{"status":"ok","message-type":"work","message-version":"1.0.0","message":{"indexed":{"date-parts":[[2026,2,5]],"date-time":"2026-02-05T04:31:58Z","timestamp":1770265918678,"version":"3.49.0"},"reference-count":14,"publisher":"Academy of Managed Care Pharmacy","issue":"2","content-domain":{"domain":[],"crossmark-restriction":false},"short-container-title":["JMCP"],"published-print":{"date-parts":[[2026,2]]},"DOI":"10.18553\/jmcp.2026.32.2.230","type":"journal-article","created":{"date-parts":[[2026,2,4]],"date-time":"2026-02-04T15:32:00Z","timestamp":1770219120000},"page":"230-235","source":"Crossref","is-referenced-by-count":0,"title":["The effectiveness and value of therapies for spinal muscular atrophy"],"prefix":"10.18553","volume":"32","author":[{"given":"Jeffrey A.","family":"Tice","sequence":"first","affiliation":[{"name":"Division of General Internal Medicine, University of California, San Francisco"}],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"Linda","family":"Luu","sequence":"additional","affiliation":[{"name":"Comparative Health Outcomes, Policy, and Economics (CHOICE) Institute, School of Pharmacy, University of Washington, Seattle"}],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"Sol","family":"Sanchez","sequence":"additional","affiliation":[{"name":"Institute for Clinical and Economic Review, Boston, MA"}],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"Woojung","family":"Lee","sequence":"additional","affiliation":[{"name":"Institute for Clinical and Economic Review, Boston, MA"}],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"Dmitriy","family":"Nikitin","sequence":"additional","affiliation":[{"name":"Institute for Clinical and Economic Review, Boston, MA"}],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"Marie","family":"Phillips","sequence":"additional","affiliation":[{"name":"Institute for Clinical and Economic Review, Boston, MA"}],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"Josh J.","family":"Carlson","sequence":"additional","affiliation":[{"name":"Comparative Health Outcomes, Policy, and Economics (CHOICE) Institute, School of Pharmacy, University of Washington, Seattle"}],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"Hui-Hsuan","family":"Chan","sequence":"additional","affiliation":[{"name":"Comparative Health Outcomes, Policy, and Economics (CHOICE) Institute, School of Pharmacy, University of Washington, Seattle"}],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"David M.","family":"Rind","sequence":"additional","affiliation":[{"name":"Institute for Clinical and Economic Review, Boston, MA"}],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"Foluso","family":"Agboola","sequence":"additional","affiliation":[{"name":"Institute for Clinical and Economic Review, Boston, MA"}],"role":[{"role":"author","vocabulary":"crossref"}]}],"member":"7818","reference":[{"key":"r1","doi-asserted-by":"publisher","DOI":"10.1016\/S1474-4422(12)70061-3"},{"key":"r2","doi-asserted-by":"publisher","DOI":"10.1186\/s13023-017-0671-8"},{"key":"r3","doi-asserted-by":"publisher","DOI":"10.1001\/jamapediatrics.2024.1911"},{"key":"r4","doi-asserted-by":"publisher","DOI":"10.1038\/344540a0"},{"key":"r5","doi-asserted-by":"publisher","DOI":"10.1016\/0092-8674(95)90460-3"},{"key":"r6","doi-asserted-by":"publisher","DOI":"10.1086\/302369"},{"key":"r7","unstructured":"Cure SMA. 100% of States Now Screening Newborns for SMA. https:\/\/www.curesma.org\/100-of-states-now-screening-newborns-for-sma\/"},{"key":"r8","unstructured":"Cure SMA.\n                      State of SMA 2024 Report\n                      . 2025. https:\/\/www.curesma.org\/wp-content\/uploads\/2025\/04\/State-of-SMA-Report2024_vWeb-1.pdf"},{"key":"r9","doi-asserted-by":"publisher","DOI":"10.18553\/jmcp.2019.25.12.1300"},{"key":"r10","doi-asserted-by":"publisher","DOI":"10.1056\/NEJMoa1706198"},{"key":"r11","doi-asserted-by":"publisher","DOI":"10.1016\/S1474-4422(25)00225-X"},{"key":"r12","doi-asserted-by":"publisher","DOI":"10.1172\/JCI193956"},{"key":"r13","doi-asserted-by":"publisher","DOI":"10.1007\/s00415-024-12318-z"},{"key":"r14","doi-asserted-by":"publisher","DOI":"10.1186\/s12883-025-04276-4"}],"container-title":["Journal of Managed Care & Specialty Pharmacy"],"original-title":[],"language":"en","deposited":{"date-parts":[[2026,2,4]],"date-time":"2026-02-04T15:32:05Z","timestamp":1770219125000},"score":1,"resource":{"primary":{"URL":"https:\/\/www.jmcp.org\/doi\/10.18553\/jmcp.2026.32.2.230"}},"subtitle":["A Summary From the Institute for Clinical and Economic Review\u2019s Midwest Comparative Effectiveness Public Advisory Council"],"short-title":[],"issued":{"date-parts":[[2026,2]]},"references-count":14,"journal-issue":{"issue":"2","published-print":{"date-parts":[[2026,2]]}},"alternative-id":["10.18553\/jmcp.2026.32.2.230"],"URL":"https:\/\/doi.org\/10.18553\/jmcp.2026.32.2.230","relation":{},"ISSN":["2376-0540","2376-1032"],"issn-type":[{"value":"2376-0540","type":"print"},{"value":"2376-1032","type":"electronic"}],"subject":[],"published":{"date-parts":[[2026,2]]}}}