],"date-time":"2025-08-27T07:10:26Z","timestamp":1756278626217,"version":"3.44.0"},"reference-count":21,"publisher":"BMJ","issue":"2","content-domain":{"domain":["bmj.com"],"crossmark-restriction":true},"short-container-title":["BMJ Case Rep"],"accepted":{"date-parts":[[2024,2,15]]},"published-print":{"date-parts":[[2024,2]]},"abstract":"<jats:p>Alagille syndrome (AGS) is a genetic disorder due to mutations in the <jats:italic>JAGGED 1<\/jats:italic> or <jats:italic>NOTCH 2<\/jats:italic> genes leading to multisystemic manifestations. Though these patients are at risk of developing various liver tumours, no cases of hepatoblastoma among young children with cirrhosis in AGS have been reported. We report a male toddler, with cirrhosis due to AGS who developed a hepatoblastoma. He underwent a liver transplant for decompensated chronic liver disease with marked pruritus, very high alpha-fetoprotein levels and malignant liver lesions on positron emission tomography CT. His explant histology revealed a paucity of bile ducts and liver lesions turned out to be hepatoblastoma for which he received postoperative chemotherapy. The genetic testing sent before transplantation confirmed the clinical diagnosis of AGS. Hepatoblastoma should be suspected in any child with AGS presenting with a right upper quadrant mass even in the setting of chronic liver disease.<\/jats:p>","DOI":"10.1136\/bcr-2022-253080","type":"journal-article","created":{"date-parts":[[2024,2,28]],"date-time":"2024-02-28T02:10:10Z","timestamp":1709086210000},"page":"e253080","update-policy":"https:\/\/doi.org\/10.1136\/crossmarkpolicy","source":"Crossref","is-referenced-by-count":1,"title":["Hepatoblastoma in a cirrhotic child with Alagille syndrome"],"prefix":"10.1136","volume":"17","author":[{"ORCID":"https:\/\/orcid.org\/0000-0002-9863-9325","authenticated-orcid":false,"given":"Sumit","family":"Agrawal","sequence":"first","affiliation":[{"name":"Pediatric Gastroenterology, Hepatology and Nutrition, Indraprastha Apollo Hospital, New Delhi, India"}],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"Bishnupriya","family":"Sahoo","sequence":"additional","affiliation":[{"name":"Pediatric Gastroenterology, Hepatology and Nutrition, Indraprastha Apollo Hospital, New Delhi, India"}],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"Karunesh","family":"Kumar","sequence":"additional","affiliation":[{"name":"Pediatric Gastroenterology, Hepatology and Nutrition, Indraprastha Apollo Hospital, New Delhi, India"}],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"Smita","family":"Malhotra","sequence":"additional","affiliation":[{"name":"Pediatric Gastroenterology, Hepatology and Nutrition, Indraprastha Apollo Hospital, New Delhi, India"}],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"Anupam","family":"Sibal","sequence":"additional","affiliation":[{"name":"Pediatric Gastroenterology, Hepatology and Nutrition, Indraprastha Apollo Hospital, New Delhi, India"}],"role":[{"role":"author","vocabulary":"crossref"}]}],"member":"239","published-online":{"date-parts":[[2024,2,27]]},"reference":[{"key":"2025082623472327000_17.2.e253080.1","unstructured":"Guarino A , Canani RB , et al . 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