{"status":"ok","message-type":"work","message-version":"1.0.0","message":{"indexed":{"date-parts":[[2026,10,5]],"date-time":"2026-10-05T18:36:53Z","timestamp":1791225413358,"version":"4.1.0"},"reference-count":81,"publisher":"Informa Healthcare","issue":"6","content-domain":{"domain":["www.tandfonline.com"],"crossmark-restriction":true},"short-container-title":["Expert Opinion on Biological Therapy"],"published-print":{"date-parts":[[2014,6]]},"DOI":"10.1517\/14712598.2014.895811","type":"journal-article","created":{"date-parts":[[2014,3,8]],"date-time":"2014-03-08T12:23:42Z","timestamp":1394281422000},"page":"789-798","update-policy":"https:\/\/doi.org\/10.1080\/tandf_crossmark_01","source":"Crossref","is-referenced-by-count":44,"title":["Gene therapy for inherited immunodeficiency"],"prefix":"10.1517","volume":"14","author":[{"given":"Fabien","family":"Touzot","sequence":"first","affiliation":[],"role":[{"vocabulary":"crossref","role":"author"}]},{"given":"Salima","family":"Hacein-Bey-Abina","sequence":"additional","affiliation":[],"role":[{"vocabulary":"crossref","role":"author"}]},{"given":"Alain","family":"Fischer","sequence":"additional","affiliation":[],"role":[{"vocabulary":"crossref","role":"author"}]},{"given":"Marina","family":"Cavazzana","sequence":"additional","affiliation":[],"role":[{"vocabulary":"crossref","role":"author"}]}],"member":"3197","published-online":{"date-parts":[[2014,3,8]]},"reference":[{"key":"CIT0001","doi-asserted-by":"publisher","DOI":"10.1586\/1744666X.2013.836061"},{"key":"CIT0002","doi-asserted-by":"publisher","DOI":"10.1146\/annurev.immunol.22.012703.104614"},{"key":"CIT0003","doi-asserted-by":"publisher","DOI":"10.1038\/nri2580"},{"key":"CIT0004","doi-asserted-by":"publisher","DOI":"10.1073\/pnas.97.1.274"},{"issue":"10","key":"CIT0005","doi-asserted-by":"crossref","first-page":"3071","DOI":"10.1182\/blood.V95.10.3071","volume":"95","author":"Soudais C","year":"2000","journal-title":"Blood"},{"issue":"11","key":"CIT0006","doi-asserted-by":"crossref","first-page":"4090","DOI":"10.1182\/blood.V92.11.4090","volume":"92","author":"Hacein-Bey S","year":"1998","journal-title":"Blood"},{"key":"CIT0007","doi-asserted-by":"publisher","DOI":"10.1056\/NEJMoa1000164"},{"issue":"97","key":"CIT0008","first-page":"97ra79","volume":"3","author":"Gaspar HB","year":"2011","journal-title":"Sci Transl Med"},{"key":"CIT0009","doi-asserted-by":"publisher","DOI":"10.1182\/blood-2004-12-4837"},{"key":"CIT0010","doi-asserted-by":"publisher","DOI":"10.1182\/blood-2006-11-058933"},{"key":"CIT0011","doi-asserted-by":"publisher","DOI":"10.1084\/jem.179.2.757"},{"key":"CIT0012","doi-asserted-by":"publisher","DOI":"10.1084\/jem.20091706"},{"key":"CIT0013","doi-asserted-by":"publisher","DOI":"10.1084\/jem.20111229"},{"key":"CIT0014","doi-asserted-by":"publisher","DOI":"10.1172\/JCI35798"},{"key":"CIT0015","doi-asserted-by":"publisher","DOI":"10.1172\/JCI35700"},{"key":"CIT0016","doi-asserted-by":"publisher","DOI":"10.1182\/blood-2009-12-257352"},{"key":"CIT0017","doi-asserted-by":"publisher","DOI":"10.1056\/NEJM200406103502422"},{"key":"CIT0018","doi-asserted-by":"publisher","DOI":"10.1126\/science.1088547"},{"issue":"97","key":"CIT0019","first-page":"97ra80","volume":"3","author":"Gaspar HB","year":"2011","journal-title":"Sci Transl Med"},{"key":"CIT0020","doi-asserted-by":"publisher","DOI":"10.1056\/NEJMoa0805817"},{"key":"CIT0021","doi-asserted-by":"publisher","DOI":"10.1172\/JCI31666"},{"key":"CIT0022","doi-asserted-by":"publisher","DOI":"10.1182\/blood-2009-02-202085"},{"key":"CIT0023","doi-asserted-by":"publisher","DOI":"10.1182\/blood-2009-06-189209"},{"key":"CIT0024","doi-asserted-by":"publisher","DOI":"10.1182\/blood-2011-12-396879"},{"key":"CIT0025","doi-asserted-by":"publisher","DOI":"10.1126\/science.1070104"},{"key":"CIT0026","doi-asserted-by":"publisher","DOI":"10.2174\/156652312799789253"},{"key":"CIT0027","doi-asserted-by":"publisher","DOI":"10.1182\/blood-2012-02-400937"},{"key":"CIT0028","doi-asserted-by":"publisher","DOI":"10.1038\/nri2724"},{"key":"CIT0029","doi-asserted-by":"publisher","DOI":"10.1182\/blood-2008-12-115253"},{"key":"CIT0030","doi-asserted-by":"publisher","DOI":"10.1182\/blood-2012-08-448118"},{"key":"CIT0031","doi-asserted-by":"publisher","DOI":"10.1182\/blood-2010-11-319376"},{"key":"CIT0032","doi-asserted-by":"publisher","DOI":"10.1038\/bmt.2012.31"},{"key":"CIT0033","doi-asserted-by":"publisher","DOI":"10.1056\/NEJMoa1003548"},{"key":"CIT0034","doi-asserted-by":"publisher","DOI":"10.1021\/mp200132u"},{"key":"CIT0035","doi-asserted-by":"publisher","DOI":"10.1038\/mt.2012.93"},{"key":"CIT0036","doi-asserted-by":"publisher","DOI":"10.1038\/nrg2985"},{"key":"CIT0037","doi-asserted-by":"publisher","DOI":"10.1016\/j.ymthe.2004.08.008"},{"key":"CIT0038","doi-asserted-by":"publisher","DOI":"10.1517\/14712598.8.2.181"},{"key":"CIT0039","doi-asserted-by":"publisher","DOI":"10.1038\/mt.2009.31"},{"key":"CIT0040","doi-asserted-by":"publisher","DOI":"10.1126\/science.1233151"},{"key":"CIT0041","doi-asserted-by":"publisher","DOI":"10.1097\/00005792-200005000-00003"},{"key":"CIT0042","doi-asserted-by":"publisher","DOI":"10.1016\/j.clim.2007.09.008"},{"key":"CIT0043","doi-asserted-by":"publisher","DOI":"10.1097\/INF.0b013e3181f13b23"},{"key":"CIT0044","doi-asserted-by":"publisher","DOI":"10.1056\/NEJMoa1007097"},{"key":"CIT0045","doi-asserted-by":"publisher","DOI":"10.1016\/j.jaci.2011.10.005"},{"key":"CIT0046","doi-asserted-by":"publisher","DOI":"10.1016\/j.jaci.2013.05.031"},{"key":"CIT0047","doi-asserted-by":"publisher","DOI":"10.1016\/S0140-6736(13)62069-3"},{"key":"CIT0048","doi-asserted-by":"publisher","DOI":"10.1038\/mt.2010.232"},{"key":"CIT0049","doi-asserted-by":"publisher","DOI":"10.1038\/nm.2088"},{"key":"CIT0050","doi-asserted-by":"publisher","DOI":"10.1182\/blood-2009-05-222760"},{"key":"CIT0051","doi-asserted-by":"publisher","DOI":"10.1038\/mt.2011.166"},{"key":"CIT0052","doi-asserted-by":"publisher","DOI":"10.1152\/physrev.00044.2005"},{"key":"CIT0053","doi-asserted-by":"publisher","DOI":"10.1038\/mt.2010.226"},{"key":"CIT0054","doi-asserted-by":"publisher","DOI":"10.1073\/pnas.83.10.3194"},{"key":"CIT0055","doi-asserted-by":"publisher","DOI":"10.1126\/science.272.5259.263"},{"issue":"11","key":"CIT0056","doi-asserted-by":"crossref","first-page":"8463","DOI":"10.1128\/JVI.72.11.8463-8471.1998","volume":"72","author":"Dull T","year":"1998","journal-title":"J Virol"},{"key":"CIT0057","doi-asserted-by":"publisher","DOI":"10.1126\/science.1083413"},{"key":"CIT0058","doi-asserted-by":"publisher","DOI":"10.1038\/mt.2009.16"},{"key":"CIT0059","doi-asserted-by":"publisher","DOI":"10.1182\/blood-2002-02-0578"},{"key":"CIT0060","doi-asserted-by":"publisher","DOI":"10.1016\/j.ymthe.2004.04.005"},{"key":"CIT0061","doi-asserted-by":"publisher","DOI":"10.1038\/nmeth.1514"},{"key":"CIT0062","doi-asserted-by":"publisher","DOI":"10.2165\/11598180-000000000-00000"},{"key":"CIT0063","doi-asserted-by":"publisher","DOI":"10.1186\/1479-5876-6-39"},{"key":"CIT0064","doi-asserted-by":"publisher","DOI":"10.1089\/hum.2013.163"},{"key":"CIT0065","doi-asserted-by":"publisher","DOI":"10.1182\/blood-2007-12-130179"},{"key":"CIT0066","doi-asserted-by":"publisher","DOI":"10.1038\/nm.2984"},{"key":"CIT0067","doi-asserted-by":"publisher","DOI":"10.1126\/science.1079512"},{"key":"CIT0068","doi-asserted-by":"publisher","DOI":"10.1126\/science.1207773"},{"key":"CIT0069","doi-asserted-by":"publisher","DOI":"10.1016\/j.jaci.2011.02.027"},{"key":"CIT0070","doi-asserted-by":"publisher","DOI":"10.1038\/nbt1353"},{"key":"CIT0071","doi-asserted-by":"publisher","DOI":"10.1182\/blood-2010-12-328161"},{"key":"CIT0072","doi-asserted-by":"publisher","DOI":"10.3389\/fimmu.2011.00054"},{"key":"CIT0073","doi-asserted-by":"publisher","DOI":"10.1038\/mt.2008.118"},{"key":"CIT0074","doi-asserted-by":"publisher","DOI":"10.1073\/pnas.0608130103"},{"key":"CIT0075","doi-asserted-by":"publisher","DOI":"10.1038\/leu.2011.106"},{"key":"CIT0076","doi-asserted-by":"publisher","DOI":"10.1038\/mt.2012.110"},{"key":"CIT0077","doi-asserted-by":"publisher","DOI":"10.1038\/mt.2013.34"},{"key":"CIT0078","doi-asserted-by":"publisher","DOI":"10.1182\/blood-2012-07-445858"},{"issue":"12","key":"CIT0079","doi-asserted-by":"crossref","first-page":"9873","DOI":"10.1128\/JVI.72.12.9873-9880.1998","volume":"72","author":"Zufferey R","year":"1998","journal-title":"J Virol"},{"key":"CIT0080","doi-asserted-by":"publisher","DOI":"10.1097\/MOH.0b013e328360aaf6"},{"key":"CIT0081","doi-asserted-by":"publisher","DOI":"10.1038\/cr.2013.139"}],"container-title":["Expert Opinion on Biological Therapy"],"original-title":[],"language":"en","link":[{"URL":"http:\/\/www.tandfonline.com\/doi\/pdf\/10.1517\/14712598.2014.895811","content-type":"unspecified","content-version":"vor","intended-application":"similarity-checking"}],"deposited":{"date-parts":[[2020,8,16]],"date-time":"2020-08-16T04:01:40Z","timestamp":1597550500000},"score":1,"resource":{"primary":{"URL":"http:\/\/www.tandfonline.com\/doi\/full\/10.1517\/14712598.2014.895811"}},"subtitle":[],"short-title":[],"issued":{"date-parts":[[2014,3,8]]},"references-count":81,"journal-issue":{"issue":"6","published-online":{"date-parts":[[2014,3,27]]},"published-print":{"date-parts":[[2014,6]]}},"alternative-id":["10.1517\/14712598.2014.895811"],"URL":"https:\/\/doi.org\/10.1517\/14712598.2014.895811","relation":{},"ISSN":["1471-2598","1744-7682"],"issn-type":[{"value":"1471-2598","type":"print"},{"value":"1744-7682","type":"electronic"}],"subject":[],"published":{"date-parts":[[2014,3,8]]},"assertion":[{"value":"The publishing and review policy for this title is described in its Aims & Scope.","order":1,"name":"peerreview_statement","label":"Peer Review Statement"},{"value":"http:\/\/www.tandfonline.com\/action\/journalInformation?show=aimsScope&journalCode=iebt20","URL":"http:\/\/www.tandfonline.com\/action\/journalInformation?show=aimsScope&journalCode=iebt20","order":2,"name":"aims_and_scope_url","label":"Aim & Scope"}]}}