{"status":"ok","message-type":"work","message-version":"1.0.0","message":{"indexed":{"date-parts":[[2026,6,12]],"date-time":"2026-06-12T21:23:55Z","timestamp":1781299435457,"version":"3.54.1"},"reference-count":17,"publisher":"Academy of Managed Care Pharmacy","issue":"4","content-domain":{"domain":[],"crossmark-restriction":false},"short-container-title":["JMCP"],"published-print":{"date-parts":[[2020,4]]},"DOI":"10.18553\/jmcp.2020.26.4.361","type":"journal-article","created":{"date-parts":[[2020,3,30]],"date-time":"2020-03-30T13:22:22Z","timestamp":1585574542000},"page":"361-366","source":"Crossref","is-referenced-by-count":7,"title":["The Effectiveness and Value of Deflazacort and Exon-Skipping Therapies for the Management of Duchenne Muscular Dystrophy"],"prefix":"10.18553","volume":"26","author":[{"given":"Foluso","family":"Agboola","sequence":"first","affiliation":[{"name":"Institute for Clinical and Economic Review, Boston, Massachusetts."}],"role":[{"vocabulary":"crossref","role":"author"}]},{"given":"Grace A.","family":"Lin","sequence":"additional","affiliation":[{"name":"Department of Medicine and Philip R Lee Institute for Health Policy Studies, University of California, San Francisco."}],"role":[{"vocabulary":"crossref","role":"author"}]},{"given":"Noemi","family":"Fluetsch","sequence":"additional","affiliation":[{"name":"Institute for Clinical and Economic Review, Boston, Massachusetts."}],"role":[{"vocabulary":"crossref","role":"author"}]},{"given":"Surrey M.","family":"Walton","sequence":"additional","affiliation":[{"name":"Center for Pharmacoepidemiology and Pharmacoeconomic Research, University of Illinois at Chicago."}],"role":[{"vocabulary":"crossref","role":"author"}]},{"given":"David M.","family":"Rind","sequence":"additional","affiliation":[{"name":"Institute for Clinical and Economic Review, Boston, Massachusetts."}],"role":[{"vocabulary":"crossref","role":"author"}]},{"given":"Steven D.","family":"Pearson","sequence":"additional","affiliation":[{"name":"Institute for Clinical and Economic Review, Boston, Massachusetts."}],"role":[{"vocabulary":"crossref","role":"author"}]}],"member":"7818","reference":[{"key":"R1","doi-asserted-by":"publisher","DOI":"10.1056\/NEJM198805263182104"},{"key":"R2","doi-asserted-by":"publisher","DOI":"10.1002\/ana.23528"},{"key":"R3","doi-asserted-by":"publisher","DOI":"10.1016\/j.jpeds.2009.02.007"},{"key":"R4","doi-asserted-by":"publisher","DOI":"10.1016\/j.ejpn.2011.07.001"},{"key":"R5","doi-asserted-by":"publisher","DOI":"10.1016\/j.rmed.2005.09.030"},{"key":"R6","doi-asserted-by":"publisher","DOI":"10.1016\/j.nmd.2015.06.412"},{"key":"R7","author":"Lin G","year":"2019","journal-title":"Institute for Clinical and Economic Review"},{"key":"R8","doi-asserted-by":"publisher","DOI":"10.1212\/WNL.0000000000003217"},{"issue":"1","key":"R9","first-page":"5","volume":"6","author":"Karimzadeh P","year":"2012","journal-title":"Iran J Child Neurol"},{"key":"R10","doi-asserted-by":"publisher","DOI":"10.1002\/1097-4598(200009)23:9<1344::AID-MUS4>3.0.CO;2-F"},{"key":"R11","doi-asserted-by":"publisher","DOI":"10.1016\/S0140-6736(17)32160-8"},{"key":"R12","doi-asserted-by":"publisher","DOI":"10.1177\/0883073814558120"},{"key":"R13","doi-asserted-by":"publisher","DOI":"10.1212\/WNL.0000000000001950"},{"key":"R14","doi-asserted-by":"publisher","DOI":"10.1002\/ana.23982"},{"key":"R15","doi-asserted-by":"publisher","DOI":"10.1002\/ana.24555"},{"key":"R16","doi-asserted-by":"publisher","DOI":"10.3233\/JND-180351"},{"key":"R17","doi-asserted-by":"crossref","first-page":"S42.004","DOI":"10.1212\/WNL.88.16_supplement.S42.004","volume":"88","author":"Mendell J","year":"2017","journal-title":"Neurology"}],"container-title":["Journal of Managed Care &amp; Specialty Pharmacy"],"original-title":[],"language":"en","deposited":{"date-parts":[[2024,8,3]],"date-time":"2024-08-03T02:32:40Z","timestamp":1722652360000},"score":1,"resource":{"primary":{"URL":"https:\/\/www.jmcp.org\/doi\/10.18553\/jmcp.2020.26.4.361"}},"subtitle":["<i>A Summary from the Institute for Clinical and Economic Review\u2019s New England Comparative Effectiveness Public Advisory Council<\/i>"],"short-title":[],"issued":{"date-parts":[[2020,4]]},"references-count":17,"journal-issue":{"issue":"4","published-print":{"date-parts":[[2020,4]]}},"alternative-id":["10.18553\/jmcp.2020.26.4.361"],"URL":"https:\/\/doi.org\/10.18553\/jmcp.2020.26.4.361","relation":{},"ISSN":["2376-0540","2376-1032"],"issn-type":[{"value":"2376-0540","type":"print"},{"value":"2376-1032","type":"electronic"}],"subject":[],"published":{"date-parts":[[2020,4]]}}}