{"status":"ok","message-type":"work","message-version":"1.0.0","message":{"indexed":{"date-parts":[[2025,10,29]],"date-time":"2025-10-29T03:19:37Z","timestamp":1761707977746},"reference-count":32,"publisher":"Japanese Circulation Society","issue":"11","content-domain":{"domain":[],"crossmark-restriction":false},"short-container-title":["Circ J"],"published-print":{"date-parts":[[2006]]},"DOI":"10.1253\/circj.70.1503","type":"journal-article","created":{"date-parts":[[2006,10,25]],"date-time":"2006-10-25T05:45:32Z","timestamp":1161755132000},"page":"1503-1508","source":"Crossref","is-referenced-by-count":27,"title":["Correction of Cardiac Abnormalities in Fabry Mice by Direct Intraventricular Injection of a Recombinant Lentiviral Vector That Engineers Expression of .ALPHA.-Galactosidase A"],"prefix":"10.1253","volume":"70","author":[{"given":"Makoto","family":"Yoshimitsu","sequence":"first","affiliation":[{"name":"Division of Stem Cell and Developmental Biology, Ontario Cancer Institute, University Health Network, Toronto"}],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"Koji","family":"Higuchi","sequence":"additional","affiliation":[{"name":"Division of Stem Cell and Developmental Biology, Ontario Cancer Institute, University Health Network, Toronto"}],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"Fayez","family":"Dawood","sequence":"additional","affiliation":[{"name":"The Heart and Stroke\/Richard Lewar Centre of Excellence, Toronto"}],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"Vanessa I.","family":"Rasaiah","sequence":"additional","affiliation":[{"name":"Division of Stem Cell and Developmental Biology, Ontario Cancer Institute, University Health Network, Toronto"}],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"Bilal","family":"Ayach","sequence":"additional","affiliation":[{"name":"The Heart and Stroke\/Richard Lewar Centre of Excellence, Toronto"},{"name":"The University of Toronto, Toronto"}],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"Manyin","family":"Chen","sequence":"additional","affiliation":[{"name":"The Heart and Stroke\/Richard Lewar Centre of Excellence, Toronto"},{"name":"The University of Toronto, Toronto"}],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"Peter","family":"Liu","sequence":"additional","affiliation":[{"name":"The Heart and Stroke\/Richard Lewar Centre of Excellence, Toronto"},{"name":"The University of Toronto, Toronto"}],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"Jeffrey A.","family":"Medin","sequence":"additional","affiliation":[{"name":"Division of Stem Cell and Developmental Biology, Ontario Cancer Institute, University Health Network, Toronto"},{"name":"Department of Medical Biophysics and the Institute of Medical Sciences, The University of Toronto, Toronto"}],"role":[{"role":"author","vocabulary":"crossref"}]}],"member":"330","reference":[{"key":"1","doi-asserted-by":"crossref","first-page":"1163","DOI":"10.1056\/NEJM196705252762101","volume":"276","author":"Brady RO, Gal AE, Bradley RM, Marte","year":"1967","journal-title":"N Engl J Med","ISSN":"http:\/\/id.crossref.org\/issn\/0028-4793","issn-type":"print"},{"key":"2","first-page":"3733","author":"Desnick RJ, Ioannou YA, Eng CM","year":"2001","ISSN":"http:\/\/id.crossref.org\/issn\/0028-7369","issn-type":"print"},{"issue":"6","key":"3","doi-asserted-by":"crossref","first-page":"395","DOI":"10.1056\/NEJM199102073240607","volume":"324","year":"1991","journal-title":"N Engl J Med","ISSN":"http:\/\/id.crossref.org\/issn\/0028-4793","issn-type":"print"},{"key":"4","doi-asserted-by":"crossref","first-page":"288","DOI":"10.1056\/NEJM199508033330504","volume":"333","author":"Nakao S, Takenaka T, Maeda M, Kodam","year":"1995","journal-title":"N Engl J Med","ISSN":"http:\/\/id.crossref.org\/issn\/0028-4793","issn-type":"print"},{"key":"5","doi-asserted-by":"publisher","DOI":"10.1161\/01.CIR.0000012626.81324.38"},{"key":"6","first-page":"1659","author":"Wynne J, Braunwald E","year":"2005"},{"key":"7","doi-asserted-by":"publisher","DOI":"10.1001\/jama.285.21.2743"},{"key":"8","doi-asserted-by":"publisher","DOI":"10.1056\/NEJM200107053450102"},{"key":"9","doi-asserted-by":"publisher","DOI":"10.1161\/01.CIR.0000091253.71282.04"},{"key":"10","doi-asserted-by":"publisher","DOI":"10.1073\/pnas.93.15.7917"},{"key":"11","doi-asserted-by":"publisher","DOI":"10.1073\/pnas.120177997"},{"key":"12","doi-asserted-by":"publisher","DOI":"10.1073\/pnas.061020598"},{"key":"13","doi-asserted-by":"publisher","DOI":"10.1073\/pnas.0407572101"},{"key":"14","doi-asserted-by":"crossref","unstructured":"14. Yoshimitsu M, Higuchi K, Ramsubir S, Nonaka T, Rasaiah VI, Siatskas C, et al. Efficient correction of Fabry mice and patient cells mediated by lentiviral transduction of hematopoietic stem\/progenitor cells. Gene Ther 2006; Aug 24 [Epub ahead of print].","DOI":"10.1038\/sj.gt.3302839"},{"key":"15","doi-asserted-by":"publisher","DOI":"10.1056\/NEJMoa012616"},{"key":"16","doi-asserted-by":"publisher","DOI":"10.1126\/science.1070104"},{"key":"17","doi-asserted-by":"crossref","first-page":"2181","DOI":"10.1016\/S0140-6736(04)17590-9","volume":"364","author":"Gaspar HB, Parsley KL, Howe S, King","year":"2004","journal-title":"Lancet","ISSN":"http:\/\/id.crossref.org\/issn\/0140-6736","issn-type":"print"},{"key":"18","doi-asserted-by":"publisher","DOI":"10.1056\/NEJM200301163480314"},{"key":"19","doi-asserted-by":"publisher","DOI":"10.1126\/science.1088547"},{"key":"20","doi-asserted-by":"crossref","first-page":"661","DOI":"10.1016\/S0022-2828(86)80939-7","volume":"18","author":"Jacobson SL, Piper HM","year":"1986","journal-title":"J Mol Cell Cardiol","ISSN":"http:\/\/id.crossref.org\/issn\/0022-2828","issn-type":"print"},{"key":"21","doi-asserted-by":"crossref","first-page":"2407","DOI":"10.1161\/01.CIR.91.9.2407","volume":"91","author":"Schulick AH, Newman KD, Virmani R,","year":"1995","journal-title":"Circulation","ISSN":"http:\/\/id.crossref.org\/issn\/0009-7322","issn-type":"print"},{"issue":"5259","key":"22","doi-asserted-by":"crossref","first-page":"263","DOI":"10.1126\/science.272.5259.263","volume":"272","year":"1996","journal-title":"Science","ISSN":"http:\/\/id.crossref.org\/issn\/0036-8075","issn-type":"print"},{"key":"23","doi-asserted-by":"publisher","DOI":"10.1038\/365666a0"},{"issue":"8","key":"24","doi-asserted-by":"crossref","first-page":"3053","DOI":"10.1002\/j.1460-2075.1992.tb05376.x","volume":"11","year":"1992","journal-title":"EMBO J","ISSN":"http:\/\/id.crossref.org\/issn\/0261-4189","issn-type":"print"},{"issue":"15","key":"25","doi-asserted-by":"crossref","first-page":"6992","DOI":"10.1073\/pnas.91.15.6992","volume":"91","year":"1994","journal-title":"Proc Natl Acad Sci USA","ISSN":"http:\/\/id.crossref.org\/issn\/0027-8424","issn-type":"print"},{"key":"26","doi-asserted-by":"publisher","DOI":"10.1073\/pnas.93.21.11382"},{"key":"27","doi-asserted-by":"crossref","first-page":"348","DOI":"10.1007\/s00395-002-0360-0","volume":"97","author":"Zhao J, Pettigrew GJ, Thomas J, Van","year":"2002","journal-title":"Basic Res Cardiol","ISSN":"http:\/\/id.crossref.org\/issn\/0300-8428","issn-type":"print"},{"key":"28","doi-asserted-by":"crossref","first-page":"630","DOI":"10.1038\/sj.gt.3301936","volume":"10","author":"Bonci D, Cittadini A, Latronico MVG","year":"2003","journal-title":"Gene Ther"},{"key":"29","doi-asserted-by":"publisher","DOI":"10.1073\/pnas.94.6.2540"},{"key":"30","doi-asserted-by":"crossref","first-page":"858","DOI":"10.1172\/JCI118132","volume":"96","author":"Orenstein TL, Parker TG, Butany JW,","year":"1995","journal-title":"J Clin Invest","ISSN":"http:\/\/id.crossref.org\/issn\/0021-9738","issn-type":"print"},{"key":"31","doi-asserted-by":"publisher","DOI":"10.1161\/01.CIR.0000070596.30552.8B"},{"key":"32","doi-asserted-by":"publisher","DOI":"10.1073\/pnas.222221899"}],"container-title":["Circulation Journal"],"original-title":[],"language":"en","link":[{"URL":"http:\/\/www.jstage.jst.go.jp\/article\/circj\/70\/11\/70_11_1503\/_pdf","content-type":"unspecified","content-version":"vor","intended-application":"similarity-checking"}],"deposited":{"date-parts":[[2021,3,25]],"date-time":"2021-03-25T03:36:39Z","timestamp":1616643399000},"score":1,"resource":{"primary":{"URL":"http:\/\/www.jstage.jst.go.jp\/article\/circj\/70\/11\/70_11_1503\/_article"}},"subtitle":[],"short-title":[],"issued":{"date-parts":[[2006]]},"references-count":32,"journal-issue":{"issue":"11","published-print":{"date-parts":[[2006]]}},"URL":"https:\/\/doi.org\/10.1253\/circj.70.1503","relation":{},"ISSN":["1346-9843","1347-4820"],"issn-type":[{"value":"1346-9843","type":"print"},{"value":"1347-4820","type":"electronic"}],"subject":[],"published":{"date-parts":[[2006]]}}}