{"status":"ok","message-type":"work","message-version":"1.0.0","message":{"indexed":{"date-parts":[[2026,9,26]],"date-time":"2026-09-26T03:53:57Z","timestamp":1790394837117,"version":"4.1.0"},"reference-count":6,"publisher":"American Academy of Pediatrics (AAP)","issue":"4","content-domain":{"domain":[],"crossmark-restriction":false},"short-container-title":[],"published-print":{"date-parts":[[2019,10,1]]},"DOI":"10.1542\/peds.2019-0226","type":"journal-article","created":{"date-parts":[[2019,9,10]],"date-time":"2019-09-10T12:25:13Z","timestamp":1568118313000},"source":"Crossref","is-referenced-by-count":3,"title":["Nusinersen for Type 1 Spinal Muscular Atrophy: A Father\u2019s Perspective"],"prefix":"10.1542","volume":"144","author":[{"given":"Nathan R.","family":"Hoot","sequence":"first","affiliation":[{"name":"Department of Emergency Medicine, McGovern Medical School, The University of Texas Health Science Center at Houston, Houston, Texas"}],"role":[{"vocabulary":"crossref","role":"author"}]}],"member":"417","published-online":{"date-parts":[[2019,10,1]]},"reference":[{"issue":"18","key":"2025062311031023000_B1","doi-asserted-by":"crossref","first-page":"1723","DOI":"10.1056\/NEJMoa1702752","article-title":"Nusinersen versus sham control in infantile-onset spinal muscular atrophy","volume":"377","author":"Finkel","year":"2017","journal-title":"N Engl J Med"},{"issue":"2 pt 1","key":"2025062311031023000_B2","doi-asserted-by":"crossref","first-page":"153","DOI":"10.1016\/S0022-3476(99)70016-8","article-title":"Optimality score for the neurologic examination of the infant at 12 and 18 months of age","volume":"135","author":"Haataja","year":"1999","journal-title":"J Pediatr"},{"issue":"11","key":"2025062311031023000_B3","doi-asserted-by":"crossref","first-page":"754","DOI":"10.1016\/j.nmd.2016.10.002","article-title":"Developmental milestones in type I spinal muscular atrophy","volume":"26","author":"De Sanctis","year":"2016","journal-title":"Neuromuscul Disord"},{"issue":"9","key":"2025062311031023000_B4","doi-asserted-by":"crossref","first-page":"810","DOI":"10.1212\/WNL.0000000000000741","article-title":"Observational study of spinal muscular atrophy type I and implications for clinical trials","volume":"83","author":"Finkel","year":"2014","journal-title":"Neurology"},{"issue":"2","key":"2025062311031023000_B5","doi-asserted-by":"crossref","first-page":"123","DOI":"10.1001\/jamapediatrics.2017.4360","article-title":"Nusinersen for spinal muscular atrophy: are we paying too much for too little?","volume":"172","author":"Prasad","year":"2018","journal-title":"JAMA Pediatr"},{"issue":"3","key":"2025062311031023000_B6","first-page":"141","article-title":"Pancreatic extracts in the treatment of diabetes mellitus","volume":"12","author":"Banting","year":"1922","journal-title":"Can Med Assoc J"}],"container-title":["Pediatrics"],"original-title":[],"language":"en","link":[{"URL":"https:\/\/publications.aap.org\/pediatrics\/article-pdf\/doi\/10.1542\/peds.2019-0226\/1078079\/peds_20190226.pdf","content-type":"application\/pdf","content-version":"vor","intended-application":"syndication"},{"URL":"https:\/\/publications.aap.org\/pediatrics\/article-pdf\/doi\/10.1542\/peds.2019-0226\/1078079\/peds_20190226.pdf","content-type":"unspecified","content-version":"vor","intended-application":"similarity-checking"}],"deposited":{"date-parts":[[2025,6,23]],"date-time":"2025-06-23T15:03:18Z","timestamp":1750690998000},"score":1,"resource":{"primary":{"URL":"https:\/\/publications.aap.org\/pediatrics\/article\/144\/4\/e20190226\/38454\/Nusinersen-for-Type-1-Spinal-Muscular-Atrophy-A"}},"subtitle":[],"short-title":[],"issued":{"date-parts":[[2019,10,1]]},"references-count":6,"journal-issue":{"issue":"4","published-online":{"date-parts":[[2019,10,1]]},"published-print":{"date-parts":[[2019,10,1]]}},"URL":"https:\/\/doi.org\/10.1542\/peds.2019-0226","relation":{},"ISSN":["0031-4005","1098-4275"],"issn-type":[{"value":"0031-4005","type":"print"},{"value":"1098-4275","type":"electronic"}],"subject":[],"published":{"date-parts":[[2019,10,1]]},"article-number":"e20190226"}}