{"status":"ok","message-type":"work","message-version":"1.0.0","message":{"indexed":{"date-parts":[[2026,3,28]],"date-time":"2026-03-28T06:18:20Z","timestamp":1774678700805,"version":"3.50.1"},"reference-count":29,"publisher":"Informa UK Limited","issue":"3","license":[{"start":{"date-parts":[[2019,6,1]],"date-time":"2019-06-01T00:00:00Z","timestamp":1559347200000},"content-version":"vor","delay-in-days":0,"URL":"http:\/\/creativecommons.org\/licenses\/by-nc-nd\/4.0\/"}],"content-domain":{"domain":["www.tandfonline.com"],"crossmark-restriction":true},"short-container-title":["Neurodegener. Dis. Manag."],"published-print":{"date-parts":[[2019,6]]},"DOI":"10.2217\/nmt-2019-0002","type":"journal-article","created":{"date-parts":[[2019,6,5]],"date-time":"2019-06-05T14:31:11Z","timestamp":1559745071000},"page":"123-133","update-policy":"https:\/\/doi.org\/10.1080\/tandf_crossmark_01","source":"Crossref","is-referenced-by-count":20,"title":["Current Management of Duchenne Muscular Dystrophy in the Middle East: Expert Report"],"prefix":"10.1080","volume":"9","author":[{"given":"Mohammed Al","family":"Jumah","sequence":"first","affiliation":[{"name":"King Fahad Medical City\rRiyadh\rSaudi Arabia"}],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"Mohammad Al","family":"Muhaizea","sequence":"additional","affiliation":[{"name":"King Faisal Specialist Hospital &amp; Research Centre\rRiyadh\rSaudi Arabia"}],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"Ahmed Al","family":"Rumayyan","sequence":"additional","affiliation":[{"name":"National Guard Health Affairs\rRiyadh\rSaudi Arabia"}],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"Abdulaziz Al","family":"Saman","sequence":"additional","affiliation":[{"name":"King Fahad Medical City\rRiyadh\rSaudi Arabia"}],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"Ali Al","family":"Shehri","sequence":"additional","affiliation":[{"name":"King Faisal Specialist Hospital &amp; Research Centre\rRiyadh\rSaudi Arabia"}],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"Edward","family":"Cupler","sequence":"additional","affiliation":[{"name":"King Faisal Specialist Hospital &amp; Research Centre\rTihamah\rSaudi Arabia"}],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"Mohammed","family":"Jan","sequence":"additional","affiliation":[{"name":"Pedia Care Clinic\rTihamah\rSaudi Arabia"}],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"Abubaker Al","family":"Madani","sequence":"additional","affiliation":[{"name":"Rashid Hospital\rDubai\rUnited Arab Emirates"}],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"Waseem","family":"Fathalla","sequence":"additional","affiliation":[{"name":"Mafraq Hospital\rAbu Dhabi\rUnited Arab Emirates"}],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"Pawan","family":"Kashyape","sequence":"additional","affiliation":[{"name":"Latifa Hospital\rDubai\rUnited Arab Emirates"}],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"Gururaj","family":"Kodavooru","sequence":"additional","affiliation":[{"name":"Latifa Hospital\rDubai\rUnited Arab Emirates"}],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"Khalid Al","family":"Thihli","sequence":"additional","affiliation":[{"name":"Sultan Qaboos University Hospital Genetic Centre\rMuscat\rOman"}],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"Laila","family":"Bastaki","sequence":"additional","affiliation":[{"name":"Kuwait Medical Genetic Centre\rKuwait"}],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"Andre","family":"Megarbane","sequence":"additional","affiliation":[{"name":"Universit\u00e9 Saint-Joseph\rBeirut\rLebanon"}],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"Cristina","family":"Skrypnyk","sequence":"additional","affiliation":[{"name":"Center of Princess Al-Jawhara (ACMID) Arabian Gulf University\rBahrain"}],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"Gholamreza","family":"Zamani","sequence":"additional","affiliation":[{"name":"Children\u2019s Medical Center Tehran University of Medical Sciences\rTehran\rIran"}],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"Sylvie","family":"Tuffery-Giraud","sequence":"additional","affiliation":[{"name":"Laboratoire de G\u00e9n\u00e9tique de Maladies Rares IURC\rOccitanie\rFrance"}],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"Andoni","family":"Urtizberea","sequence":"additional","affiliation":[{"name":"H\u00f4pital Marin de Hendaye Route de la Corniche\rHendaye\r64700\rFrance"}],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"Carlos Ignacio","family":"Ortez Gonz\u00e1lez","sequence":"additional","affiliation":[{"name":"Unidad de Patolog\u00eda Neuromuscular Servicio de Neurolog\u00eda Hospital Sant Joan de D\u00e9u\rBarcelona\rSpain"}],"role":[{"role":"author","vocabulary":"crossref"}]}],"member":"301","published-online":{"date-parts":[[2019,6,5]]},"reference":[{"key":"e_1_3_4_2_1","doi-asserted-by":"publisher","DOI":"10.1016\/S1474-4422(09)70271-6"},{"key":"e_1_3_4_3_1","doi-asserted-by":"publisher","DOI":"10.1016\/j.neubiorev.2013.03.016"},{"key":"e_1_3_4_4_1","doi-asserted-by":"publisher","DOI":"10.1371\/journal.pone.0008803"},{"key":"e_1_3_4_5_1","doi-asserted-by":"publisher","DOI":"10.1164\/rccm.200503-322OC"},{"key":"e_1_3_4_6_1","doi-asserted-by":"publisher","DOI":"10.1002\/ppul.23413"},{"key":"e_1_3_4_7_1","doi-asserted-by":"publisher","DOI":"10.1136\/archdischild-2014-306366"},{"key":"e_1_3_4_8_1","doi-asserted-by":"publisher","DOI":"10.3390\/molecules201018168"},{"key":"e_1_3_4_9_1","doi-asserted-by":"publisher","DOI":"10.2147\/TCRM.S55889"},{"key":"e_1_3_4_10_1","doi-asserted-by":"publisher","DOI":"10.1002\/mus.21544"},{"key":"e_1_3_4_11_1","doi-asserted-by":"publisher","DOI":"10.1002\/mus.23902"},{"key":"e_1_3_4_12_1","doi-asserted-by":"publisher","DOI":"10.17925\/ENR.2014.09.01.78"},{"key":"e_1_3_4_13_1","doi-asserted-by":"publisher","DOI":"10.1097\/00002060-200211001-00012"},{"key":"e_1_3_4_14_1","doi-asserted-by":"publisher","DOI":"10.1080\/165019701750300609"},{"key":"e_1_3_4_15_1","doi-asserted-by":"publisher","DOI":"10.1016\/j.ejpn.2011.07.001"},{"key":"e_1_3_4_16_1","doi-asserted-by":"publisher","DOI":"10.1177\/0883073810371004"},{"key":"e_1_3_4_17_1","doi-asserted-by":"publisher","DOI":"10.1136\/jnnp-2012-303902"},{"key":"e_1_3_4_18_1","doi-asserted-by":"publisher","DOI":"10.1002\/mus.23831"},{"key":"e_1_3_4_19_1","doi-asserted-by":"publisher","DOI":"10.1212\/WNL.0b013e318282334e"},{"key":"e_1_3_4_20_1","doi-asserted-by":"publisher","DOI":"10.1016\/j.nmd.2010.09.006"},{"key":"e_1_3_4_21_1","doi-asserted-by":"publisher","DOI":"10.1016\/j.rehab.2013.06.002"},{"key":"e_1_3_4_22_1","doi-asserted-by":"publisher","DOI":"10.1007\/s00415-014-7585-3"},{"key":"e_1_3_4_23_1","first-page":"121","article-title":"Improvement of survival in Duchenne Muscular Dystrophy: retrospective analysis of 835 patients","volume":"31","author":"Passamano L","year":"2012","unstructured":"Passamano L , TagliaA, PalladinoAet al. Improvement of survival in Duchenne Muscular Dystrophy: retrospective analysis of 835 patients. Acta Myol., 31, 121\u2013125 (2012).","journal-title":"Acta Myol."},{"key":"e_1_3_4_24_1","doi-asserted-by":"publisher","DOI":"10.1016\/j.nmd.2012.06.256"},{"key":"e_1_3_4_25_1","first-page":"117","article-title":"Survival in Duchenne muscular dystrophy","volume":"31","author":"Rall S","year":"2012","unstructured":"Rall S , GrimmT. Survival in Duchenne muscular dystrophy. Acta Myol., 31, 117\u2013120 (2012).","journal-title":"Acta Myol."},{"key":"e_1_3_4_26_1","doi-asserted-by":"publisher","DOI":"10.1016\/j.nmd.2007.03.002"},{"key":"e_1_3_4_27_1","doi-asserted-by":"publisher","DOI":"10.1177\/0883073810371129"},{"key":"e_1_3_4_28_1","doi-asserted-by":"publisher","DOI":"10.1016\/j.nmd.2014.11.011"},{"key":"e_1_3_4_29_1","doi-asserted-by":"publisher","DOI":"10.1002\/mus.23810"},{"key":"e_1_3_4_30_1","first-page":"965235","article-title":"Corticosteroid treatment impact on spinal deformity in Duchenne muscular dystrophy","volume":"2014","author":"Sanzarello I","year":"2014","unstructured":"Sanzarello I , MerliniL, TrainaF, RosaMA, FaldiniC. Corticosteroid treatment impact on spinal deformity in Duchenne muscular dystrophy. Int. Sch. Res. Notices, 2014, 965235 (2014).","journal-title":"Int. Sch. Res. Notices"}],"container-title":["Neurodegenerative Disease Management"],"original-title":[],"language":"en","link":[{"URL":"https:\/\/www.tandfonline.com\/doi\/pdf\/10.2217\/nmt-2019-0002","content-type":"unspecified","content-version":"vor","intended-application":"similarity-checking"}],"deposited":{"date-parts":[[2024,5,23]],"date-time":"2024-05-23T19:45:52Z","timestamp":1716493552000},"score":1,"resource":{"primary":{"URL":"https:\/\/www.tandfonline.com\/doi\/full\/10.2217\/nmt-2019-0002"}},"subtitle":[],"short-title":[],"issued":{"date-parts":[[2019,6]]},"references-count":29,"journal-issue":{"issue":"3","published-print":{"date-parts":[[2019,6]]}},"alternative-id":["10.2217\/nmt-2019-0002"],"URL":"https:\/\/doi.org\/10.2217\/nmt-2019-0002","relation":{},"ISSN":["1758-2024","1758-2032"],"issn-type":[{"value":"1758-2024","type":"print"},{"value":"1758-2032","type":"electronic"}],"subject":[],"published":{"date-parts":[[2019,6]]},"assertion":[{"value":"The publishing and review policy for this title is described in its Aims & Scope.","order":1,"name":"peerreview_statement","label":"Peer Review Statement"},{"value":"http:\/\/www.tandfonline.com\/action\/journalInformation?show=aimsScope&journalCode=inmt20","URL":"http:\/\/www.tandfonline.com\/action\/journalInformation?show=aimsScope&journalCode=inmt20","order":2,"name":"aims_and_scope_url","label":"Aim & Scope"},{"value":"2019-01-17","order":0,"name":"received","label":"Received","group":{"name":"publication_history","label":"Publication History"}},{"value":"2019-04-02","order":1,"name":"accepted","label":"Accepted","group":{"name":"publication_history","label":"Publication History"}},{"value":"2019-06-05","order":2,"name":"published","label":"Published","group":{"name":"publication_history","label":"Publication History"}}]}}