{"status":"ok","message-type":"work","message-version":"1.0.0","message":{"indexed":{"date-parts":[[2026,2,24]],"date-time":"2026-02-24T15:34:05Z","timestamp":1771947245104,"version":"3.50.1"},"reference-count":127,"publisher":"Informa UK Limited","issue":"9","content-domain":{"domain":[],"crossmark-restriction":false},"short-container-title":["Expert Review of Neurotherapeutics"],"published-print":{"date-parts":[[2010,9]]},"DOI":"10.1586\/ern.10.127","type":"journal-article","created":{"date-parts":[[2010,9,7]],"date-time":"2010-09-07T09:35:02Z","timestamp":1283852102000},"page":"1449-1466","source":"Crossref","is-referenced-by-count":28,"title":["Myelin lesions associated with lysosomal and peroxisomal disorders"],"prefix":"10.1586","volume":"10","author":[{"given":"Phyllis L","family":"Faust","sequence":"first","affiliation":[],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"Edward M","family":"Kaye","sequence":"additional","affiliation":[],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"James M","family":"Powers","sequence":"additional","affiliation":[],"role":[{"role":"author","vocabulary":"crossref"}]}],"member":"301","published-online":{"date-parts":[[2014,1,9]]},"reference":[{"key":"CIT0001","doi-asserted-by":"crossref","unstructured":"Powers JM. The leukodystrophies: overview and classification. In:Myelin Biology and Disorders (Volume 2).Lazzarini RA (Ed.). Elsevier Academic Press, CA, USA, 663\u2013690 (2004).","DOI":"10.1016\/B978-012439510-7\/50081-4"},{"key":"CIT0002","doi-asserted-by":"crossref","unstructured":"van der Knaap MS, Valk J (Eds).Magnetic Resonance of Myelination and Myelin Disorders (3rdEdition). Springer, NY, USA (2005).","DOI":"10.1007\/3-540-27660-2"},{"key":"CIT0003","doi-asserted-by":"publisher","DOI":"10.1038\/ncb0905-847"},{"key":"CIT0004","first-page":"99","volume":"25","author":"Jovic","year":"2010","journal-title":"Histol. Histopathol."},{"key":"CIT0005","doi-asserted-by":"publisher","DOI":"10.1016\/j.cell.2007.12.018"},{"key":"CIT0006","doi-asserted-by":"publisher","DOI":"10.1007\/s10545-008-1040-5"},{"key":"CIT0007","doi-asserted-by":"publisher","DOI":"10.1016\/j.bbamcr.2008.12.001"},{"key":"CIT0008","doi-asserted-by":"publisher","DOI":"10.1016\/j.bbamcr.2008.11.004"},{"key":"CIT0009","doi-asserted-by":"publisher","DOI":"10.1038\/nrm2745"},{"key":"CIT0010","doi-asserted-by":"publisher","DOI":"10.1016\/j.bbamcr.2008.11.015"},{"key":"CIT0011","doi-asserted-by":"publisher","DOI":"10.1016\/j.bbamcr.2008.11.014"},{"key":"CIT0012","doi-asserted-by":"publisher","DOI":"10.1016\/j.cell.2006.02.025"},{"key":"CIT0013","doi-asserted-by":"publisher","DOI":"10.1016\/S0300-9084(03)00047-6"},{"key":"CIT0014","doi-asserted-by":"publisher","DOI":"10.1007\/s00401-004-0848-9"},{"key":"CIT0015","doi-asserted-by":"crossref","unstructured":"Suzuki K, Suzuki K. Lysosomal diseases. In:Greenfield\u2019s Neuropathology (8th Edition). Love S, Louis DN, Ellison DW (Eds). Hodder Arnold, London, UK, 515\u2013599 (2008).","DOI":"10.1201\/b13319-8"},{"key":"CIT0016","doi-asserted-by":"publisher","DOI":"10.1002\/humu.21093"},{"key":"CIT0017","doi-asserted-by":"publisher","DOI":"10.1073\/pnas.93.25.14821"},{"key":"CIT0018","doi-asserted-by":"publisher","DOI":"10.1093\/hmg\/ddn135"},{"key":"CIT0019","doi-asserted-by":"publisher","DOI":"10.1016\/j.nbd.2004.03.008"},{"key":"CIT0020","doi-asserted-by":"publisher","DOI":"10.1515\/BC.2009.009"},{"key":"CIT0021","doi-asserted-by":"publisher","DOI":"10.1042\/bj2970479"},{"key":"CIT0022","doi-asserted-by":"publisher","DOI":"10.1523\/JNEUROSCI.2329-07.2007"},{"key":"CIT0023","doi-asserted-by":"publisher","DOI":"10.1523\/JNEUROSCI.2287-07.2007"},{"key":"CIT0024","doi-asserted-by":"publisher","DOI":"10.1006\/mgme.2000.2990"},{"key":"CIT0025","doi-asserted-by":"publisher","DOI":"10.1007\/s10038-006-0396-3"},{"key":"CIT0026","doi-asserted-by":"publisher","DOI":"10.1096\/fj.01-0798com"},{"key":"CIT0027","doi-asserted-by":"publisher","DOI":"10.1007\/s00401-007-0296-4"},{"key":"CIT0028","doi-asserted-by":"publisher","DOI":"10.1016\/S1357-4310(00)01800-1"},{"key":"CIT0029","doi-asserted-by":"publisher","DOI":"10.1002\/jemt.1070320304"},{"key":"CIT0030","doi-asserted-by":"publisher","DOI":"10.1111\/j.1471-4159.2008.05279.x"},{"key":"CIT0031","doi-asserted-by":"publisher","DOI":"10.1523\/JNEUROSCI.5597-08.2009"},{"key":"CIT0032","doi-asserted-by":"publisher","DOI":"10.1111\/j.1471-4159.2007.04709.x"},{"key":"CIT0033","doi-asserted-by":"publisher","DOI":"10.1146\/annurev.biochem.74.082803.133329"},{"key":"CIT0034","doi-asserted-by":"publisher","DOI":"10.1016\/j.bbamcr.2006.09.010"},{"key":"CIT0035","doi-asserted-by":"publisher","DOI":"10.1016\/j.bbamcr.2006.08.010"},{"key":"CIT0036","doi-asserted-by":"publisher","DOI":"10.1038\/ncpneuro0421"},{"key":"CIT0037","doi-asserted-by":"publisher","DOI":"10.1002\/ana.20702"},{"key":"CIT0038","doi-asserted-by":"publisher","DOI":"10.1086\/498880"},{"key":"CIT0039","doi-asserted-by":"publisher","DOI":"10.1016\/j.bbalip.2010.01.001"},{"key":"CIT0040","doi-asserted-by":"publisher","DOI":"10.1016\/j.bbamcr.2006.09.006"},{"key":"CIT0041","doi-asserted-by":"publisher","DOI":"10.1016\/j.bbamcr.2006.08.038"},{"key":"CIT0042","doi-asserted-by":"publisher","DOI":"10.1002\/cne.21448"},{"key":"CIT0043","doi-asserted-by":"publisher","DOI":"10.1111\/j.1750-3639.1998.tb00139.x"},{"key":"CIT0044","doi-asserted-by":"crossref","first-page":"89","DOI":"10.1093\/jnen\/59.2.89","volume":"59","author":"Powers","year":"2000","journal-title":"J. Neuropathol. Exp. Neurol."},{"key":"CIT0045","doi-asserted-by":"publisher","DOI":"10.1096\/fj.08-110866"},{"key":"CIT0046","doi-asserted-by":"crossref","first-page":"1004","DOI":"10.1093\/jnen\/60.10.1004","volume":"60","author":"Ito","year":"2001","journal-title":"J. Neuropathol. Exp. Neurol."},{"key":"CIT0047","doi-asserted-by":"publisher","DOI":"10.1093\/hmg\/ddi140"},{"key":"CIT0048","doi-asserted-by":"publisher","DOI":"10.1007\/s00415-009-5114-6"},{"key":"CIT0049","doi-asserted-by":"crossref","unstructured":"Powers JM. Peroxisomal diseases. In:Greenfield\u2019s Neuropathology (8th Edition). Love S, Louis DN, Ellison DW (Eds). Hodder Arnold, London, UK, 643\u2013673 (2008).","DOI":"10.1201\/b13319-10"},{"key":"CIT0050","doi-asserted-by":"publisher","DOI":"10.1097\/01.jnen.0000190064.28559.a4"},{"key":"CIT0051","doi-asserted-by":"publisher","DOI":"10.1038\/labinvest.3700512"},{"key":"CIT0052","doi-asserted-by":"publisher","DOI":"10.1093\/hmg\/ddn085"},{"key":"CIT0053","doi-asserted-by":"crossref","first-page":"493","DOI":"10.1093\/jnen\/60.5.493","volume":"60","author":"Powers","year":"2001","journal-title":"J. Neuropathol. Exp. Neurol."},{"key":"CIT0054","doi-asserted-by":"publisher","DOI":"10.1016\/j.nbd.2007.07.007"},{"key":"CIT0055","doi-asserted-by":"publisher","DOI":"10.1097\/WCO.0b013e328300c71f"},{"key":"CIT0056","doi-asserted-by":"publisher","DOI":"10.1177\/1073858409336297"},{"key":"CIT0057","doi-asserted-by":"publisher","DOI":"10.1038\/ng2070"},{"key":"CIT0058","doi-asserted-by":"publisher","DOI":"10.1523\/JNEUROSCI.4968-07.2008"},{"key":"CIT0059","doi-asserted-by":"publisher","DOI":"10.1093\/brain\/awn295"},{"key":"CIT0060","doi-asserted-by":"crossref","first-page":"1766","DOI":"10.1111\/j.1471-4159.2008.05513.x","volume":"106","author":"Khan","year":"2008","journal-title":"J. Neurochem."},{"key":"CIT0061","doi-asserted-by":"publisher","DOI":"10.2353\/ajpath.2006.041220"},{"key":"CIT0062","doi-asserted-by":"publisher","DOI":"10.1016\/j.ymgme.2006.10.001"},{"key":"CIT0063","doi-asserted-by":"publisher","DOI":"10.1152\/ajpendo.90736.2008"},{"key":"CIT0064","doi-asserted-by":"publisher","DOI":"10.1126\/science.172.3989.1263"},{"key":"CIT0065","doi-asserted-by":"publisher","DOI":"10.1146\/annurev.med.57.110104.115650"},{"key":"CIT0066","doi-asserted-by":"publisher","DOI":"10.1093\/glycob\/cwp171"},{"key":"CIT0067","doi-asserted-by":"publisher","DOI":"10.1056\/NEJM199001043220106"},{"key":"CIT0068","doi-asserted-by":"publisher","DOI":"10.1038\/bmt.2008.275"},{"key":"CIT0069","doi-asserted-by":"publisher","DOI":"10.1016\/j.jpeds.2007.04.054"},{"key":"CIT0070","doi-asserted-by":"publisher","DOI":"10.1038\/sj.bmt.1703839"},{"key":"CIT0071","doi-asserted-by":"crossref","unstructured":"Peters C. Hematopoietic stem cell transplantation for storage diseases. In:Thomas\u2019 Hematopoietic Cell Transplantation: Stem Cell Transplantation (4th Edition).Appelbaum FR, Forman SJ, Negrin RS (Eds). Wiley, Oxford, UK, 1136\u20131162 (2009).","DOI":"10.1002\/9781444303537.ch77"},{"key":"CIT0072","doi-asserted-by":"publisher","DOI":"10.1038\/mt.2008.305"},{"key":"CIT0073","doi-asserted-by":"publisher","DOI":"10.1007\/s11011-008-9107-4"},{"key":"CIT0074","doi-asserted-by":"publisher","DOI":"10.1093\/hmg\/ddq099"},{"key":"CIT0075","doi-asserted-by":"publisher","DOI":"10.1093\/hmg\/ddp475"},{"key":"CIT0076","doi-asserted-by":"publisher","DOI":"10.1002\/jgm.1325"},{"key":"CIT0077","doi-asserted-by":"publisher","DOI":"10.1172\/JCI28873"},{"key":"CIT0078","doi-asserted-by":"publisher","DOI":"10.1111\/j.1750-3639.1995.tb00601.x"},{"key":"CIT0079","doi-asserted-by":"publisher","DOI":"10.1016\/j.ymgme.2005.06.023"},{"key":"CIT0080","doi-asserted-by":"publisher","DOI":"10.2165\/00003495-200262050-00002"},{"key":"CIT0081","doi-asserted-by":"publisher","DOI":"10.1542\/peds.2006-0747"},{"key":"CIT0082","doi-asserted-by":"publisher","DOI":"10.1038\/sj.bmt.1705970"},{"key":"CIT0083","doi-asserted-by":"publisher","DOI":"10.1038\/sj.bmt.1705984"},{"key":"CIT0084","doi-asserted-by":"publisher","DOI":"10.1096\/fj.04-2591hyp"},{"key":"CIT0085","doi-asserted-by":"publisher","DOI":"10.1096\/fj.06-6169com"},{"key":"CIT0086","doi-asserted-by":"publisher","DOI":"10.1016\/j.ymthe.2004.12.020"},{"key":"CIT0087","doi-asserted-by":"publisher","DOI":"10.1203\/00006450-200201000-00009"},{"key":"CIT0088","doi-asserted-by":"publisher","DOI":"10.1016\/j.brainres.2009.09.017"},{"key":"CIT0089","doi-asserted-by":"publisher","DOI":"10.1016\/j.ymgme.2010.03.021"},{"key":"CIT0090","doi-asserted-by":"publisher","DOI":"10.1212\/WNL.34.11.1410"},{"key":"CIT0091","doi-asserted-by":"publisher","DOI":"10.1056\/NEJM199006283222607"},{"key":"CIT0092","doi-asserted-by":"publisher","DOI":"10.1186\/1476-511X-7-48"},{"key":"CIT0093","doi-asserted-by":"publisher","DOI":"10.1016\/S0140-6736(00)02629-5"},{"key":"CIT0094","doi-asserted-by":"publisher","DOI":"10.1182\/blood-2003-10-3402"},{"key":"CIT0095","doi-asserted-by":"publisher","DOI":"10.1016\/S1474-4422(07)70177-1"},{"key":"CIT0096","doi-asserted-by":"publisher","DOI":"10.1586\/14737175.8.9.1367"},{"key":"CIT0097","doi-asserted-by":"publisher","DOI":"10.2217\/clp.09.11"},{"key":"CIT0098","doi-asserted-by":"publisher","DOI":"10.1126\/science.1171242"},{"key":"CIT0099","doi-asserted-by":"publisher","DOI":"10.1001\/archneur.62.7.1073"},{"key":"CIT0100","doi-asserted-by":"publisher","DOI":"10.1007\/s12031-007-0041-4"},{"key":"CIT0102","first-page":"471","volume":"10","author":"Cartier","year":"2008","journal-title":"Curr. Opin. Mol. Ther."},{"key":"CIT0103","doi-asserted-by":"publisher","DOI":"10.1016\/j.braindev.2009.03.001"},{"key":"CIT0104","doi-asserted-by":"publisher","DOI":"10.1016\/j.ymgme.2004.09.015"},{"key":"CIT0105","doi-asserted-by":"publisher","DOI":"10.1002\/emmm.201000061"},{"key":"CIT0106","doi-asserted-by":"publisher","DOI":"10.1111\/j.1471-4159.2006.03986.x"},{"key":"CIT0107","doi-asserted-by":"publisher","DOI":"10.1016\/j.nbd.2005.07.016"},{"key":"CIT0108","doi-asserted-by":"publisher","DOI":"10.1089\/scd.2006.0092"},{"key":"CIT0109","doi-asserted-by":"publisher","DOI":"10.1016\/j.ymgme.2009.01.005"},{"key":"CIT0110","doi-asserted-by":"publisher","DOI":"10.1016\/j.brainres.2006.03.116"},{"key":"CIT0111","doi-asserted-by":"publisher","DOI":"10.1038\/sj.gt.3302834"},{"key":"CIT0112","doi-asserted-by":"publisher","DOI":"10.1159\/000150127"},{"key":"CIT0113","doi-asserted-by":"publisher","DOI":"10.1016\/j.ymgme.2006.02.013"},{"key":"CIT0114","doi-asserted-by":"publisher","DOI":"10.1373\/clinchem.2009.141622"},{"key":"CIT0115","doi-asserted-by":"publisher","DOI":"10.1007\/BF03256261"},{"key":"CIT0116","doi-asserted-by":"publisher","DOI":"10.1016\/j.ymgme.2009.03.010"},{"key":"CIT0117","doi-asserted-by":"publisher","DOI":"10.1016\/j.pediatrneurol.2008.11.010"},{"key":"CIT0118","doi-asserted-by":"publisher","DOI":"10.1523\/JNEUROSCI.3379-07.2007"},{"key":"CIT0119","doi-asserted-by":"publisher","DOI":"10.1002\/eji.200939639"},{"key":"CIT0120","doi-asserted-by":"publisher","DOI":"10.1111\/j.1399-0039.2009.01256.x"},{"key":"CIT0121","doi-asserted-by":"publisher","DOI":"10.1002\/jnr.20529"},{"key":"CIT0122","doi-asserted-by":"publisher","DOI":"10.1016\/j.molmed.2009.05.002"},{"key":"CIT0123","doi-asserted-by":"publisher","DOI":"10.2217\/17460751.2.5.817"},{"key":"CIT0124","doi-asserted-by":"publisher","DOI":"10.1002\/ana.21677"},{"key":"CIT0125","doi-asserted-by":"publisher","DOI":"10.1093\/hmg\/ddq082"},{"key":"CIT0126","doi-asserted-by":"publisher","DOI":"10.1677\/JME-09-0067"},{"key":"CIT0127","unstructured":"Damjanov I. Central nervous system. In:Anderson\u2019s Pathology.Damjanov I, Linder J, Anderson WAD (Eds). CRC Press, MO, USA, 2693\u20132798 (1996)"},{"key":"CIT0128","unstructured":"Rosenberg R. Metabolic disease of the nervous system. In:The Clinical Neurosciences.Churchill Livingstone, NY, USA, 447\u2013493 (1983)"}],"container-title":["Expert Review of Neurotherapeutics"],"original-title":[],"language":"en","link":[{"URL":"http:\/\/www.tandfonline.com\/doi\/pdf\/10.1586\/ern.10.127","content-type":"unspecified","content-version":"vor","intended-application":"similarity-checking"}],"deposited":{"date-parts":[[2024,3,30]],"date-time":"2024-03-30T06:04:12Z","timestamp":1711778652000},"score":1,"resource":{"primary":{"URL":"http:\/\/www.tandfonline.com\/doi\/full\/10.1586\/ern.10.127"}},"subtitle":[],"short-title":[],"issued":{"date-parts":[[2010,9]]},"references-count":127,"journal-issue":{"issue":"9","published-online":{"date-parts":[[2014,1,9]]},"published-print":{"date-parts":[[2010,9]]}},"alternative-id":["10.1586\/ern.10.127"],"URL":"https:\/\/doi.org\/10.1586\/ern.10.127","relation":{},"ISSN":["1473-7175","1744-8360"],"issn-type":[{"value":"1473-7175","type":"print"},{"value":"1744-8360","type":"electronic"}],"subject":[],"published":{"date-parts":[[2010,9]]}}}