{"status":"ok","message-type":"work","message-version":"1.0.0","message":{"indexed":{"date-parts":[[2025,12,31]],"date-time":"2025-12-31T12:16:46Z","timestamp":1767183406657},"reference-count":22,"publisher":"Informa UK Limited","issue":"5","funder":[{"name":"NIH K08","award":["NS083739"],"award-info":[{"award-number":["NS083739"]}]}],"content-domain":{"domain":[],"crossmark-restriction":false},"short-container-title":["Regen. Med."],"published-print":{"date-parts":[[2013,9]]},"DOI":"10.2217\/rme.13.46","type":"journal-article","created":{"date-parts":[[2013,9,2]],"date-time":"2013-09-02T13:42:59Z","timestamp":1378129379000},"page":"527-529","source":"Crossref","is-referenced-by-count":5,"title":["Prospects for Stem Cell Therapy in Neuronal Ceroid Lipofuscinosis"],"prefix":"10.1080","volume":"8","author":[{"given":"Michael C","family":"Kruer","sequence":"first","affiliation":[{"name":"Sanford Children\u2018s Health Research Center, Sioux Falls, SD57104, USA."}],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"David A","family":"Pearce","sequence":"additional","affiliation":[{"name":"Sanford Children\u2018s Health Research Center, Sioux Falls, SD57104, USA."}],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"Paul J","family":"Orchard","sequence":"additional","affiliation":[{"name":"University of Minnesota, Minneapolis, MN55455, USA"}],"role":[{"role":"author","vocabulary":"crossref"}]},{"given":"Robert D","family":"Steiner","sequence":"additional","affiliation":[{"name":"Oregon Health & Science University, Portland, OR97239, USA"},{"name":"Marshfield Clinic Research Foundation, Marshfield, WI54449, USA"}],"role":[{"role":"author","vocabulary":"crossref"}]}],"member":"301","published-online":{"date-parts":[[2013,9,2]]},"reference":[{"key":"e_1_3_2_2_1_1","doi-asserted-by":"publisher","DOI":"10.1016\/j.bbadis.2013.01.019"},{"key":"e_1_3_2_2_2_1","doi-asserted-by":"publisher","DOI":"10.1016\/S0065-2660(01)45002-4"},{"key":"e_1_3_2_2_3_1","doi-asserted-by":"publisher","DOI":"10.3171\/2013.3.PEDS12397"},{"key":"e_1_3_2_2_4_1","doi-asserted-by":"publisher","DOI":"10.1053\/ejpn.2000.0460"},{"key":"e_1_3_2_2_5_1","doi-asserted-by":"publisher","DOI":"10.1016\/j.bbadis.2006.08.010"},{"key":"e_1_3_2_2_6_1","unstructured":"Vieira C LucenaR. Use of cyclodextrin in two Brazilian girls with Niemann-pick type C \u2013 intrathecal report. Presented at: 2012 Michael Marcia and Christa Parseghian Scientific Conference for Niemann-Pick Type C Research. University of Notre Dame IN USA 7\u20139 June 2012."},{"key":"e_1_3_2_2_7_1","doi-asserted-by":"publisher","DOI":"10.1126\/scitranslmed.3004373"},{"key":"e_1_3_2_2_8_1","doi-asserted-by":"publisher","DOI":"10.1038\/sj.gt.3302549"},{"key":"e_1_3_2_2_9_1","doi-asserted-by":"publisher","DOI":"10.1016\/j.stem.2009.05.022"},{"key":"e_1_3_2_2_10_1","doi-asserted-by":"publisher","DOI":"10.1002\/ana.23545"},{"key":"e_1_3_2_2_11_1","doi-asserted-by":"publisher","DOI":"10.1182\/blood-2011-01-329235"},{"key":"e_1_3_2_2_12_1","doi-asserted-by":"publisher","DOI":"10.1126\/science.1171242"},{"key":"e_1_3_2_2_13_1","doi-asserted-by":"publisher","DOI":"10.1016\/j.celrep.2012.08.024"},{"key":"e_1_3_2_2_14_1","doi-asserted-by":"publisher","DOI":"10.1002\/emmm.201202176"},{"key":"e_1_3_2_2_15_1","doi-asserted-by":"publisher","DOI":"10.1038\/nm1746"},{"key":"e_1_3_2_2_16_1","doi-asserted-by":"publisher","DOI":"10.1371\/journal.pone.0038310"},{"key":"e_1_3_2_2_17_1","doi-asserted-by":"publisher","DOI":"10.1016\/j.nbd.2006.09.005"},{"key":"e_1_3_2_2_18_1","doi-asserted-by":"publisher","DOI":"10.1093\/hmg\/dds038"},{"key":"e_1_3_2_2_19_1","doi-asserted-by":"publisher","DOI":"10.1016\/j.expneurol.2009.01.022"},{"key":"e_1_3_2_2_20_1","doi-asserted-by":"publisher","DOI":"10.1093\/hmg\/11.12.1421"},{"key":"e_1_3_2_2_21_1","doi-asserted-by":"publisher","DOI":"10.1016\/j.jneuroim.2010.08.024"},{"key":"e_1_3_2_3_2_1","unstructured":"ClinicalTrials.govs http:\/\/clinicaltrials.gov"}],"container-title":["Regenerative Medicine"],"original-title":[],"language":"en","link":[{"URL":"https:\/\/www.tandfonline.com\/doi\/pdf\/10.2217\/rme.13.46","content-type":"unspecified","content-version":"vor","intended-application":"similarity-checking"}],"deposited":{"date-parts":[[2024,5,17]],"date-time":"2024-05-17T21:37:22Z","timestamp":1715981842000},"score":1,"resource":{"primary":{"URL":"https:\/\/www.tandfonline.com\/doi\/full\/10.2217\/rme.13.46"}},"subtitle":[],"short-title":[],"issued":{"date-parts":[[2013,9]]},"references-count":22,"journal-issue":{"issue":"5","published-print":{"date-parts":[[2013,9]]}},"alternative-id":["10.2217\/rme.13.46"],"URL":"https:\/\/doi.org\/10.2217\/rme.13.46","relation":{},"ISSN":["1746-0751","1746-076X"],"issn-type":[{"value":"1746-0751","type":"print"},{"value":"1746-076X","type":"electronic"}],"subject":[],"published":{"date-parts":[[2013,9]]}}}