{"status":"ok","message-type":"work","message-version":"1.0.0","message":{"indexed":{"date-parts":[[2026,8,21]],"date-time":"2026-08-21T14:48:04Z","timestamp":1787323684420,"version":"build-2736575974"},"reference-count":23,"publisher":"Ovid Technologies (Wolters Kluwer Health)","issue":"5","content-domain":{"domain":[],"crossmark-restriction":false},"short-container-title":[],"published-print":{"date-parts":[[2012,5]]},"DOI":"10.1249\/mss.0b013e31823e6579","type":"journal-article","created":{"date-parts":[[2011,10,26]],"date-time":"2011-10-26T05:18:38Z","timestamp":1319606318000},"page":"771-775","source":"Crossref","is-referenced-by-count":12,"title":["Improved Exercise Tolerance after Enzyme Replacement Therapy in Pompe Disease"],"prefix":"10.1249","volume":"44","author":[{"given":"MAURO","family":"MARZORATI","sequence":"first","affiliation":[],"role":[{"vocabulary":"crossref","role":"author"}]},{"given":"SIMONE","family":"PORCELLI","sequence":"additional","affiliation":[],"role":[{"vocabulary":"crossref","role":"author"}]},{"given":"BARBARA","family":"REGGIORI","sequence":"additional","affiliation":[],"role":[{"vocabulary":"crossref","role":"author"}]},{"given":"LUCIA","family":"MORANDI","sequence":"additional","affiliation":[],"role":[{"vocabulary":"crossref","role":"author"}]},{"given":"BRUNO","family":"GRASSI","sequence":"additional","affiliation":[],"role":[{"vocabulary":"crossref","role":"author"}]}],"member":"276","reference":[{"issue":"5","key":"R1-1-20210211","doi-asserted-by":"crossref","first-page":"377","DOI":"10.1249\/00005768-198205000-00012","article-title":"Psychophysical bases of perceived exertion.","volume":"14","author":"Borg","year":"1982","journal-title":"Med Sci Sports Exerc"},{"key":"R2-1-20210211","doi-asserted-by":"crossref","first-page":"233","DOI":"10.1016\/j.ymgme.2008.09.001","article-title":". Improvement with ongoing enzyme replacement therapy in advanced late-onset Pompe disease: a case study.","volume":"95","author":"Case","year":"2008","journal-title":"Mol Genet Metab"},{"key":"R3-1-20210211","doi-asserted-by":"crossref","first-page":"1820","DOI":"10.1152\/japplphysiol.00907.2004","article-title":"Muscle capillary blood flow kinetics estimated from pulmonary O2 uptake and near-infrared spectroscopy.","volume":"98","author":"Ferreira","year":"2005","journal-title":"J Appl Physiol"},{"key":"R4-1-20210211","doi-asserted-by":"crossref","first-page":"831","DOI":"10.1016\/j.ymthe.2006.08.009","article-title":". Autophagy and mistargeting of therapeutic enzyme in skeletal muscle in Pompe disease.","volume":"14","author":"Fukuda","year":"2006","journal-title":"Mol Ther"},{"key":"R5-1-20210211","first-page":"46","article-title":"Management of muscular dystrophy.","volume":"63","author":"Gardner-Medwin","year":"1977","journal-title":"Physiotherapy"},{"key":"R6-1-20210211","doi-asserted-by":"crossref","first-page":"510","DOI":"10.1002\/mus.20708","article-title":". Impaired oxygen extraction in metabolic myopathies: detection and quantification by near-infrared spectroscopy.","volume":"35","author":"Grassi","year":"2007","journal-title":"Muscle Nerve"},{"key":"R7-1-20210211","doi-asserted-by":"crossref","first-page":"149","DOI":"10.1152\/japplphysiol.00695.2002","article-title":". Muscle oxygenation and gas exchange kinetics during cycling exercise on-transitions in humans.","volume":"95","author":"Grassi","year":"2003","journal-title":"J Appl Physiol"},{"issue":"11","key":"R9-1-20210211","doi-asserted-by":"crossref","first-page":"2046","DOI":"10.1249\/MSS.0b013e31821fcfc1","article-title":"The slow component of VO2 kinetics: mechanistic bases and practical applications.","volume":"43","author":"Jones","year":"2011","journal-title":"Med Sci Sports Exerc"},{"key":"R10-1-20210211","doi-asserted-by":"crossref","first-page":"99","DOI":"10.1212\/01.wnl.0000251268.41188.04","article-title":". Recombinant human acid alpha-glucodisase: major clinical benefits in infantile-onset Pompe disease.","volume":"68","author":"Kishnani","year":"2007","journal-title":"Neurology"},{"key":"R12-1-20210211","doi-asserted-by":"crossref","first-page":"617","DOI":"10.1212\/01.wnl.0000299892.81127.8e","article-title":"Molecular pathology and enzyme processing in various phenotypes of acid maltase deficiency.","volume":"70","author":"Nascimbene","year":"2008","journal-title":"Neurology"},{"key":"R13-1-20210211","doi-asserted-by":"crossref","first-page":"948","DOI":"10.1183\/09031936.05.00035205","article-title":". Interpretive strategies for lung function tests.","volume":"26","author":"Pellegrino","year":"2005","journal-title":"Eur Respir J"},{"key":"R14-1-20210211","doi-asserted-by":"crossref","first-page":"48","DOI":"10.1016\/j.ymthe.2004.09.017","article-title":". Replacing acid alpha-glucosidase in Pompe disease: recombinant and transgenic enzymes are equipotent, but neither completely clears glycogen from Type II muscle fibers.","volume":"11","author":"Raben","year":"2005","journal-title":"Mol Ther"},{"key":"R15-1-20210211","doi-asserted-by":"crossref","first-page":"202","DOI":"10.1007\/s004210100458","article-title":". Non-invasive cardiac output evaluation during a maximal progressive exercise test, using a new impedance cardiograph device.","volume":"85","author":"Richard","year":"2001","journal-title":"Eur J Appl Physiol"},{"key":"R16-1-20210211","doi-asserted-by":"crossref","first-page":"565","DOI":"10.1177\/0883073807302598","article-title":". Long-term enzyme replacement therapy for Pompe disease with recombinant human alpha-glucosidase derived from Chinese hamster ovary cells.","volume":"22","author":"Rossi","year":"2007","journal-title":"J Child Neurol"},{"key":"R17-1-20210211","doi-asserted-by":"crossref","first-page":"154","DOI":"10.1117\/12.268963","article-title":"Study of an algorithm based on model experiments and diffusion theory for a portable tissue oximeter.","volume":"2","author":"Shiga","year":"1997","journal-title":"J Biomed Optics"},{"key":"R18-1-20210211","doi-asserted-by":"crossref","first-page":"70","DOI":"10.1002\/mus.20665","article-title":". Modification of the natural history of adult-onset acid maltase deficiency by nutrition and exercise therapy.","volume":"35","author":"Slonim","year":"2007","journal-title":"Muscle Nerve"},{"key":"R19-1-20210211","doi-asserted-by":"crossref","first-page":"447","DOI":"10.1016\/j.nmd.2008.04.009","article-title":". Eight years experience with enzyme replacement therapy in two children and one adult with Pompe disease.","volume":"18","author":"Van Capelle","year":"2008","journal-title":"Neuromuscul Disord"},{"key":"R20-1-20210211","doi-asserted-by":"crossref","first-page":"397","DOI":"10.1016\/S0140-6736(00)02533-2","article-title":"Recombinant human alpha-glucosidase from rabbit milk in Pompe patients.","volume":"356","author":"Van den Hout","year":"2000","journal-title":"Lancet"},{"key":"R21-1-20210211","doi-asserted-by":"crossref","first-page":"984","DOI":"10.1183\/09031936.05.00112005","article-title":"Monitoring of pulmonary function in Pompe disease: a muscle disease with new therapeutic perspectives.","volume":"26","author":"van der Ploeg","year":"2005","journal-title":"Eur Respir J"},{"key":"R22-1-20210211","doi-asserted-by":"crossref","first-page":"1396","DOI":"10.1056\/NEJMoa0909859","article-title":". A randomized study of alglucosidase alfa in late-onset Pompes disease.","volume":"362","author":"van der Ploeg","year":"2010","journal-title":"N Engl J Med"},{"key":"R23-1-20210211","doi-asserted-by":"crossref","first-page":"1342","DOI":"10.1016\/S0140-6736(08)61555-X","article-title":"Pompes disease.","volume":"372","author":"van der Ploeg","year":"2008","journal-title":"Lancet"},{"key":"R24-1-20210211","doi-asserted-by":"crossref","first-page":"743","DOI":"10.1002\/mus.10381","article-title":". Morphological changes in muscle tissue of patients with infantile Pompes disease receiving enzyme replacement therapy.","volume":"27","author":"Winkel","year":"2003","journal-title":"Muscle Nerve"},{"key":"R25-1-20210211","doi-asserted-by":"crossref","first-page":"495","DOI":"10.1002\/ana.20019","article-title":". Enzyme replacement therapy in late-onset Pompes disease: a three-year follow-up.","volume":"55","author":"Winkel","year":"2004","journal-title":"Ann Neurol"}],"container-title":["Medicine &amp; Science in Sports &amp; Exercise"],"original-title":[],"language":"en","link":[{"URL":"https:\/\/www.ovid.com\/00005768-201205000-00001","content-type":"unspecified","content-version":"vor","intended-application":"similarity-checking"}],"deposited":{"date-parts":[[2026,8,21]],"date-time":"2026-08-21T14:12:05Z","timestamp":1787321525000},"score":1,"resource":{"primary":{"URL":"https:\/\/www.ovid.com\/00005768-201205000-00001"}},"subtitle":[],"short-title":[],"issued":{"date-parts":[[2012,5]]},"references-count":23,"journal-issue":{"issue":"5","published-print":{"date-parts":[[2012]]}},"URL":"https:\/\/doi.org\/10.1249\/mss.0b013e31823e6579","relation":{},"ISSN":["0195-9131"],"issn-type":[{"value":"0195-9131","type":"print"}],"subject":[],"published":{"date-parts":[[2012,5]]}}}