{"status":"ok","message-type":"work","message-version":"1.0.0","message":{"indexed":{"date-parts":[[2026,10,1]],"date-time":"2026-10-01T12:49:09Z","timestamp":1790858949863,"version":"4.1.0"},"reference-count":15,"publisher":"Springer Science and Business Media LLC","issue":"1","license":[{"start":{"date-parts":[[2018,5,2]],"date-time":"2018-05-02T00:00:00Z","timestamp":1525219200000},"content-version":"tdm","delay-in-days":0,"URL":"http:\/\/creativecommons.org\/licenses\/by\/4.0\/"}],"funder":[{"DOI":"10.13039\/100008308","name":"Comprehensive Cancer Center, City of Hope","doi-asserted-by":"publisher","id":[{"id":"10.13039\/100008308","id-type":"DOI","asserted-by":"publisher"}]},{"name":"Stemline Therapeutics, Inc"}],"content-domain":{"domain":["link.springer.com"],"crossmark-restriction":false},"short-container-title":["J Hematol Oncol"],"published-print":{"date-parts":[[2018,12]]},"DOI":"10.1186\/s13045-018-0604-6","type":"journal-article","created":{"date-parts":[[2018,5,2]],"date-time":"2018-05-02T12:45:55Z","timestamp":1525265155000},"update-policy":"https:\/\/doi.org\/10.1007\/springer_crossmark_policy","source":"Crossref","is-referenced-by-count":45,"title":["First pediatric experience of SL-401, a CD123-targeted therapy, in patients with blastic plasmacytoid dendritic cell neoplasm: report of three cases"],"prefix":"10.1186","volume":"11","author":[{"given":"Weili","family":"Sun","sequence":"first","affiliation":[],"role":[{"vocabulary":"crossref","role":"author"}]},{"given":"Huaying","family":"Liu","sequence":"additional","affiliation":[],"role":[{"vocabulary":"crossref","role":"author"}]},{"given":"Young","family":"Kim","sequence":"additional","affiliation":[],"role":[{"vocabulary":"crossref","role":"author"}]},{"given":"Nicole","family":"Karras","sequence":"additional","affiliation":[],"role":[{"vocabulary":"crossref","role":"author"}]},{"given":"Anna","family":"Pawlowska","sequence":"additional","affiliation":[],"role":[{"vocabulary":"crossref","role":"author"}]},{"given":"Debbie","family":"Toomey","sequence":"additional","affiliation":[],"role":[{"vocabulary":"crossref","role":"author"}]},{"given":"Wade","family":"Kyono","sequence":"additional","affiliation":[],"role":[{"vocabulary":"crossref","role":"author"}]},{"given":"Paul","family":"Gaynon","sequence":"additional","affiliation":[],"role":[{"vocabulary":"crossref","role":"author"}]},{"given":"Joseph","family":"Rosenthal","sequence":"additional","affiliation":[],"role":[{"vocabulary":"crossref","role":"author"}]},{"given":"Anthony","family":"Stein","sequence":"additional","affiliation":[],"role":[{"vocabulary":"crossref","role":"author"}]}],"member":"297","published-online":{"date-parts":[[2018,5,2]]},"reference":[{"issue":"3","key":"604_CR1","doi-asserted-by":"publisher","first-page":"579","DOI":"10.1111\/bjd.12412","volume":"169","author":"F Julia","year":"2013","unstructured":"Julia F, Petrella T, Beylot-Barry M, Bagot M, Lipsker D, Machet L, Joly P, Dereure O, Wetterwald M, d\u2019Incan M, et al. Blastic plasmacytoid dendritic cell neoplasm: clinical features in 90 patients. Br J Dermatol. 2013;169(3):579\u201386.","journal-title":"Br J Dermatol"},{"issue":"2","key":"604_CR2","doi-asserted-by":"publisher","first-page":"239","DOI":"10.3324\/haematol.2012.072645","volume":"98","author":"L Pagano","year":"2013","unstructured":"Pagano L, Valentini CG, Pulsoni A, Fisogni S, Carluccio P, Mannelli F, Lunghi M, Pica G, Onida F, Cattaneo C, et al. Blastic plasmacytoid dendritic cell neoplasm with leukemic presentation: an Italian multicenter study. Haematologica. 2013;98(2):239\u201346.","journal-title":"Haematologica"},{"issue":"11","key":"604_CR3","doi-asserted-by":"publisher","first-page":"1873","DOI":"10.3324\/haematol.2010.026179","volume":"95","author":"AG Jegalian","year":"2010","unstructured":"Jegalian AG, Buxbaum NP, Facchetti F, Raffeld M, Pittaluga S, Wayne AS, Jaffe ES. Blastic plasmacytoid dendritic cell neoplasm in children: diagnostic features and clinical implications. Haematologica. 2010;95(11):1873\u20139.","journal-title":"Haematologica"},{"issue":"7","key":"604_CR4","doi-asserted-by":"publisher","first-page":"E38","DOI":"10.1002\/pbc.24483","volume":"60","author":"KD Wright","year":"2013","unstructured":"Wright KD, Onciu MM, Coustan-Smith E, Campana D, Raimondi SC, Inaba H, Ribeiro R, Pui CH, Sandlund JT. Successful treatment of pediatric plasmacytoid dendritic cell tumors with a contemporary regimen for acute lymphoblastic leukemia. Pediatr Blood Cancer. 2013;60(7):E38\u201341.","journal-title":"Pediatr Blood Cancer"},{"issue":"6","key":"604_CR5","doi-asserted-by":"publisher","first-page":"510","DOI":"10.1007\/s11899-017-0425-7","volume":"12","author":"N Pemmaraju","year":"2017","unstructured":"Pemmaraju N. Novel pathways and potential therapeutic strategies for blastic plasmacytoid dendritic cell neoplasm (BPDCN): CD123 and beyond. Curr Hematol Malig Rep. 2017;12(6):510\u20132.","journal-title":"Curr Hematol Malig Rep"},{"issue":"3","key":"604_CR6","doi-asserted-by":"publisher","first-page":"440","DOI":"10.1182\/blood-2012-08-448613","volume":"121","author":"D Roos-Weil","year":"2013","unstructured":"Roos-Weil D, Dietrich S, Boumendil A, Polge E, Bron D, Carreras E, Iriondo Atienza A, Arcese W, Beelen DW, Cornelissen JJ, et al. Stem cell transplantation can provide durable disease control in blastic plasmacytoid dendritic cell neoplasm: a retrospective study from the European Group for Blood and Marrow Transplantation. Blood. 2013;121(3):440\u20136.","journal-title":"Blood"},{"issue":"12","key":"604_CR7","doi-asserted-by":"publisher","first-page":"924","DOI":"10.1097\/DAD.0000000000000348","volume":"37","author":"CM Nguyen","year":"2015","unstructured":"Nguyen CM, Stuart L, Skupsky H, Lee YS, Tsuchiya A, Cassarino DS. Blastic plasmacytoid dendritic cell neoplasm in the pediatric population: a case series and review of the literature. Am J Dermatopathol. 2015;37(12):924\u20138.","journal-title":"Am J Dermatopathol"},{"issue":"1","key":"604_CR8","doi-asserted-by":"publisher","first-page":"142","DOI":"10.1111\/j.1525-1470.2011.01586.x","volume":"30","author":"T Gambichler","year":"2013","unstructured":"Gambichler T, Pantelaki I, Stucker M. Childhood blastic plasmacytoid dendritic cell neoplasm treated with allogenic stem cell transplantation. Pediatr Dermatol. 2013;30(1):142\u20134.","journal-title":"Pediatr Dermatol"},{"issue":"3","key":"604_CR9","doi-asserted-by":"publisher","first-page":"385","DOI":"10.1182\/blood-2014-04-566737","volume":"124","author":"AE Frankel","year":"2014","unstructured":"Frankel AE, Woo JH, Ahn C, Pemmaraju N, Medeiros BC, Carraway HE, Frankfurt O, Forman SJ, Yang XA, Konopleva M, et al. Activity of SL-401, a targeted therapy directed to interleukin-3 receptor, in blastic plasmacytoid dendritic cell neoplasm patients. Blood. 2014;124(3):385\u201392.","journal-title":"Blood"},{"key":"604_CR10","unstructured":"Pemmaraju NSK, Lane A, Stein A, Vasu S, Blum W, Rizzieri D, Wang E, Duvic M, Aung P, Shubert D, Spence S, Chen J, Brooks, C, Bergstein I, McDonald P, Goswami T, Sloan J, Lancet J, Kantarjian H, Konopleva M. Results of pivotal phase 2 trial of SL-401 in patients with blastic plasmacytoid dendritic cll neoplasm (BPDCN). Blood. 2017;130:1298."},{"key":"604_CR11","doi-asserted-by":"crossref","unstructured":"Pemmaraju NSK, Lane A, Stein A, Vasu S, Blum W, Rizzieri D, Wang E, Duvic M, Chen J, Shemesh S, McDonald P, Brooks C, Lancet J, Kantarjian H, Konopleva M: Ongoing phase 2 clinical trial of SL-401 in patients with blastic plasmacytoid dendritic cell neoplasm (BPDCN): stage 1 and stage 2 results. 2017. https:\/\/learningcenter.ehaweb.org\/eha\/2017\/22nd\/181478\/naveen.pemmaraju.ongoing.phase.2.clinical.trial.of.sl-401.in.patients.with.html . Accessed 26 Apr 2018.","DOI":"10.1182\/blood.V128.22.342.342"},{"issue":"5","key":"604_CR12","doi-asserted-by":"publisher","first-page":"345","DOI":"10.1097\/MPH.0000000000000560","volume":"38","author":"KK Yeo","year":"2016","unstructured":"Yeo KK, Gaynon PS, Fu CH, Wayne AS, Sun W. Bortezomib, dexamethasone, mitoxantrone, and vinorelbine (BDMV): an active reinduction regimen for children with relapsed acute lymphoblastic leukemia and asparaginase intolerance. J Pediatr Hematol Oncol. 2016;38(5):345\u20139.","journal-title":"J Pediatr Hematol Oncol"},{"issue":"4","key":"604_CR13","doi-asserted-by":"publisher","first-page":"618","DOI":"10.1016\/j.bbmt.2017.01.067","volume":"23","author":"A Stein","year":"2017","unstructured":"Stein A, Palmer J, Tsai NC, Al Malki MM, Aldoss I, Ali H, Aribi A, Farol L, Karanes C, Khaled S, et al. Phase I trial of total marrow and lymphoid irradiation transplantation conditioning in patients with relapsed\/refractory acute leukemia. Biol Blood Marrow Transplant. 2017;23(4):618\u201324.","journal-title":"Biol Blood Marrow Transplant"},{"key":"604_CR14","doi-asserted-by":"crossref","unstructured":"Stephansky J TK, Ghandi M, Montero J, vonEgypt N, Lindsay R, Brooks C, Aster J, Johannessen C, Lane A. Resistence to SL-401 in AML and BPDCN is associated with loss of the diphthamide synthesis pathway enzyme DPH1 and is reversible by azacitidine. Blood. 2017;130:797.","DOI":"10.1182\/blood.V130.Suppl_1.797.797"},{"issue":"2","key":"604_CR15","doi-asserted-by":"publisher","first-page":"156","DOI":"10.1158\/2159-8290.CD-16-0999","volume":"7","author":"J Montero","year":"2017","unstructured":"Montero J, Stephansky J, Cai T, Griffin GK, Cabal-Hierro L, Togami K, Hogdal LJ, Galinsky I, Morgan EA, Aster JC, et al. Blastic plasmacytoid dendritic cell neoplasm is dependent on BCL2 and sensitive to venetoclax. Cancer Discov. 2017;7(2):156\u201364.","journal-title":"Cancer Discov"}],"container-title":["Journal of Hematology &amp; Oncology"],"original-title":[],"language":"en","link":[{"URL":"http:\/\/link.springer.com\/content\/pdf\/10.1186\/s13045-018-0604-6.pdf","content-type":"application\/pdf","content-version":"vor","intended-application":"text-mining"},{"URL":"http:\/\/link.springer.com\/article\/10.1186\/s13045-018-0604-6\/fulltext.html","content-type":"text\/html","content-version":"vor","intended-application":"text-mining"},{"URL":"http:\/\/link.springer.com\/content\/pdf\/10.1186\/s13045-018-0604-6.pdf","content-type":"application\/pdf","content-version":"vor","intended-application":"similarity-checking"}],"deposited":{"date-parts":[[2022,8,21]],"date-time":"2022-08-21T15:25:06Z","timestamp":1661095506000},"score":1,"resource":{"primary":{"URL":"https:\/\/jhoonline.biomedcentral.com\/articles\/10.1186\/s13045-018-0604-6"}},"subtitle":[],"short-title":[],"issued":{"date-parts":[[2018,5,2]]},"references-count":15,"journal-issue":{"issue":"1","published-print":{"date-parts":[[2018,12]]}},"alternative-id":["604"],"URL":"https:\/\/doi.org\/10.1186\/s13045-018-0604-6","relation":{},"ISSN":["1756-8722"],"issn-type":[{"value":"1756-8722","type":"electronic"}],"subject":[],"published":{"date-parts":[[2018,5,2]]},"assertion":[{"value":"23 March 2018","order":1,"name":"received","label":"Received","group":{"name":"ArticleHistory","label":"Article History"}},{"value":"24 April 2018","order":2,"name":"accepted","label":"Accepted","group":{"name":"ArticleHistory","label":"Article History"}},{"value":"2 May 2018","order":3,"name":"first_online","label":"First Online","group":{"name":"ArticleHistory","label":"Article History"}},{"value":"Each patient received single patient IND approval. All signed an informed consent\/assent. This retrospective study was approved by an institutional review board of City of Hope.","order":1,"name":"Ethics","group":{"name":"EthicsHeading","label":"Ethics approval and consent to participate"}},{"value":"Consent for publication has been obtained from case 2.","order":2,"name":"Ethics","group":{"name":"EthicsHeading","label":"Consent for publication"}},{"value":"The authors declare that they have no competing interests.","order":3,"name":"Ethics","group":{"name":"EthicsHeading","label":"Competing interests"}},{"value":"Springer Nature remains neutral with regard to jurisdictional claims in published maps and institutional affiliations.","order":4,"name":"Ethics","group":{"name":"EthicsHeading","label":"Publisher\u2019s Note"}}],"article-number":"61"}}