{"status":"ok","message-type":"work","message-version":"1.0.0","message":{"indexed":{"date-parts":[[2026,7,23]],"date-time":"2026-07-23T03:43:44Z","timestamp":1784778224200,"version":"3.55.0"},"reference-count":41,"publisher":"SAGE Publications","issue":"3","content-domain":{"domain":[],"crossmark-restriction":false},"short-container-title":["PRM"],"published-print":{"date-parts":[[2021,9,28]]},"abstract":"<jats:p>PURPOSE: The purpose of this study was to examine the psychometric properties of the Pediatric Evaluation of Disability Inventory-Computer Adaptive Test (PEDI-CAT) in children and youth with Spinal Muscular Atrophy (SMA). METHODS: In this prospective cross-sectional study, caregivers of children and youth with SMA completed the PEDI-CAT Daily Activities and Mobility domains. A subset of caregivers completed a questionnaire about the measure. RESULTS: Mean ranks of scaled scores for Daily Activities (n\u200a=\u200a96) and Mobility (n\u200a=\u200a95) domains were significantly different across the three SMA types and across the three motor classifications. Normative scores indicated that 85 participants (89.5%) had limitations in Mobility and 51 in Daily Activities (53.1%). Floor effects were observed in\u226410.4% of the sample for Daily Activities and Mobility. On average, caregivers completed the Mobility domain in 5.4 minutes and the Daily Activities domain in 3.3 minutes. Most caregivers reported that they provided meaningful information (92.1%), were willing to use the PEDI-CAT format again (79%), and suggested adding content including power wheelchair mobility items. CONCLUSION: Convergent validity was demonstrated for the Daily Activities and Mobility domains. Normative scores detected limitations in Mobility and Daily Activity performance for most participants with SMA. The PEDI-CATwas feasible to administer and caregivers expressed willingness to complete the PEDI-CAT in the future.<\/jats:p>","DOI":"10.3233\/prm-190664","type":"journal-article","created":{"date-parts":[[2021,7,16]],"date-time":"2021-07-16T10:27:30Z","timestamp":1626431250000},"page":"451-461","source":"Crossref","is-referenced-by-count":8,"title":["Psychometric properties of the PEDI-CAT for children and youth with spinal muscular atrophy"],"prefix":"10.1177","volume":"14","author":[{"given":"Maria","family":"Fragala-Pinkham","sequence":"first","affiliation":[{"name":"Research Center, Franciscan Children\u2019s Hospital, Brighton, MA, USA"},{"name":"Department of Physical Therapy and Occupational Therapy Services, Boston Children\u2019s Hospital, Boston, MA, USA"}],"role":[{"vocabulary":"crossref","role":"author"}]},{"given":"Amy","family":"Pasternak","sequence":"additional","affiliation":[{"name":"Department of Physical Therapy and Occupational Therapy Services, Boston 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